SARC016: Study of Everolimus With Bevacizumab to Treat Refractory Malignant Peripheral Nerve Sheath Tumors

NCT ID: NCT01661283

Last Updated: 2019-03-06

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

25 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-09-30

Study Completion Date

2017-12-31

Brief Summary

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To determine the clinical response rate of everolimus in combination with bevacizumab for patients with chemotherapy refractory sporadic or neurofibromatosis type 1 (NF1) associated malignant peripheral nerve sheath tumor (MPNST). To evaluate the toxicity and safety of everolimus in combination with bevacizumab in individuals with MPNST

Detailed Description

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Conditions

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Malignant Peripheral Nerve Sheath Tumors MPNST Sarcoma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A

All patients with MPNST will continue everolimus 10 mg daily and bevacizumab 10 mg/kg dose every 14 days

Group Type EXPERIMENTAL

everolimus

Intervention Type DRUG

10 mg tablet once daily

bevacizumab

Intervention Type DRUG

10 mg/kg dose every 14 days

Interventions

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everolimus

10 mg tablet once daily

Intervention Type DRUG

bevacizumab

10 mg/kg dose every 14 days

Intervention Type DRUG

Other Intervention Names

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Afinitor, everolimus Avastin

Eligibility Criteria

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Inclusion Criteria

* Patients 18 or older
* Unresectable or metastatic sporadic or NF1 associated high-grade MPNST
* Experienced progression after one or more prior regimens of cytotoxic chemotherapy
* Patients must be able to swallow tablets
* Patients must have measurable disease, defined as at least one tumor that is measurable
* Patients who develop a recurrence or progression (WHO criteria) of an MPNST in a previously radiated field may be enrolled if it has been at least 4 weeks since the last dose of radiation therapy
* Patients must have recovered from the toxic effects of all prior therapy before entering this study
* Adequate organ function
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1, or 2
* Patents who received an anthracycline prior to enrollment must have an ejection fraction ≥ 50%
* Subjects of childbearing potential requires acceptable form of birth control
* Informed consent

Exclusion Criteria

* Patients currently receiving anticancer therapies or who have received anticancer therapies within 3 weeks of the start of study drug or patients receiving prior treatment with investigational drugs 4 weeks of the start of study drug
* Patients may not be currently receiving strong inhibitors of CYP3A4, and may not have received these medications within 1 week of entry
* Prior radiotherapy within 4 weeks of the start of study drug
* Patients who have had a major surgery or significant traumatic injury within 4 weeks of start of study drug,
* Patients who have not recovered from the side effects of any major surgery
* Patients that may require major surgery during the course of the study
* Less than 7 days have passed from core biopsies or other minor surgical procedures excluding placement of a vascular access device
* Patients receiving chronic, systemic treatment with corticosteroids or another immunosuppressive agent(Topical or inhaled corticosteroids are allowed)
* Uncontrolled brain or leptomeningeal metastases, including patients who continue to require glucocorticoids for brain or leptomeningeal metastases
* Other malignancies within the past 3 years except for adequately treated carcinoma of the cervix or basal or squamous cell carcinomas of the skin
* Patients who have any severe and/or uncontrolled medical conditions or other conditions that could affect their participation in the study
* Female patients who are pregnant or breast feeding
* Patients who have received prior treatment with an mTOR inhibitor or bevacizumab
* Patients with known hypersensitivity to rapamycins
* concurrent use of anti-coagulant drugs
* Patients using Seville orange, star fruit, grapefruit and their juices, and St. John's Wort
* Patients taking enzyme inducing anticonvulsants
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role collaborator

Genentech, Inc.

INDUSTRY

Sponsor Role collaborator

United States Department of Defense

FED

Sponsor Role collaborator

Sarcoma Alliance for Research through Collaboration

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Brigitte C. Widemann, MD

Role: PRINCIPAL_INVESTIGATOR

National Cancer Institute (NCI)

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

Ann and Robert Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status

University of Iowa

Iowa City, Iowa, United States

Site Status

Johns Hopkins

Baltimore, Maryland, United States

Site Status

National Cancer Institute

Bethesda, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

University of Michigan

Ann Arbor, Michigan, United States

Site Status

Washington University in St. Louis

St Louis, Missouri, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Pennsylvania Oncology Hematology Associates

Philadelphia, Pennsylvania, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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SARC016

Identifier Type: -

Identifier Source: org_study_id

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