Everolimus and Octreotide in Patients With Advanced Carcinoid Tumor

NCT ID: NCT00412061

Last Updated: 2014-11-21

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

429 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-12-31

Study Completion Date

2013-06-30

Brief Summary

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The purpose of this study was to evaluate whether everolimus 10 mg / day added to treatment with depot octreotide prolongs progression free survival compared to treatment with octreotide alone in patients with advanced carcinoid tumor.

Detailed Description

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Conditions

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Carcinoid Tumor Malignant Carcinoid Syndrome

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Octreotide+ Everolimus

Everolimus was administered in accordance with a 10-mg daily dosing regimen (two 5-mg tablets) in conjunction with octreotide 30 mg intramuscularly (i.m.) every 28 days. Patients were treated until progression or unacceptable toxicity. Each treatment cycle lasted 28 days. Patients received their first dose of everolimus at Cycle 1, Day 1. Administration of octreotide was performed every 28 days (± 4 days) starting on Cycle 1, Day 1.

Group Type EXPERIMENTAL

Octreotide

Intervention Type DRUG

Octreotide 30 mg intramuscularly (i.m.) every 28 days.

Everolimus

Intervention Type DRUG

A 10-mg oral daily dosing regimen (two 5-mg tablets) of everolimus.

Octreotide+ Placebo

Matching placebo was administered in accordance with a 10-mg daily dosing regimen (two 5-mg tablets) in conjunction with octreotide 30 mg intramuscularly (i.m.) every 28 days. Patients were treated until progression or unacceptable toxicity; Each treatment cycle lasted 28 days. Patients received their first dose of matching placebo at Cycle 1, Day 1. Administration of octreotide was performed every 28 days (± 4 days) starting on Cycle 1 Day 1.

Group Type PLACEBO_COMPARATOR

Octreotide

Intervention Type DRUG

Octreotide 30 mg intramuscularly (i.m.) every 28 days.

Placebo

Intervention Type DRUG

A 10-mg oral daily dosing regimen (two 5-mg tablets) of matching placebo.

Interventions

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Octreotide

Octreotide 30 mg intramuscularly (i.m.) every 28 days.

Intervention Type DRUG

Placebo

A 10-mg oral daily dosing regimen (two 5-mg tablets) of matching placebo.

Intervention Type DRUG

Everolimus

A 10-mg oral daily dosing regimen (two 5-mg tablets) of everolimus.

Intervention Type DRUG

Other Intervention Names

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Sandostatin LAR® Depot RAD001

Eligibility Criteria

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Inclusion Criteria

* Advanced (unresectable or metastatic) carcinoid tumor
* Confirmed low-grade or intermediate-grade neuroendocrine carcinoma
* Documented progression of disease within 12 months prior to randomization.
* Measurable disease determined by triphasic computer tomography (CT) scan or magnetic resonance imaging (MRI).

Exclusion Criteria

* Poorly differentiated neuroendocrine carcinoma, high-grade neuroendocrine carcinoma, adenocarcinoid, goblet cell carcinoma, or small cell carcinoma.
* Hepatic artery embolization within the last 6 months or cryoablation of hepatic metastasis within 2 months of enrollment.
* Previous treatment with mammalian target of rapamycin (mTOR) inhibitors (sirolimus, temsirolimus, everolimus)
* Intolerance or hypersensitivity to octreotide, everolimus, or other rapamycins.
* Severe or uncontrolled medical conditions
* Chronic treatment with corticosteroids or other immunosuppressive agent.
* Other primary cancer within 3 years.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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University of Arizona / Arizona Cancer Center Deptof Uof A/Arizona Cancer(2)

Tucson, Arizona, United States

Site Status

Highlands Oncology Group The Center for Chest Care

Fayetteville, Arkansas, United States

Site Status

Hematology Oncology Services of Arkansas

Little Rock, Arkansas, United States

Site Status

Pacific Cancer Medical Center, Inc.

Anaheim, California, United States

Site Status

Cedars Sinai Medical Center SC-2

Los Angeles, California, United States

Site Status

University of California at Los Angeles UCLA New SC Address

Los Angeles, California, United States

Site Status

University of Colorado Dept. of Univ. of Colorado

Aurora, Colorado, United States

Site Status

Rocky Mountain Cancer Centers Dept of Rocky Mountain (2)

Denver, Colorado, United States

Site Status

Eastern Connecticut Hematology & Oncology Associates Dept. of ECHO

Norwich, Connecticut, United States

Site Status

Cancer Centers of Connecticut Southington Location

Southington, Connecticut, United States

Site Status

Hematology Oncology PC Dept.of Hematology Oncology(2)

Stamford, Connecticut, United States

Site Status

Ocala Oncology Center Dept. of Ocala Oncology Center

Ocala, Florida, United States

Site Status

Cancer Care and Hematology Specialists of Chicagoland Niles

Niles, Illinois, United States

Site Status

Indiana University Dept.of IndianaUniv.CancerCtr

Indianapolis, Indiana, United States

Site Status

Central Indiana Cancer Centers CICC - South

Indianapolis, Indiana, United States

Site Status

University of Iowa Medical Center Internal Medicine

Iowa City, Iowa, United States

Site Status

University of Kansas Cancer Center Deptof Uof Kansas CancerCenter

Kansas City, Kansas, United States

Site Status

Kansas City Cancer Center KCCC Business Office

Overland Park, Kansas, United States

Site Status

Norton Cancer Institute Clinical Research Program

Louisville, Kentucky, United States

Site Status

LSU HEALTH SCIENCES CENTER/ LSU SCHOOL OF MEDICINE Deptof LSU Health Sciences (2)

New Orleans, Louisiana, United States

Site Status

Mayo Clinic - Rochester Division of Hematology

Rochester, Minnesota, United States

Site Status

Washington University School Of Medicine-Siteman Cancer Ctr Division of Oncology

St Louis, Missouri, United States

Site Status

The Center for Cancer Care and Research

St Louis, Missouri, United States

Site Status

Dartmouth Hitchcock Medical Center Medical Oncology

Lebanon, New Hampshire, United States

Site Status

New York Oncology Hematology, P.C. Dept. of New York Oncology. PC

Albany, New York, United States

Site Status

New York University Medical Center NYU Medical Center (2)

New York, New York, United States

Site Status

Duke University Medical Center Dept. of Duke Cancer Center

Durham, North Carolina, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Cancer Centers of the Carolinas CC of C -Eastside

Greenville, South Carolina, United States

Site Status

Texas Oncology, P.A. Central Austin Cancer Center

Austin, Texas, United States

Site Status

South Texas Institute of Cancer S. Tex Inst.- Corpus Christi

Corpus Christi, Texas, United States

Site Status

Sammons Cancer Center - Texas Oncology Sammons Cancer Center (SC)

Dallas, Texas, United States

Site Status

Texas Oncology, P.A. Forth Worth -- 12th Avenue

Fort Worth, Texas, United States

Site Status

University of Texas/MD Anderson Cancer Center Gastrointestinal Med. Oncology

Houston, Texas, United States

Site Status

Tyler Cancer Center

Tyler, Texas, United States

Site Status

Virginia Oncology Associates VOA - Lake Wright

Norfolk, Virginia, United States

Site Status

Northwest Cancer Specialists Compass Oncology -BKM

Vancouver, Washington, United States

Site Status

University of Wisconsin / Paul P. Carbone Comp Cancer Center GI Oncology Research Center

Madison, Wisconsin, United States

Site Status

Novartis Investigative Site

Kogarah, New South Wales, Australia

Site Status

Novartis Investigative Site

Herston, Queensland, Australia

Site Status

Novartis Investigative Site

South Brisbane, Queensland, Australia

Site Status

Novartis Investigative Site

Brussels, , Belgium

Site Status

Novartis Investigative Site

London, Ontario, Canada

Site Status

Novartis Investigative Site

Toronto, Ontario, Canada

Site Status

Novartis Investigative Site

Montreal, Quebec, Canada

Site Status

Novartis Investigative Site

Montreal, Quebec, Canada

Site Status

Novartis Investigative Site

Prague, Czech Republic, Czechia

Site Status

Novartis Investigative Site

Příbram, , Czechia

Site Status

Novartis Investigative Site

Helsinki, , Finland

Site Status

Novartis Investigative Site

Strasbourg, France, France

Site Status

Novartis Investigative Site

Clichy Cédex, , France

Site Status

Novartis Investigative Site

Lille, , France

Site Status

Novartis Investigative Site

Montpellier, , France

Site Status

Novartis Investigative Site

Paris, , France

Site Status

Novartis Investigative Site

Toulouse, , France

Site Status

Novartis Investigative Site

Villejuif, , France

Site Status

Novartis Investigative Site

Berlin, , Germany

Site Status

Novartis Investigative Site

Hamburg, , Germany

Site Status

Novartis Investigative Site

Athens, Greece, Greece

Site Status

Novartis Investigative Site

Bologna, BO, Italy

Site Status

Novartis Investigative Site

Milan, MI, Italy

Site Status

Novartis Investigative Site

Milan, MI, Italy

Site Status

Novartis Investigative Site

Perugia, PG, Italy

Site Status

Novartis Investigative Site

Pisa, PI, Italy

Site Status

Novartis Investigative Site

Groningen, , Netherlands

Site Status

Novartis Investigative Site

Rotterdam, , Netherlands

Site Status

Novartis Investigative Site

Bratislava, Slovak Republic, Slovakia

Site Status

Novartis Investigative Site

Madrid, Madrid, Spain

Site Status

Novartis Investigative Site

Uppsala, , Sweden

Site Status

Novartis Investigative Site

Basingstoke, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada Czechia Finland France Germany Greece Italy Netherlands Slovakia Spain Sweden United Kingdom

References

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Pavel ME, Baudin E, Oberg KE, Hainsworth JD, Voi M, Rouyrre N, Peeters M, Gross DJ, Yao JC. Efficacy of everolimus plus octreotide LAR in patients with advanced neuroendocrine tumor and carcinoid syndrome: final overall survival from the randomized, placebo-controlled phase 3 RADIANT-2 study. Ann Oncol. 2017 Jul 1;28(7):1569-1575. doi: 10.1093/annonc/mdx193.

Reference Type DERIVED
PMID: 28444114 (View on PubMed)

Fazio N, Granberg D, Grossman A, Saletan S, Klimovsky J, Panneerselvam A, Wolin EM. Everolimus plus octreotide long-acting repeatable in patients with advanced lung neuroendocrine tumors: analysis of the phase 3, randomized, placebo-controlled RADIANT-2 study. Chest. 2013 Apr;143(4):955-962. doi: 10.1378/chest.12-1108.

Reference Type DERIVED
PMID: 23187897 (View on PubMed)

Pavel ME, Hainsworth JD, Baudin E, Peeters M, Horsch D, Winkler RE, Klimovsky J, Lebwohl D, Jehl V, Wolin EM, Oberg K, Van Cutsem E, Yao JC; RADIANT-2 Study Group. Everolimus plus octreotide long-acting repeatable for the treatment of advanced neuroendocrine tumours associated with carcinoid syndrome (RADIANT-2): a randomised, placebo-controlled, phase 3 study. Lancet. 2011 Dec 10;378(9808):2005-2012. doi: 10.1016/S0140-6736(11)61742-X. Epub 2011 Nov 25.

Reference Type DERIVED
PMID: 22119496 (View on PubMed)

Related Links

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http://www.novartisclinicaltrials.com

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Other Identifiers

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2006-004507-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CRAD001C2325

Identifier Type: -

Identifier Source: org_study_id