Randomized Switch Study From Hydroxyurea to Ruxolitinib for RELIEF of Polycythemia Vera Symptoms: The Relief Study

NCT ID: NCT01632904

Last Updated: 2017-11-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

110 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-06-30

Study Completion Date

2016-05-31

Brief Summary

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The purpose of the RELIEF study is to compare symptoms in polycythemia vera (PV) subjects treated with ruxolitinib versus subjects treated with hydroxyurea (HU) as measured by the percent of subjects who achieve a clinically meaningful symptom improvement (ie, total symptom score reduction of ≥ 50% reduction) at Week 16 compared to Baseline. The study is also designed to demonstrate that these responses are durable with continued treatment.

Detailed Description

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This is a Phase 3 multicenter, double-blind, double-dummy, randomized study. Only subjects with PV who have received HU for at least 12 weeks, have been receiving a stable dose before screening, and still have symptoms related to PV will be enrolled.

Subjects will be randomized (1:1) to 1 of 2 treatment arms:

A: ruxolitinib and HU-placebo B: HU and ruxolitinib-placebo

Subjects randomized to either arm may be eligible to transition to open-label ruxolitinib after Week 16.

Conditions

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Polycythemia Vera

Keywords

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Polycythemia Vera PV

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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ruxolitinib and hydroxyurea (HU)-placebo

Group Type EXPERIMENTAL

Ruxolitinib

Intervention Type DRUG

Ruxolitinib will be orally self-administered at a starting dose of 10 mg (two 5 mg tablets) twice a day. Dose increases of 5 mg (1 tablet) in twice-daily increments are permitted after 4 weeks and again after 8 weeks of therapy for subjects who meet prespecified criteria for inadequate efficacy.

HU-placebo

Intervention Type DRUG

All placebo will be self-administered, and dosing will be the same as with the blinded dose.

When adjustments are made to the ruxolitinib dose, the dose of HU-placebo will be adjusted concurrently.

HU and ruxolitinib-placebo

Group Type ACTIVE_COMPARATOR

Hydroxyurea (HU)

Intervention Type DRUG

Hydroxyurea (500 mg capsules) will be orally self-administered at the dose that the subject was receiving previously. The dose may be increased after 4 weeks and again after 8 weeks of therapy to optimize efficacy for subjects meeting prespecified criteria.

Ruxolitinib-placebo

Intervention Type DRUG

All placebo will be self-administered, and dosing will be the same as with the blinded dose.

When adjustments are made to the HU dose, the dose of ruxolitinib-placebo will be adjusted concurrently.

Interventions

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Ruxolitinib

Ruxolitinib will be orally self-administered at a starting dose of 10 mg (two 5 mg tablets) twice a day. Dose increases of 5 mg (1 tablet) in twice-daily increments are permitted after 4 weeks and again after 8 weeks of therapy for subjects who meet prespecified criteria for inadequate efficacy.

Intervention Type DRUG

Hydroxyurea (HU)

Hydroxyurea (500 mg capsules) will be orally self-administered at the dose that the subject was receiving previously. The dose may be increased after 4 weeks and again after 8 weeks of therapy to optimize efficacy for subjects meeting prespecified criteria.

Intervention Type DRUG

HU-placebo

All placebo will be self-administered, and dosing will be the same as with the blinded dose.

When adjustments are made to the ruxolitinib dose, the dose of HU-placebo will be adjusted concurrently.

Intervention Type DRUG

Ruxolitinib-placebo

All placebo will be self-administered, and dosing will be the same as with the blinded dose.

When adjustments are made to the HU dose, the dose of ruxolitinib-placebo will be adjusted concurrently.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subjects must currently be reporting symptoms while on a stable dose of HU monotherapy and be eligible to continue HU on study after randomization.
* Before screening, the subject must have been receiving HU for at least 12 weeks AND be receiving a stable dose.
* Subjects must meet baseline symptom criteria
* Subjects should meet at least 1 of the following criteria:

* No more than 2 phlebotomies within the 6 months before screening OR
* No palpable splenomegaly.
* Subjects must have a hematocrit that can be controlled within 35% to 48% (inclusive) before randomization.

Exclusion Criteria

* Subjects with inadequate liver or renal function at screening.
* Subjects with clinically significant infection that requires therapy
* Subjects with known active hepatitis A, B, or C at screening or with known HIV positivity.
* Subjects with an active malignancy over the previous 2 years
* Subjects with clinically significant cardiac disease (Class III or IV).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Mark Jones, M.D.

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Scottsdale, Arizona, United States

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Fayetteville, Arkansas, United States

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Burbank, California, United States

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Glendale, California, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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San Diego, California, United States

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Aurora, Colorado, United States

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Stamford, Connecticut, United States

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Washington D.C., District of Columbia, United States

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Boynton Beach, Florida, United States

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Orlando, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Niles, Illinois, United States

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Springfield, Illinois, United States

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Ames, Iowa, United States

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Westwood, Kansas, United States

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Alexandria, Louisiana, United States

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Baltimore, Maryland, United States

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Southfield, Michigan, United States

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Minneapolis, Minnesota, United States

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Columbia, Missouri, United States

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St Louis, Missouri, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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East Orange, New Jersey, United States

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Morristown, New Jersey, United States

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Somerville, New Jersey, United States

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Albany, New York, United States

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Armonk, New York, United States

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Mineola, New York, United States

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New York, New York, United States

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Canton, Ohio, United States

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Bethlehem, Pennsylvania, United States

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Charleston, South Carolina, United States

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Chattanooga, Tennessee, United States

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Amarillo, Texas, United States

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Bedford, Texas, United States

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Dallas, Texas, United States

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Garland, Texas, United States

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Houston, Texas, United States

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Longview, Texas, United States

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Midland, Texas, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Tyler, Texas, United States

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Salt Lake City, Utah, United States

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Alexandria, Virginia, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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Antwerp, , Belgium

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Bruges, , Belgium

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Aachen, , Germany

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Berlin, , Germany

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Freiburg im Breisgau, , Germany

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Hamburg, , Germany

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Stuttgart, , Germany

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Ulm, , Germany

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Galway, , Ireland

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Florence, , Italy

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Reggio Calabria, , Italy

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Varese, , Italy

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Barcelona, , Spain

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Pamplona, , Spain

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Salamanca, , Spain

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Boston, , United Kingdom

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Leicester, , United Kingdom

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Nottingham, , United Kingdom

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West Bromwich, , United Kingdom

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Countries

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United States Belgium Germany Ireland Italy Spain United Kingdom

Other Identifiers

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18424-357

Identifier Type: -

Identifier Source: org_study_id