Efficacy and Safety of BEZ235 Compared to Everolimus in Patients With Advanced Pancreatic Neuroendocrine Tumors

NCT ID: NCT01628913

Last Updated: 2016-04-07

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

62 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-10-31

Study Completion Date

2014-09-30

Brief Summary

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This was a multicenter, open label, randomized phase II study to evaluate the efficacy and safety of BEZ235 as compared to everolimus in patients with advanced, low to intermediate grade pancreatic neuroendocrine tumor (pNET).

Detailed Description

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Patients with advanced (unresectable or metastatic), low to intermediate grade (histologically confirmed well and moderately differentiated) pancreatic neuroendocrine tumor (pNET) were randomized to either BEZ235 or everolimus. The study was planned to include 140 patients, with 70 patients in the BEZ235 treatment group and 70 patients in the everolimus treatment group. An interim analysis was conducted on 62 randomized patients. The study was terminated as the BEZ235 treatment did not demonstrate a progression free survival advantage to everolimus treatment.

Conditions

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Pancreatic Neuroendocrine Tumors (pNET)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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BEZ235

Patients received BEZ235 400 mg bid p.o. (by mouth, twice daily)

Group Type EXPERIMENTAL

BEZ235

Intervention Type DRUG

BEZ235 400 mg bid p.o. (by mouth, twice daily)

Everolimus

Patients received Everolimus 10 mg qd p.o. (by mouth, daily)

Group Type ACTIVE_COMPARATOR

Everolimus

Intervention Type DRUG

Everolimus 10 mg qd p.o. (by mouth, daily)

Interventions

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BEZ235

BEZ235 400 mg bid p.o. (by mouth, twice daily)

Intervention Type DRUG

Everolimus

Everolimus 10 mg qd p.o. (by mouth, daily)

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Advanced histologically confirmed well differentiated pancreatic neuroendocrine tumor
* Progressive disease within the last 12 months
* Measurable disease per RECIST Version 1.0 determined by multiphase MRI or triphasic CT

Exclusion Criteria

* Prior treatment with mTOR or PI3K inhibitors
* Patients with more than 2 prior systemic treatment regimens
* Previous cytotoxic chemotherapy, targeted therapy, or biotherapy within the last 4 weeks
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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Cedars Sinai Medical Center SC-3

Los Angeles, California, United States

Site Status

University of Colorado Univ Colorado

Aurora, Colorado, United States

Site Status

University of Kentucky Univ Kebtucky

Lexington, Kentucky, United States

Site Status

Montefiore Medical Center SC

The Bronx, New York, United States

Site Status

Novartis Investigative Site

Lyon, , France

Site Status

Novartis Investigative Site

Montpellier, , France

Site Status

Novartis Investigative Site

Paris, , France

Site Status

Novartis Investigative Site

Reims, , France

Site Status

Novartis Investigative Site

Toulouse, , France

Site Status

Novartis Investigative Site

Bologna, BO, Italy

Site Status

Novartis Investigative Site

Pisa, PI, Italy

Site Status

Novartis Investigative Site

Roma, RM, Italy

Site Status

Novartis Investigative Site

Amsterdam, , Netherlands

Site Status

Novartis Investigative Site

Groningen, , Netherlands

Site Status

Novartis Investigative Site

Kazan', , Russia

Site Status

Novartis Investigative Site

Seville, Andalusia, Spain

Site Status

Novartis Investigative Site

Barcelona, Catalonia, Spain

Site Status

Novartis Investigative Site

L'Hospitalet de Llobregat, Catalonia, Spain

Site Status

Novartis Investigative Site

Madrid, Madrid, Spain

Site Status

Novartis Investigative Site

Madrid, Madrid, Spain

Site Status

Novartis Investigative Site

Lucerne, , Switzerland

Site Status

Novartis Investigative Site

Glasgow, , United Kingdom

Site Status

Novartis Investigative Site

London, , United Kingdom

Site Status

Novartis Investigative Site

London, , United Kingdom

Site Status

Novartis Investigative Site

Manchester, , United Kingdom

Site Status

Novartis Investigative Site

Sheffield, , United Kingdom

Site Status

Countries

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United States France Italy Netherlands Russia Spain Switzerland United Kingdom

References

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Salazar R, Garcia-Carbonero R, Libutti SK, Hendifar AE, Custodio A, Guimbaud R, Lombard-Bohas C, Ricci S, Klumpen HJ, Capdevila J, Reed N, Walenkamp A, Grande E, Safina S, Meyer T, Kong O, Salomon H, Tavorath R, Yao JC. Phase II Study of BEZ235 versus Everolimus in Patients with Mammalian Target of Rapamycin Inhibitor-Naive Advanced Pancreatic Neuroendocrine Tumors. Oncologist. 2018 Jul;23(7):766-e90. doi: 10.1634/theoncologist.2017-0144. Epub 2017 Dec 14.

Reference Type DERIVED
PMID: 29242283 (View on PubMed)

Other Identifiers

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CBEZ235Z2401

Identifier Type: OTHER

Identifier Source: secondary_id

2012-000769-19

Identifier Type: -

Identifier Source: secondary_id

CBEZ235Z2401

Identifier Type: -

Identifier Source: org_study_id

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