Safety/Efficacy of Everolimus in Adults With Advanced Pancreatic Neuroendocrine Cancer Not Responsive to Chemotherapy

NCT ID: NCT00363051

Last Updated: 2013-05-10

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

160 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-06-30

Study Completion Date

2012-04-30

Brief Summary

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The purpose of this study was to assess the efficacy and safety of everolimus in the treatment of advanced pancreatic neuroendocrine tumor (NET) not responsive to cytotoxic chemotherapy. All patients were treated with everolimus until either tumor progression was documented using a standard criteria that measures tumor size called Response Evaluation Criteria in Solid tumors (RECIST), or until unacceptable toxicity occurred, or until the patient or investigator requested discontinuation of treatment.

Detailed Description

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This was a stratified two-stage, single-arm, phase 2 study of treatment with everolimus in patients with advanced (unresectable or metastatic) pancreatic neuroendocrine tumor (NET) after failure of cytotoxic chemotherapy.

Stratum 1, consisted of patients not receiving chronic Octreotide Depot therapy, will receive everolimus monotherapy at 10 mg/day.

Stratum 2, consisting of patients with tumors that have progressed during Octreotide Depot treatment will continue their entry dose of Octreotide Depot plus everolimus 10 mg/day.

Conditions

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Islet Cell Carcinoma Neuroendocrine Carcinoma Neuroendocrine Tumor Pancreatic Neoplasms

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Everolimus 10 mg

Stratum 1 patients who were not receiving regular Octreotide Depot therapy. These patients were to receive everolimus monotherapy at 10 mg/day.

Stratum 2 patients who were to receive everolimus 10 mg/day in addition to continuing their entry dose of Octreotide Depot therapy.

Patients were instructed to take two 5 mg tablets of everolimus orally with a glass of water, once daily (preferably in the morning). Dosing was strongly recommended to occur at the same time every day.

Group Type EXPERIMENTAL

Everolimus 10 mg

Intervention Type DRUG

Participants took two 5 mg tablets of Everolimus orally with a glass of water, once daily (preferably in the morning) in a fasting state or after no more than a light, fat-free meal. Dosing was to occur at the same time each day. If vomiting occurred, the vomited dose was not to be replaced.

Octreotide Depot

Intervention Type DRUG

Interventions

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Everolimus 10 mg

Participants took two 5 mg tablets of Everolimus orally with a glass of water, once daily (preferably in the morning) in a fasting state or after no more than a light, fat-free meal. Dosing was to occur at the same time each day. If vomiting occurred, the vomited dose was not to be replaced.

Intervention Type DRUG

Octreotide Depot

Intervention Type DRUG

Other Intervention Names

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RAD001

Eligibility Criteria

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Inclusion Criteria

* Advanced (unresectable or metastatic) biopsy-proven pancreatic Neuroendocrine tumor (NET)
* Confirmed low-grade or intermediate-grade neuroendocrine carcinoma
* Objective disease progression by Response Evaluation Criteria in Solid tumors (RECIST) criteria while receiving cytotoxic chemotherapy or at any time after receiving an adequate course of cytotoxic chemotherapy (i.e., at least 3 consecutive cycles or months of treatment with the same cytotoxic drug or regimen)
* Presence of at least one measurable disease using RECIST criteria at screening (computer tomography \[CT\] or Magnetic resonance imaging \[MRI\])
* Adequate bone marrow, liver and kidney function
* WHO Performance Status 0-2.


* Receiving treatment (at least 3 consecutive months) with Octreotide Depot.
* In addition to documentation of progressive disease on or after chemotherapy, patients in stratum 2 must have documented objective progression of disease while receiving Octreotide Depot.

Exclusion Criteria

* Anticancer therapy within 3 weeks of enrollment.
* Patients with poorly differentiated neuroendocrine carcinoma
* Hepatic artery embolization within the last 6 months
* Prior therapy with everolimus or other rapamycins (sirolimus, temsirolimus)
* Other concurrent malignancy
* Other serious intercurrent infections or nonmalignant uncontrolled medical illnesses

Exclusion Criterion for Stratum 1 only:

• Received treatment with Octreotide Depot or any other long-acting somatostatin analogue in the 60 days prior to enrollment or any short-acting somatostatin analogue in the two weeks prior to enrollment.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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The University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

USC Medical Center

Los Angeles, California, United States

Site Status

Cedars-Sinai Outpatient Cancer Center/Samuel Oschin Comprehensive Cancer Inst.

Los Angeles, California, United States

Site Status

UCLA Medical Center

Los Angeles, California, United States

Site Status

UCSF Comprehensive Cancer Center

San Francisco, California, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

H. Lee Moffit Cancer Center & Research Institute

Tampa, Florida, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

LSUHC Multispecialty Clinic

New Orleans, Louisiana, United States

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Dana Farber Cancer Institute

Boston, Massachusetts, United States

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Mayo Clinic

Rochester, Minnesota, United States

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Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Lynn Ratner, M.D.

New York, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

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Arthur G. James Cancer Hospital/Ohio State University

Columbus, Ohio, United States

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Oregon Health and Science University

Portland, Oregon, United States

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M. D Anderson Cancer Center

Houston, Texas, United States

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Scott & White Memorial Hospital

Temple, Texas, United States

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University of Wisconsin Hospital & Clinics

Madison, Wisconsin, United States

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Novartis Investigative Site

Buenos Aires, , Argentina

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Novartis Investigative Site

Santa Fe, , Argentina

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Novartis Investigative Site

Heidelberg, , Australia

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Novartis Investigative Site

Herston, , Australia

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Novartis Investigative Site

Kogarah, , Australia

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Novartis Investigative Site

Leuven, , Belgium

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Novartis Investigative Site

Vancouver, British Columbia, Canada

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Novartis Investigative Site

Halifax, Nova Scotia, Canada

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Novartis Investigative Site

London, Ontario, Canada

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Novartis Investigative Site

Toronto, Ontario, Canada

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Novartis Investigative Site

Montreal, Quebec, Canada

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Novartis Investigative Site

Billancourt, , France

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Novartis Investigative Site

Clichy, , France

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Novartis Investigative Site

Lyon, , France

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Novartis Investigative Site

Reims, , France

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Novartis Investigative Site

Toulouse, , France

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Novartis Investigative Site

Villejuif, , France

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Novartis Investigative Site

Berlin, , Germany

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Novartis Investigative Site

Erlangen, , Germany

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Novartis Investigative Site

Essen, , Germany

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Novartis Investigative Site

Frankfurt, , Germany

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Novartis Investigative Site

Heidelberg, , Germany

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Novartis Investigative Site

Marburg, , Germany

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Novartis Investigative Site

Ulm, , Germany

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Novartis Investigative Site

Milan, , Italy

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Novartis Investigative Site

Modena, , Italy

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Novartis Investigative Site

Pisa, , Italy

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Novartis Investigative Site

Rome, , Italy

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Novartis Investigative Site

Torrette Di Ancona, , Italy

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Novartis Investigative Site

Gronigen, , Netherlands

Site Status

Novartis Investigative Site

Barcelona, , Spain

Site Status

Novartis Investigative Site

L'Hospitalet de Llobregat, , Spain

Site Status

Novartis Investigative Site

Madrid, , Spain

Site Status

Novartis Investigative Site

Uppsala, , Sweden

Site Status

Countries

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United States Argentina Australia Belgium Canada France Germany Italy Netherlands Spain Sweden

Related Links

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http://www.novartisclinicaltrials.com/webapp/etrials/searchTrial.do?t=i&trialID=525&diseaseID=92

Visit NovartisClinicalTrials.com: Pre-qualify for a trial, and view a list of trials and participating study centers.

Other Identifiers

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CRAD001C2239

Identifier Type: -

Identifier Source: org_study_id

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