Study of TAS-102 in Patients With Metastatic Colorectal Cancer Refractory to Standard Chemotherapies

NCT ID: NCT01607957

Last Updated: 2024-09-19

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

800 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-06-17

Study Completion Date

2016-05-23

Brief Summary

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The purpose of this study is to compare the efficacy and safety of TAS-102 versus placebo in patients with refractory metastatic colorectal cancer.

Detailed Description

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This is a multinational, double-blind, two-arm, parallel, randomized Phase 3 comparison study evaluating the efficacy and safety of TAS-102 versus placebo in patients with refractory metastatic colorectal cancer. Patients will be randomly assigned (2:1) to TAS-102 (experimental arm) or placebo (control arm).

Conditions

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Colorectal Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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TAS-102

Group Type EXPERIMENTAL

TAS-102

Intervention Type DRUG

35 mg/m2/dose, orally, twice daily on days 1-5 and 8-12 of each 28-day cycle. Number of cycles: until at least one of the discontinuation criteria are met.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo tablets, orally, twice daily on days 1-5 and 8-12 of each 28-day cycle. Number of cycles: until at least one of the discontinuation criteria are met.

Interventions

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TAS-102

35 mg/m2/dose, orally, twice daily on days 1-5 and 8-12 of each 28-day cycle. Number of cycles: until at least one of the discontinuation criteria are met.

Intervention Type DRUG

Placebo

Placebo tablets, orally, twice daily on days 1-5 and 8-12 of each 28-day cycle. Number of cycles: until at least one of the discontinuation criteria are met.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Has provided written informed consent
2. Has adenocarcinoma of the colon or rectum
3. Has failed at least 2 prior regimens of standard chemotherapies for metastatic colorectal cancer
4. ECOG performance status of 0 or 1
5. Is able to take medications orally
6. Has adequate organ function (bone marrow, kidney and liver)
7. Women of childbearing potential must have a negative pregnancy test and must agree to adequate birth control if conception is possible. Males must agree to adequate birth control.

Exclusion Criteria

1. Certain serious illnesses or medical condition(s)
2. Has had certain other recent treatment e.g. major surgery, anticancer therapy, extended field radiation, received investigational agent, within the specified time frames prior to study drug administration
3. Has received TAS-102
4. Has unresolved toxicity of greater than or equal to CTCAE Grade 2 attributed to any prior therapies
5. Is a pregnant or lactating female
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Taiho Oncology, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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From - Boston, MA

Role: PRINCIPAL_INVESTIGATOR

Dana-Farber Cancer Institute

From - Leuven, Belgium

Role: PRINCIPAL_INVESTIGATOR

University Hospital, Gasthuisberg

From - Kashiwa, Chiba Japan

Role: PRINCIPAL_INVESTIGATOR

National Cancer Center Hospital East

Locations

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Arizona Center for Cancer Care

Glendale, Arizona, United States

Site Status

California Cancer Associates for Research and Excellence

Fresno, California, United States

Site Status

Ronald H. Yanagihara, MD

Gilroy, California, United States

Site Status

LAC and USC Medical Center

Los Angeles, California, United States

Site Status

USC Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Pacific Hematology Oncology Associates

San Francisco, California, United States

Site Status

San Jose Medical Group

San Jose, California, United States

Site Status

Coastal Integrative Cancer Care

San Luis Obispo, California, United States

Site Status

Yale Cancer Center

New Haven, Connecticut, United States

Site Status

MD Anderson Cancer Center Orlando

Orlando, Florida, United States

Site Status

Illinois Cancer Care, P.C.

Peoria, Illinois, United States

Site Status

Indiana University Simon Cancer Center

Indianapolis, Indiana, United States

Site Status

Mary Bird Perkins Cancer Center

Baton Rouge, Louisiana, United States

Site Status

Ochsner Clinic Fndtn

New Orleans, Louisiana, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

St. Joseph Mercy Hospital

Ann Arbor, Michigan, United States

Site Status

Jefferson City Medical Group

Jefferson City, Missouri, United States

Site Status

Saint Luke's Cancer Institute

Kansas City, Missouri, United States

Site Status

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

Gabrail Cancer Center

Canton, Ohio, United States

Site Status

Hickman Cancer Center at Flower Hospital

Sylvania, Ohio, United States

Site Status

Hematology/Oncology Associates of Fredericksburg

Fredericksburg, Virginia, United States

Site Status

Royal North Shore Hospital

Sydney, New South Wales, Australia

Site Status

The Queen Elisabeth Hospital

Woodville South, South Australia, Australia

Site Status

Austin Hospital

Heidelberg, Victoria, Australia

Site Status

The Royal Melbourne Hospital

Parkville, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Perth, Western Australia, Australia

Site Status

Krankenhaus der Barmherzigen Schwestern Linz

Linz, , Austria

Site Status

Universitaet Wien

Vienna, , Austria

Site Status

Universitaetsklinik fur Innere Medizin

Vienna, , Austria

Site Status

Wilhelminenspital Wien

Vienna, , Austria

Site Status

Klinikum Wels-Grieskirchen GmbH

Wels, , Austria

Site Status

Cliniques Universitaires UCL St. Luc

Brussels, , Belgium

Site Status

Erasme University Hospital-ULB-Brussels

Brussels, , Belgium

Site Status

Grand Hospital de Charleroi

Charleroi, , Belgium

Site Status

Antwerp University Hospital

Edegem, , Belgium

Site Status

University Hospital Gent

Edegem, , Belgium

Site Status

University Hospital Gent

Ghent, , Belgium

Site Status

Leuven University Hospital - Campus Gasthuiseberg

Leuven, , Belgium

Site Status

University Hospital Gasthuisberg

Leuven, , Belgium

Site Status

Klinika onkologie a radioteraie, Facultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

Institute of Oncology and Rehabilitation Ples

Nová Ves pod Pleší, , Czechia

Site Status

CHU de Becançon

Besançon, , France

Site Status

University Hospital of Bordeaux

Bordeaux, , France

Site Status

Centre Oscar Lambret

Lille, , France

Site Status

CRLC Val d'Aurelle

Montpellier, , France

Site Status

Hopital Saint Antoine

Paris, , France

Site Status

Centre Eugene Marquis

Rennes, , France

Site Status

Onkologische Schwerpunktpraxis Kurfuerstendamm

Berlin, , Germany

Site Status

Praxiskooperation Bonn-Euskirchen-Rheinbach

Bonn, , Germany

Site Status

Uniklinik Koeln

Cologne, , Germany

Site Status

Universitatsklinikum Carl Gustav Carus - Dresden

Dresden, , Germany

Site Status

Medizinische Klinik am Krankenhaus Nordwest GmbH

Frankfurt, , Germany

Site Status

Uniklinik der Martin-Luther-Universitaet Halle-Wittenberg

Halle, , Germany

Site Status

Universitätsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Johannes Gutenberg Universität Mainz

Mainz, , Germany

Site Status

Interdisziplinaeres Tumorzentrum Mannheim

Mannheim, , Germany

Site Status

Klinikum der Universität München - Großhadern

München, , Germany

Site Status

Staedtisches Klinikum Muenchen / Klinikum Neuperlach

München, , Germany

Site Status

Klinikum Oldenburg gGmbH

Oldenburg, , Germany

Site Status

Universitaetsklinikum Ulm

Ulm, , Germany

Site Status

Bon Secours Hospital

Cork, , Ireland

Site Status

Adelaide and Meath Hospital

Dublin, , Ireland

Site Status

St. Vincent's University Hospital

Dublin, , Ireland

Site Status

Fondazione Poliambulanza

Brescia, Lombardy, Italy

Site Status

Universita Delgi Studi de Genova (UNIGE)- Azienda Ospedaliera. Universitaria "San Martino" (Ospedale San Martino)

Genova, , Italy

Site Status

A.O. Ospedale Niguarda Ca' Granda

Milan, , Italy

Site Status

Fondazione IRCCS Instituto Nazionale dei Tumori Milano

Milan, , Italy

Site Status

A.O. R.N. "A.Cardarelli"

Naples, , Italy

Site Status

Seconda Universita degli Studi de Napoli

Napoli, , Italy

Site Status

AOU San Luidi di Orbassano

Orbassano, , Italy

Site Status

Azienda Ospedaliero

Pisa, , Italy

Site Status

Arcispidale S Maria Nuova

Reggio Emilia, , Italy

Site Status

Ospedale di Rimini

Rimini, , Italy

Site Status

Ospedale di Sondrio

Sondrio, , Italy

Site Status

Aichi Cancer Center Hospital

Nagoya, Aichi-ken, Japan

Site Status

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status

National Hospital Organization Shikoku Cancer Center

Matsuyama, Ehime, Japan

Site Status

KKR Sapporo Medical Center TONAN-Hospital

Sapporo, Hokkaido, Japan

Site Status

Hokkaido University Hospital

Sapporo, Hokkaido, Japan

Site Status

Kobe City Medical Center General Hospital

Kobe, Hyōgo, Japan

Site Status

Tsukuba University Hospital

Tsukuba, Ibaraki, Japan

Site Status

Kanagawa Cancer Center

Yokohama, Kanagawa, Japan

Site Status

Osaka Medical College Hospital

Takatsuki, Osaka, Japan

Site Status

Saitama Cancer Center

Kita-adachi-gun, Saitama, Japan

Site Status

Shizuoka Cancer Center

Sunto-gun, Shizuoka, Japan

Site Status

Jichi Medical University Hospital

Shimotsuke, Tochigi, Japan

Site Status

National Cancer Center Hospital

Chuo-ku, Tokyo, Japan

Site Status

The Cancer Institute Hospital of Japanese Foundation for Cancer Research

Koto-ku, Tokyo, Japan

Site Status

Keio University Hospital

Shinjuku-ku, Tokyo, Japan

Site Status

Chiba Cancer Center

Chiba, , Japan

Site Status

National Hospital Organization Kyushu Cancer Center

Fukuoka, , Japan

Site Status

Kumamoto University Hospital

Kumamoto, , Japan

Site Status

Osaka Medical Center for Cancer and Cardiovascular Diseases

Osaka, , Japan

Site Status

Tokushima University Hospital

Tokushima, , Japan

Site Status

Hospital Universitario Vall d'Hebrón

Barcelona, , Spain

Site Status

Hospital Arnau de Vilanova

Lleida, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Fundacion Jimenez Diaz - Universidad Autonoma de Madrid

Madrid, , Spain

Site Status

Hospital 12 de Octubre

Madrid, , Spain

Site Status

Hospital Carlos Haya

Málaga, , Spain

Site Status

Hospital Universitario Morales Messeguer

Murcia, , Spain

Site Status

Corporacion Sanitaria Parc Tauli

Sabadell, , Spain

Site Status

Hospital Universitario Virgen del Rocio

Seville, , Spain

Site Status

Hospital Clínico Universitario de Valencia

Valencia, , Spain

Site Status

Hospital General Universitario de Valencia

Valencia, , Spain

Site Status

Karolinska University Hospital

Stockholm, , Sweden

Site Status

Akademiska Sjukhuset

Uppsala, , Sweden

Site Status

Aberdeen Royal Infirmary

Aberdeen, , United Kingdom

Site Status

University Hospitals Bristol NHS Foundation Trust

Bristol, , United Kingdom

Site Status

St James' Institute of Oncology

Leeds, , United Kingdom

Site Status

University College London Hospitals Foundation NHS Trust

London, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

Surrey, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Czechia France Germany Ireland Italy Japan Spain Sweden United Kingdom

References

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Yoshino T, Cleary JM, Van Cutsem E, Mayer RJ, Ohtsu A, Shinozaki E, Falcone A, Yamazaki K, Nishina T, Garcia-Carbonero R, Komatsu Y, Baba H, Argiles G, Tsuji A, Sobrero A, Yamaguchi K, Peeters M, Muro K, Zaniboni A, Sugimoto N, Shimada Y, Tsuji Y, Hochster HS, Moriwaki T, Tran B, Esaki T, Hamada C, Tanase T, Benedetti F, Makris L, Yamashita F, Lenz HJ. Neutropenia and survival outcomes in metastatic colorectal cancer patients treated with trifluridine/tipiracil in the RECOURSE and J003 trials. Ann Oncol. 2020 Jan;31(1):88-95. doi: 10.1016/j.annonc.2019.10.005.

Reference Type DERIVED
PMID: 31912801 (View on PubMed)

Van Cutsem E, Mayer RJ, Laurent S, Winkler R, Gravalos C, Benavides M, Longo-Munoz F, Portales F, Ciardiello F, Siena S, Yamaguchi K, Muro K, Denda T, Tsuji Y, Makris L, Loehrer P, Lenz HJ, Ohtsu A; RECOURSE Study Group. The subgroups of the phase III RECOURSE trial of trifluridine/tipiracil (TAS-102) versus placebo with best supportive care in patients with metastatic colorectal cancer. Eur J Cancer. 2018 Feb;90:63-72. doi: 10.1016/j.ejca.2017.10.009. Epub 2017 Dec 21.

Reference Type DERIVED
PMID: 29274618 (View on PubMed)

Longo-Munoz F, Argiles G, Tabernero J, Cervantes A, Gravalos C, Pericay C, Gil-Calle S, Mizuguchi H, Carrato-Mena A, Limon ML, Garcia-Carbonero R. Efficacy of trifluridine and tipiracil (TAS-102) versus placebo, with supportive care, in a randomized, controlled trial of patients with metastatic colorectal cancer from Spain: results of a subgroup analysis of the phase 3 RECOURSE trial. Clin Transl Oncol. 2017 Feb;19(2):227-235. doi: 10.1007/s12094-016-1528-7. Epub 2016 Jul 21.

Reference Type DERIVED
PMID: 27443414 (View on PubMed)

Mayer RJ, Van Cutsem E, Falcone A, Yoshino T, Garcia-Carbonero R, Mizunuma N, Yamazaki K, Shimada Y, Tabernero J, Komatsu Y, Sobrero A, Boucher E, Peeters M, Tran B, Lenz HJ, Zaniboni A, Hochster H, Cleary JM, Prenen H, Benedetti F, Mizuguchi H, Makris L, Ito M, Ohtsu A; RECOURSE Study Group. Randomized trial of TAS-102 for refractory metastatic colorectal cancer. N Engl J Med. 2015 May 14;372(20):1909-19. doi: 10.1056/NEJMoa1414325.

Reference Type DERIVED
PMID: 25970050 (View on PubMed)

Other Identifiers

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2012-000109-66

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

TPU-TAS-102-301

Identifier Type: -

Identifier Source: org_study_id

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