Adjuvant Axitinib Therapy of Renal Cell Cancer in High Risk Patients

NCT ID: NCT01599754

Last Updated: 2019-09-20

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

724 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-04-30

Study Completion Date

2018-05-31

Brief Summary

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The purpose of this trial is to determine if adjuvant therapy with axitinib will prevent or delay the recurrence of renal cell cancer after surgery to remove the primary tumor in high risk patients.

Detailed Description

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This is a prospective, randomized, double blind placebo controlled Phase 3 trial of oral axitinib starting at 5 mg twice daily given 3 years vs. placebo.

Approximately 700 patients will be randomized in a 1:1 ratio between axitinib vs placebo.

Conditions

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Clear Cell Renal Carcinoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

PREVENTION

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Axitinib

Group Type EXPERIMENTAL

Axitinib

Intervention Type DRUG

Axitinib 5 mg twice daily

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo twice daily

Interventions

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Axitinib

Axitinib 5 mg twice daily

Intervention Type DRUG

Placebo

Placebo twice daily

Intervention Type DRUG

Other Intervention Names

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Inlyta

Eligibility Criteria

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Inclusion Criteria

1. Patients must have no evidence of macroscopic residual disease or metastatic disease.
2. Male or female, age \>=18 years (age \>=20 years in Japan, Korea and Taiwan).
3. Patients must be diagnosed with one of the following based on American Joint Committee on Cancer (AJCC) TNM staging version 2010, Eastern Collaborative Oncology Group (ECOG) performance status (PS):

* pT2, pN0 or pNx, M0 and ECOG PS 0-1
* pT3, pN0 or pNx, M0 and ECOG PS 0-1
* pT4, pN0 or pNx, M0 and ECOG PS 0-1
* Any pT, pN1, M0 and ECOG PS 0-1
4. Patients must have histologically confirmed preponderant, defined as \>50%, clear cell RCC.
5. Patients must not have received any previous systemic (includes chemotherapeutic, hormonal, or immunotherapeutic) treatment for RCC.
6. Patients must not have received any previous anti angiogenic treatment.
7. Patients must have adequate organ function.

Exclusion Criteria

1. Histologically undifferentiated carcinomas, sarcomas, collecting duct carcinoma, lymphoma, or patients with any metastatic renal sites.
2. National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) Grade 3 hemorrhage \<4 weeks of date of randomization.
3. Diagnosis of any non-RCC malignancy within the 5 years from date of randomization, except basal cell carcinoma, squamous cell skin cancer, or in situ carcinoma of the cervix uteri that has been adequately treated with no evidence of recurrent disease for 12 months.
4. Any of the following within the 12 months prior to study drug administration: myocardial infarction, uncontrolled angina, coronary/peripheral artery bypass graft, symptomatic congestive heart failure, cerebrovascular accident or transient ischemic attack and 6 months for deep vein thrombosis or pulmonary embolism.
5. Gastrointestinal abnormalities
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role collaborator

SFJ Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role collaborator

SFJ Pharma Ltd. II

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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La Jolla, California, United States

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Los Angeles, California, United States

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Palo Alto, California, United States

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Pleasant Hill, California, United States

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Denver, Colorado, United States

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Washington D.C., District of Columbia, United States

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Ocala, Florida, United States

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Atlanta, Georgia, United States

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Annapolis, Maryland, United States

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Baltimore, Maryland, United States

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Saint Paul, Minnesota, United States

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Omaha, Nebraska, United States

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Hackensack, New Jersey, United States

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Albany, New York, United States

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New York, New York, United States

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Portland, Oregon, United States

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Charleston, South Carolina, United States

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Chattanooga, Tennessee, United States

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Austin, Texas, United States

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Bedford, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Norfolk, Virginia, United States

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Seattle, Washington, United States

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Beijing, , China

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Changchun, , China

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Chongqing, , China

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Dalian, , China

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Guangzhou, , China

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Hangzhou, , China

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Jinan, , China

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Nanchang, , China

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Shanghai, , China

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Suzhou, , China

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Tianjin, , China

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Wuhan, , China

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Besançon, , France

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Bordeaux, , France

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Hyères, , France

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Le Mans, , France

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Lyon, , France

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Marseille, , France

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Paris, , France

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Rennes, , France

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Saint-Herblain, , France

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Suresnes, , France

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Vandœuvre-lès-Nancy, , France

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Hong Kong, , Hong Kong

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Ahmeadbad, , India

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Aurangabad, , India

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Bangalore, , India

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Chennai, , India

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Hyderabad, , India

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Karamsad, , India

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Kochi, , India

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Kolkota, , India

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Lucknow, , India

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Ludhiana, , India

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Mangalore, , India

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Manipal, , India

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Mumbai, , India

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Nashik, , India

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New Delhi, , India

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Pune, , India

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Surat, , India

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Visakhapatnam, , India

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Aichi, , Japan

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Akita, , Japan

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Aomori, , Japan

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Chiba, , Japan

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Fukuoka, , Japan

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Gifu, , Japan

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Hokkaido, , Japan

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Hyōgo, , Japan

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Kagawa, , Japan

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Kanagawa, , Japan

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Kumamoto, , Japan

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Kyoto, , Japan

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Nagasaki, , Japan

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Nigata-honmachi, , Japan

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Osaka, , Japan

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Shizuoka, , Japan

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Tokushima, , Japan

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Tokyo, , Japan

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Yamagata, , Japan

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Yamaguchi, , Japan

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Busan, , South Korea

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Daegu, , South Korea

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Daejeon, , South Korea

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Gyeonggi-do, , South Korea

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Jeonnam, , South Korea

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Seoul, , South Korea

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Barcelona, , Spain

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Donostia / San Sebastian, , Spain

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Leganés, , Spain

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Llobregat, , Spain

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Madrid, , Spain

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Oviedo, , Spain

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Seville, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Countries

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United States China France Hong Kong India Japan South Korea Spain Taiwan

References

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Gross-Goupil M, Kwon TG, Eto M, Ye D, Miyake H, Seo SI, Byun SS, Lee JL, Master V, Jin J, DeBenedetto R, Linke R, Casey M, Rosbrook B, Lechuga M, Valota O, Grande E, Quinn DI. Axitinib versus placebo as an adjuvant treatment of renal cell carcinoma: results from the phase III, randomized ATLAS trial. Ann Oncol. 2018 Dec 1;29(12):2371-2378. doi: 10.1093/annonc/mdy454.

Reference Type DERIVED
PMID: 30346481 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Other Identifiers

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AP311736

Identifier Type: -

Identifier Source: org_study_id

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