Irritable Bowel Syndrome With Diarrhea (IBS-D) Rifaximin Re-Treatment Study

NCT ID: NCT01543178

Last Updated: 2017-12-12

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

2583 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-02-29

Study Completion Date

2014-06-30

Brief Summary

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This study will evaluate the effectiveness and safety of repeat treatment with rifaximin 550 mg three times a day in patients with IBS with diarrhea who respond to initial treatment of rifaximin 550 mg three times a day.

Detailed Description

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It is important in chronic conditions to have information about how a product that is intended for short course administration in order to confer prolonged benefit should be administered beyond the first cycle of use once symptoms reappear. This Phase 3 study will evaluate the efficacy and safety of repeat treatment with rifaximin 550 mg three times daily (TID) for 14 days in subjects with IBS-D who respond to an initial treatment course with rifaximin 550 mg TID for 14 days.

This study consists of several treatment phases outlined below:

Screening/Treatment 1 Phase. Subjects will receive single-blind placebo TID for 7-13 days and answer daily IBS symptom-related questions.

Treatment 2 Phase. Eligible subjects will receive open-label rifaximin 550 mg TID for 2 weeks with a 4-week treatment-free follow-up. Responders will continue into Maintenance Phase 1. Nonresponders will withdraw from the study.

Maintenance Phase 1. Subjects will continue the treatment-free follow-up period for up to 18 weeks until either: 1) they experience recurrence or 2) enrollment is met in the Treatment 3 Phase (Double Blind Repeat Treatment Phase). Subjects who do not meet recurrence criteria by the end of the Maintenance Phase 1 will withdraw from the study.

Treatment 3 Phase/ Double Blind Repeat Treatment Phase. Subjects who meet criteria for recurrence will be randomized 1:1 to receive either rifaximin 550 mg TID or placebo TID for 2 weeks with a 4-week treatment-free follow-up.

Primary efficacy analysis will be performed at the end of the Treatment 3 Phase (at Week 6 of the double-blind period).

Maintenance Phase 2. All subjects continued into an additional treatment-free follow-up period of up to 6 weeks (Maintenance Phase 2).

Treatment 4 Phase/Second Repeat Treatment Phase. Subjects will receive the same double-blind treatment as previously assigned in the Treatment 3 Phase for 2 weeks with a 4-week treatment-free follow-up.

A lactulose breath test sub-study will be conducted at select sites.

Conditions

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Irritable Bowel Syndrome With Diarrhea

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Rifaximin open-label

Subjects will receive open-label rifaximin 550 mg TID for 2 weeks with a 4-week treatment-free follow-up. Responders will continue into Maintenance Phase 1 (treatment free). Nonresponders will withdraw from the study.

Subjects who meet criteria for recurrence in Maintenance Phase 1 enter the double-blind period and are randomized 1:1 to receive rifaximin 550 mg or placebo.

Group Type EXPERIMENTAL

open-label rifaximin

Intervention Type DRUG

550 mg three times a day (open-label)

Double-blind rifaximin (retreatment)

Subjects in this arm receive rifaximin 550 mg TID for 2 weeks with a 4-week treatment-free follow-up (first retreatment) followed by Maintenance Phase 2 (6 weeks \[treatment free\]) followed by a second retreatment with rifaximin 550 mg TID for 2 weeks with a 4-week treatment-free follow-up.

Group Type EXPERIMENTAL

open-label rifaximin

Intervention Type DRUG

550 mg three times a day (open-label)

double-blind rifaximin

Intervention Type DRUG

550 mg three times a day (double-blind)

Double-blind placebo (retreatment)

Subjects in this arm receive placebo TID for 2 weeks with a 4-week treatment-free follow-up (first retreatment) followed by Maintenance Phase 2 (6 weeks \[treatment free\]) followed by a second retreatment with placebo TID for 2 weeks with a 4-week treatment-free follow-up.

Group Type PLACEBO_COMPARATOR

open-label rifaximin

Intervention Type DRUG

550 mg three times a day (open-label)

double-blind placebo

Intervention Type DRUG

3 times a day (double-blind)

Interventions

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open-label rifaximin

550 mg three times a day (open-label)

Intervention Type DRUG

double-blind placebo

3 times a day (double-blind)

Intervention Type DRUG

double-blind rifaximin

550 mg three times a day (double-blind)

Intervention Type DRUG

Other Intervention Names

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rifaximin Placebo rifaximin

Eligibility Criteria

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Inclusion Criteria

* IBS confirmed by Rome III diagnostic criteria.
* At least 18 years of age.
* Colonoscopy within the past 10 years to rule out inflammatory bowel disease; or flexible sigmoidoscopy if \< 50 years of age or previous colonoscopy \> 10 years prior.
* Willing to maintain a stable diet. including vitamins, supplements, and nutraceuticals.

Exclusion Criteria

* Diabetes (Type 1 or 2).
* Lactose intolerance and not controlled by a lactose-free diet.
* Pregnant or planning to become pregnant or is lactating.
* History of HIV or hepatitis B or C.
* Participation in investigational study within past 30 days.
* Taking rifaximin or any other antibiotic within past 60 days.
* Unstable cardiovascular or pulmonary disease, with change in treatment in last 30 days due to worsening disease condition.
* History of GI surgery.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bausch Health Americas, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Enoch Bortey, PhD

Role: STUDY_DIRECTOR

Bausch Health Americas, Inc.

Locations

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Anniston, Alabama, United States

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Dothan, Alabama, United States

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Huntsville, Alabama, United States

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Montgomery, Alabama, United States

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Montgomery, Alabama, United States

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Selma, Alabama, United States

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Chandler, Arizona, United States

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Peoria, Arizona, United States

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Tempe, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Jonesboro, Arkansas, United States

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Little Rock, Arkansas, United States

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Little Rock, Arkansas, United States

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Little Rock, Arkansas, United States

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North Little Rock, Arkansas, United States

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Sherwood, Arkansas, United States

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Anaheim, California, United States

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Artesia, California, United States

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Carlsbad, California, United States

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Chula Vista, California, United States

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Chula Vista, California, United States

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Concord, California, United States

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Encinitas, California, United States

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Encino, California, United States

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Escondido, California, United States

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Garden Grove, California, United States

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Garden Grove, California, United States

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Garden Grove, California, United States

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Glendale, California, United States

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Huntington Beach, California, United States

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La Mesa, California, United States

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La Mirada, California, United States

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Laguna Hills, California, United States

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Lakewood, California, United States

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Lincoln, California, United States

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Lomita, California, United States

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Long Beach, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Los Angeles, California, United States

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Madera, California, United States

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Mill Valley, California, United States

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Montebello, California, United States

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North Hollywood, California, United States

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Orange, California, United States

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Redlands, California, United States

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Sacramento, California, United States

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San Carlos, California, United States

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San Diego, California, United States

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San Diego, California, United States

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San Diego, California, United States

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San Diego, California, United States

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Vista, California, United States

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Colorado Springs, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Denver, Colorado, United States

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Lakewood, Colorado, United States

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Lone Tree, Colorado, United States

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Bridgeport, Connecticut, United States

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Bristol, Connecticut, United States

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Danbury, Connecticut, United States

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Torrington, Connecticut, United States

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Boca Raton, Florida, United States

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Boca Raton, Florida, United States

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Boynton Beach, Florida, United States

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Boynton Beach, Florida, United States

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Brandon, Florida, United States

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Clearwater, Florida, United States

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Gainesville, Florida, United States

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Hialeah, Florida, United States

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Hialeah, Florida, United States

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Hialeah, Florida, United States

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Hollywood, Florida, United States

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Jupiter, Florida, United States

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Kissimmee, Florida, United States

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Lake Worth, Florida, United States

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Largo, Florida, United States

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Lauderdale Lakes, Florida, United States

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Maitland, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Springs, Florida, United States

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Naples, Florida, United States

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Orange Park, Florida, United States

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Orlando, Florida, United States

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Ormond Beach, Florida, United States

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Plant City, Florida, United States

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Pompano Beach, Florida, United States

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Port Orange, Florida, United States

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Sarasota, Florida, United States

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Seminole, Florida, United States

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St. Petersburg, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Wellington, Florida, United States

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West Palm Beach, Florida, United States

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West Palm Beach, Florida, United States

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Winter Haven, Florida, United States

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Winter Park, Florida, United States

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Zephyrhills, Florida, United States

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Athens, Georgia, United States

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Atlanta, Georgia, United States

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Atlanta, Georgia, United States

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Augusta, Georgia, United States

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Augusta, Georgia, United States

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Columbus, Georgia, United States

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Columbus, Georgia, United States

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Macon, Georgia, United States

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Marietta, Georgia, United States

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Norcross, Georgia, United States

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Boise, Idaho, United States

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Boise, Idaho, United States

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Hayden Lake, Idaho, United States

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Idaho Falls, Idaho, United States

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Arlington Heights, Illinois, United States

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Chicago, Illinois, United States

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Evanston, Illinois, United States

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Oak Lawn, Illinois, United States

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Elkhart, Indiana, United States

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Evansville, Indiana, United States

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Evansville, Indiana, United States

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Indianapolis, Indiana, United States

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Mishawaka, Indiana, United States

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Clive, Iowa, United States

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Iowa City, Iowa, United States

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Kansas City, Kansas, United States

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Overland Park, Kansas, United States

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Topeka, Kansas, United States

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Wichita, Kansas, United States

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Bowling Green, Kentucky, United States

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Crestview Hills, Kentucky, United States

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Hebron, Kentucky, United States

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Lexington, Kentucky, United States

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Lexington, Kentucky, United States

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Louisville, Kentucky, United States

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Madisonville, Kentucky, United States

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Metairie, Louisiana, United States

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New Orleans, Louisiana, United States

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Shreveport, Louisiana, United States

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Annapolis, Maryland, United States

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Baltimore, Maryland, United States

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Baltimore, Maryland, United States

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Hagerstown, Maryland, United States

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Hollywood, Maryland, United States

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Boston, Massachusetts, United States

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Brockton, Massachusetts, United States

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Marlborough, Massachusetts, United States

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Watertown, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Kalamazoo, Michigan, United States

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Kalamazoo, Michigan, United States

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Saginaw, Michigan, United States

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Wyoming, Michigan, United States

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Jackson, Mississippi, United States

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Ocean Springs, Mississippi, United States

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Kansas City, Missouri, United States

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Lee's Summit, Missouri, United States

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Mexico, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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St Louis, Missouri, United States

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Missoula, Montana, United States

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Bellevue, Nebraska, United States

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Fremont, Nebraska, United States

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Omaha, Nebraska, United States

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Henderson, Nevada, United States

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Las Vegas, Nevada, United States

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Las Vegas, Nevada, United States

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Reno, Nevada, United States

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Lebanon, New Hampshire, United States

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Newington, New Hampshire, United States

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Haddon Heights, New Jersey, United States

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Marlton, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albuquerque, New Mexico, United States

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Brooklyn, New York, United States

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Great Neck, New York, United States

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Great Neck, New York, United States

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Hollis, New York, United States

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Mineola, New York, United States

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New York, New York, United States

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Poughkeepsie, New York, United States

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Rochester, New York, United States

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Asheboro, North Carolina, United States

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Asheville, North Carolina, United States

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Boone, North Carolina, United States

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Cary, North Carolina, United States

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Chapel Hill, North Carolina, United States

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Charlotte, North Carolina, United States

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Greensboro, North Carolina, United States

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Greensboro, North Carolina, United States

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High Point, North Carolina, United States

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Kinston, North Carolina, United States

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Raleigh, North Carolina, United States

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Salisbury, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Fargo, North Dakota, United States

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Akron, Ohio, United States

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Akron, Ohio, United States

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Centerville, Ohio, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Dayton, Ohio, United States

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Groveport, Ohio, United States

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Kettering, Ohio, United States

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Mentor, Ohio, United States

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Norman, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Medford, Oregon, United States

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Portland, Oregon, United States

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Downingtown, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Reading, Pennsylvania, United States

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Sayre, Pennsylvania, United States

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East Providence, Rhode Island, United States

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Warwick, Rhode Island, United States

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Charleston, South Carolina, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Fort Mill, South Carolina, United States

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Gaffney, South Carolina, United States

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Greer, South Carolina, United States

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Brentwood, Tennessee, United States

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Bristol, Tennessee, United States

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Chattanooga, Tennessee, United States

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Franklin, Tennessee, United States

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Germantown, Tennessee, United States

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Hermitage, Tennessee, United States

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Kingsport, Tennessee, United States

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Nashville, Tennessee, United States

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Arlington, Texas, United States

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Austin, Texas, United States

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Austin, Texas, United States

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Austin, Texas, United States

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Austin, Texas, United States

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Corsicana, Texas, United States

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Dallas, Texas, United States

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El Paso, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Lake Jackson, Texas, United States

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Odessa, Texas, United States

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Pasadena, Texas, United States

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Plano, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Sealy, Texas, United States

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Southlake, Texas, United States

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Tyler, Texas, United States

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Bountiful, Utah, United States

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Ogden, Utah, United States

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Salt Lake City, Utah, United States

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West Jordan, Utah, United States

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Charlottesville, Virginia, United States

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Chesapeake, Virginia, United States

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Danville, Virginia, United States

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Fairfax, Virginia, United States

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Richmond, Virginia, United States

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Suffolk, Virginia, United States

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Bellevue, Washington, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Milwaukee, Wisconsin, United States

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Milwaukee, Wisconsin, United States

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Berlin, , Germany

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Hamburg, , Germany

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Manchester, , United Kingdom

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Countries

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United States Germany United Kingdom

References

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Lacy BE, Chang L, Rao SSC, Heimanson Z, Sayuk GS. Rifaximin Treatment for Individual and Multiple Symptoms of Irritable Bowel Syndrome With Diarrhea: An Analysis Using New End Points. Clin Ther. 2023 Mar;45(3):198-209. doi: 10.1016/j.clinthera.2023.01.010. Epub 2023 Mar 14.

Reference Type DERIVED
PMID: 36922331 (View on PubMed)

Fodor AA, Pimentel M, Chey WD, Lembo A, Golden PL, Israel RJ, Carroll IM. Rifaximin is associated with modest, transient decreases in multiple taxa in the gut microbiota of patients with diarrhoea-predominant irritable bowel syndrome. Gut Microbes. 2019;10(1):22-33. doi: 10.1080/19490976.2018.1460013. Epub 2018 Jul 18.

Reference Type DERIVED
PMID: 29708822 (View on PubMed)

Cash BD, Pimentel M, Rao SSC, Weinstock L, Chang L, Heimanson Z, Lembo A. Repeat treatment with rifaximin improves irritable bowel syndrome-related quality of life: a secondary analysis of a randomized, double-blind, placebo-controlled trial. Therap Adv Gastroenterol. 2017 Sep;10(9):689-699. doi: 10.1177/1756283X17726087. Epub 2017 Sep 11.

Reference Type DERIVED
PMID: 28932270 (View on PubMed)

Pimentel M, Cash BD, Lembo A, Wolf RA, Israel RJ, Schoenfeld P. Repeat Rifaximin for Irritable Bowel Syndrome: No Clinically Significant Changes in Stool Microbial Antibiotic Sensitivity. Dig Dis Sci. 2017 Sep;62(9):2455-2463. doi: 10.1007/s10620-017-4598-7. Epub 2017 Jun 6.

Reference Type DERIVED
PMID: 28589238 (View on PubMed)

DuPont HL, Wolf RA, Israel RJ, Pimentel M. Antimicrobial Susceptibility of Staphylococcus Isolates from the Skin of Patients with Diarrhea-Predominant Irritable Bowel Syndrome Treated with Repeat Courses of Rifaximin. Antimicrob Agents Chemother. 2016 Dec 27;61(1):e02165-16. doi: 10.1128/AAC.02165-16. Print 2017 Jan. No abstract available.

Reference Type DERIVED
PMID: 27795384 (View on PubMed)

Lembo A, Pimentel M, Rao SS, Schoenfeld P, Cash B, Weinstock LB, Paterson C, Bortey E, Forbes WP. Repeat Treatment With Rifaximin Is Safe and Effective in Patients With Diarrhea-Predominant Irritable Bowel Syndrome. Gastroenterology. 2016 Dec;151(6):1113-1121. doi: 10.1053/j.gastro.2016.08.003. Epub 2016 Aug 13.

Reference Type DERIVED
PMID: 27528177 (View on PubMed)

Other Identifiers

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RFIB3053

Identifier Type: -

Identifier Source: org_study_id

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