Efficacy and Safety of Liraglutide in Combination With Metformin Compared to Metformin Alone, in Children and Adolescents With Type 2 Diabetes

NCT ID: NCT01541215

Last Updated: 2021-07-02

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

135 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-11-13

Study Completion Date

2020-05-20

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This trial is conducted globally. The aim of this trial is to assess the efficacy and safety of liraglutide in the paediatric population in order to potentially address the unmet need for treatment of children and adolescents with type 2 diabetes.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Diabetes Diabetes Mellitus, Type 2

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Lira + Met

Group Type EXPERIMENTAL

liraglutide

Intervention Type DRUG

Administered subcutaneously (s.c., under the skin) once daily.1.8 mg or maximum tolerated dose (MTD: 0.6 mg, 1.2 mg, 1.8 mg) for 26 weeks. Subjects will continue treatment in a 26 week open-labelled extension. Rescue treatment will be allowed if rescue criteria are met.

metformin

Intervention Type DRUG

Tablets administered for 26 weeks. Maximum tolerated dose (MTD) between 1000-2000 mg at the discretion of the investigator. Subjects will continue treatment in a 26 week open-labelled extension.

Placebo + Met

Group Type PLACEBO_COMPARATOR

placebo

Intervention Type DRUG

Administered subcutaneously (s.c., under the skin) once daily for 26 weeks. Subjects will discontinue placebo treatment in the open-labelled extension. Rescue treatment will be allowed if rescue criteria are met.

metformin

Intervention Type DRUG

Tablets administered for 26 weeks. Maximum tolerated dose (MTD) between 1000-2000 mg at the discretion of the investigator. Subjects will continue treatment in a 26 week open-labelled extension.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

liraglutide

Administered subcutaneously (s.c., under the skin) once daily.1.8 mg or maximum tolerated dose (MTD: 0.6 mg, 1.2 mg, 1.8 mg) for 26 weeks. Subjects will continue treatment in a 26 week open-labelled extension. Rescue treatment will be allowed if rescue criteria are met.

Intervention Type DRUG

placebo

Administered subcutaneously (s.c., under the skin) once daily for 26 weeks. Subjects will discontinue placebo treatment in the open-labelled extension. Rescue treatment will be allowed if rescue criteria are met.

Intervention Type DRUG

metformin

Tablets administered for 26 weeks. Maximum tolerated dose (MTD) between 1000-2000 mg at the discretion of the investigator. Subjects will continue treatment in a 26 week open-labelled extension.

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

Inclusion Criteria: - Children and adolescents between the ages of 10-16 years. Subjects cannot turn 17 years and 11 months before the end of treatment (52 weeks) - Diagnosis of type 2 diabetes mellitus and treated for at least 30 days with: diet and exercise alone, diet and exercise in combination with metformin monotherapy, diet and exercise in combination with metformin and a stable (Stable is defined as basal insulin adjustments up to 15%) dose of basal insulin, diet and exercise in combination with a stable (Stable is defined as basal insulin adjustments up to 15%) dose of basal insulin - HbA1c: 7.0-11% (inclusive) if diet and exercise treated or 6.

Exclusion Criteria

5-11% (inclusive) if treated with metformin as monotherapy, basal insulin as monotherapy or metformin and basal insulin in combination - Body mass index (BMI) above 85% percentile of the general age and gender matched population Exclusion Criteria: - Type 1 diabetes - Maturity onset diabetes of the young (MODY) - Use of any antidiabetic agent other than metformin and/or basal insulin within 90 days prior to screening - Recurrent severe hypoglycaemia or hypoglycaemic unawareness as judged by the investigator - History of chronic pancreatitis or idiopathic acute pancreatitis - Any clinically significant disorder, except for conditions associated with type 2 diabetes history which in the investigator's opinion could interfere with results of the trial - Uncontrolled hypertension, treated or untreated above 99th percentile for age and gender in children - Known or suspected abuse of alcohol or drugs/narcotics
Minimum Eligible Age

10 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Novo Nordisk A/S

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Novo Nordisk Investigational Site

Birmingham, Alabama, United States

Site Status

Novo Nordisk Investigational Site

Phoenix, Arizona, United States

Site Status

Novo Nordisk Investigational Site

Tucson, Arizona, United States

Site Status

Novo Nordisk Investigational Site

Corona, California, United States

Site Status

Novo Nordisk Investigational Site

Costa Mesa, California, United States

Site Status

Novo Nordisk Investigational Site

Long Beach, California, United States

Site Status

Novo Nordisk Investigational Site

Los Angeles, California, United States

Site Status

Novo Nordisk Investigational Site

Los Angeles, California, United States

Site Status

Novo Nordisk Investigational Site

Moreno Valley, California, United States

Site Status

Novo Nordisk Investigational Site

Palo Alto, California, United States

Site Status

Novo Nordisk Investigational Site

San Diego, California, United States

Site Status

Novo Nordisk Investigational Site

Ventura, California, United States

Site Status

Novo Nordisk Investigational Site

New Haven, Connecticut, United States

Site Status

Novo Nordisk Investigational Site

Wilmington, Delaware, United States

Site Status

Novo Nordisk Investigational Site

Washington D.C., District of Columbia, United States

Site Status

Novo Nordisk Investigational Site

Jacksonville, Florida, United States

Site Status

Novo Nordisk Investigational Site

Melbourne, Florida, United States

Site Status

Novo Nordisk Investigational Site

Miami, Florida, United States

Site Status

Novo Nordisk Investigational Site

Miami, Florida, United States

Site Status

Novo Nordisk Investigational Site

Miami, Florida, United States

Site Status

Novo Nordisk Investigational Site

St. Petersburg, Florida, United States

Site Status

Novo Nordisk Investigational Site

Tallahassee, Florida, United States

Site Status

Novo Nordisk Investigational Site

Tampa, Florida, United States

Site Status

Novo Nordisk Investigational Site

Atlanta, Georgia, United States

Site Status

Novo Nordisk Investigational Site

Atlanta, Georgia, United States

Site Status

Novo Nordisk Investigational Site

Columbus, Georgia, United States

Site Status

Novo Nordisk Investigational Site

Bloomington, Indiana, United States

Site Status

Novo Nordisk Investigational Site

Iowa City, Iowa, United States

Site Status

Novo Nordisk Investigational Site

Topeka, Kansas, United States

Site Status

Novo Nordisk Investigational Site

Lexington, Kentucky, United States

Site Status

Novo Nordisk Investigational Site

Lexington, Kentucky, United States

Site Status

Novo Nordisk Investigational Site

Silver Spring, Maryland, United States

Site Status

Novo Nordisk Investigational Site

Worcester, Massachusetts, United States

Site Status

Novo Nordisk Investigational Site

Detroit, Michigan, United States

Site Status

Novo Nordisk Investigational Site

Grand Rapids, Michigan, United States

Site Status

Novo Nordisk Investigational Site

Saint Paul, Minnesota, United States

Site Status

Novo Nordisk Investigational Site

Columbia, Missouri, United States

Site Status

Novo Nordisk Investigational Site

Kansas City, Missouri, United States

Site Status

Novo Nordisk Investigational Site

St Louis, Missouri, United States

Site Status

Novo Nordisk Investigational Site

Las Vegas, Nevada, United States

Site Status

Novo Nordisk Investigational Site

Hackensack, New Jersey, United States

Site Status

Novo Nordisk Investigational Site

West Orange, New Jersey, United States

Site Status

Novo Nordisk Investigational Site

Buffalo, New York, United States

Site Status

Novo Nordisk Investigational Site

New York, New York, United States

Site Status

Novo Nordisk Investigational Site

New York, New York, United States

Site Status

Novo Nordisk Investigational Site

New York, New York, United States

Site Status

Novo Nordisk Investigational Site

Sleepy Hollow, New York, United States

Site Status

Novo Nordisk Investigational Site

Cincinnati, Ohio, United States

Site Status

Novo Nordisk Investigational Site

Toledo, Ohio, United States

Site Status

Novo Nordisk Investigational Site

Hershey, Pennsylvania, United States

Site Status

Novo Nordisk Investigational Site

Philadelphia, Pennsylvania, United States

Site Status

Novo Nordisk Investigational Site

Philadelphia, Pennsylvania, United States

Site Status

Novo Nordisk Investigational Site

Pittsburgh, Pennsylvania, United States

Site Status

Novo Nordisk Investigational Site

Greenville, South Carolina, United States

Site Status

Novo Nordisk Investigational Site

Rapid City, South Dakota, United States

Site Status

Novo Nordisk Investigational Site

Chattanooga, Tennessee, United States

Site Status

Novo Nordisk Investigational Site

Memphis, Tennessee, United States

Site Status

Novo Nordisk Investigational Site

Memphis, Tennessee, United States

Site Status

Novo Nordisk Investigational Site

Memphis, Tennessee, United States

Site Status

Novo Nordisk Investigational Site

Nashville, Tennessee, United States

Site Status

Novo Nordisk Investigational Site

Amarillo, Texas, United States

Site Status

Novo Nordisk Investigational Site

Dallas, Texas, United States

Site Status

Novo Nordisk Investigational Site

Edinburg, Texas, United States

Site Status

Novo Nordisk Investigational Site

Fort Worth, Texas, United States

Site Status

Novo Nordisk Investigational Site

Houston, Texas, United States

Site Status

Novo Nordisk Investigational Site

Houston, Texas, United States

Site Status

Novo Nordisk Investigational Site

Kerrville, Texas, United States

Site Status

Novo Nordisk Investigational Site

San Antonio, Texas, United States

Site Status

Novo Nordisk Investigational Site

Charlottesville, Virginia, United States

Site Status

Novo Nordisk Investigational Site

Norfolk, Virginia, United States

Site Status

Novo Nordisk Investigational Site

Charleston, West Virginia, United States

Site Status

Novo Nordisk Investigational Site

Ipswich, Queensland, Australia

Site Status

Novo Nordisk Investigational Site

Graz, , Austria

Site Status

Novo Nordisk Investigational Site

Innsbruck, , Austria

Site Status

Novo Nordisk Investigational Site

Salzburg, , Austria

Site Status

Novo Nordisk Investigational Site

Wels, , Austria

Site Status

Novo Nordisk Investigational Site

Brussels, , Belgium

Site Status

Novo Nordisk Investigational Site

Brussels, , Belgium

Site Status

Novo Nordisk Investigational Site

Leuven, , Belgium

Site Status

Novo Nordisk Investigational Site

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Novo Nordisk Investigational Site

Edmonton, Alberta, Canada

Site Status

Novo Nordisk Investigational Site

Winnipeg, Manitoba, Canada

Site Status

Novo Nordisk Investigational Site

Brampton, Ontario, Canada

Site Status

Novo Nordisk Investigational Site

Westmount, Quebec, Canada

Site Status

Novo Nordisk Investigational Site

Rijeka, , Croatia

Site Status

Novo Nordisk Investigational Site

Zagreb, , Croatia

Site Status

Novo Nordisk Investigational Site

Herlev, , Denmark

Site Status

Novo Nordisk Investigational Site

Næstved, , Denmark

Site Status

Novo Nordisk Investigational Site

Al Mansurah, , Egypt

Site Status

Novo Nordisk Investigational Site

Alexandria, , Egypt

Site Status

Novo Nordisk Investigational Site

Cairo, , Egypt

Site Status

Novo Nordisk Investigational Site

Cairo, , Egypt

Site Status

Novo Nordisk Investigational Site

Marseille, , France

Site Status

Novo Nordisk Investigational Site

Montpellier, , France

Site Status

Novo Nordisk Investigational Site

Ludwigshafen, , Germany

Site Status

Novo Nordisk Investigational Site

Mayen, , Germany

Site Status

Novo Nordisk Investigational Site

Athens, , Greece

Site Status

Novo Nordisk Investigational Site

Athens, , Greece

Site Status

Novo Nordisk Investigational Site

Goudi/ Athens, , Greece

Site Status

Novo Nordisk Investigational Site

Thessaloniki, , Greece

Site Status

Novo Nordisk Investigational Site

Budapest, , Hungary

Site Status

Novo Nordisk Investigational Site

Budapest, , Hungary

Site Status

Novo Nordisk Investigational Site

Budapest, , Hungary

Site Status

Novo Nordisk Investigational Site

Miskolc, , Hungary

Site Status

Novo Nordisk Investigational Site

Szombathely, , Hungary

Site Status

Novo Nordisk Investigational Site

Guntur, Andhra Pradesh, India

Site Status

Novo Nordisk Investigational Site

Hyderabad, Andhra Pradesh, India

Site Status

Novo Nordisk Investigational Site

Bangalore, Karnataka, India

Site Status

Novo Nordisk Investigational Site

Bangalore, Karnataka, India

Site Status

Novo Nordisk Investigational Site

Bangalore, Karnataka, India

Site Status

Novo Nordisk Investigational Site

Bangalore, Karnataka, India

Site Status

Novo Nordisk Investigational Site

Mumbai, Maharashtra, India

Site Status

Novo Nordisk Investigational Site

Mumbai, Maharashtra, India

Site Status

Novo Nordisk Investigational Site

Pune, Maharashtra, India

Site Status

Novo Nordisk Investigational Site

New Dehli, New Delhi, India

Site Status

Novo Nordisk Investigational Site

Chandigarh, Punjab, India

Site Status

Novo Nordisk Investigational Site

Ludhiana, Punjab, India

Site Status

Novo Nordisk Investigational Site

Jaipur, Rajasthan, India

Site Status

Novo Nordisk Investigational Site

Chennai, Tamil Nadu, India

Site Status

Novo Nordisk Investigational Site

Hyderbad, Telangana, India

Site Status

Novo Nordisk Investigational Site

Kolkata, West Bengal, India

Site Status

Novo Nordisk Investigational Site

Kolkata, , India

Site Status

Novo Nordisk Investigational Site

Beersheba, , Israel

Site Status

Novo Nordisk Investigational Site

Haifa, , Israel

Site Status

Novo Nordisk Investigational Site

Jerusalem, , Israel

Site Status

Novo Nordisk Investigational Site

Petah Tikva, , Israel

Site Status

Novo Nordisk Investigational Site

Tel Litwinsky, , Israel

Site Status

Novo Nordisk Investigational Site

Roma, , Italy

Site Status

Novo Nordisk Investigational Site

Hazmiyeh, , Lebanon

Site Status

Novo Nordisk Investigational Site

Lebanon - Beirut, , Lebanon

Site Status

Novo Nordisk Investigational Site

Kuala Lumpur, , Malaysia

Site Status

Novo Nordisk Investigational Site

Tampico, Tamaulipas, Mexico

Site Status

Novo Nordisk Investigational Site

Puebla City, , Mexico

Site Status

Novo Nordisk Investigational Site

Fes, , Morocco

Site Status

Novo Nordisk Investigational Site

Rabat, , Morocco

Site Status

Novo Nordisk Investigational Site

's-Hertogenbosch, , Netherlands

Site Status

Novo Nordisk Investigational Site

Grafton, , New Zealand

Site Status

Novo Nordisk Investigational Site

Skopje, , North Macedonia

Site Status

Novo Nordisk Investigational Site

Bergen, , Norway

Site Status

Novo Nordisk Investigational Site

Katowice, , Poland

Site Status

Novo Nordisk Investigational Site

Warsaw, , Poland

Site Status

Novo Nordisk Investigational Site

Wroclaw, , Poland

Site Status

Novo Nordisk Investigational Site

Braga, , Portugal

Site Status

Novo Nordisk Investigational Site

Lisbon, , Portugal

Site Status

Novo Nordisk Investigational Site

Lisbon, , Portugal

Site Status

Novo Nordisk Investigational Site

Ponce, , Puerto Rico

Site Status

Novo Nordisk Investigational Site

Timișoara, Timiș County, Romania

Site Status

Novo Nordisk Investigational Site

Bucharest, , Romania

Site Status

Novo Nordisk Investigational Site

Bucharest, , Romania

Site Status

Novo Nordisk Investigational Site

Constanța, , Romania

Site Status

Novo Nordisk Investigational Site

Chelyabinsk, , Russia

Site Status

Novo Nordisk Investigational Site

Izhevsk, , Russia

Site Status

Novo Nordisk Investigational Site

Krasnoyarsk, , Russia

Site Status

Novo Nordisk Investigational Site

Moscow, , Russia

Site Status

Novo Nordisk Investigational Site

Moscow, , Russia

Site Status

Novo Nordisk Investigational Site

Novosibirsk, , Russia

Site Status

Novo Nordisk Investigational Site

Saint Petersburg, , Russia

Site Status

Novo Nordisk Investigational Site

Saint Petersburg, , Russia

Site Status

Novo Nordisk Investigational Site

Saratov, , Russia

Site Status

Novo Nordisk Investigational Site

Tomsk, , Russia

Site Status

Novo Nordisk Investigational Site

Belgrade, , Serbia

Site Status

Novo Nordisk Investigational Site

Belgrade, , Serbia

Site Status

Novo Nordisk Investigational Site

Niš, , Serbia

Site Status

Novo Nordisk Investigational Site

Novi Sad, , Serbia

Site Status

Novo Nordisk Investigational Site

Leganés, , Spain

Site Status

Novo Nordisk Investigational Site

Madrid, , Spain

Site Status

Novo Nordisk Investigational Site

Madrid, , Spain

Site Status

Novo Nordisk Investigational Site

Vigo, , Spain

Site Status

Novo Nordisk Investigational Site

Vitoria-Gasteiz, , Spain

Site Status

Novo Nordisk Investigational Site

Gothenburg, , Sweden

Site Status

Novo Nordisk Investigational Site

Huddinge, , Sweden

Site Status

Novo Nordisk Investigational Site

Uppsala, , Sweden

Site Status

Novo Nordisk Investigational Site

Tainan City, , Taiwan

Site Status

Novo Nordisk Investigational Site

Taoyuan District, , Taiwan

Site Status

Novo Nordisk Investigational Site

Bangkok, , Thailand

Site Status

Novo Nordisk Investigational Site

Chiang Mai, , Thailand

Site Status

Novo Nordisk Investigational Site

Ankara, , Turkey (Türkiye)

Site Status

Novo Nordisk Investigational Site

Ankara, , Turkey (Türkiye)

Site Status

Novo Nordisk Investigational Site

Istanbul, , Turkey (Türkiye)

Site Status

Novo Nordisk Investigational Site

Kocaeli, , Turkey (Türkiye)

Site Status

Novo Nordisk Investigational Site

Birmingham, , United Kingdom

Site Status

Novo Nordisk Investigational Site

London, , United Kingdom

Site Status

Novo Nordisk Investigational Site

Manchester, , United Kingdom

Site Status

Novo Nordisk Investigational Site

Norwich, , United Kingdom

Site Status

Novo Nordisk Investigational Site

Southampton, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Australia Austria Belgium Brazil Canada Croatia Denmark Egypt France Germany Greece Hungary India Israel Italy Lebanon Malaysia Mexico Morocco Netherlands New Zealand North Macedonia Norway Poland Portugal Puerto Rico Romania Russia Serbia Spain Sweden Taiwan Thailand Turkey (Türkiye) United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Tamborlane WV, Barrientos-Perez M, Fainberg U, Frimer-Larsen H, Hafez M, Hale PM, Jalaludin MY, Kovarenko M, Libman I, Lynch JL, Rao P, Shehadeh N, Turan S, Weghuber D, Barrett T; Ellipse Trial Investigators. Liraglutide in Children and Adolescents with Type 2 Diabetes. N Engl J Med. 2019 Aug 15;381(7):637-646. doi: 10.1056/NEJMoa1903822. Epub 2019 Apr 28.

Reference Type BACKGROUND
PMID: 31034184 (View on PubMed)

Bensignor MO, Bomberg EM, Bramante CT, Divyalasya TVS, Hale PM, Ramesh CK, Rudser KD, Kelly AS. Effect of liraglutide treatment on body mass index and weight parameters in children and adolescents with type 2 diabetes: Post hoc analysis of the ellipse trial. Pediatr Obes. 2021 Aug;16(8):e12778. doi: 10.1111/ijpo.12778. Epub 2021 Feb 25.

Reference Type DERIVED
PMID: 33634589 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

Access external resources that provide additional context or updates about the study.

http://novonordisk-trials.com

Clinical Trials at Novo Nordisk

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2011-002605-29

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

P/288/2010

Identifier Type: OTHER

Identifier Source: secondary_id

U1111-1121-8743

Identifier Type: OTHER

Identifier Source: secondary_id

CTRI/2013/10/004082

Identifier Type: REGISTRY

Identifier Source: secondary_id

NN2211-3659

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

A Study in Patients With Type 2 Diabetes
NCT01408095 WITHDRAWN PHASE2
Glaser Obesity Study
NCT00209482 UNKNOWN PHASE2/PHASE3
Metformin & Inflammation in Pre-diabetic Children
NCT01394887 COMPLETED PHASE2/PHASE3
Precision Dosing of Metformin in Youth With T2D
NCT06120881 RECRUITING EARLY_PHASE1