A Study to Evaluate the Efficacy and Safety of Simtuzumab Combined With Gemcitabine for Metastatic Pancreatic Adenocarcinoma

NCT ID: NCT01472198

Last Updated: 2015-03-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

250 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-11-30

Study Completion Date

2015-02-28

Brief Summary

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This study will compare the efficacy of simtuzumab (GS-6624) versus placebo in combination with gemcitabine in adults with pancreatic cancer. The treatment phase of this study will be comprised of 2 sequential parts: an open label treatment phase and a double-blinded treatment phase.

Detailed Description

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Conditions

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Pancreatic Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Simtuzumab (open-label)

Participants will receive simtuzumab 700 mg plus gemcitabine in cycles of 28 days for up to 3 years.

Group Type EXPERIMENTAL

Simtuzumab

Intervention Type DRUG

Simtuzumab administered intravenously every 2 weeks for a total of 2 infusions (Days 1 and 15)

Gemcitabine

Intervention Type DRUG

Gemcitabine 1000 mg/m\^2 administered intravenously on Days 1, 8, and 15 of each 28-day cycle

Simtuzumab 200 mg (randomized)

Participants will receive simtuzumab 200 mg plus gemcitabine in cycles of 28 days for up to 3 years.

Group Type EXPERIMENTAL

Simtuzumab

Intervention Type DRUG

Simtuzumab administered intravenously every 2 weeks for a total of 2 infusions (Days 1 and 15)

Gemcitabine

Intervention Type DRUG

Gemcitabine 1000 mg/m\^2 administered intravenously on Days 1, 8, and 15 of each 28-day cycle

Simtuzumab 700 mg (randomized)

Participants will receive simtuzumab 700 mg plus gemcitabine in cycles of 28 days for up to 3 years.

Group Type EXPERIMENTAL

Simtuzumab

Intervention Type DRUG

Simtuzumab administered intravenously every 2 weeks for a total of 2 infusions (Days 1 and 15)

Gemcitabine

Intervention Type DRUG

Gemcitabine 1000 mg/m\^2 administered intravenously on Days 1, 8, and 15 of each 28-day cycle

Placebo (randomized)

Participants will receive placebo to match simtuzumab plus gemcitabine in cycles of 28 days for up to 3 years.

Group Type PLACEBO_COMPARATOR

Gemcitabine

Intervention Type DRUG

Gemcitabine 1000 mg/m\^2 administered intravenously on Days 1, 8, and 15 of each 28-day cycle

Placebo to match simtuzumab

Intervention Type DRUG

Placebo to match simtuzumab administered intravenously every 2 weeks for a total of 2 infusions (Days 1 and 15)

Interventions

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Simtuzumab

Simtuzumab administered intravenously every 2 weeks for a total of 2 infusions (Days 1 and 15)

Intervention Type DRUG

Gemcitabine

Gemcitabine 1000 mg/m\^2 administered intravenously on Days 1, 8, and 15 of each 28-day cycle

Intervention Type DRUG

Placebo to match simtuzumab

Placebo to match simtuzumab administered intravenously every 2 weeks for a total of 2 infusions (Days 1 and 15)

Intervention Type DRUG

Other Intervention Names

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GS-6624 Gemzar®

Eligibility Criteria

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Inclusion Criteria

* Initial diagnosis of metastatic pancreatic cancer must have occurred ≤6 weeks prior to the completion of screening.
* The presence of measurable metastatic pancreatic cancer documented by contrast enhanced CT (or MRI) scan in addition to 1 of the following:

1. Histological diagnosis of pancreatic adenocarcinoma confirmed by pathologist OR
2. Pathologist confirmed histological/cytological diagnosis of adenocarcinoma consistent with pancreatic origin in conjunction with either:

1. The presence of a mass in the pancreas OR
2. A history of resected pancreatic carcinoma
* Measurable disease per RECIST (ver. 1.1)
* ECOG Performance Status of 0 or 1.
* Adequate hepatic, hematologic and renal functions.

Exclusion Criteria

* A history or evidence of clinically significant disorder other than metastatic cancer of the pancreas.
* A diagnosis of pancreatic islet neoplasms.
* Subject has undergone major surgery other than diagnosis surgery within 4 weeks of randomization
* Presence of biliary obstruction requiring external drainage
* Brain metastases.
* Unstable cardiovascular function within the last 6 months of screening
* Clinically active liver disease, including active viral hepatitis (HBV or HCV) or cirrhosis
* Known HIV infection.
* Uncontrolled hypertension at Screening
* History or presence of any form of cancer, other than pancreatic cancer, within the 3 years prior to enrollment
* Prior or concurrent anti-tumor therapy (chemotherapy, antibody therapy, molecular targeted therapy, retinoid therapy, hormonal therapy) for the treatment of inoperable locally advanced or metastatic pancreatic cancer; prior radiotherapy and chemotherapy given as pre-operative neoadjuvant therapy or radio sensitizers for locally advanced pancreatic cancer are allowed.
* Uncontrolled systemic fungal, bacterial or viral infection
* Participation in an investigational drug or device trial with therapeutic intent within 30 days prior to study
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Zung Thai, MD

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Birmingham Hematology and Oncology Associates, LLC

Birmingham, Alabama, United States

Site Status

University of South Alabama Mitchell Cancer Institute

Mobile, Alabama, United States

Site Status

Central Hematology Oncology Medical Group, Inc.

Alhambra, California, United States

Site Status

Comprehensive Blood and Cancer Center

Bakersfield, California, United States

Site Status

California Cancer Associates for Research and Excellence (CCARE)

Fresno, California, United States

Site Status

Pacific Shores Medical Group

Long Beach, California, United States

Site Status

UCLA Community Oncology Practice

Los Angeles, California, United States

Site Status

Stanford University Medical Center

Palo Alto, California, United States

Site Status

Wilshire Oncology Medical Group, Inc.

Rancho Cucamonga, California, United States

Site Status

Sharp Health Care

San Diego, California, United States

Site Status

San Jose Medical Group

San Jose, California, United States

Site Status

Saint Mary's Regional Cancer Center

Grand Junction, Colorado, United States

Site Status

Hematology Oncology Associates, PC

Stamford, Connecticut, United States

Site Status

Florida Cancer Specialists

Tampa, Florida, United States

Site Status

Georgia Cancer Specialists, P.C.

Atlanta, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Oncology Hematology Care, Inc.

Crestview Hills, Kentucky, United States

Site Status

Anne Arundel Medical Center, Annapolis Oncology Center

Annapolis, Maryland, United States

Site Status

West Michigan Cancer Center

Kalamazoo, Michigan, United States

Site Status

Providence Cancer Center Oncology and Hematology Care Clinic-Eastside Portland

Southfield, Michigan, United States

Site Status

Hematology and Oncology Associates at BridgePoint

Tupelo, Mississippi, United States

Site Status

Saint Joseph Oncology, Inc.

Saint Joseph, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Montana Cancer Institute Foundation c/o Montana Cancer Specialists

Missoula, Montana, United States

Site Status

Comprehensive Cancer Centers of Nevada

Henderson, Nevada, United States

Site Status

Saint Luke's-Roosevelt Hospital Center

New York, New York, United States

Site Status

Beth Israel Comprehensive Cancer Center

New York, New York, United States

Site Status

Duke University Medical Center, Comprehensive Cancer Center

Durham, North Carolina, United States

Site Status

Emerywood Hematology and Oncology

High Point, North Carolina, United States

Site Status

Oncology Hematology Care, Inc.

Blue Ash, Ohio, United States

Site Status

PinnacleHealth

Harrisburg, Pennsylvania, United States

Site Status

Abington Hematology Oncology Associates, Inc.

Willow Grove, Pennsylvania, United States

Site Status

Charleston Hematology Oncology Associates, PA

Charleston, South Carolina, United States

Site Status

South Carolina Oncology Associates

Columbia, South Carolina, United States

Site Status

Tennessee Cancer Specialists

Knoxville, Tennessee, United States

Site Status

Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

Coastal Bend Cancer Center

Corpus Christi, Texas, United States

Site Status

University of Texas Southwestern Medical Center at Dallas

Dallas, Texas, United States

Site Status

San Antonio Military Medical Center

Fort Sam Houston, Texas, United States

Site Status

Center for Cancer and Blood Disorders, PC

Fort Worth, Texas, United States

Site Status

Joe Arrington Cancer Research and Treatment Center

Lubbock, Texas, United States

Site Status

Utah Cancer Specialists

Salt Lake City, Utah, United States

Site Status

Virginia Cancer Specialists, PC

Fairfax, Virginia, United States

Site Status

Virginia Cancer Institute

Richmond, Virginia, United States

Site Status

Republic Clinical Oncology Dispensary of the Ministry of Healthcare of Republic of Bashkortostan

Ufa, Bashkortostan Republic, Russia

Site Status

Regional Oncology Dispensary

Ivanovo, Ivanovo Oblast, Russia

Site Status

Medical Radiological Research Center of Russian Academy of Medical Sciences, Obninsk

Obninsk, Kaluga Oblast, Russia

Site Status

Kursk Regional Oncologic Dispensary

Kursk, Kursk Oblast, Russia

Site Status

Blokhin Cancer Research Center of Russia, Dept. of clinical pharmacology

Moscow, Moscow, Russia

Site Status

State Institution "Blokhin Cancer Research Centre RAMS"

Moscow, Moscow, Russia

Site Status

Non-State Institution of healthcare "Central Clinical Hospital #1 OAO RZD

Moscow, Moscow, Russia

Site Status

Non-state Healthcare Institution "N.A. Semashko Central Clinical Hospital #2 of JSC "Russian Railway

Moscow, Moscow, Russia

Site Status

State Institution of Healthcare "Arkhangelsk Regional Clinical Oncology Dispensary"

Arkhangelsk, Primorskiy (Maritime) Kray, Russia

Site Status

Republican Clinical Oncologic Dispensary of Ministry of health of Republic Tatarstan

Kazan', Tatarstan Republic, Russia

Site Status

State Budgetary Healthcare Institution "Nizhny Novgorod Regional Oncological Dispensary"

Nizhny Novgorod, , Russia

Site Status

Budgetary Healthcare Institution of Omsk Region "Clinical Oncologic Dispensary"

Omsk, , Russia

Site Status

Petrov Research Oncology Institute

Saint Petersburg, , Russia

Site Status

Countries

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United States Russia

References

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Benson AB 3rd, Wainberg ZA, Hecht JR, Vyushkov D, Dong H, Bendell J, Kudrik F. A Phase II Randomized, Double-Blind, Placebo-Controlled Study of Simtuzumab or Placebo in Combination with Gemcitabine for the First-Line Treatment of Pancreatic Adenocarcinoma. Oncologist. 2017 Mar;22(3):241-e15. doi: 10.1634/theoncologist.2017-0024. Epub 2017 Feb 28.

Reference Type DERIVED
PMID: 28246206 (View on PubMed)

Other Identifiers

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GS-US-324-0101

Identifier Type: -

Identifier Source: org_study_id

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