Pharmacokinetic Study of Fludarabine in Pediatric Hematopoietic Stem Cell Transplantation

NCT ID: NCT01472055

Last Updated: 2014-08-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

46 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-10-31

Study Completion Date

2014-09-30

Brief Summary

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The purpose of this study is to analysis of the pharmacokinetics of fludarabine for hematopoietic stem cell transplantation in pediatric patients.

Detailed Description

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Fludarabine is a commonly used chemotherapeutic agent for hematopoietic stem cell transplantation in children. However, no pharmacokinetic study has thus far been conducted in pediatric patients. Fludarabine can cause adverse reactions which include neurotoxicity, damage to lungs. Pharmacokinetic study is critical to predict the safety of fludarabine in pediatric patients.

Through an individualized pharmacokinetic study (which entails numerous samplings) of fludarabine in pediatric patients, this study aims to develop a sampling-minimized analysis method and study the population pharmacokinetics.

Through a pharmacokinetic analysis, we aim to evaluate whether pediatric patients show similar population pharmacokinetics of adults, for whom fludarabine is authorized, and evaluate the safety (toxicity) and efficacy (event free survival).

Conditions

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Acute Leukemia Chronic Leukemia Severe Aplastic Anemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Fludarabine

Analysis of the pharmacokinetics of fludarabine for hematopoietic stem cell transplantation in pediatric patients

Group Type EXPERIMENTAL

Fludarabine

Intervention Type DRUG

1. Fludarabine 40 mg/m\^2 once a day intravenous administration over 30 min
2. Development of sampling-minimized analysis method through individualized pharmacokinetics Sampling time: 0hr (pre-dose), 30 min (post-dose), 1hr, 3hr, 5hr, 8hr, 24hr
3. Population pharmacokinetics analysis
4. Comparative analysis of population pharmacokinetics in pediatric and adult patients
5. Analysis of population pharmacokinetics, toxicity, engraftment rate, survival rate

Interventions

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Fludarabine

1. Fludarabine 40 mg/m\^2 once a day intravenous administration over 30 min
2. Development of sampling-minimized analysis method through individualized pharmacokinetics Sampling time: 0hr (pre-dose), 30 min (post-dose), 1hr, 3hr, 5hr, 8hr, 24hr
3. Population pharmacokinetics analysis
4. Comparative analysis of population pharmacokinetics in pediatric and adult patients
5. Analysis of population pharmacokinetics, toxicity, engraftment rate, survival rate

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Conditioning regimen including fludarabine
2. Age: \< 19 years old
3. Functional class: ECOG 0-2
4. No loss of function of major organs. Criteria may be individualized.

* Heart: shortening fraction \> 30%, ejection fraction \> 45%.
* Liver: total bilirubin \< 2 ⅹ upper limit of normal; ALT \< 3 ⅹ upper limit of normal.
* Kidney: creatinine \< 2 ⅹ normal or a creatinine clearance (GFR) \> 60 ml/min/1.73m2.
5. No active viral or fungal infection
6. Appropriate hematopoietic stem cell donor
7. Informed consent from patients' parents

Exclusion Criteria

1. Pregnant or breast feeding
2. Disease progression due to clinical test
3. Psychiatric disease may interfere with clinical test
4. Whether attending physician consider the patient inappropriate for study enrollment
Maximum Eligible Age

19 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Ministry of Food and Drug Safety, Korea

OTHER_GOV

Sponsor Role collaborator

Seoul National University Hospital

OTHER

Sponsor Role lead

Principal Investigators

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Hyoung Jin Kang, MD., PhD

Role: PRINCIPAL_INVESTIGATOR

Seoul National University Hospital

Locations

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Seoul National University Hospital

Seoul, Daehangno, Jongno-gu, South Korea

Site Status RECRUITING

Countries

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South Korea

Central Contacts

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Hyoung Jin Kang, MD, PhD

Role: CONTACT

+82 2 2072 0177

Ji Won Lee, MD

Role: CONTACT

+82 2 2072 3452

Facility Contacts

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Hyoung Jin Kang, MD, PhD

Role: primary

+82 2 2072 0177

Ji Won Lee, MD

Role: backup

+82 2 2072 3452

Other Identifiers

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SNUCH-SCT-1101

Identifier Type: -

Identifier Source: org_study_id

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