A Study Being Conducted at Multiple Locations to Compare Safety and Efficacy of Three Different Regimens; (1) High-Dose Lenalidomide; (2) Lenalidomide + Azacitidine; or (3) Azacitidine in Subjects ≥ 65 Years With Newly-Diagnosed Acute Myeloid Leukemia

NCT ID: NCT01358734

Last Updated: 2019-06-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

88 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-04-27

Study Completion Date

2018-05-15

Brief Summary

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The study aim is to compare safety and efficacy of high-dose lenalidomide regimen, sequential azacitidine and lenalidomide and an azacitidine in persons ≥65 years with newly-diagnosed acute myeloid leukemia (AML).

Detailed Description

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On September 11, 2013, randomization into the continuous 50 mg lenalidomide only arm was temporarily suspended based on review of the data from the first 13 participants and a high rate of discontinuation (11/13 participants). The Data Monitoring Committee assessed the study data on September 20, 2013 and reported no safety concerns. The high rate of early discontinuation is inconsistent with the treatment duration required for testing the study primary endpoint of survival at one year. Consequently, Celgene has decided not to reopen the lenalidomide only arm.

Conditions

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Acute Myeloid Leukemia Acute Myelogenous Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Lenalidomide in combination with azacitidine

Repeated cycles of azacitidine 75 mg/m\^2/day subcutaneous (SC) on Days 1-7 and lenalidomide 50 mg/day by mouth (PO) on Days 8-28 followed by a 14-day break plus best supportive care

Group Type EXPERIMENTAL

Azacitidine

Intervention Type DRUG

Azacitidine at 75 mg/m\^2/day subcutaneous on Days 1-7

Lenalidomide

Intervention Type DRUG

Lenalidomide 50 mg PO daily x 28 days for the first 2 cycles then 25 mg PO daily x 28 days for the next 2 cycles followed by continuous 28-day cycles of lenalidomide 10 mg PO daily

Best Supportive Care (BSC)

Intervention Type OTHER

The use of BSC was considered as concomitant treatment and must be documented as concomitant medication.

BSC includes, but is not limited to, treatment with Red Blood Celll (RBC) or whole blood transfusions, fresh frozen plasma transfusions, platelet transfusions, antibiotic or antifungal therapy, and nutritional support

Lenalidomide - single agent

Lenalidomide 50 mg PO daily for 28 days for the first 2 cycles and lenalidomide 25 mg daily for 28 days for the next 2 cycles followed by continuous 28-day cycles of lenalidomide 10 mg daily PO plus best supportive care

Group Type EXPERIMENTAL

Lenalidomide

Intervention Type DRUG

Lenalidomide 50 mg PO daily x 28 days for the first 2 cycles then 25 mg PO daily x 28 days for the next 2 cycles followed by continuous 28-day cycles of lenalidomide 10 mg PO daily

Best Supportive Care (BSC)

Intervention Type OTHER

The use of BSC was considered as concomitant treatment and must be documented as concomitant medication.

BSC includes, but is not limited to, treatment with Red Blood Celll (RBC) or whole blood transfusions, fresh frozen plasma transfusions, platelet transfusions, antibiotic or antifungal therapy, and nutritional support

Azacitidine-single agent

Repeated cycles of azacitidine 75mg/m\^2/day subcutaneous on Days 1-7 followed by a 21-day break plus best supportive care

Group Type EXPERIMENTAL

Azacitidine

Intervention Type DRUG

Azacitidine at 75 mg/m\^2/day subcutaneous on Days 1-7

Best Supportive Care (BSC)

Intervention Type OTHER

The use of BSC was considered as concomitant treatment and must be documented as concomitant medication.

BSC includes, but is not limited to, treatment with Red Blood Celll (RBC) or whole blood transfusions, fresh frozen plasma transfusions, platelet transfusions, antibiotic or antifungal therapy, and nutritional support

Interventions

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Azacitidine

Azacitidine at 75 mg/m\^2/day subcutaneous on Days 1-7

Intervention Type DRUG

Lenalidomide

Lenalidomide 50 mg PO daily x 28 days for the first 2 cycles then 25 mg PO daily x 28 days for the next 2 cycles followed by continuous 28-day cycles of lenalidomide 10 mg PO daily

Intervention Type DRUG

Best Supportive Care (BSC)

The use of BSC was considered as concomitant treatment and must be documented as concomitant medication.

BSC includes, but is not limited to, treatment with Red Blood Celll (RBC) or whole blood transfusions, fresh frozen plasma transfusions, platelet transfusions, antibiotic or antifungal therapy, and nutritional support

Intervention Type OTHER

Other Intervention Names

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Vidaza Revlimid® CC-5013

Eligibility Criteria

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Inclusion Criteria

* Newly diagnosed acute myeloid leukemia (AML), AML with antecedent hematologic disorder or therapy-related AML
* Male or female subjects aged ≥ 65
* Eastern Cooperative Oncology Group (ECOG) performance status of 0, 1 or 2
* White blood cell (WBC) count ≤ 10 x 10⁹/L at screening

Exclusion Criteria

* Previous treatment with azacitidine, decitabine, cytarabine or lenalidomide
* Previous cytotoxic or biologic treatment of any kind for AML or prior use of targeted therapy agents.
* Suspected or proven acute promyelocytic leukemia
* Prior bone marrow or stem cell transplantation
* Candidate for allogeneic bone marrow or stem cell transplantation
* AML antecedent hematologic disorder such as chronic myelogenous leukemia or myeloproliferative neoplasms
* Presence of malignant disease within the previous 12 months with exceptions
Minimum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Robert Gale, MD

Role: STUDY_DIRECTOR

Celgene

Locations

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(210) University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

(180) University of California, San Diego

La Jolla, California, United States

Site Status

(240) Cedars-Sinai Medical Center

Los Angeles, California, United States

Site Status

(215) Hematology Oncology Medical Group

Orange, California, United States

Site Status

(130) UC Davis Medical Center

Sacramento, California, United States

Site Status

(200) Coastal Integrative Cancer Care

San Luis Obispo, California, United States

Site Status

(125) University of Stanford

Stanford, California, United States

Site Status

(115) University of Colorado Anschultz Cancer Center

Aurora, Colorado, United States

Site Status

(145) Mount Sinai Comprehensive Cancer Center

Miami Beach, Florida, United States

Site Status

(140) Rush University Medical Center

Chicago, Illinois, United States

Site Status

(185) The University of Kansas Cancer Center

Westwood, Kansas, United States

Site Status

(175) University Lousiville

Louisville, Kentucky, United States

Site Status

(195) Tulane University Hospital Tulane Cancer Center

New Orleans, Louisiana, United States

Site Status

(235) University of Minnesota

Minneapolis, Minnesota, United States

Site Status

(100) Washington University School of Medicine

St Louis, Missouri, United States

Site Status

(150) Billings Clinic

Billings, Montana, United States

Site Status

(165) Mount Sinai Medical Center New York

New York, New York, United States

Site Status

(160) The Western Pennsylvania Hospital- Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

(205) Greenville Hospital System

Greenville, South Carolina, United States

Site Status

(120) Avera Cancer Institute

Sioux Falls, South Dakota, United States

Site Status

(230) Tennessee Oncology, PLLC

Nashville, Tennessee, United States

Site Status

(105) University of Texas Southwestern Medical Center Simmons Comprehensive Cancer Center

Dallas, Texas, United States

Site Status

(155) Cancer Care Centers of South Texas

San Antonio, Texas, United States

Site Status

(135) University of Wisconsin

Madison, Wisconsin, United States

Site Status

(402) Tom Baker Cancer Centre

Calgary, Alberta, Canada

Site Status

(405) University of Alberta Hospital

Edmonton, Alberta, Canada

Site Status

(401) Cancer Care Manitoba

Winnipeg, Manitoba, Canada

Site Status

(403) Queen Elizabeth II Health Sciences Centre - VG Site

Halifax, Nova Scotia, Canada

Site Status

(404) The Ottawa Hospital

Ottawa, Ontario, Canada

Site Status

(400) Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Medeiros BC, McCaul K, Kambhampati S, Pollyea DA, Kumar R, Silverman LR, Kew A, Saini L, Beach CL, Vij R, Wang X, Zhong J, Gale RP. Randomized study of continuous high-dose lenalidomide, sequential azacitidine and lenalidomide, or azacitidine in persons 65 years and over with newly-diagnosed acute myeloid leukemia. Haematologica. 2018 Jan;103(1):101-106. doi: 10.3324/haematol.2017.172353. Epub 2017 Nov 2.

Reference Type DERIVED
PMID: 29097499 (View on PubMed)

Other Identifiers

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CC-5013-AML-001

Identifier Type: -

Identifier Source: org_study_id

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