A Study Of PF-05082566 As A Single Agent And In Combination With Rituximab

NCT ID: NCT01307267

Last Updated: 2020-03-17

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

190 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-06-21

Study Completion Date

2019-02-20

Brief Summary

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A study of PF-05082566, a 4-1BB agonist monoclonal antibody (mAb), in patients with solid tumors or b-cell lymphomas, and in combination with rituximab in patients with CD20 positive Non-Hodgkin's Lymphoma (NHL).

Detailed Description

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Conditions

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Lymphoma, Non-Hodgkin Lymphoma, Follicular Lymphoma, Large B-Cell, Diffuse Carcinoma, Non-Small-Cell Lung Carcinoma, Renal Cell Carcinoma, Squamous Cell of Head and Neck Malignant Melanoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Portion A

PF-05082566 single agent in patients with advanced cancer

Group Type EXPERIMENTAL

PF-05082566

Intervention Type DRUG

Intravenous, Dose escalation, once per month

Portion B

PF-05082566 in combination with rituximab in patients with Non-Hodgkin's Lymphoma

Group Type EXPERIMENTAL

rituximab

Intervention Type DRUG

Intravenous, 375 mg/m2, once per week for 4 weeks

PF-05082566

Intervention Type DRUG

IV, Dose escalation, once per month

Interventions

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PF-05082566

Intravenous, Dose escalation, once per month

Intervention Type DRUG

rituximab

Intravenous, 375 mg/m2, once per week for 4 weeks

Intervention Type DRUG

PF-05082566

IV, Dose escalation, once per month

Intervention Type DRUG

Other Intervention Names

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Rituxan, MabThera

Eligibility Criteria

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Inclusion Criteria

* Portion A: Histological or cytological diagnosis of advanced/metastatic solid tumor malignancy or B cell lymphoma, for which no curative therapy is available. Portion A expansion includes patients who have documented disease progression on a checkpoint inhibitor (anti CTLA 4, anti PD1/PD L1 antibodies) per RECIST criteria. Tumor types include metastatic melanoma, renal cell carcinoma (RCC), non-small cell lung cancer (NCSLC) and squamous cell carcinoma of the head and neck (SCCHN). Patients in the dose expansion stage are required to provide archival or baseline (obtained during the screening period) tumor biopsies.
* Portion B: Histological confirmed relapsed or refractory CD20 positive NHL for which no curative therapy is available. Patients enrolled in the expansion cohort must have archival tissue available, sampled within 6 months of study entry. The Expansion cohort includes patients with FL or DLBCL with relapsed or refractory disease.
* Measurable disease with at least one extranodal tumor mass \>1.0 cm in the greatest transverse diameter (GTD) or in the case of malignant lymph nodes \>1.5 cm in the GTD.
* ECOG performance status of ≤ 1.
* Adequate bone marrow function, for Portion A: absolute neutrophil count (ANC) ≥ 1.5 x 109/L, platelet count ≥100 x 109/L, hemoglobin \>9.0 g/dL. For Portion B: ANC ≥ 1.0 x 109/L, platelet count ≥ 75 x 109/L, and hemoglobin ≥ 8.0 g/dL. In both cases, patients must be transfusion independent at least 14 days prior to screening.
* Serum creatinine ≤ 2 x ULN or estimated creatinine clearance ≥ 50 ml/min.
* Total serum bilirubin ≤ 1.5 x ULN unless the patient has documented Gilbert syndrome and AST and ALT ≤ 2.5 x ULN.

Exclusion Criteria

* Patients with known symptomatic brain metastases requiring steroids.
* Prior allogeneic hematopoietic stem cell transplant.
* Immunosuppressive regimens involving systemic corticosteroids within 14 days before the first dose of study treatment.
* Therapeutic or experimental monoclonal antibodies within 28 day or prior radiation therapy within 14 days of the first dose of study drug.
* Autoimmune disorders and other diseases that compromise or impair the immune system.
* Unstable or serious concurrent medical conditions in the previous 6 months.
* Prior therapy with any anti CD137 monoclonal antibody.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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City of Hope

Duarte, California, United States

Site Status

UC San Diego Moores Cancer Center-Investigational Drug Services

La Jolla, California, United States

Site Status

UC San Diego Medical Center-La Jolla (Jacobs Medical Center/Thornton Hospital)

La Jolla, California, United States

Site Status

UC San Diego Moores Cancer Center

La Jolla, California, United States

Site Status

Research Administration Office: Clinical Research Unit

Los Angeles, California, United States

Site Status

Ronald Reagan UCLA Medical Center, Drug Information Center

Los Angeles, California, United States

Site Status

UCLA Bowyer Clinic

Los Angeles, California, United States

Site Status

UCLA Hematology-Oncology Clinic

Los Angeles, California, United States

Site Status

Stanford University Medical Center

Palo Alto, California, United States

Site Status

Stanford University Medical Center

Palo Alto, California, United States

Site Status

UC San Diego Medical Center - Hillcrest

San Diego, California, United States

Site Status

Santa Monica UCLA Hematology & Oncology Clinic

Santa Monica, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

Georgetown University Medical Center Department of Pharmacy, Research

Washington D.C., District of Columbia, United States

Site Status

MedStar Georgetown University Hospital

Washington D.C., District of Columbia, United States

Site Status

Emory University Hospital Midtown

Atlanta, Georgia, United States

Site Status

Emory University Hospital

Atlanta, Georgia, United States

Site Status

The Emory Clinic, Building A

Atlanta, Georgia, United States

Site Status

The Emory Clinic

Atlanta, Georgia, United States

Site Status

Winship Cancer Institute

Atlanta, Georgia, United States

Site Status

Brigham and Woman's Hospital

Boston, Massachusetts, United States

Site Status

Dana-Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

University of Michigan Health System

Ann Arbor, Michigan, United States

Site Status

Siteman Cancer Center - St. Peters

City of Saint Peters, Missouri, United States

Site Status

Siteman Cancer Center-West County

Creve Coeur, Missouri, United States

Site Status

Barnes-Jewish Hospital

St Louis, Missouri, United States

Site Status

Barnes-Jewish Hospital

St Louis, Missouri, United States

Site Status

Washington University Infusion Center Pharmacy

St Louis, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Siteman Cancer Center- South County

St Louis, Missouri, United States

Site Status

Memorial Sloan Kettering Cancer Center

New York, New York, United States

Site Status

The University of Texas - M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

South Texas Accelerated Research Therapeutics, LLC

San Antonio, Texas, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

Peter MacCallum Cancer Centre

Melbourne, Victoria, Australia

Site Status

Centre d'investigation clinique

Rennes, , France

Site Status

Az. Ospedaliera-Univer. di Bologna Policlinico S. Orsola Malpighi

Bologna, BO, Italy

Site Status

Ospedale San Raffaele di Milano

Milan, MI, Italy

Site Status

National Cancer Center Hospital East

Kashiwa, Chiba, Japan

Site Status

Akita University Hospital

Akita, , Japan

Site Status

The Cancer Institute Hospital of Japanese Foundation for Cancer Research

Tokyo, , Japan

Site Status

Countries

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United States Australia France Italy Japan

References

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Gopal AK, Levy R, Houot R, Patel SP, Popplewell L, Jacobson C, Mu XJ, Deng S, Ching KA, Chen Y, Davis CB, Huang B, Fly KD, Thall A, Woolfson A, Bartlett NL. First-in-Human Study of Utomilumab, a 4-1BB/CD137 Agonist, in Combination with Rituximab in Patients with Follicular and Other CD20+ Non-Hodgkin Lymphomas. Clin Cancer Res. 2020 Jun 1;26(11):2524-2534. doi: 10.1158/1078-0432.CCR-19-2973. Epub 2020 Mar 6.

Reference Type DERIVED
PMID: 32144134 (View on PubMed)

Segal NH, He AR, Doi T, Levy R, Bhatia S, Pishvaian MJ, Cesari R, Chen Y, Davis CB, Huang B, Thall AD, Gopal AK. Phase I Study of Single-Agent Utomilumab (PF-05082566), a 4-1BB/CD137 Agonist, in Patients with Advanced Cancer. Clin Cancer Res. 2018 Apr 15;24(8):1816-1823. doi: 10.1158/1078-0432.CCR-17-1922. Epub 2018 Mar 16.

Reference Type DERIVED
PMID: 29549159 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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2011-002799-17

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B1641001

Identifier Type: -

Identifier Source: org_study_id

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