Study To Test Whether PF-00547659 Is Safe And Improves Disease Symptoms In Patients With Crohn's Disease

NCT ID: NCT01276509

Last Updated: 2021-06-03

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

265 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-04-06

Study Completion Date

2015-10-09

Brief Summary

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Adults with Crohn's disease that is clinically active despite conventional treatment will be eligible for this study. Patients may receive one of three doses of PF-00547659 (experimental drug) or placebo (inactive drug). Disease activity will be measured every two weeks.

Detailed Description

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Conditions

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Crohn's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Drug Dose level 3- SC injection

Drug dose level 3 delivered SC, 3 doses separated by 4 weeks.

Group Type EXPERIMENTAL

PF-00547659 SC injection

Intervention Type DRUG

Drug dose level 3 delivered SC, 3 doses separated by 4 weeks

Placebo-SC Injection

Placebo delivered SC, 3 doses separated by 4 weeks.

Group Type PLACEBO_COMPARATOR

PF-00547659 SC injection

Intervention Type DRUG

Placebo delivered SC, 3 doses separated by 4 weeks

Drug Dose level 1- SC injection

Drug dose level 1 delivered SC, 3 doses separated by 4 weeks.

Group Type EXPERIMENTAL

PF-00547659 SC injection

Intervention Type DRUG

Drug dose level 1 delivered SC, 3 doses separated by 4 weeks

Drug Dose level 2-SC injection

Drug dose level 2 delievered SC, 3 doses separated by 4 weeks.

Group Type EXPERIMENTAL

PF-00547659 SC injection

Intervention Type DRUG

Drug dose level 2 delivered SC, 3 doses separated by 4 weeks

Interventions

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PF-00547659 SC injection

Drug dose level 3 delivered SC, 3 doses separated by 4 weeks

Intervention Type DRUG

PF-00547659 SC injection

Placebo delivered SC, 3 doses separated by 4 weeks

Intervention Type DRUG

PF-00547659 SC injection

Drug dose level 1 delivered SC, 3 doses separated by 4 weeks

Intervention Type DRUG

PF-00547659 SC injection

Drug dose level 2 delivered SC, 3 doses separated by 4 weeks

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subjects must have failed or are intolerant to anti-TNFs and/or immunosuppressants (AZA, 6-MP, and/or MTX).
* hsCRP greater than 3mg/L
* Ulcerations demonstrated by colonoscopy performed during screening or 8 weeks prior to screening

Exclusion Criteria

* Pregnant or breast feeding
* Short bowel syndrome due to multiple small bowel resections
* Presence of a stoma
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Clopton Clinic

Jonesboro, Arkansas, United States

Site Status

Gastroenterology Specialists of Arkansas

Jonesboro, Arkansas, United States

Site Status

Little Rock Diagnostic Clinic, P.A.

Little Rock, Arkansas, United States

Site Status

UCSD Medical Center-Thornton Hospital

La Jolla, California, United States

Site Status

Community Clinical Trials

Orange, California, United States

Site Status

Gastro Diagnostics

Orange, California, United States

Site Status

Inland Gastroenterology Medical Associates, Inc.

Redlands, California, United States

Site Status

BioMark Research Inc.

Whittier, California, United States

Site Status

Clinical Research of the Rockies

Lafayette, Colorado, United States

Site Status

Rocky Mountain Gastroenterology Associates

Thornton, Colorado, United States

Site Status

Connecticut Clinical Research Foundation

Bristol, Connecticut, United States

Site Status

Shands Endoscopy Center

Gainesville, Florida, United States

Site Status

Shands Hospital at the University of Florida

Gainesville, Florida, United States

Site Status

Shands Medical Plaza

Gainesville, Florida, United States

Site Status

Mayo Clinic Jacksonville

Jacksonville, Florida, United States

Site Status

Florida Center for Gastroenterology

Largo, Florida, United States

Site Status

Sylvester Comprehensive Cancer Center

Miami, Florida, United States

Site Status

University of Miami Hospital and Clinic

Miami, Florida, United States

Site Status

University of Miami Hospital

Miami, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Cirtus Ambulartory Surgery Center

Orlando, Florida, United States

Site Status

Internal Medicine Specialists

Orlando, Florida, United States

Site Status

Heartland Medical Research (Administrative Only)

Clive, Iowa, United States

Site Status

Iowa Digestive Disease Center

Clive, Iowa, United States

Site Status

Iowa Endoscopy Center (Colonoscopy Only)

Clive, Iowa, United States

Site Status

Metropolitan Gastroenterology Group, PC - Chevy Chase Clinical Research

Chevy Chase, Maryland, United States

Site Status

UMass Memorial Medical Center

Worcester, Massachusetts, United States

Site Status

University of Massachusetts Worcester

Worcester, Massachusetts, United States

Site Status

Center for Digestive Health

Troy, Michigan, United States

Site Status

Surgical Centers of Michigan

Troy, Michigan, United States

Site Status

Minneapolis Heart Institute, West Health Campus

Minneapolis, Minnesota, United States

Site Status

Noran Neurology Clinic

Minneapolis, Minnesota, United States

Site Status

Consulting Radiology (Xray testing only)

Plymouth, Minnesota, United States

Site Status

Minnesota Gastroenterology, P.A.

Plymouth, Minnesota, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

Surgery Center of Columbia

Columbia, Missouri, United States

Site Status

Audrain Medical Center

Mexico, Missouri, United States

Site Status

Center for Digestive and Liver Diseases, Inc.

Mexico, Missouri, United States

Site Status

Barnes-Jewish Hospital - Investigational Drug Services

St Louis, Missouri, United States

Site Status

Center for Advanced Medicine

St Louis, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Life Medi-Research And Management

Brooklyn, New York, United States

Site Status

New York Hospital Queens

Flushing, New York, United States

Site Status

Long Island Clinical Research Associates, LLP

Great Neck, New York, United States

Site Status

Nassau Gastroenterology Associates Office Based Surgery

Great Neck, New York, United States

Site Status

Nassau Gastroenterology Associates, P.C.

Great Neck, New York, United States

Site Status

North Shore Primary Care, P.C.

Great Neck, New York, United States

Site Status

Beth Israel Medical Center - Phillip Ambulatory Care Center

New York, New York, United States

Site Status

East side Endoscopy, LLC (for colonscopy testing only)

New York, New York, United States

Site Status

Lenox Hill Endoscopy Center

New York, New York, United States

Site Status

Premier Medical Group of the Hudson Valley

Poughkeepsie, New York, United States

Site Status

CTRC Hospital - UNC Memorial Hospital

Chapel Hill, North Carolina, United States

Site Status

North Carolina Memorial Hospital Endoscopy Center

Chapel Hill, North Carolina, United States

Site Status

UNC Hospitals Department of Pharmacy

Chapel Hill, North Carolina, United States

Site Status

UNC Hospitals Endoscopy

Chapel Hill, North Carolina, United States

Site Status

Hillsborough Campus

Hillsborough, North Carolina, United States

Site Status

Thomas Jefferson University Hospital

Philadelphia, Pennsylvania, United States

Site Status

The Offices of Dr. Vincent Armenio, M.D.

East Providence, Rhode Island, United States

Site Status

Pharma Resource

East Providence, Rhode Island, United States

Site Status

Bayside Endoscopy Center

Providence, Rhode Island, United States

Site Status

Nashville Medical Research Institute

Nashville, Tennessee, United States

Site Status

Pasadena Gastroenterology Associates, P.A. dba Digestive Health Center

Pasadena, Texas, United States

Site Status

University of Utah HSC

Salt Lake City, Utah, United States

Site Status

Charlottesville Gastroenterology Associates

Charlottesville, Virginia, United States

Site Status

Charlottesville Medical Research

Charlottesville, Virginia, United States

Site Status

University of Washington Medical Center

Seattle, Washington, United States

Site Status

Allegiance Research Specialists

Wauwatosa, Wisconsin, United States

Site Status

GI Associates

Wauwatosa, Wisconsin, United States

Site Status

AKH Wien Universitaetsklinik fuer Innere Medizin III

Vienna, , Austria

Site Status

UZ Gasthuisberg

Leuven, , Belgium

Site Status

Centre Hospitalier Universitaire de Liege

Liège, , Belgium

Site Status

Centre Hospitalier Universitaire de Liège - Labo Biologie Clinique

Liège, , Belgium

Site Status

Centre Hospitalier de Mouscron

Mouscron, , Belgium

Site Status

4-MHAT

Sofia, , Bulgaria

Site Status

MBAL Sofiamed OOD,Otdelenie po gastroenterologia

Sofia, , Bulgaria

Site Status

Vancouver Coastal Health - Vancouver General Hospital

Vancouver, British Columbia, Canada

Site Status

Vancouver Coastal Health - Vancouver Hospital

Vancouver, British Columbia, Canada

Site Status

Oshawa Clinic

Oshawa, Ontario, Canada

Site Status

Toronto Digestive Disease Associates Inc.

Vaughan, Ontario, Canada

Site Status

CHU Amiens Hopital Nord Service d'Hepato-Gastroenterologie

Amiens, , France

Site Status

Hopital Saint-Andre

Bordeaux, , France

Site Status

Hopital Beaujon- Essais cliniques

Clichy, , France

Site Status

Hopital de l'Archet 2 - CHU de Nice

Nice, , France

Site Status

Hopital Cochin-Essais Cliniques

Paris, , France

Site Status

Hopital Charles Nicolle

Rouen, , France

Site Status

Hopital Nord

Saint-Priest-en-Jarez, , France

Site Status

Hopital Rangueil

Toulouse, , France

Site Status

Charite - Campus Berlin Mitte Medizinische Klinik

Berlin, , Germany

Site Status

Krankenhaus Martha-Maria Halle-Doelau gGmbH

Halle, , Germany

Site Status

Universitaetsklinikum Schleswig-Holstein

Kiel, , Germany

Site Status

Universitaetsfrauenklinikum Schleswig-Holstein Medizinische Klinik I, Gastroenterologie/Hepatologie

Lübeck, , Germany

Site Status

Gastroenterologische Gemeinschaftspraxis Minden

Minden, , Germany

Site Status

Universitaetsklinikum Regensburg

Regensburg, , Germany

Site Status

Robert-Bosch-Krankenhaus

Stuttgart, , Germany

Site Status

Universitaetklinikum Ulm

Ulm, , Germany

Site Status

National Hospital Organization Hirosaki National Hospital

Hirosaki, Aomori, Japan

Site Status

National Hospital Organization Takasaki General Medical Center

Takasaki, Gunma, Japan

Site Status

Jikei University Hospital

Minato-ku, Tokyo, Japan

Site Status

Keio University Hospital

Shinjuku-ku, Tokyo, Japan

Site Status

Aichi Medical University Hospital

Aichi, , Japan

Site Status

Chiba University Hospital

Chiba, , Japan

Site Status

Yokohama City University Medical Center

Kanagawa, , Japan

Site Status

Academic Medical Center

Amsterdam, North Holland, Netherlands

Site Status

University Medical Center Groningen (UMCG)

Groningen, Provincie Groningen, Netherlands

Site Status

Maastricht University Medical Center

Maastricht, , Netherlands

Site Status

Asker And Baerum Hospital

Gjettum, , Norway

Site Status

Oslo Universitetssykehus

Oslo, , Norway

Site Status

Lovisenberg Diakonale Sykehus

Oslo, , Norway

Site Status

Szpital Uniwersytecki nr 2 im dr. Jana Bizieta w Bydgoszczy Centrum Endoskopii Zabiegowej

Bydgoszcz, , Poland

Site Status

Centrum Medyczne-Szpital Swietej Rodziny Sp. z o.o.

Lodz, , Poland

Site Status

Centralny Szpital Kliniczny Ministerstwa Spraw Wewnetrznych w Warszawie

Warsaw, , Poland

Site Status

Lexmedica

Wroclaw, , Poland

Site Status

Military Medical Academy

Belgrade, , Serbia

Site Status

Clinical Hospital Centre Bezanijska Kosa

Belgrade, , Serbia

Site Status

Clinical Center Nis Clinic for Gastroenterology and Hepatology

Niš, , Serbia

Site Status

Clinical Hospital Center Zemun

Zemun, , Serbia

Site Status

Gastroentero-Hepatologicke centrum THALION, LAMA MEDICAL CARE s.r.o.

Bratislava, , Slovakia

Site Status

Medak s.r.o.

Bratislava, , Slovakia

Site Status

Gastroenterologicke a hepatologicke centrum Nitra, KM Management spol. s r.o.

Nitra, , Slovakia

Site Status

Synergy group, a.s.

Nové Mesto nad Váhom, , Slovakia

Site Status

Wits Clinical Research

Johannesburg, Gauteng, South Africa

Site Status

Parklands Medical Centre

Durban, KwaZulu-Natal, South Africa

Site Status

Kingsbury Hospital

Cape Town, Western Cape, South Africa

Site Status

Pusan National University Hospital

Busan, , South Korea

Site Status

Yeungnam University Hospital

Daegu, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Kangbuk Samsung Hospital

Seoul, , South Korea

Site Status

Yonsei University College of Medicine, Severance Hospital

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Hospital Puerta de Hierro Majadahonda

Majadahonda, Madrid, Spain

Site Status

Hospital Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital Universitari Bellvitge

Barcelona, , Spain

Site Status

Hospital Universitario de La Princesa

Madrid, , Spain

Site Status

Hospital General Universitario Gregorio Maranon

Madrid, , Spain

Site Status

Corporacio Sanitaria Parc Tauli de Sabadell

Sabadell, , Spain

Site Status

Countries

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United States Austria Belgium Bulgaria Canada France Germany Japan Netherlands Norway Poland Serbia Slovakia South Africa South Korea Spain

References

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Saruta M, Park DI, Kim YH, Yang SK, Jang BI, Cheon JH, Im JP, Kanai T, Katsuno T, Ishiguro Y, Nagaoka M, Isogawa N, Li Y, Banerjee A, Ahmad A, Hassan-Zahraee M, Clare R, Gorelick KJ, Cataldi F, Watanabe M, Hibi T. Anti-MAdCAM-1 antibody (PF-00547659) for active refractory Crohn's disease in Japanese and Korean patients: the OPERA study. Intest Res. 2020 Jan;18(1):45-55. doi: 10.5217/ir.2019.00039. Epub 2020 Jan 30.

Reference Type DERIVED
PMID: 32013314 (View on PubMed)

Sandborn WJ, Lee SD, Tarabar D, Louis E, Klopocka M, Klaus J, Reinisch W, Hebuterne X, Park DI, Schreiber S, Nayak S, Ahmad A, Banerjee A, Brown LS, Cataldi F, Gorelick KJ, Cheng JB, Hassan-Zahraee M, Clare R, D'Haens GR. Phase II evaluation of anti-MAdCAM antibody PF-00547659 in the treatment of Crohn's disease: report of the OPERA study. Gut. 2018 Oct;67(10):1824-1835. doi: 10.1136/gutjnl-2016-313457. Epub 2017 Oct 5.

Reference Type DERIVED
PMID: 28982740 (View on PubMed)

Hassan-Zahraee M, Banerjee A, Cheng JB, Zhang W, Ahmad A, Page K, von Schack D, Zhang B, Martin SW, Nayak S, Reddy P, Xi L, Neubert H, Fernandez Ocana M, Gorelick K, Clare R, Vincent M, Cataldi F, Hung K. Anti-MAdCAM Antibody Increases ss7+ T Cells and CCR9 Gene Expression in the Peripheral Blood of Patients With Crohn's Disease. J Crohns Colitis. 2018 Jan 5;12(1):77-86. doi: 10.1093/ecco-jcc/jjx121.

Reference Type DERIVED
PMID: 28961803 (View on PubMed)

Related Links

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Other Identifiers

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2010-023437-30

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

OPERA

Identifier Type: OTHER

Identifier Source: secondary_id

A7281006

Identifier Type: -

Identifier Source: org_study_id

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