Short Stature Related Distress

NCT ID: NCT01246219

Last Updated: 2017-12-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-10-31

Study Completion Date

2017-11-30

Brief Summary

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The research aims to provide data on gender-related psychological impact of GH (Growth Hormone)treatment. Implicit measurable psychological metrics of the therapy outcome on males are to be evaluated in a Prospective Randomized Controlled Trial. As a secondary axis of the study, the investigators aim to provide descriptive documentation of the unique distress signal manifestation implicitly shown by Idiopathic Short Stature (ISS) boys and suggest methods of early detection and measurement of such manifestations that can be used to cement guidelines for the treatment in GH.

Detailed Description

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Study Design:

A prospective randomized, double blind, placebo controlled trial design, comparing four research groups, with 4 repeated psychological measures (before treatment, after 3 months,after 1 year, and at the end of treatment, after 4 years).

The study will be divided into two segments:

Segment 1:double blind, placebo controlled, will include the first 60 ISS (Idiopathic Short Stature)recruited patients. Patients in this segment will be randomized to one of the growth hormone treatment groups in a ratio of 2:1. 40 patients will be treated 4 years with GH and 20 patients will be treated with placebo at the first year of the study and will have the option to start GH treatment after one year, for a duration of 3 years.

Segment 2:after the enrollment to segment 1 will end, enrollment to segment 2 will begin.Participants in segment 2 (patients with ISS and short stature) will serve as control groups and therefore will not be treated with growth hormone. Patients in Segment 2 will be evaluated only once.

The 4 repeated psychological evaluations (before treatment,after 3 months, after 1 year, and at the end of treatment, after 4 years)will include the following:

1. Implicit Association Test
2. Masculine Self Image
3. Pictures Projective Test
4. The Rosenberg Self Esteem Scale-a self report measure of explicit self- esteem
5. Quality of Life Questionnaire
6. Silhouette Apperception Technique (SAT)- a self report measure assessing children's and adolescent's perception of their own body size compared with that of their age-related peers
7. Child Behavior Checklist

Conditions

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Idiopathic Short Stature Self Image

Keywords

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Idiopathic Short stature Self Image GH therapy Psychological distress

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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GH treatment

4 years of GH treatment

Group Type EXPERIMENTAL

GH treatment (Genotropin)

Intervention Type DRUG

4 years treatment with GH

Placebo

1 year treatment with placebo followed by optional 3 years of GH treatment

Group Type PLACEBO_COMPARATOR

1 year treatment with placebo followed by optional 3 years of GH treatment

Intervention Type DRUG

1 year treatment with placebo followed by optional 3 years of GH treatment

Non treatment group

Group Type NO_INTERVENTION

No interventions assigned to this group

Interventions

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GH treatment (Genotropin)

4 years treatment with GH

Intervention Type DRUG

1 year treatment with placebo followed by optional 3 years of GH treatment

1 year treatment with placebo followed by optional 3 years of GH treatment

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1 Segment 1 :Boys at the age range of 8-13 years 2. Segment 2: Boys at the age range of 12-17 years 3. Tanner stage 1 (segment 1 only) 4. more than 2 SD's (standard deviation) below the average height

Exclusion Criteria

1. Mental retardation,
2. Psychiatric illness,
3. Lack of informed consent\\assent.
4. Health status that required chronic treatment with steroids
Minimum Eligible Age

8 Years

Maximum Eligible Age

17 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role collaborator

Rabin Medical Center

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Moshe Phillip, Prof

Role: PRINCIPAL_INVESTIGATOR

Rabin Medical Center

Locations

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Schneider Children's Medical center

Petah Tikva, , Israel

Site Status

Countries

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Israel

References

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Shemesh-Iron M, Lazar L, Lebenthal Y, Nagelberg N, Tenenbaum A, Ezra R, Leffler N, Yackobovitch-Gavan M, Schoenberg-Taz M, Phillip M. Growth hormone therapy and short stature-related distress: A randomized placebo-controlled trial. Clin Endocrinol (Oxf). 2019 May;90(5):690-701. doi: 10.1111/cen.13944. Epub 2019 Mar 7.

Reference Type DERIVED
PMID: 30721549 (View on PubMed)

Other Identifiers

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rmc004981ctil

Identifier Type: -

Identifier Source: org_study_id