Post-transplant Cyclophosphamide and Sirolimus Following Reduced Intensity Conditioning (RIC) Transplant

NCT ID: NCT01244906

Last Updated: 2015-05-01

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

26 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-12-31

Study Completion Date

2014-12-31

Brief Summary

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This trial will evaluate the safety and efficacy of post-transplant Cy and sirolimus following reduced intensity allogeneic SCT. It is hoped that the combination of a reduced intensity preparative regimen with a calcineurin-free GVHD prophylaxis regimen will decrease the risk of acute and chronic GVHD, by both limiting mucosal toxicity and augmenting immune reconstitution, thereby improving the safety of the procedure. The past experience with post-transplant Cy suggests that SCT recipients will attain rapid donor T cell chimerism, which the investigators hope will translate into improved disease control through the well documented graft-versus-malignancy effects of donor T cells.

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Detailed Description

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Conditions

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Hematologic Neoplasms

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Reduced Intensity Allogeneic Stem Cell Transplantation

All patients will receive fludarabine, busulfan and cyclophosphamide as the conditioning regimen prior to an allo SCT. Patients will then receive 2 doses of cyclophosphamide post-transplant and utilize sirolimus and mycophenolate mofetil (in mismatched transplants) as GVHD prophylaxis.

Group Type EXPERIMENTAL

Allogeneic Hematopoietic Stem Cell Transplantation

Intervention Type PROCEDURE

Patients will receive fludarabine, busulfan and cyclophosphamide as the conditioning regimen prior to an allo SCT. Patients will then receive 2 doses of cyclophosphamide post-transplant and utilize sirolimus and mycophenolate mofetil (in mismatched transplants) as GVHD prophylaxis.

Interventions

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Allogeneic Hematopoietic Stem Cell Transplantation

Patients will receive fludarabine, busulfan and cyclophosphamide as the conditioning regimen prior to an allo SCT. Patients will then receive 2 doses of cyclophosphamide post-transplant and utilize sirolimus and mycophenolate mofetil (in mismatched transplants) as GVHD prophylaxis.

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Availability of a 7/8 or 8/8 (HLA-A, B, C, DR) related or unrelated donor
* Age 18-75
* One of the following high-risk malignancies
* Chronic Myelogenous Leukemia
* Acute Myelogenous Leukemia
* Myelodysplastic Syndrome
* Myelofibrosis
* Acute Lymphocytic Leukemia
* Acute Lymphoblastic Lymphoma
* Chronic Lymphocytic Leukemia
* Prolymphocytic Leukemia
* Low-grade non-Hodgkin's Lymphoma
* Mantle Cell Lymphoma
* Hodgkin Lymphoma
* Myeloma

Exclusion Criteria

* Poor cardiac function (EF \<40%)
* Poor pulmonary function (FEV1 and FVC \<50% predicted)
* Poor liver function (bilirubin \>/= 2 mg/dl not due to hemolysis, Gilbert's or primary malignancy)
* Poor renal function (creatinine \>/= 2 mg/dl or creatinine clearance \<40mL/min)
* Karnofsky status \<70%
* HIV positive
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Blood and Marrow Transplant Group of Georgia

OTHER

Sponsor Role collaborator

Northside Hospital, Inc.

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Scott R Solomon, MD

Role: PRINCIPAL_INVESTIGATOR

Blood and Marrow Transplant Group of Georgia

Locations

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Northside Hospital

Atlanta, Georgia, United States

Site Status

Countries

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United States

References

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Other Identifiers

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NSH 911

Identifier Type: -

Identifier Source: org_study_id

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