Studying First Line Treatment of Chronic Myeloid Leukemia (CML) in a Real-world Setting

NCT ID: NCT01244750

Last Updated: 2022-06-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

1494 participants

Study Classification

OBSERVATIONAL

Study Start Date

2010-12-02

Study Completion Date

2020-01-08

Brief Summary

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The purpose of this study is to better understand the use of tyrosine kinase inhibitors (TKI) in patients newly diagnosed with CML and their quality of life in a real-world setting.

Detailed Description

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Time Perspective : Most patients are expected to be a mix of retrospective and prospective data collection. Patients can be enrolled after their study index date (retrospective component) and have to be followed until 5 years from study index date are complete (time between enrollment and 5 year follow-up is the prospective component)

Conditions

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Chronic Myeloid Leukemia

Study Design

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Observational Model Type

COHORT

Study Time Perspective

OTHER

Study Groups

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First line TKI treatment: Imatinib

Diagnosed CML patients who receive first line TKI treatment: Imatinib

No interventions assigned to this group

First line TKI treatment: Nilotinib

Diagnosed CML patients who receive first line TKI treatment: Nilotinib

No interventions assigned to this group

First line TKI treatment: Dasatinib

Diagnosed CML patients who receive first line TKI treatment: Dasatinib

No interventions assigned to this group

Imatinib treated patients

Imatinib treated patients if their study index date is between January 2, 2008 and September 30, 2010

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

* Newly-diagnosed chronic phase chronic myeloid leukemia (CP-CML) patients who started their first-line Tyrosine Kinase Inhibitor (TKI) treatment on imatinib, dasatinib or nilotinib in accordance with the timelines below
* 18 years or older at time of of CP-CML diagnosis

a) Imatinib Cohorts
* Patients who started their first-line Imatinib treatment between January 2, 2008 and September 30, 2010.Patients fitting this criterion are defined as retrospective Imatinib patients
* Patients who started their first-line Imatinib treatment on or after October 1, 2010

b) Dasatinib Cohort
* Patients who started their first-line Dasatinib treatment after the drug was approved in this indication

c) Nilotinib Cohort
* Patients who started their first-line Nilotinib treatment after the drug was approved in this indication
* Patients are also eligible when they have already switched to a subsequent therapy (TKI or other) at the time of enrollment, as long as their first-line and subsequent CML treatment information is available at site for data entry into the study Electronic Case Report Form (eCRF)
* Receiving treatment at medical practice (eg. community-based, office-based, hospital-based, academic setting, oncology center)

Exclusion Criteria

* Patients who are participating in an interventional trial which may influence the management of their CML disease will be excluded

Discontinuation Criteria:

* Enrolled patients who join an interventional trial which may influence the management of their CML disease will be excluded at the time of entry into the interventional trial
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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ICON Clinical Research

INDUSTRY

Sponsor Role collaborator

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Northwest Alabama Cancer Center

Muscle Shoals, Alabama, United States

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Arizona Oncology Associates, PC - HAL

Phoenix, Arizona, United States

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Arizona Oncology Associates, PC - NAHOA

Sedona, Arizona, United States

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Arizona Oncology Associates, PC - HOPE

Tucson, Arizona, United States

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Genesis Cancer Center

Hot Springs, Arkansas, United States

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NEA Baptist Clinic

Jonesboro, Arkansas, United States

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Little Rock Hematology Oncology Associates

Little Rock, Arkansas, United States

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Pacific Cancer Medical Center, Inc

Anaheim, California, United States

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Southwest Cancer Care Medical Group

Escondido, California, United States

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Wilshire Oncology Medical Group, Inc

Glendora, California, United States

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University of Southern California

Los Angeles, California, United States

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St. Joseph's Hospital

Orange, California, United States

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PMK Medical Group, Inc. DBA Ventura

Oxnard, California, United States

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Stockton Hematology Oncology

Stockton, California, United States

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Tahoe Forest Health System Cancer Center

Truckee, California, United States

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Rocky Mountain Cancer Centers

Boulder, Colorado, United States

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Medical Oncology and Blood Disorders, LLP

Manchester, Connecticut, United States

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Stamford Hospital

Stamford, Connecticut, United States

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Washington Hospital Center, Washington Cancer Institute

Washington D.C., District of Columbia, United States

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George Washington University

Washington D.C., District of Columbia, United States

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Hematology And Medical Oncology Of Southern Palm Beach County

Boynton Beach, Florida, United States

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Broward Oncology Associates

Fort Lauderdale, Florida, United States

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Palm Springs Research Institute

Hialeah, Florida, United States

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Baptist Cancer Institute

Jacksonville, Florida, United States

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University Of Florida

Jacksonville, Florida, United States

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Watson Clinic

Lakeland, Florida, United States

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Central Florida Health Alliance

Leesburg, Florida, United States

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Baptist Cancer Center

Miami, Florida, United States

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Florida Cancer Specialists

New Port Richey, Florida, United States

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Cancer Centers of Florida

Orlando, Florida, United States

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Lake County Oncology and Hematology

Tavares, Florida, United States

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Space Coast Cancer Center

Titusville, Florida, United States

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Peachtree Hematology-Oncology

Atlanta, Georgia, United States

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Emory University

Atlanta, Georgia, United States

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Northwest Georgia Oncology Centers, PC

Marietta, Georgia, United States

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Georgia Cancer Specialist

Sandy Springs, Georgia, United States

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Lewis Hall Singeltary Oncology Center

Thomasville, Georgia, United States

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OnCare

Honolulu, Hawaii, United States

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Straub Clinical & Hospital

Honolulu, Hawaii, United States

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Kaiser Permanente Honolulu

Honolulu, Hawaii, United States

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Mahafzah Medical Center

Evergreen Park, Illinois, United States

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Delnor Community Hospital

Geneva, Illinois, United States

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Mid-Illinois Hem/Onc Asoc

Normal, Illinois, United States

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North Chicago VA Medical Center

North Chicago, Illinois, United States

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Southern Illinois School of Medicine

Springfield, Illinois, United States

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Carle Cancer Center

Urbana, Illinois, United States

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Central DuPage Hospital

Winfield, Illinois, United States

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Saint John's Cancer Center

Anderson, Indiana, United States

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Indiana Blood and Marrow Transplantation

Indianapolis, Indiana, United States

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Investigative Clinical Research of Indiana

Indianapolis, Indiana, United States

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Horizon Oncology Research, Inc

Lafayette, Indiana, United States

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Cancer Care Center, Inc. PC

New Albany, Indiana, United States

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N. Iowa Mercy Cancer Center

Mason City, Iowa, United States

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Hutchinson Clinic

Hutchinson, Kansas, United States

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Cotton O'Neil Cancer Center

Topeka, Kansas, United States

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Cancer Center of Kansas

Wichita, Kansas, United States

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Central Baptist Hospital

Lexington, Kentucky, United States

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University of Louisville Hospital - Brown Cancer Center

Louisville, Kentucky, United States

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Consultants In Blood Disorders

Saint Matthews, Kentucky, United States

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Ochsner Clinic Foundation

New Orleans, Louisiana, United States

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Willis-Knighton Cancer System

Shreveport, Louisiana, United States

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Maryland Oncology Hematology Pa

Columbia, Maryland, United States

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Frederick Memorial Hospital

Frederick, Maryland, United States

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Sturdy Hematology & Oncology Associates

Attleboro, Massachusetts, United States

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Boston VA Healthcare System

Boston, Massachusetts, United States

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South Coast Health System

Fall River, Massachusetts, United States

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Commonwealth Hematology-Oncology, P.C.

Quincy, Massachusetts, United States

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UMass Medical Center

Worcester, Massachusetts, United States

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Cancer & Hematology Centers of Western Michigan

Grand Rapids, Michigan, United States

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West Michigan Cancer Center

Kalamazoo, Michigan, United States

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Michigan State University

Lansing, Michigan, United States

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North Mississippi Hematology & Oncology

Tupelo, Mississippi, United States

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St John's Clinic for Cancer and Hematology

Springfield, Missouri, United States

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Billings Clinic

Billings, Montana, United States

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Omaha VAMC

Omaha, Nebraska, United States

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Portsmouth Regional Hospital

Portsmouth, New Hampshire, United States

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Bms Clinical Research Center

Does Not Exist, New Jersey, United States

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Hackensack University Medical Center

Hackensack, New Jersey, United States

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Hematology-Oncology Associates of Northern NJ, PA

Morristown, New Jersey, United States

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Southern Oncology Hematology

Vineland, New Jersey, United States

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Broome Oncology

Johnson City, New York, United States

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Advanced Oncology

New York, New York, United States

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St. Lukes Roosevelt Medical Center

New York, New York, United States

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Vassar Brothers Medical Center

Poughkeepsie, New York, United States

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Stony Brook University Hospital

Stony Brook, New York, United States

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Montefiore Medical Center / AECOM

The Bronx, New York, United States

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Alamance Regional Cancer Center

Burlington, North Carolina, United States

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Waverly Hematology Oncology

Cary, North Carolina, United States

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Duke University Medical Center

Durham, North Carolina, United States

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Gaston Hematology Oncology

Gastonia, North Carolina, United States

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East Carolina University

Greenville, North Carolina, United States

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Akron General Medical Center

Akron, Ohio, United States

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Gabrail Cancer Center

Canton, Ohio, United States

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Signal Point Clinical Research Center, LLC

Middletown, Ohio, United States

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Medical Center of Newark

Newark, Ohio, United States

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Cancer Care Associates

Tulsa, Oklahoma, United States

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Oregon Health & Science University

Portland, Oregon, United States

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Hematology/Oncology Salem LLP

Salem, Oregon, United States

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Lehigh Valley Hospital

Allentown, Pennsylvania, United States

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St. Luke's Hospital and Health Network

Bethlehem, Pennsylvania, United States

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Medical Oncology Associates of Wyoming Valley, PC

Kingston, Pennsylvania, United States

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Lancaster General Health

Lancaster, Pennsylvania, United States

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Veterans Research Foundation of Pittsburgh

Pittsburgh, Pennsylvania, United States

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Berks Hematology-Oncology

West Reading, Pennsylvania, United States

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Geisinger Health System

Wilkes-Barre, Pennsylvania, United States

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Cancer Care Association Of York

York, Pennsylvania, United States

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Hematology and Oncology Associates of RI

Cranston, Rhode Island, United States

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The Cancer Center at Memorial Hospital

Pawtucket, Rhode Island, United States

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Charleston Cancer Center

Charleston, South Carolina, United States

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Avera Research Institute

Sioux Falls, South Dakota, United States

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Prairie Lakes Healthcare System, Inc

Watertown, South Dakota, United States

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Tennessee Cancer Specialists

Knoxville, Tennessee, United States

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University of Tennessee Medical Center

Knoxville, Tennessee, United States

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Texas Oncology

Amarillo, Texas, United States

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Texas Oncology - Arlington South

Arlington, Texas, United States

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Texas Oncology-Austin North

Austin, Texas, United States

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Julie & Ben Rogers Cancer Institute

Beaumont, Texas, United States

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Texas Oncology-Medical City Dallas

Dallas, Texas, United States

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Texas Oncology-Dallas Presbyterian Hospital

Dallas, Texas, United States

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Texas Oncology-Methodist Charlton Cancer Center

Dallas, Texas, United States

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MD Anderson Cancer Center

Houston, Texas, United States

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Michael DeBakey VA Medical Center

Houston, Texas, United States

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Texas Oncology

Lewisville, Texas, United States

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Texas Oncology-McAllen South Second

McAllen, Texas, United States

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Texas Oncology

Mesquite, Texas, United States

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Texas Oncology-Midland Allison Cancer Center

Midland, Texas, United States

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Texas Oncology-Odessa West Texas Cancer Center

Odessa, Texas, United States

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Texas Oncology

Paris, Texas, United States

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North Texas Regional Cancer Center

Plano, Texas, United States

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Cancer Care Centers of South Texas

San Antonio, Texas, United States

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Texas Oncology

Waco, Texas, United States

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Danville Hematology & Oncology

Danville, Virginia, United States

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Hematology Oncology Associates of Fredricksburg

Fredericksburg, Virginia, United States

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Peninsula Cancer Institute

Newport News, Virginia, United States

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Blue Ridge Cancer Care

Roanoke, Virginia, United States

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Swedish Cancer Institute-Eastside Hematology/Oncology

Bellevue, Washington, United States

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Providence Cancer Center at Sacred Heart Medical Center

Spokane, Washington, United States

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Wenatchee Valley Medical Center

Wenatchee, Washington, United States

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Yakima Valley Memorial Hospital/North Star Lodge

Yakima, Washington, United States

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Charleston Area Medical Center

Charleston, West Virginia, United States

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City Hospital - West Virginia University Hospital East

Martinsburg, West Virginia, United States

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Wheeling Hospital

Wheeling, West Virginia, United States

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Aspirus Regional Cancer Center

Wausau, Wisconsin, United States

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Local Institution

Blois, , France

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Bordeaux, , France

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Chalon/Saone Cedex, , France

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Chambéry, , France

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Le Mans, , France

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Pierre-Bénite, , France

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Pringy, , France

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Amberg, , Germany

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Aschaffenburg, , Germany

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Baden-Baden, , Germany

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Bamberg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bonn, , Germany

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Bottrop, , Germany

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Coburg, , Germany

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Cologne, , Germany

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Cologne, , Germany

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Darmstadt, , Germany

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Essen, , Germany

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Frankfurt am Main, , Germany

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Frankurt Am Main, , Germany

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Greifswald, , Germany

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Hamm, , Germany

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Hof, , Germany

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Idar-Oberstein, , Germany

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Kaiserslautern, , Germany

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Kassel, , Germany

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Koblenz, , Germany

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Landshut, , Germany

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Lebach, , Germany

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Leipzig, , Germany

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Mülheim A. D. Ruhr, , Germany

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Offenbach, , Germany

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Potsdam, , Germany

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Rostock, , Germany

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Rötha, , Germany

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Singen, , Germany

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Soest, , Germany

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Ulm, , Germany

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Velbert, , Germany

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Weiden, , Germany

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Würzburg, , Germany

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Bari, , Italy

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Brescia, , Italy

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Brindisi, , Italy

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Catania, , Italy

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Florence, , Italy

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Milan, , Italy

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Milan, , Italy

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Modena, , Italy

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Monza, , Italy

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Pavia, , Italy

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Perugia, , Italy

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Pesaro, , Italy

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Rionero in Vulture, , Italy

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Roma, , Italy

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Rome, , Italy

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Rome, , Italy

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Siena, , Italy

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Terni, , Italy

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Udine, , Italy

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Hoofddorp, , Netherlands

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Puerto Rico Hematology Oncology Group

Bayamón, , Puerto Rico

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Saint Petersburg, , Russia

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Santiago de Compostela-A Coruña, Spain, Spain

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A Coruña, , Spain

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Oviedo - Asturias, , Spain

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Pamplona, , Spain

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Salamanca, , Spain

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Local Insitution

Toledo, , Spain

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Countries

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United States France Germany Italy Netherlands Puerto Rico Russia Spain

References

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Hehlmann R, Cortes JE, Zyczynski T, Gambacorti-Passerini C, Goldberg SL, Mauro MJ, Michallet M, Simonsson B, Williams LA, Gajavelli S, DeGutis I, Sen GP, Paquette RL. Tyrosine kinase inhibitor interruptions, discontinuations and switching in patients with chronic-phase chronic myeloid leukemia in routine clinical practice: SIMPLICITY. Am J Hematol. 2019 Jan;94(1):46-54. doi: 10.1002/ajh.25306. Epub 2018 Oct 31.

Reference Type DERIVED
PMID: 30290003 (View on PubMed)

Related Links

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Other Identifiers

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CA180-330

Identifier Type: -

Identifier Source: org_study_id

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