Bosutinib For Autosomal Dominant Polycystic Kidney Disease

NCT ID: NCT01233869

Last Updated: 2016-03-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

172 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-12-31

Study Completion Date

2014-08-31

Brief Summary

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This purpose of this study is to determine if bosutinib reduces the rate of kidney enlargement in subjects with autosomal dominant polycystic kidney disease (ADPKD) entering the study with a total kidney volume greater than or equal to 750 cc and eGFR greater than or equal to 60 mL/min/1.73m2.

Detailed Description

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Conditions

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Polycystic Kidney, Autosomal Dominant

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Cohort A

Group Type EXPERIMENTAL

Bosutinib

Intervention Type DRUG

Once daily oral dose of 200 mg of bosutinib

Cohort B

Group Type EXPERIMENTAL

Bosutinib

Intervention Type DRUG

Once daily oral dose of 400 mg of bosutinib transitioned to 200 mg/day

Cohort C

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Once daily oral dose of placebo

Interventions

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Bosutinib

Once daily oral dose of 200 mg of bosutinib

Intervention Type DRUG

Bosutinib

Once daily oral dose of 400 mg of bosutinib transitioned to 200 mg/day

Intervention Type DRUG

Placebo

Once daily oral dose of placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Males and females, 18 to 50 years old at the time of consent.
* Documented diagnosis of ADPKD (PKD-1 or PKD-2 genotypes allowed).
* Total kidney volume ≥ 750 cc, as measured by centrally evaluated MRI.

Exclusion Criteria

* eGFR \< 60 mL/min/1.73m2.
* Uncontrolled hypertension (defined as systolic blood pressure ≥140 or diastolic blood pressure ≥90 mm Hg).
* Any previous exposure to the bosutinib test article or receipt of other polycystic kidney disease (PKD) therapies.
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Southwest Kidney Institute, PLC

Phoenix, Arizona, United States

Site Status

Southwest Clinical Research Institute, LLC

Tempe, Arizona, United States

Site Status

Southwest Kidney Institute, PLC

Tempe, Arizona, United States

Site Status

Capital Nephrology Clinical Research

Sacramento, California, United States

Site Status

Boise Kidney & Hypertension Institute, PLLC

Caldwell, Idaho, United States

Site Status

Boise Kidney & Hypertension Institute, PLLC

Meridian, Idaho, United States

Site Status

Renal Associates of Baton Rouge

Baton Rouge, Louisiana, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

New York University - HHC CTSI Clinical Research Center

New York, New York, United States

Site Status

Doylestown Hospital MRI

Doylestown, Pennsylvania, United States

Site Status

Doylestown Hospital

Doylestown, Pennsylvania, United States

Site Status

Nephrology/Hypertension Specialists

Doylestown, Pennsylvania, United States

Site Status

Renal Associates, PA

San Antonio, Texas, United States

Site Status

San Antonio Kidney Disease Center Physicians Group, P.L.L.C.

San Antonio, Texas, United States

Site Status

University of Virginia Health System - Nephrology

Charlottesville, Virginia, United States

Site Status

University of Virginia Health System

Charlottesville, Virginia, United States

Site Status

The Polyclinic

Seattle, Washington, United States

Site Status

Renal Remission and Hypertension Clinic

Silverdale, Washington, United States

Site Status

Monash Medical Centre

Clayton, Victoria, Australia

Site Status

Toronto General Hospital

Toronto, Ontario, Canada

Site Status

Hopital du Sacre-Coeur de Montreal

Montreal, Quebec, Canada

Site Status

Klinika gerontologicka a metabolicka

Hradec Králové, , Czechia

Site Status

Krajska nemocnice Liberec

Liberec, , Czechia

Site Status

Nemocnice Nove Mesto na Morave

Nové Město na Moravě, , Czechia

Site Status

Fakultni poliklinika VFN

Prague, , Czechia

Site Status

Vseobecna fakultni nemocnice v Praze

Prague, , Czechia

Site Status

Pharmaceutical Research Associates CZ, s.r.o.

Prague, , Czechia

Site Status

PRA Magyarorszag Kft. Klinikai Farmakologiai Vizsgalohely

Budapest, , Hungary

Site Status

Fovarosi Onkormanyzat Szent Imre Korhaz BSZMI Klinikai Farmakologiai Reszlege

Budapest, , Hungary

Site Status

Szegedi Tudomanyegyetem, AOK, Szent-Gyorgyi Albert Klinikai Kozpont I.sz.Belgyogyaszati Klinika

Szeged, , Hungary

Site Status

Istituti Ospitalieri di Cremona

Cremona, , Italy

Site Status

A.O. Universitaria Ospedali Riuniti di Foggia

Foggia, , Italy

Site Status

Vilnius University Hospital Santariskiu Clinic, Public Institution, Centre of Nephrology

Vilnius, , Lithuania

Site Status

Spitalul Clinic Republican

Chisinau, , Moldova

Site Status

Zaklad Diagnostyki Chorob Serca, II Katedra Kardiologii

Gdansk, , Poland

Site Status

Klinika Nefrologii, Transplantologii i Chorob Wewnetrznych

Gdansk, , Poland

Site Status

Specjalistyczny Szpital Zachodni im. Jana Pawla II w Grodzisku Mazowieckim

Grodzisk Mazowiecki, , Poland

Site Status

Krakowskie Centrum Medyczne NZOZ

Krakow, , Poland

Site Status

Klinika Nefrologii, Hipertensjologii i Chorob Wewnetrznych Katedry Chorob Wewnetrznych UWM

Olsztyn, , Poland

Site Status

Pracownia Echokardiografii, Oddzial Kardiologii

Olsztyn, , Poland

Site Status

Centrum Medyczne Aesculap

Radom, , Poland

Site Status

Klinika Kardiologii

Szczecin, , Poland

Site Status

Klinika Nefrologii, Transplantologii i Chorob Wewnetrznych

Szczecin, , Poland

Site Status

Szpital Powiatowy w Wolominie

Wołomin, , Poland

Site Status

SPZOZ Akademicki Szpital Kliniczny im. J. Mikulicza - Radeckiego

Wroclaw, , Poland

Site Status

Spitalul Clinic Municipal Dr. Gavril Curteanu Oradea

Oradea, Jud. Bihor, Romania

Site Status

Spitalul Clinic Dr. C. I. Parhon Iasi

Iași, Jud. Iasi, Romania

Site Status

Institutul Clinic Fundeni, Centrul de Medicina Interna-Nefrologie

Bucharest, , Romania

Site Status

SPITALUL CLINIC JUDETEAN DE URGENTA TIMISOARA ,Clinica de Nefrologie

Timișoara, , Romania

Site Status

Univerzitna nemocnica Bratislava

Limbova 5, Bratislava Region, Slovakia

Site Status

SUMMIT CLINICAL RESEARCH, s.r.o., Oddelenie internej mediciny a klinickej farmakologie

Bratislava, , Slovakia

Site Status

Seoul National University Hospital, Department of Internal Medicine

Seoul, , South Korea

Site Status

Samsung Medical Center/Division of Nephrology

Seoul, , South Korea

Site Status

Eulji General Hospital

Seoul, , South Korea

Site Status

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Clinic I Provincial de Barcelona

Barcelona, , Spain

Site Status

Sahlgrenska Universitetssjukhuset, Njurmedicin

Gothenburg, , Sweden

Site Status

Karolinska Universitetssjukhuset Huddinge

Stockholm, , Sweden

Site Status

Karolinska Universitetssjukhuset Solna

Stockholm, , Sweden

Site Status

Universitaetsspital Zuerich

Zurich, , Switzerland

Site Status

Istanbul University, Istanbul Tip Fakultesi

Istanbul, Capa, Turkey (Türkiye)

Site Status

Dokuz Eylul Universitesi Hastanesi Ic Hastaliklari Anabilim Dali

Izmir, Inciralti/ Narlidere, Turkey (Türkiye)

Site Status

Morriston Hospital

Swansea, Wales, United Kingdom

Site Status

BHF Glasgow Cardiovascular Research Centre, University of Glasgow

Glasgow, , United Kingdom

Site Status

Renal and Urology Directorate, Leicester General Hospital

Leicester, , United Kingdom

Site Status

Countries

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United States Australia Canada Czechia Hungary Italy Lithuania Moldova Poland Romania Slovakia South Korea Spain Sweden Switzerland Turkey (Türkiye) United Kingdom

References

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St Pierre K, Cashmore BA, Bolignano D, Zoccali C, Ruospo M, Craig JC, Strippoli GF, Mallett AJ, Green SC, Tunnicliffe DJ. Interventions for preventing the progression of autosomal dominant polycystic kidney disease. Cochrane Database Syst Rev. 2024 Oct 2;10(10):CD010294. doi: 10.1002/14651858.CD010294.pub3.

Reference Type DERIVED
PMID: 39356039 (View on PubMed)

Tesar V, Ciechanowski K, Pei Y, Barash I, Shannon M, Li R, Williams JH, Levisetti M, Arkin S, Serra A. Bosutinib versus Placebo for Autosomal Dominant Polycystic Kidney Disease. J Am Soc Nephrol. 2017 Nov;28(11):3404-3413. doi: 10.1681/ASN.2016111232. Epub 2017 Aug 24.

Reference Type DERIVED
PMID: 28838955 (View on PubMed)

Related Links

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Other Identifiers

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3160A7-2211

Identifier Type: OTHER

Identifier Source: secondary_id

2010-023017-65

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B1871019

Identifier Type: -

Identifier Source: org_study_id

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