Study Comparing Orteronel Plus Prednisone in Participants With Chemotherapy-Naive Metastatic Castration-Resistant Prostate Cancer

NCT ID: NCT01193244

Last Updated: 2017-05-17

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1560 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-10-01

Study Completion Date

2016-04-07

Brief Summary

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This is a randomized, double-blind, multicenter, phase 3 study evaluating orteronel (TAK-700) plus prednisone compared with placebo plus prednisone in the treatment of men with progressive, chemotherapy-naive, metastatic, castration-resistant prostate cancer (mCRPC)

Detailed Description

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Conditions

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Prostate Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Orteronel + prednisone

Group Type EXPERIMENTAL

Orteronel

Intervention Type DRUG

Orteronel will be administered orally twice a day continuously throughout the study. Patients will also receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and have a testosterone concentration of \<50 ng/dL.

Prednisone

Intervention Type DRUG

Prednisone will be administered orally twice a day continuously throughout the study. Patients will also receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and have a testosterone concentration of \<50 ng/dL.

Placebo + prednisone

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo will be administered orally twice a day continuously throughout the study. Additionally, all patients will receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and a testosterone concentration of \<50 ng/dL.

Prednisone

Intervention Type DRUG

Prednisone will be administered orally twice a day continuously throughout the study. Patients will also receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and have a testosterone concentration of \<50 ng/dL.

Interventions

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Orteronel

Orteronel will be administered orally twice a day continuously throughout the study. Patients will also receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and have a testosterone concentration of \<50 ng/dL.

Intervention Type DRUG

Placebo

Placebo will be administered orally twice a day continuously throughout the study. Additionally, all patients will receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and a testosterone concentration of \<50 ng/dL.

Intervention Type DRUG

Prednisone

Prednisone will be administered orally twice a day continuously throughout the study. Patients will also receive concomitant gonadotropin-releasing hormone (GnRH) analogue therapy unless they have previously undergone orchiectomy and have a testosterone concentration of \<50 ng/dL.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Voluntary written consent
* Male patients 18 years or older
* Histologically or cytologically confirmed diagnosis of prostate adenocarcinoma
* Radiograph-documented metastatic disease
* Progressive disease
* Prior surgical castration or concurrent use of an agent for medical castration
* Either absence of pain or pain not requiring use of any opioid or narcotic analgesia in the 2 weeks prior to study entry
* Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1
* Even if surgically sterilized, patients must practice effective barrier contraception during the entire study treatment and for 4 months after the last dose of study drug, OR abstain from heterosexual intercourse
* Meet screening laboratory values as specified in protocol
* Stable medical condition

Exclusion Criteria

* Known hypersensitivity to orteronel, prednisone or gonadotropin-releasing hormone (GnRH) analogue
* Received prior therapy with orteronel, aminoglutethimide, ketoconazole or abiraterone
* Received antiandrogen therapy within 6 weeks for bicalutamide and 4 weeks for all others prior to first dose of study drug
* Continuous daily use of oral prednisone or oral dexamethasone for more than 14 days within 3 months prior to study
* Received prior chemotherapy for prostate cancer with exception of neoadjuvant/adjuvant therapy as part of initial primary treatment for local disease that was completed 2 or more years prior to screening
* Exposure to radioisotope therapy within 4 weeks of receiving first dose of study drug; exposure to external beam radiation within 2 weeks of start of screening until receiving the first dose of study drug
* Documented central nervous system metastases
* Treatment with any investigational compound within 30 days prior to first dose of study drug
* Current spinal cord compression, bilateral hydronephrosis or current bladder neck outlet obstruction
* Diagnosis or treatment of another malignancy within 2 years preceding first dose of study drug except nonmelanoma skin cancer or in situ malignancy completely resected
* Uncontrolled cardiovascular condition as specified in study protocol
* Known history of human immunodeficiency virus (HIV) infection, hepatitis B, or hepatitis C
* Unwilling or unable to comply with protocol
* Uncontrolled nausea, vomiting or diarrhea
* Known gastrointestinal disease or procedure that could interfere with oral absorption or tolerance of orteronel
Minimum Eligible Age

18 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Millennium Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Monitor

Role: STUDY_DIRECTOR

Millennium Pharmaceuticals, Inc.

Locations

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Anchorage, Alaska, United States

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Tucson, Arizona, United States

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Duarte, California, United States

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Highland, California, United States

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Orange, California, United States

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Sacramento, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Denver, Colorado, United States

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Deerfield Beach, Florida, United States

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Fort Myers, Florida, United States

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Jacksonville, Florida, United States

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Orlando, Florida, United States

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Port Saint Lucie, Florida, United States

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Jeffersonville, Indiana, United States

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Kansas City, Kansas, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Lansing, Michigan, United States

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Duluth, Minnesota, United States

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Corinth, Mississippi, United States

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Columbia, Missouri, United States

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Jefferson City, Missouri, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Hackensack, New Jersey, United States

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East Syracuse, New York, United States

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New York, New York, United States

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Durham, North Carolina, United States

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Raleigh, North Carolina, United States

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Kettering, Ohio, United States

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Tualatin, Oregon, United States

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Hershey, Pennsylvania, United States

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Lancaster, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Piitsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Columbia, South Carolina, United States

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Chattanooga, Tennessee, United States

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Nashville, Tennessee, United States

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Amarillo, Texas, United States

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Bedford, Texas, United States

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Dallas, Texas, United States

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Denton, Texas, United States

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Tyler, Texas, United States

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Salt Lake City, Utah, United States

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Norfolk, Virginia, United States

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Garran, , Australia

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Hobart, , Australia

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Kurralta Park, , Australia

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Nedlands, , Australia

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Perth, , Australia

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Redcliffe, , Australia

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Wodonga, , Australia

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Graz, , Austria

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Linz, , Austria

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Vienna, , Austria

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Minsk, , Belarus

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Edegem, , Belgium

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Hasselt, , Belgium

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Kortrijk, , Belgium

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Leuven, , Belgium

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Namur, , Belgium

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Bairro Nazare - Salvador, , Brazil

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Barretos/sp, , Brazil

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Belo Horizonte, , Brazil

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Campinas, , Brazil

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Caxias do Sul, , Brazil

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Curitiba, , Brazil

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Fortaleza/ce, , Brazil

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Ijuí, , Brazil

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Joinville, , Brazil

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Lajeado - Rs, , Brazil

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Piracicaba - Sp, , Brazil

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Porto Alegre- Rs, , Brazil

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Porto Alegre/rs, , Brazil

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Ribeirao Preto - Sp, , Brazil

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Rio de Janeiro, , Brazil

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Rio de Janeiro Rj, , Brazil

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Santo André, , Brazil

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São José do Rio Preto, , Brazil

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São José dos Campos, , Brazil

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São Paulo, , Brazil

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Sorocaba - Sp, , Brazil

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Varna, , Bulgaria

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Kelowna, British Columbia, Canada

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Burlington, Ontario, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Owen Sound, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Pointe-Claire, Quebec, Canada

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Québec, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Las Condes, , Chile

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Santiago, , Chile

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Temuco, , Chile

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Valparaíso, , Chile

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Cali, , Colombia

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Hradec Králové, , Czechia

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Prague, , Czechia

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Joensuu, , Finland

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Oulu, , Finland

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Seinäjoki, , Finland

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Tampere, , Finland

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Angers, , France

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Bordeaux, , France

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Caen, , France

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Créteil, , France

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La Roche-sur-Yon, , France

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Lyon, , France

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Marseille, , France

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Nancy, , France

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Nantes, , France

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Paris, , France

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Poitiers, , France

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Saint-Etienne, , France

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Villejuif, , France

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Braunschweig, , Germany

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Dresden, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Kassel, , Germany

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Kempen, , Germany

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Nürtingen, , Germany

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Tübingen, , Germany

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Wuppertal, , Germany

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Athens, , Greece

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Heraklion Crete, , Greece

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Larissa, , Greece

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Pátrai, , Greece

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Thessaloniki, , Greece

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Kowloon, , Hong Kong

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Shatin, , Hong Kong

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Dublin, , Ireland

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Galway, , Ireland

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Haifa, , Israel

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Holon, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Ramat Gan, , Israel

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Tel Aviv, , Israel

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Ẕerifin, , Israel

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Aviano, , Italy

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Novara, , Italy

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Roma, , Italy

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Torino, , Italy

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Chiba, , Japan

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Fukuoka, , Japan

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Hamamatsu, , Japan

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Hokkaido, , Japan

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Kanazawa, , Japan

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Kita-gun, , Japan

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Maebashi, , Japan

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Mito, , Japan

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Osaka, , Japan

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Sakura, , Japan

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Sayama, , Japan

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Sendai, , Japan

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Shimizucho Sunto-gun, , Japan

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Suntou-gun, , Japan

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Tokyo, , Japan

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Yamagata, , Japan

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Yokohama, , Japan

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Yufu, , Japan

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Riga, , Latvia

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Vilnius, , Lithuania

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Durango Durango, , Mexico

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Mexico City Distrito Federal, , Mexico

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Zapopan Jalisco, , Mexico

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Amsterdam, , Netherlands

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Arnhem, , Netherlands

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Breda, , Netherlands

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Eindhoven, , Netherlands

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Heerlen, , Netherlands

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Nieuwegein, , Netherlands

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Nijmegen, , Netherlands

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Rotterdam, , Netherlands

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Dunedin, , New Zealand

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Takapuna, , New Zealand

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Tauranga, , New Zealand

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Lima, , Peru

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Bielsko-Biala, , Poland

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Wroclaw, , Poland

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Liepaja, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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San Juan, PR, Puerto Rico

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Bucharest, , Romania

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Cluj-Napoca, , Romania

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Moscow, , Russia

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Saint Petersburg, , Russia

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Singapore, , Singapore

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Nitra, , Slovakia

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Prešov, , Slovakia

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Trenčín, , Slovakia

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Žilina, , Slovakia

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Cape Town, , South Africa

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Durban, , South Africa

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George, , South Africa

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Port Elizabeth, , South Africa

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A Coruña, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Majadahonda, , Spain

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Pamplona, , Spain

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Seville, , Spain

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Valencia, , Spain

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Gothenburg, , Sweden

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Stockholm, , Sweden

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Uppsala, , Sweden

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Aarau, , Switzerland

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Lausanne, , Switzerland

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Winterthur, , Switzerland

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Zurich, , Switzerland

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Taichung, , Taiwan

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Taipei, , Taiwan

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Dnipropetrovsk, , Ukraine

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Donetsk, , Ukraine

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Kyiv, , Ukraine

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Zaporizhzhya, , Ukraine

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Aberdeen, , United Kingdom

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Belfast, , United Kingdom

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Bristol, , United Kingdom

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Cottingham, , United Kingdom

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Coventry, , United Kingdom

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Glasgow, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Northwood, , United Kingdom

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Preston, , United Kingdom

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Southampton, , United Kingdom

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Countries

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United States Australia Austria Belarus Belgium Brazil Bulgaria Canada Chile Colombia Czechia Finland France Germany Greece Hong Kong Ireland Israel Italy Japan Latvia Lithuania Mexico Netherlands New Zealand Peru Poland Portugal Puerto Rico Romania Russia Singapore Slovakia South Africa Spain Sweden Switzerland Taiwan Ukraine United Kingdom

References

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Heller G, McCormack R, Kheoh T, Molina A, Smith MR, Dreicer R, Saad F, de Wit R, Aftab DT, Hirmand M, Limon A, Fizazi K, Fleisher M, de Bono JS, Scher HI. Circulating Tumor Cell Number as a Response Measure of Prolonged Survival for Metastatic Castration-Resistant Prostate Cancer: A Comparison With Prostate-Specific Antigen Across Five Randomized Phase III Clinical Trials. J Clin Oncol. 2018 Feb 20;36(6):572-580. doi: 10.1200/JCO.2017.75.2998. Epub 2017 Dec 22.

Reference Type DERIVED
PMID: 29272162 (View on PubMed)

Suri A, Chapel S, Lu C, Venkatakrishnan K. Physiologically based and population PK modeling in optimizing drug development: A predict-learn-confirm analysis. Clin Pharmacol Ther. 2015 Sep;98(3):336-44. doi: 10.1002/cpt.155. Epub 2015 Jul 14.

Reference Type DERIVED
PMID: 26031410 (View on PubMed)

Saad F, Fizazi K, Jinga V, Efstathiou E, Fong PC, Hart LL, Jones R, McDermott R, Wirth M, Suzuki K, MacLean DB, Wang L, Akaza H, Nelson J, Scher HI, Dreicer R, Webb IJ, de Wit R; ELM-PC 4 investigators. Orteronel plus prednisone in patients with chemotherapy-naive metastatic castration-resistant prostate cancer (ELM-PC 4): a double-blind, multicentre, phase 3, randomised, placebo-controlled trial. Lancet Oncol. 2015 Mar;16(3):338-48. doi: 10.1016/S1470-2045(15)70027-6. Epub 2015 Feb 18.

Reference Type DERIVED
PMID: 25701170 (View on PubMed)

Other Identifiers

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2010-018661-35

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

0991413276

Identifier Type: OTHER

Identifier Source: secondary_id

10/H0406/75

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1181-0387

Identifier Type: REGISTRY

Identifier Source: secondary_id

C21004

Identifier Type: -

Identifier Source: org_study_id

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