Substudy 01A: Safety and Efficacy of Opevesostat (MK-5684)-Based Treatment Combinations or Opevesostat Alone in Participants With Metastatic Castration-resistant Prostate Cancer (mCRPC) (MK-5684-01A)

NCT ID: NCT06353386

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

220 participants

Study Classification

INTERVENTIONAL

Study Start Date

2024-05-20

Study Completion Date

2029-01-15

Brief Summary

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Substudy 01A is part of a larger research study that is testing experimental treatments for metastatic castration-resistant prostate cancer (mCRPC). The larger study is the umbrella study (U01).

The goal of substudy 01A is to evaluate the safety and efficacy of opevesostat-based treatment combinations, or as a single agent, in participants with mCRPC.

This substudy will have two phases: a safety lead-in phase and an efficacy phase. The safety lead-in phase will be used to evaluate the safety and tolerability, and to establish a recommended Phase 2 dose (RP2D) for the opevesostat-based treatment combinations. There will be no hypothesis testing in this study.

Detailed Description

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Conditions

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Prostatic Neoplasms, Castration-Resistant

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A1: Opevesostat

Participants receive 5 mg of opevesostat twice daily (BID) via oral tablet plus dexamethasone 1.5 mg by oral tablets once daily (QD) and 0.1 mg fludrocortisone acetate by oral tablet QD until progression or discontinuation.

Group Type EXPERIMENTAL

Opevesostat

Intervention Type DRUG

Oral Tablet

Fludrocortisone acetate

Intervention Type DRUG

Oral Tablet

Dexamethasone

Intervention Type DRUG

Oral Tablet

Arm A2: Olaparib + Opevesostat

Participants receive 5 mg of opevesostat BID via oral tablet plus dexamethasone 1.5 mg by oral tablets QD and 0.1 mg fludrocortisone acetate by oral tablet QD, PLUS 300 mg of olaparib BID via oral tablet until progressive disease or discontinuation.

Group Type EXPERIMENTAL

Opevesostat

Intervention Type DRUG

Oral Tablet

Olaparib

Intervention Type DRUG

Oral Tablet

Fludrocortisone acetate

Intervention Type DRUG

Oral Tablet

Dexamethasone

Intervention Type DRUG

Oral Tablet

Arm A3: Docetaxel + Opevesostat

Participants receive 5 mg of opevesostat BID via oral tablet plus dexamethasone 1.5 mg by oral tablets QD and 0.1 mg fludrocortisone acetate by oral tablet QD, PLUS 75 mg/m\^2 of docetaxel once every 3 weeks (Q3W) via IV infusion, plus prednisone per approved product label BID by oral tablets until progressive disease or discontinuation.

Group Type EXPERIMENTAL

Opevesostat

Intervention Type DRUG

Oral Tablet

Docetaxel

Intervention Type DRUG

IV Infusion

Fludrocortisone acetate

Intervention Type DRUG

Oral Tablet

Dexamethasone

Intervention Type DRUG

Oral Tablet

Prednisone

Intervention Type DRUG

Oral Tablet

Arm A4: Cabazitaxel + Opevesostat

Participants receive 5 mg of opevesostat BID via oral tablet plus dexamethasone 1.5 mg by oral tablets QD and 0.1 mg fludrocortisone acetate by oral tablet QD, PLUS 20 mg/m\^2 of cabazitaxel Q3W via IV infusion, plus prednisone per approved product label BID by oral tablets until progressive disease or discontinuation.

Group Type EXPERIMENTAL

Opevesostat

Intervention Type DRUG

Oral Tablet

Cabazitaxel

Intervention Type DRUG

IV Infusion

Fludrocortisone acetate

Intervention Type DRUG

Oral Tablet

Dexamethasone

Intervention Type DRUG

Oral Tablet

Prednisone

Intervention Type DRUG

Oral Tablet

Interventions

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Opevesostat

Oral Tablet

Intervention Type DRUG

Olaparib

Oral Tablet

Intervention Type DRUG

Docetaxel

IV Infusion

Intervention Type DRUG

Cabazitaxel

IV Infusion

Intervention Type DRUG

Fludrocortisone acetate

Oral Tablet

Intervention Type DRUG

Dexamethasone

Oral Tablet

Intervention Type DRUG

Prednisone

Oral Tablet

Intervention Type DRUG

Other Intervention Names

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MK-5684 LYNPARZA® TAXOTERE® JEVTANA®

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed diagnosis of adenocarcinoma of the prostate without small cell histology.
* Prostate cancer progression and received androgen deprivation therapy (ADT) or post bilateral orchiectomy within 6 months before screening.
* Evidence of disease progression from either, \>4 weeks from last flutamide treatment, or \>6 weeks from last bicalutamide or nilutamide treatment, if receiving first generation anti-androgen therapy as last treatment therapy.
* Current evidence of metastatic disease.
* Prior treatment with 1 to 2 novel hormonal agent(s) (NHA) for non-metastatic, or metastatic, hormone-sensitive prostate cancer or castration-resistant prostate cancer and have disease progression during or after treatment.
* Treatment with bone resorptive therapy (including, but not limited to, bisphosphonate or denosumab) must have been on stable doses for \>4 weeks before randomization.
* Participants who experienced adverse events (AEs) due to previous anticancer therapies must have recovered to \<Grade 1 or baseline.
* Human immunodeficiency virus (HIV)-infected participants must have well controlled HIV on antiretroviral therapy.
* Participants who are Hepatitis B surface antigen (HBsAg) positive are eligible if they have received Hepatitis B Virus (HBV) antiviral therapy for at least 4 weeks, and have undetectable HBV viral load.
* Participants with a history of Hepatitis C virus (HCV) infection are eligible if HCV viral load is undetectable.

Exclusion Criteria

* History of pituitary dysfunction.
* Poorly controlled diabetes mellitus.
* Active or unstable cardio/cerebro-vascular disease, including thromboembolic events and history of stroke or transient ischemic attack within 6 months before the first dose of study intervention, history of myocardial infarction within 6 months before the first dose of study intervention, New York Heart Association Class III or IV cardiac disease or congestive heart failure, coronary heart disease that is symptomatic, or unstable angina
* History or family history of long corrected QT interval (QTc) syndrome.
* Myelodysplastic syndrome (MDS)/acute myeloid leukemia (AML) or features suggestive of MDS/AML.
* History or current condition of adrenal insufficiency.
* History of (noninfectious) pneumonitis requiring steroids, or current pneumonitis.
* HIV-infected participants with a history of Kaposi's sarcoma and/or Multicentric Castleman's Disease.
* Undergone major surgery, including local prostate intervention (except prostate biopsy) within 28 days before randomization, and has not recovered from the toxicities and/or complications.
* Is on an unstable dose of thyroid hormone therapy within 6 months prior to first dose of study intervention.
* Received a whole blood transfusion in the last 120 days before randomization (packed red blood cells and platelet transfusions are acceptable if not given within 28 days before randomization).
* Received prior systemic anticancer therapy including investigational agents within 4 weeks before randomization.
* Received prior radiotherapy within 2 weeks of start of study intervention or radiation-related toxicities, requiring corticosteroids.
* Received a live or live-attenuated vaccine within 30 days before the first does of study intervention. Administration of killed vaccines is allowed.
* Diagnosis of immunodeficiency, or is receiving chronic systemic steroid therapy, or any other form of immunosuppressive therapy, within 7 days prior to the first dose of study intervention.
* Known additional malignancy that is progressing or has required active treatment within the past 3 years.
* Known active central nervous system (CNS) metastases and/or carcinomatous meningitis.
* Active autoimmune disease that has required systemic treatment in the past 2 years.
* Active infection requiring systemic therapy.
* Concurrent active HBV or HCV infections.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Orion Corporation, Orion Pharma

INDUSTRY

Sponsor Role collaborator

Merck Sharp & Dohme LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Merck Sharp & Dohme LLC

Locations

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UCSD Moores Cancer Center ( Site 0039)

La Jolla, California, United States

Site Status RECRUITING

UCLA Hematology/Oncology - Santa Monica ( Site 0044)

Los Angeles, California, United States

Site Status RECRUITING

University of Miami Hospital and Clinics, Sylvester Cancer Center-Cancer Research Services ( Site 0051)

Miami, Florida, United States

Site Status RECRUITING

University of Maryland-Greenebaum Comprehensive Cancer Center ( Site 0049)

Baltimore, Maryland, United States

Site Status RECRUITING

Rutgers Cancer Institute of New Jersey ( Site 0033)

New Brunswick, New Jersey, United States

Site Status RECRUITING

University Hospitals Cleveland Medical Center ( Site 0043)

Cleveland, Ohio, United States

Site Status RECRUITING

MEDICAL COLLEGE OF WISCONSIN-Cancer Center Clinical Trials Office ( Site 0020)

Milwaukee, Wisconsin, United States

Site Status RECRUITING

Macquarie University-MQ Health Clinical Trials Unit ( Site 0108)

Macquarie University, New South Wales, Australia

Site Status RECRUITING

Gallipoli Medical Research Ltd-GMRF CTU ( Site 0107)

Greenslopes, Queensland, Australia

Site Status RECRUITING

Peter MacCallum Cancer Centre-Parkville Cancer Clinical Trials Unit (PCCTU) ( Site 0110)

Melbourne, Victoria, Australia

Site Status RECRUITING

Centre Hospitalier de l'Université de Montréal ( Site 0200)

Montreal, Quebec, Canada

Site Status RECRUITING

Jewish General Hospital ( Site 0206)

Montreal, Quebec, Canada

Site Status RECRUITING

Centre intégré de cancérologie du CHU de Québec Université Laval, Hôpital de l'Enfant-Jésus ( Site 0207)

Québec, Quebec, Canada

Site Status RECRUITING

Clinica Universidad Catolica del Maule-Oncology ( Site 0304)

Talca, Maule Region, Chile

Site Status RECRUITING

FALP ( Site 0301)

Santiago, Region M. de Santiago, Chile

Site Status RECRUITING

Pontificia Universidad Catolica de Chile ( Site 0303)

Santiago, Region M. de Santiago, Chile

Site Status RECRUITING

Bradfordhill ( Site 0300)

Santiago, Region M. de Santiago, Chile

Site Status RECRUITING

CIDO SpA-Oncology ( Site 0302)

Temuco, Región del Biobío, Chile

Site Status RECRUITING

FUNDACION CTIC CENTRO DE TRATAMIENTO E INVESTIGACION SOBRE CANCER LUIS CARLOS SARMIENTO ANGULO ( Site 0406)

Bogotá, Bogota D.C., Colombia

Site Status RECRUITING

Clinica Colsanitas S.A, Sede Clínica Universitaria Colombia ( Site 0402)

Bogotá, Bogota D.C., Colombia

Site Status RECRUITING

Sociedad De Oncología y Hematología Del Cesar SAS-Oncology ( Site 0400)

Valledupar, Cesar Department, Colombia

Site Status RECRUITING

IMAT S.A.S ( Site 0404)

Montería, Departamento de Córdoba, Colombia

Site Status RECRUITING

Fundación Valle del Lili-Oncology CIC ( Site 0403)

Cali, Valle del Cauca Department, Colombia

Site Status RECRUITING

Herlev and Gentofte Hospital ( Site 0501)

Copenhagen, Capital Region, Denmark

Site Status RECRUITING

Aalborg Universitetshospital, Syd ( Site 0503)

Aalborg, North Denmark, Denmark

Site Status RECRUITING

Vaasan Keskussairaala ( Site 0603)

Vaasa, Pohjanmaa, Finland

Site Status RECRUITING

Helsinki University Hospital - Comprehensive Cancer Center (HYKS - Syöpäkeskus) ( Site 0604)

Helsinki, Uusimaa, Finland

Site Status RECRUITING

Docrates Syöpäsairaala ( Site 0602)

Helsinki, Uusimaa, Finland

Site Status RECRUITING

Institut de cancérologie Strasbourg Europe (ICANS) ( Site 0700)

Strasbourg, Alsace, France

Site Status RECRUITING

Institut Bergonié - Centre Régional de Lutte Contre Le Cancer de Bordeaux et Sud Ouest ( Site 0703)

Bordeaux, Aquitaine, France

Site Status RECRUITING

Hôpital Européen Georges Pompidou-Service d'Oncologie Médicale ( Site 0702)

Paris, , France

Site Status RECRUITING

Gustave Roussy ( Site 0701)

Villejuif, Île-de-France Region, France

Site Status RECRUITING

Universitaetsklinikum Heidelberg ( Site 0805)

Heidelberg, Baden-Wurttemberg, Germany

Site Status RECRUITING

Universitaetsklinikum Tuebingen-Urologie ( Site 0801)

Tübingen, Baden-Wurttemberg, Germany

Site Status RECRUITING

klinikum rechts der isar der technischen universität münchen-Urologische Klinik und Poliklinik ( Site 0802)

Munich, Bavaria, Germany

Site Status RECRUITING

Charité Universitaetsmedizin Berlin - Campus Mitte ( Site 0800)

Berlin, , Germany

Site Status RECRUITING

Universitaetsklinikum Hamburg-Eppendorf-Onkologisches Zentrum ( Site 0804)

Hamburg, , Germany

Site Status RECRUITING

St. Vincent's University Hospital ( Site 0901)

Dublin, Dublin, Ireland

Site Status RECRUITING

Cork University Hospital ( Site 0902)

Cork, , Ireland

Site Status RECRUITING

Tallaght University Hospital ( Site 0900)

Dublin, , Ireland

Site Status RECRUITING

Rambam Health Care Campus-Oncology Division ( Site 1002)

Haifa, , Israel

Site Status RECRUITING

Rabin Medical Center ( Site 1001)

Petah Tikva, , Israel

Site Status RECRUITING

Sheba Medical Center ( Site 1000)

Ramat Gan, , Israel

Site Status RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS -Medical Oncology ( Site 1102)

Rome, Lazio, Italy

Site Status RECRUITING

Fondazione IRCCS Istituto Nazionale dei Tumori-Struttura Complessa Oncologia Medica 1 ( Site 1103)

Milan, Lombardy, Italy

Site Status RECRUITING

Istituto Clinico Humanitas-U.O di Oncologia medica ed Ematologia ( Site 1101)

Rozzano, Milano, Italy

Site Status RECRUITING

Azienda Ospedaliera Universitaria Integrata Verona - Ospedal-Centro Ricerche Cliniche di Verona ( Site 1100)

Verona, , Italy

Site Status RECRUITING

Toho University Sakura Medical Center ( Site 1201)

Sakura, Chiba, Japan

Site Status RECRUITING

Yokohama City University Medical Center ( Site 1203)

Yokohama, Kanagawa, Japan

Site Status RECRUITING

The Jikei University Hospital ( Site 1202)

Mitato, Tokyo, Japan

Site Status COMPLETED

Kyushu University Hospital ( Site 1204)

Fukuoka, , Japan

Site Status RECRUITING

Auckland City Hospital ( Site 1333)

Auckland, , New Zealand

Site Status RECRUITING

Centrum Onkologii im. Prof. Franciszka Lukaszczyka-Ambulatorium Chemioterapii ( Site 1402)

Bydgoszcz, Kuyavian-Pomeranian Voivodeship, Poland

Site Status RECRUITING

Narodowy Instytut Onkologii im. Marii Sklodowskiej-Curie - P-Oddzial Badan Wczesnych Faz ( Site 1400)

Warsaw, Masovian Voivodeship, Poland

Site Status RECRUITING

Uniwersyteckie Centrum Kliniczne ( Site 1405)

Gdansk, Pomeranian Voivodeship, Poland

Site Status RECRUITING

Asan Medical Center-Oncology ( Site 1500)

Songpagu, Seoul, South Korea

Site Status RECRUITING

Severance Hospital, Yonsei University Health System-Medical oncology ( Site 1502)

Seoul, , South Korea

Site Status RECRUITING

Samsung Medical Center-Division of Hematology/Oncology ( Site 1501)

Seoul, , South Korea

Site Status RECRUITING

Institut Català d'Oncologia - L'Hospitalet-Medical Oncology ( Site 1603)

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status RECRUITING

Hospital Universitario Ramón y Cajal-Medical Oncology ( Site 1600)

Madrid, Madrid, Comunidad de, Spain

Site Status RECRUITING

Hospital Universitari Vall d'Hebron-Departamento de Oncologia- VHIO ( Site 1602)

Barcelona, , Spain

Site Status RECRUITING

Hospital General Universitario Gregorio Marañón ( Site 1601)

Madrid, , Spain

Site Status RECRUITING

Hospital Clinico San Carlos-Oncology Department ( Site 1604)

Madrid, , Spain

Site Status RECRUITING

Chang Gung Memorial Hospital at Kaohsiung-Oncology and Hematology ( Site 1704)

Kaohsiung Niao Sung Dist, Kaohsiung, Taiwan

Site Status RECRUITING

China Medical University Hospital ( Site 1703)

Taichung, , Taiwan

Site Status RECRUITING

Taipei Veterans General Hospital ( Site 1701)

Taipei, , Taiwan

Site Status RECRUITING

Chang Gung Medical Foundation-Linkou Branch-Medical Oncology ( Site 1702)

Taoyuan District, , Taiwan

Site Status RECRUITING

Baskent University Dr. Turgut Noyan Research and Training Center-ONCOLOGY ( Site 1802)

Adana, , Turkey (Türkiye)

Site Status RECRUITING

Hacettepe Universite Hastaneleri-oncology hospital ( Site 1800)

Ankara, , Turkey (Türkiye)

Site Status RECRUITING

Ankara Bilkent Şehir Hastanesi ( Site 1801)

Ankara, , Turkey (Türkiye)

Site Status RECRUITING

Istanbul Universitesi Cerrahpasa-Medical Oncology ( Site 1804)

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

TC Saglik Bakanligi Goztepe Prof. Dr. Suleyman Yalcin Sehir Hastanesi-oncology ( Site 1803)

Istanbul, , Turkey (Türkiye)

Site Status RECRUITING

Addenbrooke's Hospital ( Site 1902)

Cambridge, Cambridgeshire, United Kingdom

Site Status RECRUITING

The Beatson West of Scotland Cancer Centre ( Site 1904)

Glasgow, Glasgow City, United Kingdom

Site Status RECRUITING

Royal Preston Hospital-Lancashire Clinical Research Facility ( Site 1900)

Preston, Lancashire, United Kingdom

Site Status RECRUITING

University College London Hospital ( Site 1905)

London, London, City of, United Kingdom

Site Status RECRUITING

Queen Elizabeth Hospital Birmingham ( Site 1903)

Birmingham, , United Kingdom

Site Status RECRUITING

Countries

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United States Australia Canada Chile Colombia Denmark Finland France Germany Ireland Israel Italy Japan New Zealand Poland South Korea Spain Taiwan Turkey (Türkiye) United Kingdom

Central Contacts

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Toll Free Number

Role: CONTACT

Phone: 1-888-577-8839

Email: [email protected]

Facility Contacts

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Study Coordinator

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Related Links

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Other Identifiers

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MK-5684-01A

Identifier Type: OTHER

Identifier Source: secondary_id

2023-506288-33-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

U1111-1292-6912

Identifier Type: REGISTRY

Identifier Source: secondary_id

jRCT2031240224

Identifier Type: REGISTRY

Identifier Source: secondary_id

5684-01A

Identifier Type: -

Identifier Source: org_study_id