Study of Debio 0932 in Patients With Advanced Solid Tumours or Lymphoma

NCT ID: NCT01168752

Last Updated: 2014-02-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

81 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-04-30

Study Completion Date

2013-04-30

Brief Summary

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The purpose of this study is to determine the maximum tolerated dose of Debio 0932 when administered orally, every-other-day or daily during the first 30 days, in patients with solid tumours or lymphoma.

Detailed Description

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This is an open-label, non-randomised, dose-escalation phase I, pharmacokinetic and pharmacodynamic study in patients with advanced and/or refractory malignancies (solid tumours or lymphoma), to determine the maximum tolerated doses (MTD) of Debio 0932 administered orally every-other-day (schedule A) or every day (schedule B) and to assess its safety profile, pharmakokinetic, antitumor activity and pharmacodynamic biomarkers.

Increments used in dose escalation will be determined according to the maximum grade of treatment-related adverse events observed during the first 30-day treatment period of each schedule in the previous in the preceding dose level Once reaching the recommended dose (RD) for each schedule, up to 40 additional patients will be enrolled and treated at the RD of the retained schedule, as part of an expansion phase.

Conditions

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Cancer Neoplasms Solid Tumors Lymphoma

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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schedule A

Debio 0932 will be administered orally to sequential escalating dose cohorts, as an every-other-day schedule.

Each dose level (DL) for each schedule will be determined according to the maximum grade of treatment-related AEs observed during the first 30 days treatment period (DLT period) in the previous DL.

Dose-escalation could be undertaken only after a minimum of 3 (or 6 in case of DLT) patients have been followed up and evaluated for at least 1 DLT period.

Group Type EXPERIMENTAL

Debio 0932

Intervention Type DRUG

Gelatin capsules of 2 dosage strengths (25 mg or 100 mg) The maximum dose will depend on the number of dose levels necessary to determine the MTD.

In both schedules the study treatment will be continued, until one of the study treatment discontinuation criteria is met.

schedule B

Debio 0932 will be administered orally to sequential escalating dose cohorts, as a daily schedule.

Each dose level (DL) for each schedule will be determined according to the maximum grade of treatment-related AEs observed during the first 30 days treatment period (DLT period) in the previous DL.

Dose-escalation could be undertaken only after a minimum of 3 (or 6 in case of DLT) patients have been followed up and evaluated for at least 1 DLT period.

Group Type EXPERIMENTAL

Debio 0932

Intervention Type DRUG

Gelatin capsules of 2 dosage strengths (25 mg or 100 mg) The maximum dose will depend on the number of dose levels necessary to determine the MTD.

In both schedules the study treatment will be continued, until one of the study treatment discontinuation criteria is met.

Interventions

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Debio 0932

Gelatin capsules of 2 dosage strengths (25 mg or 100 mg) The maximum dose will depend on the number of dose levels necessary to determine the MTD.

In both schedules the study treatment will be continued, until one of the study treatment discontinuation criteria is met.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically confirmed diagnosis of advanced solid tumours or lymphoma, except for primitive hepatocarcinoma for which radiological diagnosis only is permitted;
* Advanced or metastatic disease refractory to standard curative or palliative therapy or contraindication or have refused standard therapy,
* Measurable and/or evaluable disease,
* Age ≥ 18 years,
* ECOG performance ≤ 1
* Life expectancy ≥ 3 months,
* If female, neither pregnant or lactating,
* Negative pregnancy test for females at screening, preferably done within 1 week before Day 1 of treatment (not applicable to patients with bilateral oophorectomy and/or hysterectomy),
* Agreeing to use appropriate medically approved contraception (physical barrier contraception is recommended) from study entry to 6 months after the last day of treatment for the patient,
* Absolute neutrophil count ≥ 1,500/µL; platelets ≥ 100,000/µL; calculated creatinine clearance ≥ 60mL/min (calculated according to the formula of Cockroft and Gault); total bilirubin ≤ 1.5x ULN; AST/ALT ≤ 2.5x ULN. In patients with documented liver metastases, the AST/ALT may be ≤ 3.5x ULN; prothrombin time ≤1.5x ULN, kalemia, magnesemia and phosphatemia \> LLN (Lower Limit of Normal)
* Able to render informed consent and to follow protocol requirements,
* Able to swallow capsules,
* Able to comply with scheduled plans, laboratory tests, and other study procedures.

Exclusion Criteria

* Received investigational agents or systemic anti-cancer agents within 14 days of Day 1 of treatment, or 28 days for those agents with unknown elimination half-lives, or known elimination half-lives greater than 50 hours; or 6 weeks for Mitomycine C or for nitrosourea agents,
* Unresolved toxicity from previous treatment or previous investigational agents,
* Patients with history of prior radiation that potentially included the heart in the field (e.g. mantle),

* History of significant coronary artery disease or congestive heart failure that meets NYHA class III or IV, within 12 months (see Appendix D),
* Significant cardiovascular dysfunction : pulmonary hypertension, right ventricular systolic dysfunction, aortic stenosis, mitral insufficiency \> grade 2 and/or Left Ventricular Ejection fraction \< 45% or \< 55% if prior exposure to anthracyclines, based on MUGA or echocardiography,
* Uncontrolled hypertension (Systolic \> 150 or diastolic \>100),
* Permanent and uncontrolled cardiac rhythm disorders and clinical relevant abnormalities in 12-lead ECG/Holter, such as WPW (Wolff-Parkinson-White) syndrome, QRS \> 120 msec, PR \> 220 msec, heart rate \< 50 bpm, Q wave, ST deviation, left bundle branch block, atrial fibrillation, flutter, tachysystoly.
* Prolonged QTc interval \> 450 msec in men and \> 470 msec in women using Fridericia formula,
* Congenital long QT syndrome,
* Use of any medication associated with known QTc interval prolongation (a non-exhaustive list will be provided separately)
* Known infection with human immunodeficiency virus (HIV), hepatitis B or hepatitis C,
* Patients with uncontrolled brain metastases,
* Gastrointestinal diseases or disorders that could affect drug absorption such as diarrhoea, major abdominal surgery, significant bowel obstruction and/or gastrointestinal diseases that could alter the assessment of safety, including any of the following:

* Irritable bowel syndrome
* Ulcerative colitis
* Crohn disease
* Haemorrhagic coloproctitis
* Concurrent participation with any other anticancer therapy.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Debiopharm International SA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Hein van Ingen, M.D.

Role: STUDY_DIRECTOR

Debiopharm International SA

Locations

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Centre Georges-François Leclerc

Dijon, , France

Site Status

Institut Claudius Regaud

Toulouse, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Countries

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France

References

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Maloney A, Workman P. HSP90 as a new therapeutic target for cancer therapy: the story unfolds. Expert Opin Biol Ther. 2002 Jan;2(1):3-24. doi: 10.1517/14712598.2.1.3.

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Isambert N, Delord JP, Soria JC, Hollebecque A, Gomez-Roca C, Purcea D, Rouits E, Belli R, Fumoleau P. Debio0932, a second-generation oral heat shock protein (HSP) inhibitor, in patients with advanced cancer-results of a first-in-man dose-escalation study with a fixed-dose extension phase. Ann Oncol. 2015 May;26(5):1005-1011. doi: 10.1093/annonc/mdv031. Epub 2015 Feb 2.

Reference Type DERIVED
PMID: 25646368 (View on PubMed)

Related Links

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Other Identifiers

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2009-017720-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

Debio 0932-101

Identifier Type: -

Identifier Source: org_study_id

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