Clinical Trial to Investigate the Safety, Tolerability, and Immunogenicity of the Novel Antituberculous Vaccine RUTI® Following One Month of Isoniazid Treatment in Subjects With Latent Tuberculosis Infection

NCT ID: NCT01136161

Last Updated: 2013-01-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

95 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-06-30

Study Completion Date

2011-05-31

Brief Summary

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The aim of the trial is to assess the safety, tolerability and immunogenicity of two doses of RUTI® vaccine administered four weeks apart after one month pre-treatment with INH.

The trial will be double-blinded, randomized and placebo-controlled with 96 subjects (48 HIV- and 48 HIV+ subjects).

Three different RUTI® doses and placebo will be tested, randomizing assigned both in HIV+ and HIV- subjects. Each subject will be randomized to receive one of the four treatments (placebo, 5, 25, 50 μg), after completion of one month INH pre-treatment (one tablet of 300mg/day, vp.o.). Each subject will receive two administrations of the same treatment, 28 days apart. Subjects will be monitored until one month after the second inoculation with RUTI®.

Detailed Description

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RUTI is a therapeutic vaccine made from virulent M.tuberculosis bacteria, grown in stressful conditions, fragmented, detoxified, heat inactivated (FCMtb) and liposomed. RUTI provides a strong humoral and cellular immune response against antigens from active growing and latent bacilli but also against structural antigens, as it has been proved in animal models of latent tuberculosis infection and in phase I clinical trial of Healthy Volunteers. The vaccine has been designed to be used against Latent Tuberculosis Infection as a therapeutic vaccine after 1-month of chemotheraputic treatment, instead the current treatment based on 6-9 months of chemotherapy.

Conditions

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Latent Tuberculosis Infection Tuberculosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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RUTI 5 micrograms of FCMtb in HIV -

n=12

Group Type EXPERIMENTAL

RUTI

Intervention Type BIOLOGICAL

dose:5 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

RUTI 25 micrograms of FCMtb in HIV -

n=12

Group Type EXPERIMENTAL

RUTI

Intervention Type BIOLOGICAL

dose:25 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

RUTI 50 micrograms of FCMtb in HIV -

n=12

Group Type EXPERIMENTAL

RUTI

Intervention Type BIOLOGICAL

dose:50 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

RUTI Matching Placebo in HIV -

n=12

Group Type PLACEBO_COMPARATOR

RUTI Matching Placebo

Intervention Type BIOLOGICAL

Placebo of the vaccine RUTI; given subcutaneously twice, on days 28 and 56.

RUTI 5 micrograms of FCMtb in HIV +

n=12

Group Type EXPERIMENTAL

RUTI

Intervention Type BIOLOGICAL

dose:5 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

RUTI 25 micrograms of FCMtb in HIV +

n=12

Group Type EXPERIMENTAL

RUTI

Intervention Type BIOLOGICAL

dose:25 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

RUTI 50 micrograms of FCMtb in HIV +

n=12

Group Type EXPERIMENTAL

RUTI

Intervention Type BIOLOGICAL

dose:50 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

RUTI Matching Placebo in HIV +

n=12

Group Type PLACEBO_COMPARATOR

RUTI Matching Placebo

Intervention Type BIOLOGICAL

Placebo of the vaccine RUTI; given subcutaneously twice, on days 28 and 56.

Interventions

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RUTI

dose:5 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

Intervention Type BIOLOGICAL

RUTI

dose:25 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

Intervention Type BIOLOGICAL

RUTI

dose:50 micrograms of FCMtb (Fragmented cells of M. tuberculosis); given subcutaneously twice, on days 28 and 56.

Intervention Type BIOLOGICAL

RUTI Matching Placebo

Placebo of the vaccine RUTI; given subcutaneously twice, on days 28 and 56.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

1. Asymptomatic adult aged 18 up to 50 years.
2. No evidence of active TB (Section 8).
3. No clinically significant finding at the discretion of the investigator.
4. Willingness to undergo an HIV test.
5. Resident in or near trial site for the duration of the trial.
6. Willingness to allow the investigators to discuss the patient's medical history with his usual doctor or HIV physician.
7. No donation of blood for 56 days prior to screening and agreement to refrain from blood donation during the trial.
8. Willing and able to provide written informed consent.
9. Positive tuberculin skin test (TST +), (≥5 mm induration) and Quantiferon TB Gold positive result (according to manufacturers instructions).
10. Reliable contraception to be used by female subjects during the clinical trial.

* HIV antibody positive.
* CD4 count ≥350 cells/mL3 on a single CD4 count at the period of screening.
* Subjects on anti-retroviral treatment can be included if clinically stable.

Exclusion Criteria

1. Any deviation from the normal range in biochemistry or haematology blood tests or in urine analysis that is considered to be clinically significant at the discretion of the investigator. Values of Hb, WCC, platelet count, AST/ALT and creatinine should be in a normal range accordingly to the normal laboratory values.
2. Use of any investigational or non-registered drug, vaccine, or medical device other than the trial vaccine within 30 days prior to dosing of trial vaccine, or planned use during the trial period.
3. Administration of chronic (defined as more than 14 days) immunosuppressive drugs within six months of vaccination and required throughout the duration of the trial (for corticosteroids this means prednisolone or equivalent at ≥ 0.5 mg/kg/day).
4. Female of child bearing potential who intends to become pregnant during the trial.
5. Females who are pregnant, lactating, or of child bearing potential with a blood HCG positive result 24-48 hours at the screening period, or prior to every injection of RUTI®.
6. Any AIDS defining illness according to the CDC classification system for HIV infection.
7. Presence of active (previously undiagnosed) TB or being on TB treatment.
8. Suspected or known current alcohol abuse (alcohol intake questionnaire.
9. Suspected or known substance abuse.
10. Presence of any underlying disease, specifically autoimmune disease, asthma, angioedema, bleeding disorders, uncontrolled hypertension and diabetes, and any other disease that compromises the diagnosis and evaluation of response to the vaccine, excluding HIV.
11. Administration of immunoglobulins and/or any blood products within three months prior to the planned administration of the vaccine.
12. Any history of anaphylaxis in reaction to vaccination and/or other medication.
13. Investigator assessment of lack of understanding or willingness to participate and comply with all requirements of the trial protocol.
14. Any other finding which in the opinion of the investigator would significantly increase the risk of having an adverse outcome from participating in the trial.

* Weight less than 40 kg.
* Known or suspected hypersensitivity to INH.
* Self reported chronic liver disease or symptoms suggesting active hepatitis (jaundice, nausea, vomiting, right upper quadrant pain, dark urine, pale stools).
* Alcohol use exceeding 28 units per week (men) or 21 units per week (women) (see alcohol intake questionnaire, Appendix 17.2).
* History of convulsions.
* History of psychosis.
* Peripheral neuropathy grade 2 or greater.
* Three months post-partum.
* Concomitant medication with phenytoin, carbamazepine; warfarin; theophylline; disulfiram; selective serotonin re-uptake inhibitor antidepressants (e.g. citalopram, fluoxetine, paroxetine, sertraline); oral ketoconazole or itraconazole.
16. Additional exclusion criterion for HIV negative groups:

• Any confirmed or suspected immunosuppressive or immunodeficient condition, including asplenia.
17. Additional exclusion criterion for HIV+ groups • CD4 count \< 350 cells/mL3.
Minimum Eligible Age

18 Years

Maximum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Parexel

INDUSTRY

Sponsor Role collaborator

Archivel Farma S.L.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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André S Nell, MD

Role: PRINCIPAL_INVESTIGATOR

Parexel Int. Bloemfontein

Pere Joan Cardona, MD, PhD

Role: STUDY_CHAIR

Archivel Farma S.L.

Locations

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Parexel Int. Bloemfontein

Bloemfontein, , South Africa

Site Status

Parexel Int. George

George, , South Africa

Site Status

Parexel Int. Port Elizabeth

Port Elizabeth, , South Africa

Site Status

Countries

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South Africa

References

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Gil O, Diaz I, Vilaplana C, Tapia G, Diaz J, Fort M, Caceres N, Pinto S, Cayla J, Corner L, Domingo M, Cardona PJ. Granuloma encapsulation is a key factor for containing tuberculosis infection in minipigs. PLoS One. 2010 Apr 6;5(4):e10030. doi: 10.1371/journal.pone.0010030.

Reference Type BACKGROUND
PMID: 20386605 (View on PubMed)

Cardona PJ. Revisiting the natural history of tuberculosis. The inclusion of constant reinfection, host tolerance, and damage-response frameworks leads to a better understanding of latent infection and its evolution towards active disease. Arch Immunol Ther Exp (Warsz). 2010 Feb;58(1):7-14. doi: 10.1007/s00005-009-0062-5. Epub 2010 Jan 5.

Reference Type BACKGROUND
PMID: 20049645 (View on PubMed)

Vilaplana C, Montane E, Pinto S, Barriocanal AM, Domenech G, Torres F, Cardona PJ, Costa J. Double-blind, randomized, placebo-controlled Phase I Clinical Trial of the therapeutical antituberculous vaccine RUTI. Vaccine. 2010 Jan 22;28(4):1106-16. doi: 10.1016/j.vaccine.2009.09.134. Epub 2009 Oct 22.

Reference Type BACKGROUND
PMID: 19853680 (View on PubMed)

Domingo M, Gil O, Serrano E, Guirado E, Nofrarias M, Grassa M, Caceres N, Perez B, Vilaplana C, Cardona PJ. Effectiveness and safety of a treatment regimen based on isoniazid plus vaccination with Mycobacterium tuberculosis cells' fragments: field-study with naturally Mycobacterium caprae-infected goats. Scand J Immunol. 2009 Jun;69(6):500-7. doi: 10.1111/j.1365-3083.2009.02251.x.

Reference Type BACKGROUND
PMID: 19439010 (View on PubMed)

Cardona PJ. A dynamic reinfection hypothesis of latent tuberculosis infection. Infection. 2009 Apr;37(2):80-6. doi: 10.1007/s15010-008-8087-y. Epub 2009 Mar 23.

Reference Type BACKGROUND
PMID: 19308318 (View on PubMed)

Gil O, Vilaplana C, Guirado E, Diaz J, Caceres N, Singh M, Cardona PJ. Enhanced gamma interferon responses of mouse spleen cells following immunotherapy for tuberculosis relapse. Clin Vaccine Immunol. 2008 Nov;15(11):1742-4. doi: 10.1128/CVI.00255-08. Epub 2008 Sep 30.

Reference Type BACKGROUND
PMID: 18827194 (View on PubMed)

Guirado E, Gil O, Caceres N, Singh M, Vilaplana C, Cardona PJ. Induction of a specific strong polyantigenic cellular immune response after short-term chemotherapy controls bacillary reactivation in murine and guinea pig experimental models of tuberculosis. Clin Vaccine Immunol. 2008 Aug;15(8):1229-37. doi: 10.1128/CVI.00094-08. Epub 2008 Jun 4.

Reference Type BACKGROUND
PMID: 18524883 (View on PubMed)

Vilaplana C, Ruiz-Manzano J, Gil O, Cuchillo F, Montane E, Singh M, Spallek R, Ausina V, Cardona PJ. The tuberculin skin test increases the responses measured by T cell interferon-gamma release assays. Scand J Immunol. 2008 Jun;67(6):610-7. doi: 10.1111/j.1365-3083.2008.02103.x. Epub 2008 Apr 4.

Reference Type BACKGROUND
PMID: 18397200 (View on PubMed)

Cardona PJ. New insights on the nature of latent tuberculosis infection and its treatment. Inflamm Allergy Drug Targets. 2007 Mar;6(1):27-39. doi: 10.2174/187152807780077282.

Reference Type BACKGROUND
PMID: 17352686 (View on PubMed)

Guirado E, Amat I, Gil O, Diaz J, Arcos V, Caceres N, Ausina V, Cardona PJ. Passive serum therapy with polyclonal antibodies against Mycobacterium tuberculosis protects against post-chemotherapy relapse of tuberculosis infection in SCID mice. Microbes Infect. 2006 Apr;8(5):1252-9. doi: 10.1016/j.micinf.2005.12.004. Epub 2006 Jan 27.

Reference Type BACKGROUND
PMID: 16702016 (View on PubMed)

Cardona PJ. RUTI: a new chance to shorten the treatment of latent tuberculosis infection. Tuberculosis (Edinb). 2006 May-Jul;86(3-4):273-89. doi: 10.1016/j.tube.2006.01.024. Epub 2006 Mar 20.

Reference Type BACKGROUND
PMID: 16545981 (View on PubMed)

Cardona PJ, Amat I, Gordillo S, Arcos V, Guirado E, Diaz J, Vilaplana C, Tapia G, Ausina V. Immunotherapy with fragmented Mycobacterium tuberculosis cells increases the effectiveness of chemotherapy against a chronical infection in a murine model of tuberculosis. Vaccine. 2005 Feb 3;23(11):1393-8. doi: 10.1016/j.vaccine.2004.09.008.

Reference Type BACKGROUND
PMID: 15661388 (View on PubMed)

Nell AS, D'lom E, Bouic P, Sabate M, Bosser R, Picas J, Amat M, Churchyard G, Cardona PJ. Safety, tolerability, and immunogenicity of the novel antituberculous vaccine RUTI: randomized, placebo-controlled phase II clinical trial in patients with latent tuberculosis infection. PLoS One. 2014 Feb 26;9(2):e89612. doi: 10.1371/journal.pone.0089612. eCollection 2014.

Reference Type DERIVED
PMID: 24586912 (View on PubMed)

Related Links

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http://www.germanstrias.org/

Fundació Institut Investigació en Ciències de la Salut Germans Trias i Pujol homepage

http://www.archivelfarma.com

Archivel Farma, S.L. homepage

Other Identifiers

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RUTISAPH2

Identifier Type: -

Identifier Source: org_study_id

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