Exploration of Genotype Based Personalized Prescription of Cyclophosphamide in Systemic Lupus Erythematosus Treatment

NCT ID: NCT01060410

Last Updated: 2012-06-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

222 participants

Study Classification

OBSERVATIONAL

Study Start Date

2010-05-31

Study Completion Date

2012-06-30

Brief Summary

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The purpose of this study is to investigate the relationship between the side effects of cyclophosphamide in the treatment of systemic lupus erythematosus (SLE) in Han Chinese and the genetic polymorphisms of drug metabolizing enzymes and pharmacokinetics of cyclophosphamide.

Detailed Description

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Cyclophosphamide is a widely applied agent in treatment of systemic lupus erythematosus. As an alkylating agent, cyclophosphamide is able to induce several side effects, including thinned hair, loss of appetite, nausea, vomiting, infection, myelosuppression, etc. However, the remarkable variability of the reactions to the drug -- the incidence of side effect or the outcome of the treatment -- has been observed among patients. Cyclophosphamide is a pro-drug, which require some enzymes in the liver to transform it into an active chemical to arouse alkylating function. And then it undergoes a series of detoxification steps catalyzed by the specific metabolic enzymes. This study is designed to explore the genetic variation among individuals in the key processes of the activation and elimination of cyclophosphamide in order to find out whether these genetic factors are associated to the side effects or efficacy. The further understanding into the factors concerning on the drug might imply possible solution to minimize the incidence of side effects in patients of systemic lupus erythematosus.

Conditions

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Lupus Erythematosus, Systemic Adverse Effects

Study Design

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Observational Model Type

CASE_ONLY

Study Time Perspective

PROSPECTIVE

Study Groups

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Cyclophosphamide,low dose,continuous

Polymorphism Analysis

Intervention Type GENETIC

Analysis of genetic polymorphisms of the drug metabolic enzymes involving in the bio-activation and elimination of cyclophosphamide

Cyclophosphamide

Intervention Type DRUG

intravenous injection, 0.2g, once every two days

Pharmacokinetic analysis

Intervention Type OTHER

laboratory analysis of concentration of cyclophosphamide and 4-OH-cyclophosphamide in plasma

Interventions

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Polymorphism Analysis

Analysis of genetic polymorphisms of the drug metabolic enzymes involving in the bio-activation and elimination of cyclophosphamide

Intervention Type GENETIC

Cyclophosphamide

intravenous injection, 0.2g, once every two days

Intervention Type DRUG

Pharmacokinetic analysis

laboratory analysis of concentration of cyclophosphamide and 4-OH-cyclophosphamide in plasma

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

1. The patients must have been diagnosed as SLE according to the American College of Rheumatology (ACR) criteria published in 1997.
2. The patients must sign the informed consent. And for the patients who are under 18 years old, both the signatures of their legal guardians and that of the patients are required on the written informed consent.
3. The patients are receiving the standard regimen of 0.2g cyclophosphamide given as intravenous injection once every two days.

Exclusion Criteria

1. Pregnant women, women in breast-feeding period and the women who refuse to take contraception measures during treatment.
2. Patients with poor compliance.
3. Patients who are also diagnosed of cancer or who are receiving cyclophosphamide in treatment of cancer, or other anti-cancer therapy.
Minimum Eligible Age

12 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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First Affiliated Hospital, Sun Yat-Sen University

OTHER

Sponsor Role collaborator

Sun Yat-sen University

OTHER

Sponsor Role lead

Responsible Party

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Wenying Shu

Ph.D.

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Min Huang, PhD.

Role: STUDY_CHAIR

Institute of Clinical Pharmacology, School of Pharmaceutical Sciences, Sun Yat-sen University, Guangzhou, China

Xueding Wang, PhD.

Role: STUDY_DIRECTOR

Institute of Clinical Pharmacology, School of Pharmaceutical Sciences, Sun Yat-sen University, Guangzhou, China

Wenying Shu, PhD.

Role: PRINCIPAL_INVESTIGATOR

Institute of Clinical Pharmacology, School of Pharmaceutical Sciences, Sun Yat-sen University, Guangzhou, China

Xiuyan Yang, MD.

Role: STUDY_DIRECTOR

Department of Rheumatology, the First Affiliated Hospital, Sun Yat-sen University, Guangzhou, China

Liuqin Liang, MD.

Role: PRINCIPAL_INVESTIGATOR

Department of Rheumatology, the First Affiliated Hospital, Sun Yat-sen University, Guangzhou, China

Locations

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Institute of Clinical Pharmacology, School of Pharmaceutical Sciences, Sun Yat-sen University

Guangzhou, Guangdong, China

Site Status

Countries

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China

Related Links

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Other Identifiers

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30873124-CTX2008

Identifier Type: -

Identifier Source: org_study_id

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