Assessment of Efficacy and Safety of Perifosine, Bortezomib and Dexamethasone in Multiple Myeloma Patients

NCT ID: NCT01002248

Last Updated: 2018-02-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

135 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-12-31

Study Completion Date

2013-03-31

Brief Summary

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This is a randomized Phase III study to evaluate the efficacy and safety of perifosine when added to the combination of bortezomib and dexamethasone in multiple myeloma patients who have relapsed on a prior bortezomib treatment regimen.

Detailed Description

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A pre-planned interim analysis is expected to take place in Q1 of 2013.

Conditions

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Multiple Myeloma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Perifosine added to combination

Perifosine added to the combination of Bortezomib and Dexamethasone. Perifosine is is supplied as a film-coated tablet containing 50 mg of active ingredient. Perifosine will be administered orally on an outpatient basis throughout the study. Daily administration will be one 50 mg tablet.

The first dose of perifosine should be taken on the same day that bortezomib and dexamethasone are administered (Cycle 1 Day 1).

Group Type EXPERIMENTAL

Perifosine

Intervention Type DRUG

Perifosine will be dosed as one 50 mg pill every day of each cycle.

Bortezomib

Intervention Type DRUG

Bortezomib will be dosed at 1.3 mg/m2 on Days 1, 4, 8, and 11 every 21 days.

Dexamethasone

Intervention Type DRUG

Dexamethasone will be administered orally at 20 mg on Days 1, 2, 4, 5, 8, 9, 11, and 12 of each 21-day cycle.

Perifosine Placebo added to combination

Perifosine placebo added to the combination of Bortezomib and Dexamethasone. The placebo for perifosine is provided in 256 mg white to off-white, round, biconvex film-coated tablets to permit a blinded trial with perifosine 50 mg film coated tablets. Placebo will be administered orally on an outpatient basis throughout the study. Daily administration will be one perifosine placebo tablet. The first dose of placebo should be taken on the same day that bortezomib and dexamethasone are administered (Cycle 1 Day 1).

Group Type PLACEBO_COMPARATOR

Perifosine Placebo

Intervention Type DRUG

Perifosine placebo will be dosed as one 50 mg pill every day of each cycle.

Bortezomib

Intervention Type DRUG

Bortezomib will be dosed at 1.3 mg/m2 on Days 1, 4, 8, and 11 every 21 days.

Dexamethasone

Intervention Type DRUG

Dexamethasone will be administered orally at 20 mg on Days 1, 2, 4, 5, 8, 9, 11, and 12 of each 21-day cycle.

Interventions

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Perifosine

Perifosine will be dosed as one 50 mg pill every day of each cycle.

Intervention Type DRUG

Perifosine Placebo

Perifosine placebo will be dosed as one 50 mg pill every day of each cycle.

Intervention Type DRUG

Bortezomib

Bortezomib will be dosed at 1.3 mg/m2 on Days 1, 4, 8, and 11 every 21 days.

Intervention Type DRUG

Dexamethasone

Dexamethasone will be administered orally at 20 mg on Days 1, 2, 4, 5, 8, 9, 11, and 12 of each 21-day cycle.

Intervention Type DRUG

Other Intervention Names

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D-21266 KRX-0401

Eligibility Criteria

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Inclusion Criteria

* Patient was previously diagnosed with multiple myeloma based on standard diagnostic criteria.
* Patients must have relapsed (progressed \> 60 days) after their last dose of bortezomib-based therapy. In addition, patients may be relapsed or refractory to other non-bortezomib-based therapies.
* Patient has received at least 1 but not more than 4 prior anti-myeloma regimens and has progressive disease after the most recent treatment regimen.
* Patients must have adequate organ and marrow function.

Exclusion Criteria

* Patients must not be refractory to any bortezomib-containing regimen.
* History of allergic reactions or intolerance attributed to compounds of similar chemical or biologic composition to perifosine (miltefosine or edelfosine), bortezomib or dexamethasone or any of their components.
* Prior treatment with perifosine or an investigational proteasome inhibitor.
* Chemotherapy or other therapy experimental or proven that is or may be active against myeloma within two weeks (14 days) prior to Cycle 1 Day 1.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Dana-Farber Cancer Institute

OTHER

Sponsor Role collaborator

AEterna Zentaris

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Paul Richardson, MD

Role: PRINCIPAL_INVESTIGATOR

Dana-Farber Cancer Institute

Locations

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La Verne, California, United States

Site Status

San Francisco, California, United States

Site Status

San Pablo, California, United States

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Aurora, Colorado, United States

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Boulder, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Lakewood, Colorado, United States

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Littleton, Colorado, United States

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Longmont, Colorado, United States

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Parker, Colorado, United States

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Pueblo, Colorado, United States

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Thornton, Colorado, United States

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Niles, Illinois, United States

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Winfield, Illinois, United States

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Baltimore, Maryland, United States

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Columbia, Maryland, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

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Morristown, New Jersey, United States

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Great Neck, New York, United States

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Fargo, North Dakota, United States

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Portland, Oregon, United States

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Tualatin, Oregon, United States

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Kingsport, Tennessee, United States

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Bedford, Texas, United States

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Dallas, Texas, United States

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Fort Worth, Texas, United States

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Kerrville, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Tyler, Texas, United States

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Ogden, Utah, United States

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Christiansburg, Virginia, United States

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Roanoke, Virginia, United States

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Salem, Virginia, United States

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Seattle, Washington, United States

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Spokane, Washington, United States

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Vancouver, Washington, United States

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Milwaukee, Wisconsin, United States

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Winnipeg, Manitoba, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Québec, Quebec, Canada

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Brno, Czech Republic, Czechia

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Prague, Czech Republic, Czechia

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Keryx / AOI Pharmaceuticals Investigative Site

Dublin, , Ireland

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Dublin, , Ireland

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Galway, , Ireland

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Limerick, , Ireland

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Sligo, , Ireland

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Tullamore, , Ireland

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Waterford, , Ireland

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Afula, , Israel

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Ashkelon, , Israel

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Beersheba, , Israel

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Haifa, , Israel

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Jerusalem, , Israel

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Jerusalem, , Israel

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Nahariya, , Israel

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Petah Tikva, , Israel

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Rehovot, , Israel

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Tel Aviv, , Israel

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Tel Litwinsky, , Israel

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Moscow, , Russia

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Moscow, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Samara, , Russia

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Košice, Slovak Republic, Slovakia

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

Site Status

Seoul, , South Korea

Site Status

Seoul, , South Korea

Site Status

Badalona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Madrid, , Spain

Site Status

Madrid, , Spain

Site Status

Madrid, , Spain

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Pamplona, , Spain

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San Cristóbal de La Laguna, , Spain

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Valencia, , Spain

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Zaragoza, , Spain

Site Status

Countries

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United States Canada Czechia Ireland Israel Russia Slovakia South Korea Spain

References

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Richardson PG, Nagler A, Ben-Yehuda D, Badros A, Hari P, Hajek R, Spicka I, Kaya H, Le Blanc R, Yoon SS, Kim K, Martinez-Lopez J, Mittelman M, Shpilberg O, Tothova E, Laubach JP, Ghobria IM, Leiba M, Gatt ME, Sportelli P, Chen M, Anderson KC. Randomized Placebo-Controlled Phase III Study Of Perifosine Combined With Bortezomib and Dexamethasone In Relapsed, Refractory Multiple Myeloma Patients Previously Treated With Bortezomib. Blood 2013 ASH Meeting Proceedings;122:abstract 3189

Reference Type RESULT

Other Identifiers

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Perifosine 339

Identifier Type: -

Identifier Source: org_study_id

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