Safety of 40K Pegylated Recombinant Factor IX in Non-Bleeding Patients With Haemophilia B

NCT ID: NCT00956345

Last Updated: 2017-01-20

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

18 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-08-31

Study Completion Date

2010-07-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This trial is conducted in Europe, Japan and the United States of America (USA).

The aim of this clinical trial is to investigate the safety and pharmacokinetics (the determination of the concentration of the administered medication in blood over time) of Pegylated Recombinant Factor IX (nonacog beta pegol) in Non-Bleeding Patients with Haemophilia B.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Congenital Bleeding Disorder Haemophilia B

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

25U/kg

Group Type EXPERIMENTAL

nonacog beta pegol

Intervention Type DRUG

Cohort to receive a single dose of 25U/kg nonacog beta pegol administered intravenously (into the vein)

50U/kg

Group Type EXPERIMENTAL

nonacog beta pegol

Intervention Type DRUG

Cohort to receive a single dose of 50U/kg nonacog beta pegol administered intravenously (into the vein)

100U/kg

Group Type EXPERIMENTAL

nonacog beta pegol

Intervention Type DRUG

Cohort to receive a single dose of 100U/kg nonacog beta pegol administered intravenously (into the vein)

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

nonacog beta pegol

Cohort to receive a single dose of 25U/kg nonacog beta pegol administered intravenously (into the vein)

Intervention Type DRUG

nonacog beta pegol

Cohort to receive a single dose of 50U/kg nonacog beta pegol administered intravenously (into the vein)

Intervention Type DRUG

nonacog beta pegol

Cohort to receive a single dose of 100U/kg nonacog beta pegol administered intravenously (into the vein)

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

40K PEG-rFIX 40K PEG-rFIX 40K PEG-rFIX

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Diagnosed with haemophilia B (baseline level of Factor IX less than or equal to 2%)
* History of at least 150 exposure days to any Factor IX products
* Body Mass Index (BMI) below 30.0 kg/m2 (inclusive)

Exclusion Criteria

* History of Factor IX inhibitors
* Platelet count less than 50,000 platelets/microlitre (assessed by laboratory)
* Kidney or liver dysfunction
* Scheduled surgery requiring Factor IX replacement therapy, during the trial period
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Novo Nordisk A/S

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Global Clinical Registry (GCR, 1452)

Role: STUDY_DIRECTOR

Novo Nordisk A/S

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Novo Nordisk Investigational Site

Cincinnati, Ohio, United States

Site Status

Novo Nordisk Investigational Site

Portland, Oregon, United States

Site Status

Novo Nordisk Investigational Site

Richmond, Virginia, United States

Site Status

Novo Nordisk Investigational Site

Copenhagen, , Denmark

Site Status

Novo Nordisk Investigational Site

Le Kremlin-Bicêtre, , France

Site Status

Novo Nordisk Investigational Site

Lyon, , France

Site Status

Novo Nordisk Investigational Site

Berlin, , Germany

Site Status

Novo Nordisk Investigational Site

Bonn, , Germany

Site Status

Novo Nordisk Investigational Site

Frankfurt/M., , Germany

Site Status

Novo Nordisk Investigational Site

Hanover, , Germany

Site Status

Novo Nordisk Investigational Site

Kashihara-shi, Nara, , Japan

Site Status

Novo Nordisk Investigational Site

Nagoya-shi, Aichi, , Japan

Site Status

Novo Nordisk Investigational Site

Nishinomiya-shi, , Japan

Site Status

Novo Nordisk Investigational Site

Madrid, , Spain

Site Status

Novo Nordisk Investigational Site

Stockholm, , Sweden

Site Status

Novo Nordisk Investigational Site

London, , United Kingdom

Site Status

Novo Nordisk Investigational Site

London, , United Kingdom

Site Status

Novo Nordisk Investigational Site

Manchester, , United Kingdom

Site Status

Novo Nordisk Investigational Site

Oxford, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Denmark France Germany Japan Spain Sweden United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Negrier C, Knobe K, Tiede A, Giangrande P, Moss J. Enhanced pharmacokinetic properties of a glycoPEGylated recombinant factor IX: a first human dose trial in patients with hemophilia B. Blood. 2011 Sep 8;118(10):2695-701. doi: 10.1182/blood-2011-02-335596. Epub 2011 May 9.

Reference Type BACKGROUND
PMID: 21555744 (View on PubMed)

Collins PW, Moss J, Knobe K, Groth A, Colberg T, Watson E. Population pharmacokinetic modeling for dose setting of nonacog beta pegol (N9-GP), a glycoPEGylated recombinant factor IX. J Thromb Haemost. 2012 Nov;10(11):2305-12. doi: 10.1111/jth.12000.

Reference Type BACKGROUND
PMID: 22998153 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

http://novonordisk-trials.com

Clinical Trials at Novo Nordisk

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2009-011085-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

090857

Identifier Type: REGISTRY

Identifier Source: secondary_id

NN7999-3639

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

A Gene Therapy Study for Hemophilia B
NCT02484092 COMPLETED PHASE2