An Extension Protocol for Multiple Sclerosis Patients Who Participated in Genzyme-Sponsored Studies of Alemtuzumab

NCT ID: NCT00930553

Last Updated: 2017-05-15

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1314 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-08-31

Study Completion Date

2016-02-29

Brief Summary

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This open-label, rater-blinded extension study enrolled participants who had relapsing-remitting multiple sclerosis (RRMS) and who participated in one of three prior Genzyme-sponsored studies of alemtuzumab (CAMMS223 \[NCT00050778\], CAMMS323 \[NCT00530348\] also known as CARE-MS I, or CAMMS324 \[NCT00548405\] also known as CARE-MS II). The purposes of this study were:

1. To examine the long term safety and efficacy of alemtuzumab treatment in participants who received alemtuzumab as their study treatment in one of the prior studies.
2. To examine the safety and efficacy of initial alemtuzumab treatment in this study for participants who received Rebif® (interferon beta-1a) as their study treatment in one of the prior studies.
3. To determine the safety and efficacy of additional "as needed" alemtuzumab treatment courses. This applied both to participants who received alemtuzumab for the first time in one of the prior studies or for the first time in this extension study.

Detailed Description

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Alemtuzumab treatment was on a fixed schedule of two treatment courses a year apart for participants who received Rebif® in one of the prior Genzyme-sponsored studies of alemtuzumab or on an as needed schedule (e.g. due to documented evidence of resumed Multiple Sclerosis \[MS\] activity) for participants who had already completed a fixed schedule of treatment with alemtuzumab in one of the prior Genzyme-sponsored studies. There was no comparison treatment in this study. All participants were required to return to their study site every 3 months for neurologic and other assessments. In addition, safety-related laboratory tests and surveys were performed at least monthly. Participation in the extension study was at least 48 months from enrollment. Study duration could be extended to allow participants to remain in the study until a follow-up study was available in their country or through month 60 (month 72 in USA), whichever occurred first.

Conditions

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Multiple Sclerosis, Relapsing-Remitting

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Outcome Assessors

Study Groups

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Previously treated with alemtuzumab

Alemtuzumab 12 mg per day administered through IV, once a day for 3 consecutive days (participants might receive additional cycles of alemtuzumab upon documented evidence of resumed disease activity, but not within same 12-month period)

Group Type EXPERIMENTAL

alemtuzumab

Intervention Type BIOLOGICAL

Alemtuzumab 12 mg/day IV infusion on 5 consecutive days if the participants had no prior alemtuzumab exposure (ie, first treatment course). All subsequent treatment courses were for 3 days only.

Previously treated with interferon beta-1a (Rebif®)

Alemtuzumab 12 mg per day administered through IV, once a day for 5 consecutive days during the first cycle and 12 mg per day administered through IV, once a day for 3 consecutive days during the second cycle, 12 months later. Participants might qualify for as-needed retreatment (12 mg per day administered through IV, once a day for 3 consecutive days) after their second fixed annual cycle.

Group Type EXPERIMENTAL

alemtuzumab

Intervention Type BIOLOGICAL

Alemtuzumab 12 mg/day IV infusion on 5 consecutive days if the participants had no prior alemtuzumab exposure (ie, first treatment course). All subsequent treatment courses were for 3 days only.

Interventions

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alemtuzumab

Alemtuzumab 12 mg/day IV infusion on 5 consecutive days if the participants had no prior alemtuzumab exposure (ie, first treatment course). All subsequent treatment courses were for 3 days only.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* 1.Received alemtuzumab in CAMMS323 or CAMMS324, completed the 2-year study period, and had not subsequently received disease modifying treatments (other than glatiramer acetate or interferon beta); or
* 2.Received Rebif® in CAMMS323 or CAMMS324, completed the 2-year study period, and had not subsequently received alternative disease modifying treatments (other than glatiramer acetate or another interferon beta); or
* 3.Participated in CAMMS223.
* NOTE: Criteria 1 and 2 above meant that participants who enrolled in CAMMS323 or CAMMS324 but did not complete the 2-year study period or went on to receive non-study drug DMTs after randomization were not eligible for inclusion in the Extension Study. Participants who enrolled in CAMMS324 after participation in CAMMS223 must meet criteria 1 or 2 to be eligible for inclusion in the Extension Study.

Exclusion Criteria

* Any alemtuzumab participant from CAMMS223, CAMMS323, or CAMMS324 who had received alemtuzumab off-label (ie, outside of one of the prior Genzyme-sponsored studies), or was participating in any other investigational study, unless approved by Genzyme. In addition, these participants must be screened for disqualifying safety concerns before receiving alemtuzumab retreatment.
* Any Rebif® participants from CAMMS223, CAMMS323, or CAMMS324 who met any of the following criteria. In addition, these participants must be screened for disqualifying safety concerns before receiving alemtuzumab treatment. a) Did not wish to receive alemtuzumab; b) Ongoing participation in any other investigational study, unless approved by Genzyme; c) Had received alemtuzumab off-label (ie, outside of one of the prior Genzyme-sponsored studies); d) Known bleeding disorder or therapeutic anticoagulation; e) Diagnosis of idiopathic thrombocytopenia purpura or other autoimmune hematologic abnormality; f) History of malignancy, except basal cell skin carcinoma; g) Intolerance of pulsed corticosteroids, especially a history of steroid psychosis h) Significant Autoimmune disorder (other than MS); i) Major psychiatric disorder or epileptic seizures not adequately controlled by treatment; j) Active infection or high risk for infection k) Unwilling to use a reliable and acceptable contraceptive method during and for at least 6 months following each alemtuzumab treatment cycle (fertile participants only).
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role collaborator

Genzyme, a Sanofi Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Monitor

Role: STUDY_DIRECTOR

Genzyme Coorporation

Locations

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North Central Neurology Associates, P.C.

Cullman, Alabama, United States

Site Status

HOPE Research Institute

Phoenix, Arizona, United States

Site Status

St. Joseph's Hospital and Medical Center Barrow Neurology Clinics - Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

Mayo Clinic Arizona (Scottsdale)

Scottsdale, Arizona, United States

Site Status

Northwest NeuroSpecialists, PLLC

Tucson, Arizona, United States

Site Status

East Bay Physicians Medical Group/ Sutter East Bay Medical Foundation

Berkeley, California, United States

Site Status

Neurology Center North Orange County

La Habra, California, United States

Site Status

University of Southern California Keck School of Medicine/University of Southern California LAC & USC Medical Center

Los Angeles, California, United States

Site Status

Neuro-Therapeutics, Inc.

Pasadena, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

University of Colorado Health Science Center - Aurora

Aurora, Colorado, United States

Site Status

Advanced Neurology of Colorado

Fort Collins, Colorado, United States

Site Status

Yale MS Research Center

New Haven, Connecticut, United States

Site Status

The George Washington University Medical Faculty Associates

Washington D.C., District of Columbia, United States

Site Status

University of Florida Neuroscience Institute

Jacksonville, Florida, United States

Site Status

Neurology Associates, P.A.

Maitland, Florida, United States

Site Status

Neurological Associates

Pompano Beach, Florida, United States

Site Status

Negroski, Stein, Sutherland and Hanes Neurology

Sarasota, Florida, United States

Site Status

Axiom Clinical Research of Florida

Tampa, Florida, United States

Site Status

University of South Florida College of Medicine

Tampa, Florida, United States

Site Status

Emory University Department of Neurology

Atlanta, Georgia, United States

Site Status

Shepherd Center Multiple Sclerosis Institute

Atlanta, Georgia, United States

Site Status

University of Chicago Medical Center

Chicago, Illinois, United States

Site Status

Consultants in Neurology, LTD

Northbrook, Illinois, United States

Site Status

Fort Wayne Neurological Center

Fort Wayne, Indiana, United States

Site Status

Indiana University Multiple Sclerosis Center

Indianapolis, Indiana, United States

Site Status

Iowa Health Physicians

Des Moines, Iowa, United States

Site Status

Ruan Neurology Clinic and Clinical Research Center, Mercy Medical Center

Des Moines, Iowa, United States

Site Status

University of Kansas Medical Center, Department of Neurology

Kansas City, Kansas, United States

Site Status

MidAmerica Neuroscience Institute

Lenexa, Kansas, United States

Site Status

Associates in Neurology, P.S.C.

Lexington, Kentucky, United States

Site Status

Kentucky Neuroscience Research

Louisville, Kentucky, United States

Site Status

University of Maryland, Maryland Center for MS

Baltimore, Maryland, United States

Site Status

The MS Center at St. Elizabeth's

Boston, Massachusetts, United States

Site Status

UMass Memorial Medical Center

Worcester, Massachusetts, United States

Site Status

University of Michigan Medical School

Ann Arbor, Michigan, United States

Site Status

Michigan Neurology Association

Clinton, Michigan, United States

Site Status

Wayne State University, The School of Medicine, Department of Neurology

Detroit, Michigan, United States

Site Status

Spectrum Health Medical Group, Neurology/Michigan Medical P.C., West Michigan MS Clinic

Grand Rapids, Michigan, United States

Site Status

Northern Michigan Neurology

Traverse City, Michigan, United States

Site Status

Saint Luke's Brain & Stroke Institute

Kansas City, Missouri, United States

Site Status

Renown Institute for Neurosciences

Reno, Nevada, United States

Site Status

Dartmouth Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

MS Center at Holy Name Hospital

Teaneck, New Jersey, United States

Site Status

University of New Mexico, Dept. of Neurology

Albuquerque, New Mexico, United States

Site Status

Empire Neurology P.C.

Latham, New York, United States

Site Status

Winthrop University Hospital Multiple Sclerosis Treatment Center

Mineola, New York, United States

Site Status

MS Care Center at NYUMC and HJD

New York, New York, United States

Site Status

The Corinne Goldsmith Dickinson Center for Multiple Sclerosis at Mount Sinai

New York, New York, United States

Site Status

South Shore Neurologic Associates, P.C.

Patchogue, New York, United States

Site Status

Rochester Multiple Sclerosis Center

Rochester, New York, United States

Site Status

SUNY Upstate Medical University, Department of Neurology

Syracuse, New York, United States

Site Status

The University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Wake Forest University Health Science Department of Neurology

Winston-Salem, North Carolina, United States

Site Status

Cleveland Clinic Foundation

Cleveland, Ohio, United States

Site Status

Oak Clinic for Multiple Sclerosis

Uniontown, Ohio, United States

Site Status

OMRF Multiple Sclerosis Center of Excellence

Oklahoma City, Oklahoma, United States

Site Status

Lehigh Valley Hospital Neurosciences and Pain Research

Allentown, Pennsylvania, United States

Site Status

Rhode Island Hospital MS Center - The Neurology Foundation, Inc

Providence, Rhode Island, United States

Site Status

Neurology Clinic PC

Cordova, Tennessee, United States

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Advanced Neurosciences Institute

Franklin, Tennessee, United States

Site Status

Hope Neurology

Knoxville, Tennessee, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor College of Medicine, Maxine Mesinger MS Clinic

Houston, Texas, United States

Site Status

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status

Integra Clinical Research

San Antonio, Texas, United States

Site Status

Neurology Center of San Antonio

San Antonio, Texas, United States

Site Status

MS Center of Greater Washington

Vienna, Virginia, United States

Site Status

Swedish Medical MS Center

Seattle, Washington, United States

Site Status

DIABAID

Buenos Aires, , Argentina

Site Status

Concord Repatriation General Hospital

Concord, New South Wales, Australia

Site Status

Southern Neurology

Kogarah, New South Wales, Australia

Site Status

Liverpool Hospital

Liverpool, New South Wales, Australia

Site Status

Westmead Hospital

Westmead, New South Wales, Australia

Site Status

Gold Coast Hospital

Southport, Queensland, Australia

Site Status

Royal Hobart Hospital

Hobart, Tasmania, Australia

Site Status

St. Vincent's Hospital

Fitzroy, Victoria, Australia

Site Status

Austin Health

Heidelberg, Victoria, Australia

Site Status

Royal Melbourne Hospital

Parkville, Victoria, Australia

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The Wesley Research Institute

Auchenflower QLD, , Australia

Site Status

The Queen Elizabeth Hospital

Woodville, SA, , Australia

Site Status

AKH Wien-Universitätskliniken für Neurologie

Vienna, , Austria

Site Status

Cliniques Universitaires Saint-luc

Brussels, , Belgium

Site Status

CHU Ourthe Amblève

Esneux, , Belgium

Site Status

University Hospital Leuven, Campus Gasthuisberg

Leuven, , Belgium

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Hospital Mae de Deus

Porto Alegre, , Brazil

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Hospital da Restauração, Neurology department

Recife, PE, , Brazil

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Irmandade da Santa Casa de Misericórdio de São Paulo, Neurology department

São Paulo, SP, , Brazil

Site Status

Hospital das Clínicas da Faculdade de Medicina da USP, Neurology department

São Paulo,SP, , Brazil

Site Status

University of Calgary, Department of Neurology

Calgary, Alberta, Canada

Site Status

Kingston General Hospital MS Clinic

Kingston, Ontario, Canada

Site Status

Clinique Neuro-Outaouais

Gatineau, Quebec, Canada

Site Status

Recherche Sepmus, Inc.

Greenfield Park, Quebec, Canada

Site Status

Hopital Maisonneuve-Rosemont

Montreal, Quebec, Canada

Site Status

London Health Sciences Centre - University Hospital

London, on, , Canada

Site Status

The Ottawa Hospital - MS Research

Ottawa, Ontario, , Canada

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University of British Columbia

Vancouver, BC, , Canada

Site Status

Clinical Hospital Osijek

Osijek, , Croatia

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Clinical Hospital Centre Rijeka

Rijeka, , Croatia

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General Hospital Varazdin, Department for Neurology

Varaždin, , Croatia

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Clinical Hospital Centre "Sestre Milosrdnice"

Zagreb, , Croatia

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Clinical Hospital Centre Zagreb

Zagreb, , Croatia

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Clinical Hospital Sveti Duh

Zagreb, , Croatia

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St. Anne's University Hospital Brno

Brno, , Czechia

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University Hospital Hradec Králové

Hradec Králové, , Czechia

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General Hospital, 128 21 Praha 2

Prague, , Czechia

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Hospital Teplice, Neurology Department, MS centrum

Teplice, , Czechia

Site Status

Aarhus Sygehus

Århus C, , Denmark

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Rigshospitalet Department of Neurology

Copenhagen, , Denmark

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Hôpital Général

Dijon, , France

Site Status

Groupe Hospitalier Pitié-Salpêtrière, Fédération de Maladies du System Nerveux Central

Paris, , France

Site Status

CHU Pontchaillou

Rennes, , France

Site Status

Hôpital Civil

Strasbourg, , France

Site Status

CHU de Toulouse, Hôpital Purpan

Toulouse, , France

Site Status

Klinik und Poliklinik für Neurologie, Universitätsklinikum Bonn

Bonn, DE, Germany

Site Status

Universitätsklinik Carl Gustav Carus Dresden

Dresden, , Germany

Site Status

Klinikum der JW Goethe Universität

Frankfurt am Main, , Germany

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Asklepios Klinik Barmbek

Hamburg, , Germany

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Medizinische Hochschule Hannover

Hanover, , Germany

Site Status

Oberhavel Klinicum GmbH - Krankenhaus Hennigsdorf

Hennigsdorf, , Germany

Site Status

Klinikum Ingolstadt

Ingolstadt, , Germany

Site Status

Jüdisches Krankenhaus Berlin

Mitte, , Germany

Site Status

Klinikum rechts der Isar

München, , Germany

Site Status

Medizinische Fakultät der Universität Rostock,Zentrum für Nervenheilkunde

Rostock, , Germany

Site Status

Universitätsklinikum Ulm, Klinik für Neurologie im RKU

Ulm, , Germany

Site Status

Fachkrankenhaus Hubertusburg GmbH, Klinik für Neurologie und Neurologische Intensivmedizin

Wermsdorf, , Germany

Site Status

Hadassah Medical Center Ein Karem

Ein Karem, Jerusalem, , Israel

Site Status

Sheba Medical Center

Ramat Gan, , Israel

Site Status

Sourasky Tel Aviv Medical Center

Tel Aviv, , Israel

Site Status

Università di Cagliari

Cagliari, , Italy

Site Status

Ospedale S. Antonio Abate di Gallarate

Gallarate (Varese), , Italy

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Ospedale S. Luigi Gonzaga

Orbassano (TO), , Italy

Site Status

Universita Degli Studi di Roma "La Sapienza"

Roma, , Italy

Site Status

Unidad de Investigación en Salud

Chihuahua, CHH, , Mexico

Site Status

Medica Sur

Mexico City, DFE, , Mexico

Site Status

Jeroen Bosch Ziekenhuis

's-Hertogenbosch, , Netherlands

Site Status

Orbis Medisch Concern

Sittard-Geleen, , Netherlands

Site Status

Centrum Neurologii Klinicznej Sp. Zo.o.

Krakow, , Poland

Site Status

Samodzielny Publiczny ZOZ, Uniwersytecki Szpital Kliniczny Nr1 im. Norberta Barlickiego

Lodz, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny Nr 4 w Lublinie

Lublin, , Poland

Site Status

Szpital Kliniczny im. Heliodora Swiecickiego Uniwersytetu Med. im. Karola Marcinkowskiego w Poznaniu

Poznan, , Poland

Site Status

Institute of Psychiatry and Neurology/Instytut Psychiatrii i Neurologii

Warsaw, , Poland

Site Status

Research Medical Complex "Your Health" Ltd

Kazan', , Russia

Site Status

Moscow State Public Medical Institution Clinical Hospital #11, Neurology Department

Moscow, , Russia

Site Status

Neurology Research Center under the Russian Academy of Medical Sciences

Moscow, , Russia

Site Status

Russian State Medical University, Department of Neurology and Neurosurgery

Moscow, , Russia

Site Status

Municipal Treatment and Prevention Institution, City Hospital #33

Nizhny Novgorod, , Russia

Site Status

Federal State Public Medical Institution: Siberian District Medical Center under the Federal Agency

Novosibirsk, , Russia

Site Status

Municipal Public Medical Institution: City Hospital #2 of Pyatigorsk, Neurology Department

Pyatigorsk, , Russia

Site Status

Institute of Human Brain RAS, Laboratory of Neuroimmunology

Saint Petersburg, , Russia

Site Status

St Petersburg State Pavlov Medical University, Dept of Neurology and Neurosurgery with a Hospital

Saint Petersburg, , Russia

Site Status

St. Petersburg General Hospital #2, Neurology Department #2

Saint Petersburg, , Russia

Site Status

St. Petersburg State Public Medical Institution: Nikolayevskaya Hospital

Saint Petersburg, , Russia

Site Status

Samara Regional Clinical Hospital n.a. Kalinin

Samara, , Russia

Site Status

State Public Medical Institution: Republican Clinical Hospital n.a. G.G. Kuvatov

Ufa, , Russia

Site Status

Clinical Centre Serbia, Institute of Neurology,Dr.Subotica 6,Belgrade

Belgrade, , Serbia

Site Status

Military Medical Academy, Institute of Neurology

Belgrade, , Serbia

Site Status

Clinical Centre Kragujevac, Clinic of Neurology

Kragujevac, , Serbia

Site Status

Clinical Centre Nis, Clinic of Neurology

Niš, , Serbia

Site Status

Clinical Centre Vojvodina

Novi Sad, , Serbia

Site Status

Hospital Universitario Vall d' Hebron

Barcelona, , Spain

Site Status

Hospital Clínico Universitario San Carlos

Madrid, , Spain

Site Status

Hospital Carlos Haya, Neurology Service

Málaga, , Spain

Site Status

Hospital Virgen Macarena

Seville, , Spain

Site Status

SU/Östra sjukhuset

Gothenburg, , Sweden

Site Status

Norrlands Universitets sjukhus

Umeå, , Sweden

Site Status

Institute of Neurology, Psychiatry and Narcology under the AMS of Ukraine, Dep of Neuroinfection& MS

Kharkiv, , Ukraine

Site Status

Kiev Municipal Clinical Hospital #4, Department of Demyelinating Diseases of the Nervous System

Kiev, , Ukraine

Site Status

Hospital of Directorate of the Medical Corps within the Ukrainian Security Service, Neurology Dept.

Kiev-21, , Ukraine

Site Status

Lviv National Medical University n.a. Danylo Galytsky, Department of Neurology

Lviv, , Ukraine

Site Status

Frenchay Hospital

Bristol, , United Kingdom

Site Status

Addenbrookes Hospital

Cambridge, , United Kingdom

Site Status

University Hospital of Wales, Dept of Neurology

Cardiff, , United Kingdom

Site Status

Royal London Hospital

London, , United Kingdom

Site Status

Salford Royal NHS Foundation Trust

Salford, , United Kingdom

Site Status

Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status

Countries

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United States Argentina Australia Austria Belgium Brazil Canada Croatia Czechia Denmark France Germany Israel Italy Mexico Netherlands Poland Russia Serbia Spain Sweden Ukraine United Kingdom

References

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CAMMS223 Trial Investigators; Coles AJ, Compston DA, Selmaj KW, Lake SL, Moran S, Margolin DH, Norris K, Tandon PK. Alemtuzumab vs. interferon beta-1a in early multiple sclerosis. N Engl J Med. 2008 Oct 23;359(17):1786-801. doi: 10.1056/NEJMoa0802670.

Reference Type BACKGROUND
PMID: 18946064 (View on PubMed)

Cohen JA, Coles AJ, Arnold DL, Confavreux C, Fox EJ, Hartung HP, Havrdova E, Selmaj KW, Weiner HL, Fisher E, Brinar VV, Giovannoni G, Stojanovic M, Ertik BI, Lake SL, Margolin DH, Panzara MA, Compston DA; CARE-MS I investigators. Alemtuzumab versus interferon beta 1a as first-line treatment for patients with relapsing-remitting multiple sclerosis: a randomised controlled phase 3 trial. Lancet. 2012 Nov 24;380(9856):1819-28. doi: 10.1016/S0140-6736(12)61769-3. Epub 2012 Nov 1.

Reference Type BACKGROUND
PMID: 23122652 (View on PubMed)

Coles AJ, Twyman CL, Arnold DL, Cohen JA, Confavreux C, Fox EJ, Hartung HP, Havrdova E, Selmaj KW, Weiner HL, Miller T, Fisher E, Sandbrink R, Lake SL, Margolin DH, Oyuela P, Panzara MA, Compston DA; CARE-MS II investigators. Alemtuzumab for patients with relapsing multiple sclerosis after disease-modifying therapy: a randomised controlled phase 3 trial. Lancet. 2012 Nov 24;380(9856):1829-39. doi: 10.1016/S0140-6736(12)61768-1. Epub 2012 Nov 1.

Reference Type BACKGROUND
PMID: 23122650 (View on PubMed)

Ziemssen T, Bass AD, Van Wijmeersch B, Eichau S, Richter S, Hoffmann F, Armstrong NM, Chirieac M, Cunha-Santos J, Singer BA. Long-term efficacy and safety of alemtuzumab in participants with highly active MS: TOPAZ clinical trial and interim analysis of TREAT-MS real-world study. Ther Adv Neurol Disord. 2025 Feb 10;18:17562864241306575. doi: 10.1177/17562864241306575. eCollection 2025.

Reference Type DERIVED
PMID: 39935588 (View on PubMed)

Coles AJ, Achiron A, Traboulsee A, Singer BA, Pozzilli C, Oreja-Guevara C, Giovannoni G, Comi G, Freedman MS, Ziemssen T, Shiota D, Rawlings AM, Wong AT, Chirieac M, Montalban X. Safety and efficacy with alemtuzumab over 13 years in relapsing-remitting multiple sclerosis: final results from the open-label TOPAZ study. Ther Adv Neurol Disord. 2023 Sep 21;16:17562864231194823. doi: 10.1177/17562864231194823. eCollection 2023.

Reference Type DERIVED
PMID: 37745914 (View on PubMed)

Dayan CM, Lecumberri B, Muller I, Ganesananthan S, Hunter SF, Selmaj KW, Hartung HP, Havrdova EK, LaGanke CC, Ziemssen T, Van Wijmeersch B, Meuth SG, Margolin DH, Poole EM, Baker DP, Senior PA. Endocrine and multiple sclerosis outcomes in patients with autoimmune thyroid events in the alemtuzumab CARE-MS studies. Mult Scler J Exp Transl Clin. 2023 Jan 3;9(1):20552173221142741. doi: 10.1177/20552173221142741. eCollection 2023 Jan-Mar.

Reference Type DERIVED
PMID: 36619856 (View on PubMed)

Coles AJ, Jones JL, Vermersch P, Traboulsee A, Bass AD, Boster A, Chan A, Comi G, Fernandez O, Giovannoni G, Kubala Havrdova E, LaGanke C, Montalban X, Oreja-Guevara C, Piehl F, Wiendl H, Ziemssen T. Autoimmunity and long-term safety and efficacy of alemtuzumab for multiple sclerosis: Benefit/risk following review of trial and post-marketing data. Mult Scler. 2022 Apr;28(5):842-846. doi: 10.1177/13524585211061335. Epub 2021 Dec 9.

Reference Type DERIVED
PMID: 34882037 (View on PubMed)

Kuhle J, Daizadeh N, Benkert P, Maceski A, Barro C, Michalak Z, Sormani MP, Godin J, Shankara S, Samad TA, Jacobs A, Chung L, Rӧsch N, Kaiser C, Mitchell CP, Leppert D, Havari E, Kappos L. Sustained reduction of serum neurofilament light chain over 7 years by alemtuzumab in early relapsing-remitting MS. Mult Scler. 2022 Apr;28(4):573-582. doi: 10.1177/13524585211032348. Epub 2021 Aug 11.

Reference Type DERIVED
PMID: 34378446 (View on PubMed)

Coles AJ, Arnold DL, Bass AD, Boster AL, Compston DAS, Fernandez O, Havrdova EK, Nakamura K, Traboulsee A, Ziemssen T, Jacobs A, Margolin DH, Huang X, Daizadeh N, Chirieac MC, Selmaj KW. Efficacy and safety of alemtuzumab over 6 years: final results of the 4-year CARE-MS extension trial. Ther Adv Neurol Disord. 2021 Apr 23;14:1756286420982134. doi: 10.1177/1756286420982134. eCollection 2021.

Reference Type DERIVED
PMID: 34035833 (View on PubMed)

Bass AD, Arroyo R, Boster AL, Boyko AN, Eichau S, Ionete C, Limmroth V, Navas C, Pelletier D, Pozzilli C, Ravenscroft J, Sousa L, Tintore M, Uitdehaag BMJ, Baker DP, Daizadeh N, Choudhry Z, Rog D; CARE-MS I, CARE-MS II, CAMMS03409, and TOPAZ investigators. Alemtuzumab outcomes by age: Post hoc analysis from the randomized CARE-MS studies over 8 years. Mult Scler Relat Disord. 2021 Apr;49:102717. doi: 10.1016/j.msard.2020.102717. Epub 2020 Dec 24.

Reference Type DERIVED
PMID: 33476880 (View on PubMed)

Horakova D, Boster A, Bertolotto A, Freedman MS, Firmino I, Cavalier SJ, Jacobs AK, Thangavelu K, Daizadeh N, Poole EM, Baker DP, Margolin DH, Ziemssen T; CARE-MS I, CARE-MS II, and CAMMS03409 Investigators. Proportion of alemtuzumab-treated patients converting from relapsing-remitting multiple sclerosis to secondary progressive multiple sclerosis over 6 years. Mult Scler J Exp Transl Clin. 2020 Dec 18;6(4):2055217320972137. doi: 10.1177/2055217320972137. eCollection 2020 Oct-Dec.

Reference Type DERIVED
PMID: 33414927 (View on PubMed)

Ziemssen T, Bass AD, Berkovich R, Comi G, Eichau S, Hobart J, Hunter SF, LaGanke C, Limmroth V, Pelletier D, Pozzilli C, Schippling S, Sousa L, Traboulsee A, Uitdehaag BMJ, Van Wijmeersch B, Choudhry Z, Daizadeh N, Singer BA; CARE-MS I, CARE-MS II, CAMMS03409, and TOPAZ investigators. Efficacy and Safety of Alemtuzumab Through 9 Years of Follow-up in Patients with Highly Active Disease: Post Hoc Analysis of CARE-MS I and II Patients in the TOPAZ Extension Study. CNS Drugs. 2020 Sep;34(9):973-988. doi: 10.1007/s40263-020-00749-x.

Reference Type DERIVED
PMID: 32710396 (View on PubMed)

Gilmore W, Lund BT, Li P, Levy AM, Kelland EE, Akbari O, Groshen S, Cen SY, Pelletier D, Weiner LP, Javed A, Dunn JE, Traboulsee AL. Repopulation of T, B, and NK cells following alemtuzumab treatment in relapsing-remitting multiple sclerosis. J Neuroinflammation. 2020 Jun 15;17(1):189. doi: 10.1186/s12974-020-01847-9.

Reference Type DERIVED
PMID: 32539719 (View on PubMed)

Comi G, Alroughani R, Boster AL, Bass AD, Berkovich R, Fernandez O, Kim HJ, Limmroth V, Lycke J, Macdonell RA, Sharrack B, Singer BA, Vermersch P, Wiendl H, Ziemssen T, Jacobs A, Daizadeh N, Rodriguez CE, Traboulsee A; CARE-MS I, CARE-MS II, CAMMS03409, and TOPAZ Investigators. Efficacy of alemtuzumab in relapsing-remitting MS patients who received additional courses after the initial two courses: Pooled analysis of the CARE-MS, extension, and TOPAZ studies. Mult Scler. 2020 Dec;26(14):1866-1876. doi: 10.1177/1352458519888610. Epub 2019 Nov 25.

Reference Type DERIVED
PMID: 31762387 (View on PubMed)

Van Wijmeersch B, Singer BA, Boster A, Broadley S, Fernandez O, Freedman MS, Izquierdo G, Lycke J, Pozzilli C, Sharrack B, Steingo B, Wiendl H, Wray S, Ziemssen T, Chung L, Margolin DH, Thangavelu K, Vermersch P. Efficacy of alemtuzumab over 6 years in relapsing-remitting multiple sclerosis patients who relapsed between courses 1 and 2: Post hoc analysis of the CARE-MS studies. Mult Scler. 2020 Nov;26(13):1719-1728. doi: 10.1177/1352458519881759. Epub 2019 Nov 1.

Reference Type DERIVED
PMID: 31675266 (View on PubMed)

Okai AF, Amezcua L, Berkovich RR, Chinea AR, Edwards KR, Steingo B, Walker A, Jacobs AK, Daizadeh N, Williams MJ; CARE-MS I, CARE-MS II, CAMMS03409, and TOPAZ Investigators. Efficacy and Safety of Alemtuzumab in Patients of African Descent with Relapsing-Remitting Multiple Sclerosis: 8-Year Follow-up of CARE-MS I and II (TOPAZ Study). Neurol Ther. 2019 Dec;8(2):367-381. doi: 10.1007/s40120-019-00159-2. Epub 2019 Oct 25.

Reference Type DERIVED
PMID: 31654272 (View on PubMed)

Arroyo R, Bury DP, Guo JD, Margolin DH, Melanson M, Daizadeh N, Cella D. Impact of alemtuzumab on health-related quality of life over 6 years in CARE-MS II trial extension patients with relapsing-remitting multiple sclerosis. Mult Scler. 2020 Jul;26(8):955-963. doi: 10.1177/1352458519849796. Epub 2019 May 30.

Reference Type DERIVED
PMID: 31144568 (View on PubMed)

Havrdova E, Arnold DL, Cohen JA, Hartung HP, Fox EJ, Giovannoni G, Schippling S, Selmaj KW, Traboulsee A, Compston DAS, Margolin DH, Thangavelu K, Rodriguez CE, Jody D, Hogan RJ, Xenopoulos P, Panzara MA, Coles AJ; CARE-MS I and CAMMS03409 Investigators. Alemtuzumab CARE-MS I 5-year follow-up: Durable efficacy in the absence of continuous MS therapy. Neurology. 2017 Sep 12;89(11):1107-1116. doi: 10.1212/WNL.0000000000004313. Epub 2017 Aug 23.

Reference Type DERIVED
PMID: 28835401 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2009-010788-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

LTE12824

Identifier Type: OTHER

Identifier Source: secondary_id

CAMMS03409

Identifier Type: -

Identifier Source: org_study_id

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