Effect of Goserelin (Zoladex®) in Spinal and Bulbar Muscular Atrophy

NCT ID: NCT00851461

Last Updated: 2015-05-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

10 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-04-30

Study Completion Date

2013-11-30

Brief Summary

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This is a therapeutic trial study to demonstrate whether Goserelin, a LHRH agonist has benefit in SBMA

Objective:

1. To study effects of Goserelin to clinical course of patients with spinal and bulbar muscular atrophy in Thailand
2. To demonstrate physiological and pathological changes in treated patients with Goserelin.
3. To assess tolerability and adverse effect of Goserelin therapy

Detailed Description

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Conditions

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Spinobulbar Muscular Atrophy Kennedy's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Interventions

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Goserelin

Goserelin 10.8 mg SC every 3 months

Intervention Type DRUG

Electrophysiologic study

Nerve conduction study Electromyogram

Intervention Type PROCEDURE

tissue biopsy

skin and muscle biopsy before and after treatment every year

Intervention Type PROCEDURE

Other Intervention Names

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Zoladex LA NCV EMG

Eligibility Criteria

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Inclusion Criteria

1. Provision of informed consent
2. Males, age over 20 years, undesired fertility
3. Have positive family history of muscle weakness with these clinical signs:

* bulbar involvement (difficulty in breathing, swallowing, talking)
* muscle atrophy with or without fasciculation
* decrease or normal deep tendon reflex
* normal Babinski response
* no sensory impairment
* mild tremor (either postural or intention)
* gynecomastia
* decrease libido and infertility
4. Subjects have a confirmed diagnosis to SBMA by both NCV test and DNA study demonstrated the number of CAG repeated more than 35.

Exclusion Criteria

1. Have weakness caused by other etiologies and have liver or kidney disease.
2. Have currently prostatic cancer
3. Want to have a child
4. Participation in a clinical study during the last 30 days.
5. Females and children age \< 20 years old
Minimum Eligible Age

20 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role collaborator

Ramathibodi Hospital

OTHER

Sponsor Role lead

Responsible Party

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Faculty of Medicine, Ramathibodi Hospital, Bangkok, Thailand

Principal Investigators

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Thanyachau Sura, M.D., MRCP

Role: PRINCIPAL_INVESTIGATOR

Ramathibodi Hospital

Locations

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Medical Genetics and Molecular Medicine Unit,, Department of Medicine, Ramathibodi Hospital

Bangkok, Bangkok, Thailand

Site Status

Countries

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Thailand

Other Identifiers

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ID11-50-17

Identifier Type: -

Identifier Source: org_study_id

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