Trial Outcomes & Findings for Docetaxel and Hydroxychloroquine in Treating Patients With Metastatic Prostate Cancer (NCT NCT00786682)

NCT ID: NCT00786682

Last Updated: 2023-08-14

Results Overview

We will use a two-stage optimal Simon's design with a 5% significance level and 80% power to detect an increase in response rate from 50% to 70%. The first stage will enroll 15 patients. If there are 8 or fewer responses among these 15 patients, we will consider the combination therapy to not be worthy of further study, and stop the trial. If we find 9 or more responses, we will proceed to the second stage, and accrual continues for a total of 43 patients. If we see 26 or fewer responses out of 43, then no further investigation of the drug is warranted. If we see 27 or more responses out of 43, then further investigation of the drug will be considered. The "expected" sample size of the trial is 23.5 with the null response rate of 50%.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

11 participants

Primary outcome timeframe

4 years

Results posted on

2023-08-14

Participant Flow

Subjects were recruited from the Cancer Institute of New Jersey (a comprehensive cancer center) and a community hospital in New Jersey, part of the CINJ Oncology Group, from February 2009 through August 2010.

Participant milestones

Participant milestones
Measure
Docetaxel and Hydroxychloroquine
Drug: Docetaxel 75 mg/m2 intravenously every 21 days on Day 1 of the treatment cycle Drug: hydroxychloroquine 200 mg twice daily A cycle is defined as an interval of 21 days.
Overall Study
STARTED
11
Overall Study
COMPLETED
11
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Docetaxel and Hydroxychloroquine in Treating Patients With Metastatic Prostate Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Docetaxel and Hydroxychloroquine
n=11 Participants
Drug: Docetaxel 75 mg/m2 intravenously every 21 days on Day 1 of the treatment cycle Drug: hydroxychloroquine 200 mg twice daily A cycle is defined as an interval of 21 days.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
5 Participants
n=5 Participants
Age, Categorical
>=65 years
6 Participants
n=5 Participants
Age, Continuous
65.7 years
STANDARD_DEVIATION 6.0 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
11 Participants
n=5 Participants
Region of Enrollment
United States
11 participants
n=5 Participants

PRIMARY outcome

Timeframe: 4 years

Population: Upon reviewing response data for the first 8 patients, we noted that there were no responses thus far. As per the two-stage optimal Simon's design, we would need 8 responses in 15 patients to proceed to stage 2 but we would not have crossed that threshold. The study was stopped due to lack of improved efficacy compared to historical controls.

We will use a two-stage optimal Simon's design with a 5% significance level and 80% power to detect an increase in response rate from 50% to 70%. The first stage will enroll 15 patients. If there are 8 or fewer responses among these 15 patients, we will consider the combination therapy to not be worthy of further study, and stop the trial. If we find 9 or more responses, we will proceed to the second stage, and accrual continues for a total of 43 patients. If we see 26 or fewer responses out of 43, then no further investigation of the drug is warranted. If we see 27 or more responses out of 43, then further investigation of the drug will be considered. The "expected" sample size of the trial is 23.5 with the null response rate of 50%.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 10 years

Population: Study was terminated prematurely and insufficient data was collected to assess this outcome measure.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 10 years

Population: Study was terminated prematurely and insufficient data was collected to assess this outcome measure.

Outcome measures

Outcome data not reported

Adverse Events

Docetaxel and Hydroxychloroquine

Serious events: 3 serious events
Other events: 8 other events
Deaths: 9 deaths

Serious adverse events

Serious adverse events
Measure
Docetaxel and Hydroxychloroquine
n=11 participants at risk
Drug: Docetaxel 75 mg/m2 intravenously every 21 days on Day 1 of the treatment cycle Drug: hydroxychloroquine 200 mg twice daily A cycle is defined as an interval of 21 days.
Blood and lymphatic system disorders
Hemorrhage, GU - Bladder
9.1%
1/11 • Number of events 1 • 3 years
Nervous system disorders
Neuropathy: sensory
9.1%
1/11 • Number of events 1 • 3 years
Infections and infestations
Infection
18.2%
2/11 • Number of events 2 • 3 years

Other adverse events

Other adverse events
Measure
Docetaxel and Hydroxychloroquine
n=11 participants at risk
Drug: Docetaxel 75 mg/m2 intravenously every 21 days on Day 1 of the treatment cycle Drug: hydroxychloroquine 200 mg twice daily A cycle is defined as an interval of 21 days.
General disorders
Fatigue (asthenia, lethargy, malaise)
36.4%
4/11 • Number of events 6 • 3 years
Skin and subcutaneous tissue disorders
Hair loss/alopecia (scalp or body)
27.3%
3/11 • Number of events 3 • 3 years
Skin and subcutaneous tissue disorders
Dermatology/Skin
9.1%
1/11 • Number of events 1 • 3 years
Skin and subcutaneous tissue disorders
Pruritus/itching
9.1%
1/11 • Number of events 1 • 3 years
Gastrointestinal disorders
Diarrhea
27.3%
3/11 • Number of events 5 • 3 years
Gastrointestinal disorders
Nausea
18.2%
2/11 • Number of events 3 • 3 years
Gastrointestinal disorders
Hemorrhoids
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Back
18.2%
2/11 • Number of events 3 • 3 years
General disorders
Pain - Joint
18.2%
2/11 • Number of events 2 • 3 years
General disorders
Pain - Abdomen NOS
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Chest wall
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Chest/thorax NOS
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Dental/teeth/peridontal
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Extremity-limb
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Head/headache
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain - Neck
9.1%
1/11 • Number of events 1 • 3 years
General disorders
Pain
9.1%
1/11 • Number of events 1 • 3 years
Blood and lymphatic system disorders
Neutrophils/granulocytes (ANC/AGC)
18.2%
2/11 • Number of events 7 • 3 years
Blood and lymphatic system disorders
Hemoglobin
9.1%
1/11 • Number of events 1 • 3 years
Nervous system disorders
Neuropathy: sensory
27.3%
3/11 • Number of events 4 • 3 years
Nervous system disorders
Dizziness
9.1%
1/11 • Number of events 1 • 3 years
Cardiac disorders
Cardiac General
9.1%
1/11 • Number of events 1 • 3 years
Cardiac disorders
Hypertension
9.1%
1/11 • Number of events 3 • 3 years
Endocrine disorders
Hot flashes/flushes
9.1%
1/11 • Number of events 1 • 3 years
Renal and urinary disorders
Hemorrhage, GU - Bladder
9.1%
1/11 • Number of events 1 • 3 years
Blood and lymphatic system disorders
Hemorrhage, GU - Urinary NOS
9.1%
1/11 • Number of events 1 • 3 years
Infections and infestations
Infection with unknown ANC - Skin (cellulitis)
9.1%
1/11 • Number of events 1 • 3 years
Blood and lymphatic system disorders
Edema: limb
9.1%
1/11 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Cough
9.1%
1/11 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Dyspnea (shortness of breath)
9.1%
1/11 • Number of events 1 • 3 years
Respiratory, thoracic and mediastinal disorders
Pulmonary/Upper Respiratory )
9.1%
1/11 • Number of events 1 • 3 years
Renal and urinary disorders
Urinary frequency/urgency
9.1%
1/11 • Number of events 1 • 3 years

Additional Information

Dr. Mark Stein

Cancer Institute of New Jersey

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place