Safinamide in Idiopathic Parkinson's Disease (IPD) With Motor Fluctuations, as add-on to Levodopa

NCT ID: NCT00627640

Last Updated: 2013-03-29

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

549 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-02-28

Study Completion Date

2012-03-31

Brief Summary

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Parkinson's Disease is a major neurodegenerative disorder in which there is a progressive loss of dopamine-containing neurons. The understanding that PD is a syndrome of dopamine (DA) deficiency led to the introduction in the clinical practice of L-dopa, a precursor of DA that crosses the blood brain barrier, and also to the use of selective inhibitors of MAO-B, the major DA metabolising enzyme in man.

Safinamide is an inhibitor of MAO-B. This is a phase III trial to evaluate the efficacy and safety of safinamide (50 and 100 mg p.o. q.a.m.) compared to placebo as add-on therapy to a stable dose to levodopa in subjects with advance idiopathic Parkinson's Disease.

The principal efficacy measure is the increase in mean daily "on" time during the 18-hr diary recording period.

Detailed Description

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Conditions

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Idiopathic Parkinson's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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1

1 active (50 - 100 mg/day)

Group Type EXPERIMENTAL

Safinimide 50-100 mg/day

Intervention Type DRUG

Safinamide, (S)-(+)-2-\[4-(3-fluorobenzyloxy) benzylamino\] propanamide methanesulfonate, is an a-aminoamide derivative

2

Group Type PLACEBO_COMPARATOR

Matching Placebo

Intervention Type DRUG

Matching Placebo

Interventions

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Safinimide 50-100 mg/day

Safinamide, (S)-(+)-2-\[4-(3-fluorobenzyloxy) benzylamino\] propanamide methanesulfonate, is an a-aminoamide derivative

Intervention Type DRUG

Matching Placebo

Matching Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Male and female between the ages of 30 to 80 years with diagnosis of idiopathic Parkinson's Disease of more than 5 years duration, with a Hoehn and Yahr stage of I-IV during an "off" phase.

Be levodopa-responsive and have been receiving treatment with a stable dose of levodopa for at least 4 weeks.

Have motor fluctuations, with \>1.5 hours "off" time during the day. Be able to maintain an accurate and complete diary (18-hour)

Exclusion Criteria

Patients with medical conditions and/or taking concomitant medications that would have put them at risk, interfered with the study evaluations, or made them unable to complete the requirements of the study;.

Be in a late stage of Parkinson's Disease, and experiencing severe, disabling peak-dose or biphasic dyskinesia and/or unpredictable or widely swinging fluctuations in their symptoms.

Current diagnosis of substance abuse or history of alcohol or drug abuse in the past 3 months.

Have received treatment with safinamide previously. History of, or current depression psychosis (e.g. schizophrenia or psychotic depression) Evidence of dementia or cognitive dysfunction. History of allergic response to anticonvulsants, levodopa, or other anti-Parkinsonian agents.

Hypersensitivity or contraindications to MAO-B inhibitors. Ophthalmologic history including any of the following conditions: albino subjects, family history of hereditary retinal disease, progressive and/or severe diminution of visual acuity (i.e., 20/70), retinitis pigmentosa, retinal pigmentation due to any cause, any active retinopathy or ocular inflammation (uveitis), or diabetic retinopathy.
Minimum Eligible Age

30 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Newron Pharmaceuticals SPA

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Algirdas Kakarieka, MD

Role: STUDY_DIRECTOR

Merck Serono S.A., Geneva

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Barrow Neurological Institute

Phoenix, Arizona, United States

Site Status

Mayo Clinic Scottsdale

Scottsdale, Arizona, United States

Site Status

San Francisco Clinical Research Center

San Francisco, California, United States

Site Status

Parkinson's Institute

Sunnyvale, California, United States

Site Status

Institute for Neurodegenerative Disorders

New Haven, Connecticut, United States

Site Status

Parkinson's Disease and Movement Disorder Center

Boca Raton, Florida, United States

Site Status

Neurologic Consultants P.A.

Fort Lauderdale, Florida, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

Parkinson's Disease Treatment Center of SW Florida

Port Charlotte, Florida, United States

Site Status

Neurology Clinical Research Inc.

Sunrise, Florida, United States

Site Status

University Of South Florida Medical Center

Tampa, Florida, United States

Site Status

Wesley Woods Geriatric Center

Atlanta, Georgia, United States

Site Status

Columbus Research Institute

Columbus, Georgia, United States

Site Status

Northwestern University PD and Movement Disorders Center

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

University of Maryland Medical Center

Baltimore, Maryland, United States

Site Status

Boston University School of Medicine

Boston, Massachusetts, United States

Site Status

Quest Research Institute

Bingham Farms, Michigan, United States

Site Status

Parkinson's Disease and Movement Disorder Center

Albany, New York, United States

Site Status

North Shore Medical Center

Manhasset, New York, United States

Site Status

Neurological Institute of New York

New York, New York, United States

Site Status

The Neurological Institute

Charlotte, North Carolina, United States

Site Status

Duke Movement Disorders Clinic

Durham, North Carolina, United States

Site Status

Pennsylvania Hospital

Philadelphia, Pennsylvania, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Concord Repatriation General Hospital

Concord, , Australia

Site Status

Central Coast Neuroscience Research

East Gosford, , Australia

Site Status

Univ.Klinik Graz

Graz, , Austria

Site Status

Univ.Klinik Innsbruck

Innsbruck, , Austria

Site Status

Cliniques Universitaires Saint-Luc

Brussels, , Belgium

Site Status

U.Z Antwerpen

Edegem, , Belgium

Site Status

Jessa Ziekenhuis - Campus Virga Jesse

Hasselt, , Belgium

Site Status

ZNA Hoge Beuken

Hoboken, , Belgium

Site Status

Heilig Hart Roeselare - Campus westlaan

Roeselare, , Belgium

Site Status

AZ Sint-Augustinus

Wilrijk, , Belgium

Site Status

Research Site

Halifax, Nova Scotia, Canada

Site Status

Parkinson's and Neurodegenerative Disorders Clinic

Ottawa, Ontario, Canada

Site Status

University Health Network -Toronto Western Hosp.

Toronto, Ontario, Canada

Site Status

Dynamic Clinical Research Group

Pointe-Claire, Quebec, Canada

Site Status

King David

Halifax, , Canada

Site Status

Kingston General Hospital

Kingston, , Canada

Site Status

Tartu University Hospital

Tartu, , Estonia

Site Status

CHU Hopital Gabriel Montpied

Clermont-Ferrand, , France

Site Status

CHU La Miletrie

Miletrie Poitiers, , France

Site Status

CHU Nantes Hôpital Laennec - CIC Neurologie

Nantes, , France

Site Status

CHU de Nimes, Hopital Caremeau

Nîmes, , France

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CIC-Hospital Purpan

Pavillon Riser Toulouse, , France

Site Status

Kliniken Beelitz GmbH

Beelitz-Heilstätten, , Germany

Site Status

Charité Campus Virchow Universitaetsmedizin Berlin

Berlin, , Germany

Site Status

Ehret Reinhard

Berlin, , Germany

Site Status

St. Joseph-Krankenhaus Berlin-Weißensee

Berlin, , Germany

Site Status

Universitaetsklinikum Goettingen

Göttingen, , Germany

Site Status

Arzneimittelforschung Leipzig GmbH

Leipzig, , Germany

Site Status

Philipps-Universitaet Marburg

Marburg, , Germany

Site Status

Praxis Dipl med Bodenschatz

Mittweida, , Germany

Site Status

Neurologisches Krankenhaus Muenchen

München, , Germany

Site Status

Eberhard-Karls-Universität

Tübingen, , Germany

Site Status

Universitätsklinikum

Ulm, , Germany

Site Status

Deutsche Klinik fuer Diagnostik

Wiesbaden, , Germany

Site Status

Clinexpert Kereskedelmi es Szolgaltato Kft.

Budapest, , Hungary

Site Status

Fov.Onk.Peterfy S.Utcai Korh.-Rend.Int es Baleseti Kozp.

Budapest, , Hungary

Site Status

Fővárosi Önkormányzat Nyírő Gyula Kórhaz Neurologiai Osztály

Budapest, , Hungary

Site Status

Nyiro Gyula Korhaz

Budapest, , Hungary

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

SOTE Neurlogia

Budapest, , Hungary

Site Status

Debreceni Egyetem Orvos- es Egeszsegtudomanyi Centrum

Debrecen, , Hungary

Site Status

Borsod-Abauj-Zemplen Megyei Korhaz es Egyetemi Oktato Korhaz

Miskolc, , Hungary

Site Status

DE OEC Neurologiai Klinika

Móricz, , Hungary

Site Status

Peterfy S. Utcai Korhaz

Peterfy Sandor, , Hungary

Site Status

Sopron Medical Egeszsegugyi Szolgaltato Kft.

Sopron, , Hungary

Site Status

BAZ Country Hospital and Outpatient Clinic Dept. of Neurology Toxicology and Stroke

Szentpetri, , Hungary

Site Status

Nizam's Institute of Medical Sciences

Hyderabad, Andh Prad, India

Site Status

King George Hospital

Visakhapatnam, Andh Prad, India

Site Status

M. S. Ramaiah Medical College and Hospital

Bangalore, Karna, India

Site Status

All India Institute of Medical Sciences (AIIMS)

New Delhi, National Capital Territory of Delhi, India

Site Status

Mallikatta Neuro and Research Centre

Mangalore, , India

Site Status

BYL Nair Hospital ¬ TN Medical College

Mumbai Mahara, , India

Site Status

Brain & Mind Institute

Nagpur, , India

Site Status

Christian Medical College Hospital

Vellore, , India

Site Status

Barzilai Medical Center

Ashkelon, , Israel

Site Status

Rambam Health Care Campus

Haifa, , Israel

Site Status

Rabin Medical Center

Petah Tikva, , Israel

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Sheba Medical Center

Ramat Gan, , Israel

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Sieff Government Hospital

Safed, , Israel

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Sourasky Medical Center

Tel Aviv, , Israel

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Hospital Pulau Pinang

George Town, , Malaysia

Site Status

University of Malaya Medical Center

Kuala Lumpur, , Malaysia

Site Status

Jeroen Bosch Ziekenhuis

's-Hertogenbosch, , Netherlands

Site Status

Auckland City Hospital

Aucklan, , New Zealand

Site Status

Van der Veer Institute for Parkinson's & Brain Research

Christchurch, , New Zealand

Site Status

Waikato Hospital

Hamilton, , New Zealand

Site Status

MU Dr.Beata Dupejová neurologicka ambulancia s.r.o

Banská Bystrica, , Slovakia

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Poliklinika Tehelna

Bratislava, , Slovakia

Site Status

Vseobecna nemocnica s poliklinikou Levoca

Levoča, , Slovakia

Site Status

Fakultna nemocnica Trnava Interna klinika

Slovak Republic, , Slovakia

Site Status

Nestatne zdravotnicke zariadenie Neurologicka ambulancia

Slovak Republic, , Slovakia

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Asan Medical Center

Seoul, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Severance Hospital, Yonsei University College of Medicine

Seoul, , South Korea

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Policlinica Guipuzcoa

Donostia / San Sebastian, , Spain

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Fundacion Hospital de Alcorcon

Madrid, , Spain

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Fundacion Jimenez Diaz

Madrid, , Spain

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HU Carlos Haya

Málaga, , Spain

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Inselspital Bern

Bern, , Switzerland

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Hopitaux Universitaires de Geneve - Hug

Geneva, , Switzerland

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Chang-Hua Christian Hospital

Chang-hua, , Taiwan

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Kaohsiung Veterans General Hospital

Kaohsiung City, , Taiwan

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Shin Kong Wu Ho-Su Memorial Hospital

Taipei, , Taiwan

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King Chulalongkorn Memorial Hospital

Bangkok, , Thailand

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Phramongkutklao Hospital

Bangkok, , Thailand

Site Status

Rajavithi Hospital

Bangkok, , Thailand

Site Status

Lampang Hospital

Lampang, , Thailand

Site Status

Sappasithiprasong Hospital

Ubonratchathani, , Thailand

Site Status

Fylde Coast Hospital

Blackpool, , United Kingdom

Site Status

Addenbrookes NHS Trust

Cambridge, , United Kingdom

Site Status

Southern General Hospital

Glasgow, , United Kingdom

Site Status

Royal Free Hospital

London, , United Kingdom

Site Status

Clinical Ageing Research Unit

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Canada Estonia France Germany Hungary India Israel Malaysia Netherlands New Zealand Slovakia South Korea Spain Switzerland Taiwan Thailand United Kingdom

References

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Cattaneo C, Kulisevsky J. The Effects of Safinamide in Chinese and Non-Chinese Patients with Parkinson's Disease. Adv Ther. 2024 Feb;41(2):638-648. doi: 10.1007/s12325-023-02736-2. Epub 2023 Dec 9.

Reference Type DERIVED
PMID: 38070039 (View on PubMed)

Schapira AH, Fox SH, Hauser RA, Jankovic J, Jost WH, Kenney C, Kulisevsky J, Pahwa R, Poewe W, Anand R. Assessment of Safety and Efficacy of Safinamide as a Levodopa Adjunct in Patients With Parkinson Disease and Motor Fluctuations: A Randomized Clinical Trial. JAMA Neurol. 2017 Feb 1;74(2):216-224. doi: 10.1001/jamaneurol.2016.4467.

Reference Type DERIVED
PMID: 27942720 (View on PubMed)

Other Identifiers

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IND: 63,901

Identifier Type: -

Identifier Source: secondary_id

EudraCT Number: 2007-002964-90

Identifier Type: -

Identifier Source: secondary_id

27919

Identifier Type: -

Identifier Source: org_study_id

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