Compare Bosutinib To Imatinib In Subjects With Newly Diagnosed Chronic Phase Philadelphia Chromosome Positive CML

NCT ID: NCT00574873

Last Updated: 2019-01-08

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

502 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-02-05

Study Completion Date

2015-05-27

Brief Summary

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Two-arm, randomized, open-label trial designed to evaluate the efficacy and safety of bosutinib alone compared to imatinib alone in subjects newly diagnosed with chronic phase Chronic Myelogenous Leukemia (CML). The primary endpoint is cytogenetic response rate at one year.

Detailed Description

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Conditions

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Chronic Myeloid Leukemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

Bosutinib

Group Type EXPERIMENTAL

Bosutinib

Intervention Type DRUG

500 mg once daily, by mouth (tablet) with food preferably in the morning. Drug can be increased up to 600mg daily in case of lack of efficacy, and can be reduced to 300mg daily in case of toxicity. The drug will be given daily for up to 8 years until treatment failure, unacceptable toxicity, death or withdrawal of consent.

2

Imatinib

Group Type ACTIVE_COMPARATOR

imatinib

Intervention Type DRUG

400 mg once daily, by mouth (tablet). Drug can be increased up to 600mg daily in case of lack of efficacy, and can be reduced to 300mg daily in case of toxicity. The drug will be given daily for up to 8 years until treatment failure, unacceptable toxicity, death or withdrawal of consent.

Interventions

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Bosutinib

500 mg once daily, by mouth (tablet) with food preferably in the morning. Drug can be increased up to 600mg daily in case of lack of efficacy, and can be reduced to 300mg daily in case of toxicity. The drug will be given daily for up to 8 years until treatment failure, unacceptable toxicity, death or withdrawal of consent.

Intervention Type DRUG

imatinib

400 mg once daily, by mouth (tablet). Drug can be increased up to 600mg daily in case of lack of efficacy, and can be reduced to 300mg daily in case of toxicity. The drug will be given daily for up to 8 years until treatment failure, unacceptable toxicity, death or withdrawal of consent.

Intervention Type DRUG

Other Intervention Names

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SKI 606 Gleevec

Eligibility Criteria

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Inclusion Criteria

* Cytogenetic diagnosis of chronic phase Ph+ CML diagnosed less than 6 months.
* Diagnosis of CML chronic phase confirmed.
* Adequate hepatic and renal function.
* Able to take oral tablets.

Exclusion Criteria

* Exclusions include Philadelphia negative CML.
* Prior anti-leukemia treatment.
* Prior stem cell transplant.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Wyeth is now a wholly owned subsidiary of Pfizer

INDUSTRY

Sponsor Role collaborator

Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Pacific Cancer Medical Center Inc

Anaheim, California, United States

Site Status

Tower Cancer Research Foundation (TCRF)

Beverly Hills, California, United States

Site Status

Robert A Moss, MD, FACP, Inc

Fountain Valley, California, United States

Site Status

UCSD Medical Center-Thornton

La Jolla, California, United States

Site Status

UCSD Moores Cancer Center

La Jolla, California, United States

Site Status

UCSD Medical Center-Hillcrest

San Diego, California, United States

Site Status

Stanford Hospital and Clinics Investigational Drug Services

Stanford, California, United States

Site Status

Stanford Hospitals and Clinics

Stanford, California, United States

Site Status

Stanford University Medical Center

Stanford, California, United States

Site Status

Cancer Care Centers of Florida

Hudson, Florida, United States

Site Status

Cancer Care Centers of Florida

New Port Richey, Florida, United States

Site Status

Pasco Pinellas Cancer Center

New Port Richey, Florida, United States

Site Status

Orlando Health, Inc.

Orlando, Florida, United States

Site Status

Pasco Pinellas Cancer Center

Tarpon Springs, Florida, United States

Site Status

Northside Hospital, Inc. - GCS/Annex

Atlanta, Georgia, United States

Site Status

Indiana Blood and Marrow Transplantation Research Franciscan St. Francis Health Center Inc.

Indianapolis, Indiana, United States

Site Status

Indiana Blood and Marrow Transplantation Research

Indianapolis, Indiana, United States

Site Status

Siouxland Hematology-Oncology Associates, LLP

Sioux City, Iowa, United States

Site Status

Cancer Center of Kansas

Salinas, Kansas, United States

Site Status

Cancer Center of Kansas

Wichita, Kansas, United States

Site Status

Kentucky Cancer Clinic

Hazard, Kentucky, United States

Site Status

Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

Site Status

Josephine Ford Cancer - Downriver

Brownstown, Michigan, United States

Site Status

Henry Ford Medical Center- Fairlane

Dearborn, Michigan, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Henry Ford Hospital - West Bloomfield

Detroit, Michigan, United States

Site Status

Regional Cancer Care Associates

Cherry Hill, New Jersey, United States

Site Status

Study Supplies: Regional Cancer Care Associates

Cherry Hill, New Jersey, United States

Site Status

Somerset Hematology Oncology Associates

Somerville, New Jersey, United States

Site Status

San Juan Oncology Associates

Farmington, New Mexico, United States

Site Status

Associates In Oncology and Hematology

Chattanooga, Tennessee, United States

Site Status

The University of Texas M.D. Anderson Cancer Center

Houston, Texas, United States

Site Status

Hospital Italiano de la Plata

La Plata, Buenos Aires, Argentina

Site Status

Hospital Privado de Cordoba

Córdoba, Prov. de Cordoba, Argentina

Site Status

Centro de Investigaciones Oncologicas

Bahía Blanca, Provincia Buenos Aires, Argentina

Site Status

Instituto Medico Especializado Alexander Fleming

Buenos Aires, , Argentina

Site Status

Cliniques Universitaires Saint Luc

Brussels, , Belgium

Site Status

C.H.R.ST. - R. Fabiola (N-D)

Charleroi, , Belgium

Site Status

University Hospital Gent - Department of Hematology

Ghent, , Belgium

Site Status

Centre Hospitalier de Jolimont - Lobbes

La Louvière, , Belgium

Site Status

CHU de Charleroi - Hopital civil Marie Curie

Lodelinsart, , Belgium

Site Status

H.-Hartziekenhuis Roeselare-Menen

Roeselare, , Belgium

Site Status

Centro De Hematologia E Hemoterapia Da Unicamp

Campinas/ SP, , Brazil

Site Status

Vancouver General Hospital

Vancouver, British Columbia, Canada

Site Status

University Health Network, Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

Hopital Maisonneuve Rosemont

Montreal, Quebec, Canada

Site Status

Instituto Oncologico del Sur

Temuco, , Chile

Site Status

Instituto Oncologico

Viña del Mar, , Chile

Site Status

Ruiging Hospital Affiliated to Shanghai Jiaotong University School of Medicine

Shanghai, P.R. China, China

Site Status

Peking Union Medical College Hospital of Chinese Academy of Medical Sciences

Beijing, , China

Site Status

The Chinese PLA General Hospital

Beijing, , China

Site Status

The Hematology Hospital of Chinese Academy of Medical Science

Tianjin, , China

Site Status

Fundacion Santa Fe de Bogota

Bogota, Cundinamarca, Colombia

Site Status

Fundacion Cardiovascular de Colombia

Floridablanca, Santander Department, Colombia

Site Status

CIOSAD Centro de Investigaciones Oncologicas

Bogotá, , Colombia

Site Status

Institut Bergonie

Bordeaux, , France

Site Status

CHU Caen - Cote de Nacre

Caen, , France

Site Status

Centre Hospitalier de Versailles Hopital Andre Mignot

Le Chesnay, , France

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Hopital EDOUARD HERRIOT

Lyon, , France

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Hopital HOTEL DIEU

Nantes, , France

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Hospital Archet 1

Nice, , France

Site Status

Centre d'Investigation Clinique- CIC INSERM802

Poitiers, , France

Site Status

CHU de Poitiers

Poitiers, , France

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Clinique Sainte Anne

Strasbourg, , France

Site Status

Hopitaux Universitaires de Strasbourg - Hopital Civil

Strasbourg, , France

Site Status

Charite University Medical Center - Campus Virchow Klinikum

Berlin, , Germany

Site Status

Universitätsklinikum Carl Gustav Carus

Dresden, , Germany

Site Status

Univeristatsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Universitaetsklinikum Leipzig Zentrum fur Innere Medizin

Leipzig, , Germany

Site Status

III. Medizinische Klinik, Universitaetsklinikum Mannheim gGmbH

Mannheim, , Germany

Site Status

III. Medizinischen Klinik und Poliklinik des Klinikums Rechts der Isar der TU-MUNCHEN

München, , Germany

Site Status

Prince Of Wales Hospital

Shatin N.T., HONG KONG, Hong Kong

Site Status

Egyesitett Szent Istvan es Szent Laszlo Korhaz-Rendelointezet

Budapest, , Hungary

Site Status

Petz Aladar Megyei Oktato Korhaz

Győr, , Hungary

Site Status

Kaposi Mor Oktato Korhaz, Belgyogyaszati Osztaly

Kaposvár, , Hungary

Site Status

Josa Andras Hospital

Nyíregyháza, , Hungary

Site Status

Tata Memorial Center, Tata Memorial Hospital

Mumbai, Maharashtra, India

Site Status

Advanced Centre for Treatment, Research and Education in Cancer

Mumbai, Maharashtra, India

Site Status

Jehangir Clinical Development Centre,

Pune, Maharashtra, India

Site Status

Birla Cancer Centre

Jaipur, Rajasthan, India

Site Status

SEAROC Cancer Center, Soni Manipal Hospital

Jaipur, Rajasthan, India

Site Status

Azienda Ospedaliera San Gerardo

Monza, Lombardy, Italy

Site Status

Azienda Ospedaliera Universitaria San Luigi Gonzaga

Orbassano, Torino, Italy

Site Status

Ospedale Ferrarotto - Divisione di Ematologia

Catania, , Italy

Site Status

Dipartimento Di Ematologia Ospedale Santo Eugenio

Roma, , Italy

Site Status

Toyohashi Municipal Hospital

Toyohashi, Aichi-ken, Japan

Site Status

Akita University Hospital

Akita, Akita, Japan

Site Status

National Hospital Organization Kyushu Cancer Center

Fukuoka, Fukuoka, Japan

Site Status

Kanazawa University Hospital

Kanazawa, Ishikawa-ken, Japan

Site Status

Tohoku Univesity Hospital

Sendai, Miyagi, Japan

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Kinki University School Of Medicine

Sayama, Osaka, Japan

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Jikei University Hospital Daisan

Komae-shi, Tokyo, Japan

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Japanese Red Cross Nagoya First Hospital

Aichi, , Japan

Site Status

Aichi Cancer Center Hospital

Aichi, , Japan

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Chiba University Hospital

Chiba, , Japan

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Tokai University Hospital

Kanagawa, , Japan

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Nagasaki University Hospital

Nagasaki, , Japan

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Niigata University Medical and Dental Hospital

Niigata, , Japan

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Osaka University Hospital

Osaka, , Japan

Site Status

Hamamatsu Medical University Hospital Faculty of Medicine

Shizuoka, , Japan

Site Status

Tokyo Metropolitan Cancer & Infectious Disease Centre Komagome Hp

Tokyo, , Japan

Site Status

Riga Centre Of Haematology

Riga, , Latvia

Site Status

Hematology, Oncology & Transfusion Medicine Center

Vilnius, , Lithuania

Site Status

Centro Medico de las Americas

Mérida, , Mexico

Site Status

Uniwersyteckie Centrum Kliniczne

Gdansk, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny Im. A. Mieleckiego Slaskiego Uniwersytetu Medycznego

Katowice, , Poland

Site Status

SP ZOZ Szpital Uniwersytecki w Krakowie

Krakow, , Poland

Site Status

Wojewodzki Szpital Specjalistyczny im. M. Kopernika

Lodz, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny nr 1 w Lublinie

Lublin, , Poland

Site Status

GUZ Komi Republican Oncology Center

Syktyvkar, Komi, Russia

Site Status

Regional State Budgetary Healthcare Institution "Barnaul City Hospital #8"

Barnaul, , Russia

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Kirov Research Institute of Hematology and Blood Transfusion of

Kirov, , Russia

Site Status

Federal State Budget Institution Hematology Scientific Center of Minzdravsotsrazvitiya of Russia

Moscow, , Russia

Site Status

State Novosibirsk Regional Clinical Hospital

Novosibirsk, , Russia

Site Status

Perm Territory State Budgetary Healthcare Inst

Perm, , Russia

Site Status

Republican Hospital na Baranov

Petrozavodsk, , Russia

Site Status

Rostov Regional Clinical Hospital

Rostov-on-Don, , Russia

Site Status

Rostov State Medical University of the Minzdravsotsrazvitiya of Russia

Rostov-on-Don, , Russia

Site Status

Leningrad Regional Clinical Hospital

Saint Petersburg, , Russia

Site Status

St-Petersburg Pavlov's State Medical University

Saint Petersburg, , Russia

Site Status

St-Petersburg State Medical University

Saint Petersburg, , Russia

Site Status

Samara Regional Clinical Hospital M.I. Kalinin

Samara, , Russia

Site Status

Yaroslavl Region State Budgetary Healthcare Institution Regional Clinical Hospital

Yaroslavl, , Russia

Site Status

Sverdlovsk Regional Clinical Hospital #1

Yekaterinburg, , Russia

Site Status

Central City Hospital #7

Yekaterinburg, , Russia

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Singapore General Hospital

Singapore, , Singapore

Site Status

University Witwatersrand and Oncology

Johannesburg, , South Africa

Site Status

Johannesburg Hospital, Department of Medical Oncology

Parktown, , South Africa

Site Status

Clinical Haematology Unit - Department of Medicine

Soweto, , South Africa

Site Status

Department of Cardiology, Chris Hani Baragwanath Hospital

Soweto, , South Africa

Site Status

Department of Radiology, Chris Hani Baragwanath Hospital

Soweto, , South Africa

Site Status

The Catholic University of Korea, Seoul St. Mary's Hospital/Division of Hematology

Seoul, , South Korea

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Hospital Universitari Clinic de Barcelona

Barcelona, , Spain

Site Status

Hospital De La Princesa

Madrid, , Spain

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Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital de Madrid Norte-Sanchinarro Centro Integral Oncologico

Madrid, , Spain

Site Status

Complejo Hospitalario de Toledo- Servicio de Hematologia.

Toledo, , Spain

Site Status

Hospital Clinico Universitario de Valencia (CHUV)

Valencia, , Spain

Site Status

Changhua Christian Hospital

Changhua, , Taiwan

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National Taiwan University Hospital

Taipei TOC, , Taiwan

Site Status

Division of Hematology, Department of Medicine

Bangkoknoi, Bangkok, Thailand

Site Status

Hacettepe Universitesi Tip Fakultesi

Ankara, Sihhiye, Turkey (Türkiye)

Site Status

Ankara Universitesi Tip Fakultesi Cebeci Hastanesi

Ankara, , Turkey (Türkiye)

Site Status

Gaziantep Universitesi Tip Fakultesi

Gaziantep, , Turkey (Türkiye)

Site Status

Cherkaskiy oblasniy onkologichniy dispanser

Cherkassy, , Ukraine

Site Status

Clinical Assocation of Emergency Care

Dnipropetrovsk, , Ukraine

Site Status

Clinical Diagnostic Laboratory of Komunalnyj Zaklad

Dnipropetrovsk, , Ukraine

Site Status

Komunalnyj Zaklad "Dnipropetrovska Miska Bagatoprofilna Klinichna Likarnja #4"

Dnipropetrovsk, , Ukraine

Site Status

Instytut Nevidkladnoi ta Vidnovnoi Hirurgii im. P.K. Husaka NAMN Ukrainy, Viddilennja Hematologii

Donetsk, , Ukraine

Site Status

Oleksandrovska clinical hospital cardiological rehabilitation department

Kiev, , Ukraine

Site Status

Institut Klinichnoi Radiologii DU "Natsionalnyj Naukovyj Centr Radiacijnoi Medicini NAMN Ukraini"

Kyiv, , Ukraine

Site Status

Institut Klinichnoi Radiologii Naukovogo Centru Radiacijnoi Medicini NAMN Ukraini

Kyiv, , Ukraine

Site Status

Institut Klinichnoi Radiologii Naukovogo

Kyiv, , Ukraine

Site Status

Miska klinichna likarnja # 9

Kyiv, , Ukraine

Site Status

Ultrasaund Educational and Diagnostic Center

Lviv, , Ukraine

Site Status

Instutut Patologii Krovi to Transfuziynoi Medicinu AMN Ukraini

Lviv, , Ukraine

Site Status

Polyclinic of 5th Municipal Hospital

Lviv, , Ukraine

Site Status

3rd Floor Centre for Clinical Haematology

Nottingham, EAST Midlands, United Kingdom

Site Status

The Park Hospital

Nottingham, EAST Midlands, United Kingdom

Site Status

Hammersmith Hospital Clinical Trial Units

Hammersmith, London, United Kingdom

Site Status

Good Hope Hospital

Birmingham, WEST Midlands, United Kingdom

Site Status

Birmingham Heartlands Hospital

Birmingham, WEST Midlands, United Kingdom

Site Status

Department of Haematology - Level 3, Bexley Wing

Leeds, WEST Yorkshire, United Kingdom

Site Status

Department of Haematology

London, , United Kingdom

Site Status

Hammersmith Hospital

London, , United Kingdom

Site Status

Countries

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United States Argentina Belgium Brazil Canada Chile China Colombia France Germany Hong Kong Hungary India Italy Japan Latvia Lithuania Mexico Poland Russia Singapore South Africa South Korea Spain Taiwan Thailand Turkey (Türkiye) Ukraine United Kingdom

References

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Garrett M, Knight B, Cortes JE, Deininger MW. Population modeling of bosutinib exposure-response in patients with newly diagnosed chronic phase chronic myeloid leukemia. Cancer Med. 2023 Sep;12(17):17981-17992. doi: 10.1002/cam4.6439. Epub 2023 Aug 8.

Reference Type DERIVED
PMID: 37553873 (View on PubMed)

Takahashi N, Cortes JE, Sakaida E, Ishizawa K, Ono T, Doki N, Matsumura I, Garcia-Gutierrez V, Rosti G, Ono C, Ohkura M, Tanetsugu Y, Viqueira A, Brummendorf TH. Safety profile of bosutinib in Japanese versus non-Japanese patients with chronic myeloid leukemia: a pooled analysis. Int J Hematol. 2022 Jun;115(6):838-851. doi: 10.1007/s12185-022-03314-y. Epub 2022 Mar 2.

Reference Type DERIVED
PMID: 35235189 (View on PubMed)

Gambacorti-Passerini C, Cortes JE, Lipton JH, Dmoszynska A, Wong RS, Rossiev V, Pavlov D, Gogat Marchant K, Duvillie L, Khattry N, Kantarjian HM, Brummendorf TH. Safety of bosutinib versus imatinib in the phase 3 BELA trial in newly diagnosed chronic phase chronic myeloid leukemia. Am J Hematol. 2014 Oct;89(10):947-53. doi: 10.1002/ajh.23788. Epub 2014 Jul 21.

Reference Type DERIVED
PMID: 24944159 (View on PubMed)

Hsyu PH, Mould DR, Abbas R, Amantea M. Population pharmacokinetic and pharmacodynamic analysis of bosutinib. Drug Metab Pharmacokinet. 2014;29(6):441-8. doi: 10.2133/dmpk.DMPK-13-RG-126. Epub 2014 Jun 10.

Reference Type DERIVED
PMID: 24919837 (View on PubMed)

Trask PC, Cella D, Powell C, Reisman A, Whiteley J, Kelly V. Health-related quality of life in chronic myeloid leukemia. Leuk Res. 2013 Jan;37(1):9-13. doi: 10.1016/j.leukres.2012.09.013. Epub 2012 Oct 29.

Reference Type DERIVED
PMID: 23116602 (View on PubMed)

Cortes JE, Kim DW, Kantarjian HM, Brummendorf TH, Dyagil I, Griskevicius L, Malhotra H, Powell C, Gogat K, Countouriotis AM, Gambacorti-Passerini C. Bosutinib versus imatinib in newly diagnosed chronic-phase chronic myeloid leukemia: results from the BELA trial. J Clin Oncol. 2012 Oct 1;30(28):3486-92. doi: 10.1200/JCO.2011.38.7522. Epub 2012 Sep 4.

Reference Type DERIVED
PMID: 22949154 (View on PubMed)

O'Hare T, Zabriskie MS, Eiring AM, Deininger MW. Pushing the limits of targeted therapy in chronic myeloid leukaemia. Nat Rev Cancer. 2012 Jul 24;12(8):513-26. doi: 10.1038/nrc3317.

Reference Type DERIVED
PMID: 22825216 (View on PubMed)

Related Links

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Other Identifiers

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B1871008

Identifier Type: OTHER

Identifier Source: secondary_id

2007-003780-50

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

3160A4-3000

Identifier Type: -

Identifier Source: org_study_id

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