Safety And Efficacy Study Of Bosutinib In Patients With Philadelphia Chromosome Positive Chronic Myeloid Leukemia Previously Treated With One Or More Tyrosine Kinase Inhibitors

NCT ID: NCT02228382

Last Updated: 2021-12-30

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE4

Total Enrollment

163 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-11-07

Study Completion Date

2020-10-13

Brief Summary

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The purpose of this study is to fulfill the post-authorization commitment made by Pfizer to the European Medicines Agency in providing additional safety and efficacy data in approximately 150 Philadelphia Chromosome Positive Chronic Myeloid Leukemia patients with high unmet medical need, including 75 Chronic Phase, Accelerated Phase or Blast Phase patients in the fourth or later line treatment setting (i.e., after treatment with at least 3 other Tyrosine Kinase Inhibitors).

Detailed Description

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Conditions

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Previously Treated PH + CML

Keywords

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Bosutinib Chronic Myeloid Leukemia CML Leukemia Myelogenous Chronic BC-ABL Positive

Study Design

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Allocation Method

NA

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Bosutinib

Group Type EXPERIMENTAL

Bosutinib

Intervention Type DRUG

100 mg and 500 mg tablets, once daily dosage up to 4 years duration

Interventions

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Bosutinib

100 mg and 500 mg tablets, once daily dosage up to 4 years duration

Intervention Type DRUG

Other Intervention Names

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BOSULIF

Eligibility Criteria

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Inclusion Criteria

* Confirmed Philadelphia Chromosome positive Chronic Myeloid Leukemia or Confirmed BCR-ABL1 (Abelson-break point cluster) Positive if Philadelphia Chromosome negative Chronic Myeloid Leukemia (from initial diagnosis).
* Prior treatment with 1 or more tyrosine kinase inhibitor drugs (imatinib, dasatinib and/or nilotinib) for Philadelphia Chromosome positive Chronic Myeloid Leukemia (CML).
* Any Chronic Myeloid Leukemia disease phase, as long as the patient is unable to receive treatment with imatinib, dasatinib and/or nilotinib for any reason.

Exclusion Criteria

* Participation in any other clinical studies involving investigational drug(s) within 14 days or within 3 half-lives of drug levels in blood (whichever is longer) prior to the first dose of bosutinib.
* Prior treatment with bosutinib.
* Prior treatment with ponatinib.
* Known T315I or V299L mutation.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Developmental Therapeutics Consortium

OTHER

Sponsor Role collaborator

Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Keck Hospital of USC

Los Angeles, California, United States

Site Status

LAC+USC Medical Center

Los Angeles, California, United States

Site Status

USC/Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Sylvester Deerfield Beach

Deerfield Beach, Florida, United States

Site Status

University of Miami Hospital & Clinics

Miami, Florida, United States

Site Status

Indiana Blood and Marrow Transplantation-Clinic

Indianapolis, Indiana, United States

Site Status

Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

Baltimore, Maryland, United States

Site Status

Siteman Cancer Center - West County

Creve Coeur, Missouri, United States

Site Status

Barnes-Jewish Hospital

St Louis, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Siteman Cancer Center - South County

St Louis, Missouri, United States

Site Status

Weill Cornell Medical College - New York-Presbyterian Hospital

New York, New York, United States

Site Status

Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

Medizinische Universitaet Innsbruck

Innsbruck, , Austria

Site Status

Ordensklinikum Linz Gmbh Barmherzige Schwestern

Linz, , Austria

Site Status

Institut Bergonie

Bordeaux, , France

Site Status

Centre Hospitalier de Versailles (CHV)-Hopital Andre Mignot Service d'Hematologie Clinique- Oncology

Le Chesnay, , France

Site Status

Centre Regional De Lutte Contre Le Cancer

Marseille, , France

Site Status

Hopital Archet I

Nice, , France

Site Status

Institut Universitaire du Cancer Toulouse - Oncopole

Toulouse, , France

Site Status

CHU Brabois

Vandœuvre-lès-Nancy, , France

Site Status

RWTH Uniklinik Aachen Klinik fur Onkologie, Hamatologie und Stammzelltransplantation

Aachen, , Germany

Site Status

Charite - Universitaetsmedizin Berlin - Campus Virchow-Klinikum (CVK)

Berlin, , Germany

Site Status

Universitaetsklinikum Koeln (AoeR)

Cologne, , Germany

Site Status

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Klinik fur Innere Medizin II

Jena, , Germany

Site Status

III. Medizinische Klinik Universitaetsmedizin Mannheim

Mannheim, , Germany

Site Status

AOU Policlinico Consorziale di Bari - UO Ematologia con Trapianto

Bari, BA, Italy

Site Status

A.O.U. Policlinico S. Orsola-Malpighi

Bologna, BO, Italy

Site Status

Azienda Socio Sanitaria Territoriale - ASST Monza

Monza, MB, Italy

Site Status

Ospedale S. Eugenio - UOC Ematologia

Rome, RM, Italy

Site Status

AOU San Luigi Gonzaga SCDU Medicina Interna II ad indirizzo Ematologico

Orbassano, TO, Italy

Site Status

AOU Policlinico Vittorio Emanuele-P.O.G. Rodolico

Catania, , Italy

Site Status

SOD Ematologia

Florence, , Italy

Site Status

A.O. Ospedale Niguarda Ca Granda - SC Ematologia

Milan, , Italy

Site Status

Haukeland Universitetssjukehus

Bergen, , Norway

Site Status

St Olav Hospital

Trondheim, , Norway

Site Status

Hospital Universitario Quiron Madrid

Pozuelo de Alarcón, Madrid, Spain

Site Status

Hospital Universitari Vall d' Hebron

Barcelona, , Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Clinic De Barcelona

Barcelona, , Spain

Site Status

Hospital Universitario de La Princesa

Madrid, , Spain

Site Status

Hospital Universitario Ramon y Cajal

Madrid, , Spain

Site Status

Hospital Clinico Universitario de Salamanca

Salamanca, , Spain

Site Status

Hospital Universitari i Politecnic La Fe de Valencia

Valencia, , Spain

Site Status

Hospital de dia Quiron Zaragoza

Zaragoza, , Spain

Site Status

Hematologiskt centrum

Stockholm, , Sweden

Site Status

Akademiska Sjukhuset

Uppsala, , Sweden

Site Status

Countries

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Belgium Finland Netherlands United States Austria France Germany Italy Norway Spain Sweden

References

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Gambacorti-Passerini C, Brummendorf TH, Abruzzese E, Kelly KR, Oehler VG, Garcia-Gutierrez V, Hjorth-Hansen H, Ernst T, Leip E, Purcell S, Luscan G, Viqueira A, Giles FJ, Hochhaus A. Efficacy and safety of bosutinib in previously treated patients with chronic myeloid leukemia: final results from the BYOND trial. Leukemia. 2024 Oct;38(10):2162-2170. doi: 10.1038/s41375-024-02372-x. Epub 2024 Aug 20.

Reference Type DERIVED
PMID: 39164407 (View on PubMed)

Smith BD, Brummendorf TH, Roboz GJ, Gambacorti-Passerini C, Charbonnier A, Viqueira A, Leip E, Purcell S, Goldman EH, Giles F, Ernst T, Hochhaus A, Rosti G. Efficacy and safety of bosutinib in patients treated with prior imatinib and/or dasatinib and/or nilotinib: Subgroup analyses from the phase 4 BYOND study. Leuk Res. 2024 Apr;139:107481. doi: 10.1016/j.leukres.2024.107481. Epub 2024 Mar 11.

Reference Type DERIVED
PMID: 38484432 (View on PubMed)

Rosti G, Brummendorf TH, Gjertsen BT, Giraldo-Castellano P, Castagnetti F, Gambacorti-Passerini C, Ernst T, Zhao H, Kuttschreuter L, Purcell S, Giles FJ, Hochhaus A. Impact of age and comorbidities on the efficacy and tolerability of bosutinib in previously treated patients with chronic myeloid leukemia: results from the phase 4 BYOND study. Leukemia. 2024 Jan;38(1):126-135. doi: 10.1038/s41375-023-02080-y. Epub 2023 Nov 25.

Reference Type DERIVED
PMID: 38007586 (View on PubMed)

Takahashi N, Cortes JE, Sakaida E, Ishizawa K, Ono T, Doki N, Matsumura I, Garcia-Gutierrez V, Rosti G, Ono C, Ohkura M, Tanetsugu Y, Viqueira A, Brummendorf TH. Safety profile of bosutinib in Japanese versus non-Japanese patients with chronic myeloid leukemia: a pooled analysis. Int J Hematol. 2022 Jun;115(6):838-851. doi: 10.1007/s12185-022-03314-y. Epub 2022 Mar 2.

Reference Type DERIVED
PMID: 35235189 (View on PubMed)

Hochhaus A, Gambacorti-Passerini C, Abboud C, Gjertsen BT, Brummendorf TH, Smith BD, Ernst T, Giraldo-Castellano P, Olsson-Stromberg U, Saussele S, Bardy-Bouxin N, Viqueira A, Leip E, Russell-Smith TA, Leone J, Rosti G, Watts J, Giles FJ; BYOND Study Investigators. Bosutinib for pretreated patients with chronic phase chronic myeloid leukemia: primary results of the phase 4 BYOND study. Leukemia. 2020 Aug;34(8):2125-2137. doi: 10.1038/s41375-020-0915-9. Epub 2020 Jun 22.

Reference Type DERIVED
PMID: 32572189 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

Other Identifiers

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2013-003250-25

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

BYOND

Identifier Type: OTHER

Identifier Source: secondary_id

B1871039

Identifier Type: -

Identifier Source: org_study_id