Trial Outcomes & Findings for Comparison of Two Different Lipid Emulsions for Parenteral Nutrition in Preterm Infants (NCT NCT00497289)

NCT ID: NCT00497289

Last Updated: 2021-03-10

Results Overview

Change in ALT between pre/post treatment

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

48 participants

Primary outcome timeframe

on Study day -1 & 6

Results posted on

2021-03-10

Participant Flow

Participant milestones

Participant milestones
Measure
Lipidem 20 %
Lipidem 20 % Lipidem 20%: daily i.v. infusion for up to 5 days
Lipofundin MCT/LCT 20%
Lipofundin MCT/LCT 20% Lipofundin MCT/LCT 20 %: daily i.v. infusion for up to 5 days
Overall Study
STARTED
24
24
Overall Study
COMPLETED
19
18
Overall Study
NOT COMPLETED
5
6

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Comparison of Two Different Lipid Emulsions for Parenteral Nutrition in Preterm Infants

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
MCT:LCT:FO / 5:4:1
n=24 Participants
Lipidem 20%: daily i.v. infusion for up to 5 days
MCT:LCT / 1:1
n=24 Participants
Lipofundin MCT/LCT 20 %: daily i.v. infusion for up to 5 days
Total
n=48 Participants
Total of all reporting groups
Age, Categorical
<=18 years
24 Participants
n=5 Participants
24 Participants
n=7 Participants
48 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Continuous
12.38 hours
STANDARD_DEVIATION 19.38 • n=5 Participants
13.74 hours
STANDARD_DEVIATION 21.89 • n=7 Participants
13.06 hours
STANDARD_DEVIATION 20.46 • n=5 Participants
Sex: Female, Male
Female
13 Participants
n=5 Participants
13 Participants
n=7 Participants
26 Participants
n=5 Participants
Sex: Female, Male
Male
11 Participants
n=5 Participants
11 Participants
n=7 Participants
22 Participants
n=5 Participants
Region of Enrollment
Germany
24 participants
n=5 Participants
24 participants
n=7 Participants
48 participants
n=5 Participants

PRIMARY outcome

Timeframe: on Study day -1 & 6

Population: A duration of treatment with study medication over less than 6 days was regarded as the only major deviation from the protocol. Therefore all available values were used for analysis.

Change in ALT between pre/post treatment

Outcome measures

Outcome measures
Measure
MCT:LCT:FO / 5:4:1
n=15 Participants
Lipidem 20%: daily i.v. infusion for up to 5 days
MCT:LCT / 1:1
n=19 Participants
Lipofundin MCT/LCT 20 %: daily i.v. infusion for up to 5 days
Safety: Alanine Transaminase (ALT)
-0.83 U/L
Standard Deviation 4.61
-3.27 U/L
Standard Deviation 7.81

PRIMARY outcome

Timeframe: on Study day -1 & 6

Population: Per protocol population

Change of IL-6 Measurement pre/post treatment

Outcome measures

Outcome measures
Measure
MCT:LCT:FO / 5:4:1
n=19 Participants
Lipidem 20%: daily i.v. infusion for up to 5 days
MCT:LCT / 1:1
n=17 Participants
Lipofundin MCT/LCT 20 %: daily i.v. infusion for up to 5 days
Efficacy: Interleukin-6 (IL-6)
-42.23 pg/mL
Standard Deviation 197.10
-68.74 pg/mL
Standard Deviation 101.67

Adverse Events

MCT/LCT/FO-containing 20% Fat Emulsion

Serious events: 22 serious events
Other events: 24 other events
Deaths: 0 deaths

MCT/LCT Emulsion (20%)

Serious events: 19 serious events
Other events: 24 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
MCT/LCT/FO-containing 20% Fat Emulsion
n=24 participants at risk
Preterm infants received a study treatment by parenteral route with MCT/LCT/FO Lipidem 20%: daily i.v. infusion for up to 6 days
MCT/LCT Emulsion (20%)
n=24 participants at risk
Preterm infants received a study treatment by parenteral route with MCT/LCT Lipofundin MCT/LCT 20 %: daily i.v. infusion for up to 6 days
Respiratory, thoracic and mediastinal disorders
Pneumothorax
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Neonatal infection
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Amniotic infection syndrome of Blane
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Atelectasis neonatal
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Cardiac disorders
Bradycardia neonatal
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Bronchopulmonary dysplasia
16.7%
4/24 • Number of events 4 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
C-reactive protein increased
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Blood glucose decreased
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Nervous system disorders
Hemorrhage intracranial
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Interleukin level increased
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Pulmonary haemorrhage
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Neonatal respiratory distress syndrome
62.5%
15/24 • Number of events 15 • From enrolment into study at least 6 days or longer if medically indicated.
58.3%
14/24 • Number of events 14 • From enrolment into study at least 6 days or longer if medically indicated.
Congenital, familial and genetic disorders
Patent ductus arteriosus
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Congenital, familial and genetic disorders
Congenital pneumonia
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Neonatal respiratory failure
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
General disorders
Systemic inflammatory response syndrome
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Ureaplasma infection
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Gastrointestinal disorders
Vomiting
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Sepsis neonatal
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
Gastrointestinal disorders
Ileal stenosis
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
Congenital, familial and genetic disorders
Congenital inguinal hernia
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Escherichia sepsis
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
Gastrointestinal disorders
Necrotising enterocolitis neonatal
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.

Other adverse events

Other adverse events
Measure
MCT/LCT/FO-containing 20% Fat Emulsion
n=24 participants at risk
Preterm infants received a study treatment by parenteral route with MCT/LCT/FO Lipidem 20%: daily i.v. infusion for up to 6 days
MCT/LCT Emulsion (20%)
n=24 participants at risk
Preterm infants received a study treatment by parenteral route with MCT/LCT Lipofundin MCT/LCT 20 %: daily i.v. infusion for up to 6 days
Blood and lymphatic system disorders
Anemia neonatal
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Cardiac disorders
Bradycardia neonatal
83.3%
20/24 • Number of events 20 • From enrolment into study at least 6 days or longer if medically indicated.
70.8%
17/24 • Number of events 17 • From enrolment into study at least 6 days or longer if medically indicated.
Congenital, familial and genetic disorders
Congenital methemoglobinemia
50.0%
12/24 • Number of events 12 • From enrolment into study at least 6 days or longer if medically indicated.
54.2%
13/24 • Number of events 13 • From enrolment into study at least 6 days or longer if medically indicated.
Eye disorders
Eyelid oedema
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Gastrointestinal disorders
Hematemesis
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
General disorders
Infusion site erythema
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
General disorders
Oedema peripheral
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 4 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Amniotic infection syndrome of Blane
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Infections and infestations
Escherichia infection
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Injury, poisoning and procedural complications
Skin injury
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
Injury, poisoning and procedural complications
Subcutaneous haematoma
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Base excess increased
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Bilirubin conjugated increased
45.8%
11/24 • Number of events 11 • From enrolment into study at least 6 days or longer if medically indicated.
54.2%
13/24 • Number of events 13 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Blood creatinine increased
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Blood glucose increased
100.0%
24/24 • Number of events 24 • From enrolment into study at least 6 days or longer if medically indicated.
91.7%
22/24 • Number of events 22 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Blood lactic acid increased
62.5%
15/24 • Number of events 15 • From enrolment into study at least 6 days or longer if medically indicated.
66.7%
16/24 • Number of events 16 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Blood triglycerides increased
20.8%
5/24 • Number of events 5 • From enrolment into study at least 6 days or longer if medically indicated.
33.3%
8/24 • Number of events 8 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Body temperature increased
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
4.2%
1/24 • Number of events 1 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
C-reactive protein increased
20.8%
5/24 • Number of events 5 • From enrolment into study at least 6 days or longer if medically indicated.
20.8%
5/24 • Number of events 5 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Hemoglobin decreased
29.2%
7/24 • Number of events 7 • From enrolment into study at least 6 days or longer if medically indicated.
25.0%
6/24 • Number of events 6 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Interleukin level increased
79.2%
19/24 • Number of events 19 • From enrolment into study at least 6 days or longer if medically indicated.
75.0%
18/24 • Number of events 18 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Oxygen saturation decreased
20.8%
5/24 • Number of events 5 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Platelet count decreased
33.3%
8/24 • Number of events 8 • From enrolment into study at least 6 days or longer if medically indicated.
33.3%
8/24 • Number of events 8 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Prothrombin level decreased
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Prothrombin level increased
16.7%
4/24 • Number of events 4 • From enrolment into study at least 6 days or longer if medically indicated.
25.0%
6/24 • Number of events 6 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Red blood cell count decreased
45.8%
11/24 • Number of events 11 • From enrolment into study at least 6 days or longer if medically indicated.
62.5%
15/24 • Number of events 15 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
Reticulocyte count increased
62.5%
15/24 • Number of events 15 • From enrolment into study at least 6 days or longer if medically indicated.
62.5%
15/24 • Number of events 15 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
White blood cell analysis decreased
33.3%
8/24 • Number of events 8 • From enrolment into study at least 6 days or longer if medically indicated.
29.2%
7/24 • Number of events 7 • From enrolment into study at least 6 days or longer if medically indicated.
Investigations
White blood cell analysis increased
16.7%
4/24 • Number of events 4 • From enrolment into study at least 6 days or longer if medically indicated.
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Infantile apnoeic attack
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Neonatal respiratory acidosis
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
Respiratory, thoracic and mediastinal disorders
Respiratory disorder neonatal
8.3%
2/24 • Number of events 2 • From enrolment into study at least 6 days or longer if medically indicated.
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
Skin and subcutaneous tissue disorders
Erythema
0.00%
0/24 • From enrolment into study at least 6 days or longer if medically indicated.
12.5%
3/24 • Number of events 3 • From enrolment into study at least 6 days or longer if medically indicated.
Skin and subcutaneous tissue disorders
Umbilical erythema
75.0%
18/24 • Number of events 18 • From enrolment into study at least 6 days or longer if medically indicated.
58.3%
14/24 • Number of events 14 • From enrolment into study at least 6 days or longer if medically indicated.

Additional Information

Study manager

B.Braun Melsungen AG

Phone: +49 5661 71

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60