Tysabri Observational Program

NCT ID: NCT00493298

Last Updated: 2024-04-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

6620 participants

Study Classification

OBSERVATIONAL

Study Start Date

2007-06-29

Study Completion Date

2023-11-01

Brief Summary

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The primary objective of this study is to assess the long-term safety and impact on disease activity and progression of Tysabri in participants with relapsing remitting multiple sclerosis (RRMS) in a clinical practice setting.

Detailed Description

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TOP is an epidemiological observational study of participants receiving natalizumab, with each participant to be followed for up to 15 years. This study is designed to address the long-term safety profile and the long-term impact on disease activity and progression of Tysabri with marketed use, and the impact of treatment on disability in particular by comparing the results with prospectively determined controls from established databases.

Conditions

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Relapsing-Remitting Multiple Sclerosis

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Tysabri

According to the local prescribing information

Tysabri

Intervention Type DRUG

According to the local prescribing information

Interventions

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Tysabri

According to the local prescribing information

Intervention Type DRUG

Other Intervention Names

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BG00002 natalizumab

Eligibility Criteria

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Inclusion Criteria

* Documented diagnosis of Relapsing Remitting Multiple Sclerosis
* The decision to treat with Tysabri must precede enrollment
* Patient must be a new Tysabri user, and must not have had more than 3 Tysabri infusions prior to enrollment
* Must have had at least one relapse in the previous year, and must satisfy locally approved therapeutic indications for Tysabri

Exclusion Criteria

* History of Progressive Multifocal Leukoencephalopathy or other opportunistic infections, or an increased risk of opportunistic infections
* History of positive anti-Tysabri antibodies
* Concomitant Immunomodulatory or immunosuppressive therapy during therapy with Tysabri
* Patient immunocompromised at the time of enrollment
* Known active malignancy
* Women must not be breast feeding or pregnant, or planning to become pregnant (must use birth control unless surgically sterile)
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Biogen

Locations

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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Buenos Aires, , Argentina

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CABA, , Argentina

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Córdoba, , Argentina

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Santa Fe, , Argentina

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Camperdown, New South Wales, Australia

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Liverpool, New South Wales, Australia

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New Lambton Heights, New South Wales, Australia

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St Leonards, New South Wales, Australia

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Auchenflower, Queensland, Australia

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Gold Coast, Queensland, Australia

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Adelaide, South Australia, Australia

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North Adelaide, South Australia, Australia

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Box Hill, Victoria, Australia

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Fitzroy, Victoria, Australia

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Heidelberg, Victoria, Australia

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Melbourne, Victoria, Australia

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Parkville, Victoria, Australia

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Nedlands, Western Australia, Australia

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Aalst, , Belgium

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Anderlecht, , Belgium

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Antwerp, , Belgium

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Bocholt, , Belgium

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Brasschaat, , Belgium

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Bruges, , Belgium

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Brussels, , Belgium

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Brussels, , Belgium

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Charleroi, , Belgium

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Charleroi, , Belgium

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Edegem, , Belgium

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Fraiture, , Belgium

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Genk, , Belgium

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Ghent, , Belgium

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Hasselt, , Belgium

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Jette, , Belgium

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Kortrijk, , Belgium

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La Louvière, , Belgium

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Leuven, , Belgium

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Libramont, , Belgium

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Liège, , Belgium

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Malmedy, , Belgium

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Melsbroek, , Belgium

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Ostend, , Belgium

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Ottignies, , Belgium

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Overpelt, , Belgium

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Sijsele, , Belgium

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Tournai, , Belgium

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Wilrijk, , Belgium

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Woluwe-Saint-Lambert, , Belgium

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Belo Horizonte, , Brazil

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Botucatu, , Brazil

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Rio de Janeiro, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Edmonton, Alberta, Canada

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Burnaby, British Columbia, Canada

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Vancouver, British Columbia, Canada

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Winnipeg, Manitoba, Canada

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Saint John, New Brunswick, Canada

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Halifax, Nova Scotia, Canada

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Bracebridge, Ontario, Canada

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Guelph, Ontario, Canada

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Hamilton, Ontario, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Milton, Ontario, Canada

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Thunder Bay, Ontario, Canada

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Toronto, Ontario, Canada

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Gatineau, Quebec, Canada

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Greenfield Park, Quebec, Canada

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Montreal, Quebec, Canada

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Montreal, Quebec, Canada

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Regina, Saskatchewan, Canada

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Brno, , Czechia

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Brno, , Czechia

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České Budějovice, , Czechia

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Hradec Kralové, , Czechia

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Jihlava, , Czechia

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Olomouc, , Czechia

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Ostrava, , Czechia

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Pardubice, , Czechia

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Pilsen, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Teplice, , Czechia

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Teplice, , Czechia

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Zlín, , Czechia

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Helsinki, , Finland

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Jyväskylä, , Finland

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Kuopio, , Finland

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Pori, , Finland

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Seinäjoki, , Finland

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Tampere, , Finland

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Turku, , Finland

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Agen, , France

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Aix-en-Provence, , France

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Alençon, , France

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Angoulême, , France

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Research site ,1 Allée du Château- Dr Wagner

Ars-Laquenexy, , France

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Auxerre, , France

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Avranches, , France

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Bayonne, , France

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Beauvais, , France

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Belfort, , France

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Beuvry, , France

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Béthune, , France

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Boulogne-sur-Mer, , France

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Calais, , France

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Castelnau-le-Lez, , France

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Castres, , France

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Chambéry, , France

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Chambéry, , France

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Colmar, , France

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Compiègne, , France

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Dieppe, , France

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Dreux, , France

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Dunkirk, , France

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Épinal, , France

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Évreux, , France

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Haguenau, , France

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La Rochelle, , France

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Le Chesnay, , France

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Le Chesnay, , France

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Le Coudray, , France

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Le Havre, , France

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Le Mans, , France

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Lille, , France

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Lisieux, , France

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Lomme, , France

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Mantes-la-Jolie, , France

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Maubeuge, , France

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Metz, , France

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Metz-Tessy, , France

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Mont-de-Marsan, , France

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Montauban, , France

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Montluçon, , France

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Montpellier, , France

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Montpellier, , France

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Mulhouse, , France

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Nice, , France

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Paris, , France

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Paris, , France

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Pau, , France

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Quimper, , France

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Reims, , France

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Saint-Aubin-sur-Scie, , France

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Sarreguemines, , France

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Saumur, , France

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St-Malo, , France

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Talant, , France

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Tarbes, , France

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Tourcoing, , France

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Trappes, , France

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Trélazé, , France

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Valenciennes, , France

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Vesoul, , France

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Vichy, , France

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Abensberg, , Germany

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Andernach, , Germany

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Arnsdorf, , Germany

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Asperg, , Germany

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Augsburg, , Germany

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Bad Hersfeld, , Germany

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Bad Honnef, , Germany

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Bad Kissingen, , Germany

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Bad Mergentheim, , Germany

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Bad Reichenhall, , Germany

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Bamberg, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Bielefeld, , Germany

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Bielefeld, , Germany

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Bochum, , Germany

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Bogen, , Germany

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Bonn, , Germany

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Bruchsal, , Germany

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Buchholz, , Germany

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Celle, , Germany

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Chemnitz, , Germany

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Cologne, , Germany

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Cologne, , Germany

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Dillingen, , Germany

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Dresden, , Germany

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Duisburg, , Germany

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Düren, , Germany

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Düsseldorf, , Germany

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Düsseldorf, , Germany

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Eisenach, , Germany

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Emden, , Germany

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Emmendingen, , Germany

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Erbach im Odenwald, , Germany

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Erlangen, , Germany

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Essen, , Germany

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Essen, , Germany

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Essen, , Germany

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Falkenstein, , Germany

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Frankfurt, , Germany

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Freiburg im Breisgau, , Germany

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Görlitz, , Germany

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Göttingen, , Germany

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Greifswald, , Germany

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Halle, , Germany

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Hamburg, , Germany

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Hamburg, , Germany

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Hamburg, , Germany

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Heidelberg, , Germany

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Herford, , Germany

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Itzehoe, , Germany

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Jena, , Germany

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Kaiserslautern, , Germany

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Kaltenkirchen, , Germany

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Kandel, , Germany

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Kassel, , Germany

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Kastellaun, , Germany

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Kirchberg, , Germany

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Kirchheim unter Teck, , Germany

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Kreuzau, , Germany

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Ladenburg, , Germany

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Leipzig, , Germany

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Leipzig, , Germany

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Lengerich, , Germany

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Ludwigshafen, , Germany

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Lüdenscheid, , Germany

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Lüdenscheid, , Germany

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Lüneburg, , Germany

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Magdeburg, , Germany

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Mannheim, , Germany

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Mannheim, , Germany

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Marburg, , Germany

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München, , Germany

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München, , Germany

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München, , Germany

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München, , Germany

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München, , Germany

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Münster, , Germany

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Neuburg am Inn, , Germany

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Neukirchen-Vluyn, , Germany

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Neuruppin, , Germany

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Nuremberg, , Germany

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Nuremberg, , Germany

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Nuremberg, , Germany

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Oldenburg, , Germany

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Oldenburg, , Germany

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Olpe, , Germany

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Osnabrück, , Germany

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Osnabrück, , Germany

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Osnabrück, , Germany

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Paderborn, , Germany

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Potsdam, , Germany

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Regensburg, , Germany

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Remscheid, , Germany

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Rüdersdorf, , Germany

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Rülzheim, , Germany

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Schlüchtern, , Germany

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Schorndorf, , Germany

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Schwaebisch, , Germany

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Siegen, , Germany

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Sinsheim, , Germany

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Stade, , Germany

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Stadtroda, , Germany

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Stuttgart, , Germany

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Stuttgart, , Germany

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Tegel, , Germany

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Teupitz, , Germany

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Trier, , Germany

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Troisdorf, , Germany

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Ulm, , Germany

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Ulm, , Germany

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Ulm, , Germany

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Unterhaching, , Germany

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Wasserburg, , Germany

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Weimar, , Germany

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Weinheim, , Germany

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Wermsdorf, , Germany

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Wernigerode, , Germany

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Wiesbaden, , Germany

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Wolfenbüttel, , Germany

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Wolfratshausen, , Germany

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Würzburg, , Germany

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Zwickau, , Germany

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Heraklion, Crete, Greece

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Alexandroupoli, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Athens, , Greece

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Ioannina, , Greece

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Pátrai, , Greece

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Pátrai, , Greece

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Thessaloniki, , Greece

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Bari, , Italy

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Bergamo, , Italy

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Cagliari, , Italy

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Cefalù, , Italy

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Chieti, , Italy

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Cuneo, , Italy

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Fidenza, , Italy

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Florence, , Italy

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Foggia, , Italy

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Gallarate, , Italy

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Milan, , Italy

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Milan, , Italy

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Napoli, , Italy

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Orbassano, , Italy

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Roma, , Italy

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Roma, , Italy

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Roma, , Italy

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Zapopan, Jalisco, Mexico

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Monterrey, Nuevo León, Mexico

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Monterrey, Nuevo León, Mexico

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Aguascalientes, , Mexico

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Estado de México, , Mexico

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León, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Mexico City, , Mexico

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Puebla City, , Mexico

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Puebla City, , Mexico

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San Luis Potosí City, , Mexico

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's-Hertogenbosch, , Netherlands

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Almelo, , Netherlands

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Blaricum, , Netherlands

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Breda, , Netherlands

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Eindhoven, , Netherlands

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Geldrop, , Netherlands

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Gouda, , Netherlands

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Heerenveen, , Netherlands

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Heerlen, , Netherlands

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Helmond, , Netherlands

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Hengelo, , Netherlands

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Hoorn, , Netherlands

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Leeuwarden, , Netherlands

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Meppel, , Netherlands

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Nieuwegein, , Netherlands

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Nijmegen, , Netherlands

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Roermond, , Netherlands

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Rotterdam, , Netherlands

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Sittard-Geleen, , Netherlands

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The Hague, , Netherlands

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Tilburg, , Netherlands

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Venray, , Netherlands

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Woerden, , Netherlands

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Zwolle, , Netherlands

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Bergen, , Norway

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Bodø, , Norway

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Drammen, , Norway

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Fredrikstad, , Norway

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Førde, , Norway

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Haugesund, , Norway

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Lillehammer, , Norway

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Lørenskog, , Norway

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Molde, , Norway

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Namsos, , Norway

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Oslo, , Norway

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Oslo, , Norway

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Skien, , Norway

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Stavanger, , Norway

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Tromsø, , Norway

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Trondheim, , Norway

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Tønsberg, , Norway

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Aveiro, , Portugal

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Beja, , Portugal

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Evora, , Portugal

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Funchal, , Portugal

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Lisbon, , Portugal

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Lisbon, , Portugal

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Porto, , Portugal

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Setúbal, , Portugal

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Banská Bystrica, , Slovakia

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Bratislava, , Slovakia

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Bratislava, , Slovakia

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Bratislava, , Slovakia

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Košice, , Slovakia

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Nitra, , Slovakia

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Ávila, , Spain

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Badalona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Donostia / San Sebastian, , Spain

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Girona, , Spain

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Langreo, , Spain

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Logroño, , Spain

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Palma de Mallorca, , Spain

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Ponferrada, , Spain

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Tarragona, , Spain

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Tarragona, , Spain

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Vitoria-Gasteiz, , Spain

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Edgbaston, Birmingham, United Kingdom

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Canterbury, Kent, United Kingdom

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Hammersmith, London, United Kingdom

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Salford, Manchester, United Kingdom

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Belfast, , United Kingdom

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Brighton, , United Kingdom

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Bristol, , United Kingdom

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Coventry, , United Kingdom

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Exeter, , United Kingdom

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Liverpool, , United Kingdom

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Middlesbrough, , United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Nottingham, , United Kingdom

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Stoke-on-Trent, , United Kingdom

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Countries

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Argentina Australia Belgium Brazil Canada Czechia Finland France Germany Greece Italy Mexico Netherlands Norway Portugal Slovakia Spain United Kingdom

References

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Butzkueven H, Kappos L, Spelman T, Trojano M, Wiendl H, Su R, Liao S, Hyde R, Licata S, Ho PR, Campbell N. No evidence for loss of natalizumab effectiveness with every-6-week dosing: a propensity score-matched comparison with every-4-week dosing in patients enrolled in the Tysabri Observational Program (TOP). Ther Adv Neurol Disord. 2021 Sep 27;14:17562864211042458. doi: 10.1177/17562864211042458. eCollection 2021.

Reference Type DERIVED
PMID: 34603507 (View on PubMed)

Butzkueven H, Kappos L, Wiendl H, Trojano M, Spelman T, Chang I, Kasliwal R, Jaitly S, Campbell N, Ho PR, Licata S; Tysabri Observational Program (TOP) Investigators. Long-term safety and effectiveness of natalizumab treatment in clinical practice: 10 years of real-world data from the Tysabri Observational Program (TOP). J Neurol Neurosurg Psychiatry. 2020 Jun;91(6):660-668. doi: 10.1136/jnnp-2019-322326. Epub 2020 Mar 31.

Reference Type DERIVED
PMID: 32234967 (View on PubMed)

Butzkueven H, Kappos L, Pellegrini F, Trojano M, Wiendl H, Patel RN, Zhang A, Hotermans C, Belachew S; TYSABRI Observational Program (TOP) Investigators. Efficacy and safety of natalizumab in multiple sclerosis: interim observational programme results. J Neurol Neurosurg Psychiatry. 2014 Nov;85(11):1190-7. doi: 10.1136/jnnp-2013-306936. Epub 2014 Feb 14.

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Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

IMA-06-02

Identifier Type: -

Identifier Source: org_study_id

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