PAR-101/OPT-80 Versus Vancomycin for the Treatment of Clostridium Difficile-Associated Diarrhea (CDAD)

NCT ID: NCT00468728

Last Updated: 2017-04-21

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

535 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-10-04

Study Completion Date

2009-12-11

Brief Summary

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This is a comparative study to investigate the safety and efficacy of PAR-101/OPT-80 (fidaxomicin) versus vancomycin in subjects with Clostridium difficile-associated diarrhea (CDAD).

Detailed Description

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The primary objective of this pivotal study is to investigate the safety and efficacy of PAR-101/OPT-80 versus vancomycin in subjects with Clostridium difficile-associated diarrhea (CDAD). The cure rates at end of therapy and recurrence rates will be evaluated and compared.

Conditions

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Clostridium Infections Diarrhea

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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1

Vancomycin

Group Type ACTIVE_COMPARATOR

Vancomycin

Intervention Type DRUG

Capsules

2

PAR-101/OPT-80

Group Type EXPERIMENTAL

PAR-101/OPT-80

Intervention Type DRUG

capsules

Interventions

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PAR-101/OPT-80

capsules

Intervention Type DRUG

Vancomycin

Capsules

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Males/females with CDAD
* Females must use adequate contraception
* Signed informed consent

Exclusion Criteria

* Life-threatening CDAD
* Toxic megacolon
* Pregnant
* Concurrent use of diarrheal agents
* Participation in other trials
Minimum Eligible Age

16 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Optimer Pharmaceuticals LLC, a subsidiary of Merck & Co., Inc. (Rahway, New Jersey USA)

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Dr. Sherwood Gorbach, MD

Role: STUDY_DIRECTOR

Optimer Pharmaceuticals, Inc.

Locations

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Gadsden, Alabama, United States

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Phoenix, Arizona, United States

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Hot Springs, Arkansas, United States

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La Mesa, California, United States

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Modesto, California, United States

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Palm Springs, California, United States

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Rancho Mirage, California, United States

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San Jose, California, United States

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Santa Ana, California, United States

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Vallejo, California, United States

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Washington D.C., District of Columbia, United States

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Miami, Florida, United States

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Port Orange, Florida, United States

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Sarasota, Florida, United States

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Marietta, Georgia, United States

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Savannah, Georgia, United States

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Idaho Falls, Idaho, United States

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Chicago, Illinois, United States

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Maywood, Illinois, United States

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Indianapolis, Indiana, United States

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Bowling Green, Kentucky, United States

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Jena, Louisiana, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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West Roxbury, Massachusetts, United States

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Detroit, Michigan, United States

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Keego Harbor, Michigan, United States

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Royal Oak, Michigan, United States

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Minneapolis, Minnesota, United States

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Tupelo, Mississippi, United States

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Columbia, Missouri, United States

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Butte, Montana, United States

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Cedar Knolls, New Jersey, United States

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Neptune City, New Jersey, United States

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The Bronx, New York, United States

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Charlotte, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Fargo, North Dakota, United States

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Akron, Ohio, United States

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Amherst, Ohio, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Rapid City, South Dakota, United States

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Sioux Falls, South Dakota, United States

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San Antonio, Texas, United States

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Winchester, Virginia, United States

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Seattle, Washington, United States

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Charleston, West Virginia, United States

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Aalst, , Belgium

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Alast, , Belgium

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Antwerp, , Belgium

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Brussels, , Belgium

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Columbia, , Belgium

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Ghent, , Belgium

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Kortrijk, , Belgium

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Liège, , Belgium

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Mons, , Belgium

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Montigny-le-Tilleul, , Belgium

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Wilrijk, , Belgium

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Hamilton, Ontario, Canada

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Toronto, Ontario, Canada

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Chicoutimi, Quebec, Canada

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Montreal, Quebec, Canada

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Saint-Jérôme, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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Amiens, , France

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Caen, , France

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Clichy, , France

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Garches, , France

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Grenoble, , France

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Lille, , France

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Tourcoing, , France

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Tours, , France

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Valenciennes, , France

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Cologne, , Germany

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Düsseldorf, , Germany

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Frankfurt, , Germany

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Hanover, , Germany

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Hofheim am Taunus, , Germany

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Lübeck, , Germany

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Magdeburg, , Germany

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Regensburg, , Germany

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Busto Arsizio, , Italy

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Genova, , Italy

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Milan, , Italy

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Modena, , Italy

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Torino, , Italy

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Badalona, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Palma de Mallorca, , Spain

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Seville, , Spain

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Eskilstuna, , Sweden

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Gothenburg, , Sweden

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Örebro, , Sweden

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Great Yarmouth, Norfolk, United Kingdom

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Derriford, Plymouth, United Kingdom

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Barnsley, , United Kingdom

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Brighton, , United Kingdom

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Cambridge, , United Kingdom

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Edinburgh, , United Kingdom

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Liege, , United Kingdom

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London, , United Kingdom

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Nottingham, , United Kingdom

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Oxford, , United Kingdom

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Oxon, , United Kingdom

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Surrey, , United Kingdom

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York, , United Kingdom

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Countries

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United States Belgium Canada France Germany Italy Spain Sweden United Kingdom

References

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Cornely OA, Crook DW, Esposito R, Poirier A, Somero MS, Weiss K, Sears P, Gorbach S; OPT-80-004 Clinical Study Group. Fidaxomicin versus vancomycin for infection with Clostridium difficile in Europe, Canada, and the USA: a double-blind, non-inferiority, randomised controlled trial. Lancet Infect Dis. 2012 Apr;12(4):281-9. doi: 10.1016/S1473-3099(11)70374-7. Epub 2012 Feb 8.

Reference Type RESULT
PMID: 22321770 (View on PubMed)

D'Agostino RB Sr, Collins SH, Pencina KM, Kean Y, Gorbach S. Risk estimation for recurrent Clostridium difficile infection based on clinical factors. Clin Infect Dis. 2014 May;58(10):1386-93. doi: 10.1093/cid/ciu107. Epub 2014 Mar 5.

Reference Type DERIVED
PMID: 24599770 (View on PubMed)

Cornely OA, Miller MA, Fantin B, Mullane K, Kean Y, Gorbach S. Resolution of Clostridium difficile-associated diarrhea in patients with cancer treated with fidaxomicin or vancomycin. J Clin Oncol. 2013 Jul 1;31(19):2493-9. doi: 10.1200/JCO.2012.45.5899. Epub 2013 May 28.

Reference Type DERIVED
PMID: 23715579 (View on PubMed)

Cornely OA, Miller MA, Louie TJ, Crook DW, Gorbach SL. Treatment of first recurrence of Clostridium difficile infection: fidaxomicin versus vancomycin. Clin Infect Dis. 2012 Aug;55 Suppl 2(Suppl 2):S154-61. doi: 10.1093/cid/cis462.

Reference Type DERIVED
PMID: 22752865 (View on PubMed)

Figueroa I, Johnson S, Sambol SP, Goldstein EJ, Citron DM, Gerding DN. Relapse versus reinfection: recurrent Clostridium difficile infection following treatment with fidaxomicin or vancomycin. Clin Infect Dis. 2012 Aug;55 Suppl 2(Suppl 2):S104-9. doi: 10.1093/cid/cis357.

Reference Type DERIVED
PMID: 22752857 (View on PubMed)

Other Identifiers

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101.1.C.004

Identifier Type: OTHER

Identifier Source: secondary_id

5119-019

Identifier Type: -

Identifier Source: org_study_id

NCT00427869

Identifier Type: -

Identifier Source: nct_alias

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