Open-Label C1 Esterase Inhibitor (C1INH-nf) for the Prevention of Acute Hereditary Angioedema (HAE) Attacks

NCT ID: NCT00462709

Last Updated: 2021-06-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

146 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-06-27

Study Completion Date

2009-03-31

Brief Summary

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The study objective was to evaluate the safety and efficacy of prophylactic use of C1INH-nf for the prevention of acute HAE attacks.

Detailed Description

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Conditions

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Hereditary Angioedema

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

PREVENTION

Blinding Strategy

NONE

Study Groups

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Open-label C1INH-nf

1,000 Units (U) of C1INH-nf administered intravenously (IV) every 3 to 7 days.

Group Type EXPERIMENTAL

C1 esterase inhibitor [human] (C1INH-nf)

Intervention Type BIOLOGICAL

Interventions

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C1 esterase inhibitor [human] (C1INH-nf)

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

\- History of at least 1 HAE attack per month or any history of laryngeal edema

In addition, this study was open to all subjects who:

* Completed participation in LEVP2005-1/B (NCT01005888) any time after the final prophylactic therapy in Part B
* Were enrolled but not randomized in LEVP2005-1/A (NCT00289211) after Part A was closed
* Were enrolled and randomized in LEVP2005-1/A after LEVP2005-1/B was closed to enrollment, any time after the 3-day telephone follow-up
* Were excluded from LEVP2005-1 for any of the following reasons:

* Pregnancy or lactation
* Age less than 6 years
* Narcotic addiction
* Presence of anti-C1 inhibitor (C1INH) autoantibodies
* Were not enrolled in LEVP2005-1 after enrollment in LEVP2005-1 was closed, under the following circumstances:

* Had a diagnosis of HAE: evidence of a low C4 level plus either a low C1INH antigenic level or a low C1INH functional level, or
* Had a known HAE-causing C1INH mutation, or
* Had a diagnosis of HAE based on a strong family history of HAE as determined by the principal investigator

Exclusion Criteria

* History of allergic reaction to C1INH or other blood products
* Participated in any other investigational drug study within the past 30 days other than those sponsored by Lev Pharmaceuticals
* Received blood or a blood product in the past 60 days other than C1INH-nf
Minimum Eligible Age

1 Year

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shire

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

Takeda

Locations

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Clinical Research Consultants, Inc

Hoover, Alabama, United States

Site Status

Allergy and Immunology Associates

Scottsdale, Arizona, United States

Site Status

Allergy and Asthma Clinic of Northwest Arkansas

Bentonville, Arkansas, United States

Site Status

UCLA-David Geffen School of Medicine

Los Angeles, California, United States

Site Status

University of California, San Diego

San Diego, California, United States

Site Status

Allergy and Asthma Associates of Santa Clara

San Jose, California, United States

Site Status

Allergy and Asthma Clinical Research, Inc

Walnut Creek, California, United States

Site Status

Allergy and Asthma Center

Fort Lauderdale, Florida, United States

Site Status

Allergy and Asthma Center of East Orlando

Orlando, Florida, United States

Site Status

Cleveland Clinic

Weston, Florida, United States

Site Status

Family Allergy and Asthma Center

Atlanta, Georgia, United States

Site Status

Atlanta Allergy and Asthma Clinic

Suwanee, Georgia, United States

Site Status

University Consultants in Allergy & Immunology

Chicago, Illinois, United States

Site Status

Welborn Clinic

Evansville, Indiana, United States

Site Status

Private Practice

Liberal, Kansas, United States

Site Status

Olathe Medical Center

Olathe, Kansas, United States

Site Status

Graves-Gilbert Clinic

Bowling Green, Kentucky, United States

Site Status

Family Asthma and Allergy Research Center

Louisville, Kentucky, United States

Site Status

Asthma Allergy and Sinus Center

Waldorf, Maryland, United States

Site Status

Institute for Asthma and Allergy

Wheaton, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

Grand Traverse Allergy

Traverse City, Michigan, United States

Site Status

MeritCare Clinical Research

Bemidji, Minnesota, United States

Site Status

University of Mississippi Medical Center

Jackson, Mississippi, United States

Site Status

St. Louis University School of Medicine

St Louis, Missouri, United States

Site Status

Nevada Access to Research and Education Society

Las Vegas, Nevada, United States

Site Status

UMDNJ Asthma and Allergy Research Center

Newark, New Jersey, United States

Site Status

Private Practice

Hastings-on-Hudson, New York, United States

Site Status

Winthrop University Hospital

Mineola, New York, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Allergy Partners of East Carolina

Greenville, North Carolina, United States

Site Status

Legacy Pharma Research

Bismarck, North Dakota, United States

Site Status

MeritCare Clinical Research

Fargo, North Dakota, United States

Site Status

Nationwide Childrens Hospital Clinical Research

Columbus, Ohio, United States

Site Status

Allergy Clinic of Tulsa

Tulsa, Oklahoma, United States

Site Status

Oregon Medical Group

Eugene, Oregon, United States

Site Status

Allergy Asthma and Dermatology Research Center

Lake Oswego, Oregon, United States

Site Status

Penn State University

Hershey, Pennsylvania, United States

Site Status

AARA Research Center

Dallas, Texas, United States

Site Status

University of Texas Medical Branch

Galveston, Texas, United States

Site Status

University of Texas - Pediatric Pulmonary/Allergy and Immunology

Houston, Texas, United States

Site Status

Allergy and Asthma Research Center

San Antonio, Texas, United States

Site Status

Tyler County Hospital

Woodville, Texas, United States

Site Status

Virginia Adult and Pediatric Allergy and Asthma

Richmond, Virginia, United States

Site Status

Marycliff Allergy Specialists

Spokane, Washington, United States

Site Status

Puget Sound Allergy, Asthma and Immunology

Tacoma, Washington, United States

Site Status

St. Joseph's Hospital/Cornerstone Healthcare

Parkersburg, West Virginia, United States

Site Status

Countries

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United States

References

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Beard N, Frese M, Smertina E, Mere P, Katelaris C, Mills K. Interventions for the long-term prevention of hereditary angioedema attacks. Cochrane Database Syst Rev. 2022 Nov 3;11(11):CD013403. doi: 10.1002/14651858.CD013403.pub2.

Reference Type DERIVED
PMID: 36326435 (View on PubMed)

Baker JW, Craig TJ, Riedl MA, Banerji A, Fitts D, Kalfus IN, Uknis ME. Nanofiltered C1 esterase inhibitor (human) for hereditary angioedema attacks in pregnant women. Allergy Asthma Proc. 2013 Mar-Apr;34(2):162-9. doi: 10.2500/aap.2013.34.3645.

Reference Type DERIVED
PMID: 23484892 (View on PubMed)

Lumry W, Manning ME, Hurewitz DS, Davis-Lorton M, Fitts D, Kalfus IN, Uknis ME. Nanofiltered C1-esterase inhibitor for the acute management and prevention of hereditary angioedema attacks due to C1-inhibitor deficiency in children. J Pediatr. 2013 May;162(5):1017-22.e1-2. doi: 10.1016/j.jpeds.2012.11.030. Epub 2013 Jan 11.

Reference Type DERIVED
PMID: 23312695 (View on PubMed)

Zuraw BL, Busse PJ, White M, Jacobs J, Lumry W, Baker J, Craig T, Grant JA, Hurewitz D, Bielory L, Cartwright WE, Koleilat M, Ryan W, Schaefer O, Manning M, Patel P, Bernstein JA, Friedman RA, Wilkinson R, Tanner D, Kohler G, Gunther G, Levy R, McClellan J, Redhead J, Guss D, Heyman E, Blumenstein BA, Kalfus I, Frank MM. Nanofiltered C1 inhibitor concentrate for treatment of hereditary angioedema. N Engl J Med. 2010 Aug 5;363(6):513-22. doi: 10.1056/NEJMoa0805538.

Reference Type DERIVED
PMID: 20818886 (View on PubMed)

Other Identifiers

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LEVP2006-4

Identifier Type: -

Identifier Source: org_study_id

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