An Open-label Extension Trial to Evaluate the Long-term Safety of KVD900 (Sebetralstat) for On-Demand Treatment of Angioedema Attacks in Adolescent and Adult Patients With Hereditary Angioedema (HAE)

NCT ID: NCT05505916

Last Updated: 2024-12-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

145 participants

Study Classification

INTERVENTIONAL

Study Start Date

2022-10-24

Study Completion Date

2026-06-30

Brief Summary

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This is an open-label, multicenter extension trial to evaluate the long-term safety of KVD900 in patients who are 12 years or older with HAE type I or II.

Detailed Description

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Conditions

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Hereditary Angioedema

Keywords

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KONFIDENT-S Sebetralstat

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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KVD900 600 mg

Group Type EXPERIMENTAL

KVD900 600 mg

Intervention Type DRUG

KVD900 Tablet 600 mg (2 x 300 mg)

KVD900 300 mg

Group Type EXPERIMENTAL

KVD900 300 mg

Intervention Type DRUG

KVD900 Tablet 300 mg

Interventions

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KVD900 600 mg

KVD900 Tablet 600 mg (2 x 300 mg)

Intervention Type DRUG

KVD900 300 mg

KVD900 Tablet 300 mg

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Confirmed diagnosis of HAE type I or II at any time in the medical history
2. Patient has had at least 2 documented HAE attacks within 3 months prior to the Enrollment Visit.
3. If a patient is receiving long-term prophylactic treatment with one of the protocol-allowed therapies, they must have been on a stable dose and regimen for at least 3 months prior to the Enrollment Visit (except for danazol, which requires a stable dose and regimen for at least 6 months prior to the Enrollment Visit).
4. Male or female patients 12 years of age and older.
5. Patients must meet the contraception requirements.
6. Patients must be able to swallow trial tablets whole.
7. Patients, as assessed by the Investigator, must be able to appropriately receive and store IMP, and be able to read, understand, and complete the eDiary.
8. Investigator believes that the patient is willing and able to adhere to all protocol requirements.
9. Patient provides signed informed consent or assent (when applicable). A parent or legally authorized representative (LAR) must also provide signed informed consent when required.

Exclusion Criteria

1. Discontinued from the KVD900-301 trial for reasons of noncompliance, withdrawal of consent, or safety.
2. Presence of any safety concerns that would preclude participation in the open-label trial as determined by the investigator.
3. Any concomitant diagnosis of another form of chronic angioedema, such as acquired C1 inhibitor deficiency, HAE with normal C1-INH (previously known as HAE type III), idiopathic angioedema, or angioedema associated with urticaria.
4. A clinically significant history of poor response to bradykinin receptor 2 (BR2) blocker, C1-INH therapy, or plasma kallikrein inhibitor therapy for the management of HAE, in the opinion of the Investigator.
5. Use of attenuated androgens other than danazol (e.g., stanozolol, oxandrolone, methyltestosterone, testosterone), or anti-fibrinolytics (e.g., tranexamicacid) within 28 days prior to the Enrollment Visit.
6. Use of Angiotensin-converting enzyme (ACE) inhibitors within 7 days prior to the Enrollment Visit.
7. Any estrogen-containing medications with systemic absorption (such as oral contraceptives including ethinylestradiol or hormonal replacement therapy) within 7 days prior to the Enrollment Visit.
8. Inadequate organ function, including but not limited to:

1. Alanine aminotransferase (ALT) \>2x Upper Limit Normal (ULN)
2. Aspartate aminotransferase (AST) \>2x ULN
3. Bilirubin direct \>1.25x ULN
4. International Normalized Ratio (INR) \>1.2
5. Clinically significant hepatic impairment defined as a Child-Pugh B or C
9. Any clinically significant comorbidity or systemic dysfunction, which in the opinion of the Investigator, would jeopardize the safety of the patient by participating in the trial.
10. History of substance abuse or dependence that would interfere with the completion of the trial, as determined by the Investigator.
11. Known hypersensitivity to KVD900 or to any of the excipients.
12. Participation in any gene therapy treatment or trial for HAE.
13. Participation in any interventional investigational clinical trial, including an investigational COVID-19 vaccine trial, within 4 weeks of the last dosing of investigational drug prior to the Enrollment Visit.
14. Any pregnant or breastfeeding patient.
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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KalVista Pharmaceuticals, Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Study Director

Role: STUDY_DIRECTOR

KalVista Pharmaceuticals, Ltd.

Locations

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KalVista Investigative Site

Scottsdale, Arizona, United States

Site Status

KalVista Investigative Site

Little Rock, Arkansas, United States

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KalVista Investigative Site

San Diego, California, United States

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KalVista Investigative Site

San Diego, California, United States

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KalVista Investigative Site

Santa Monica, California, United States

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KalVista Investigative Site

Centennial, Colorado, United States

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KalVista Investigative Site

Colorado Springs, Colorado, United States

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KalVista Investigative Site

Evansville, Indiana, United States

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KalVista Investigative Site

Overland Park, Kansas, United States

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KalVista Investigative Site

Louisville, Kentucky, United States

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KalVista Investigative Site

Chevy Chase, Maryland, United States

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KalVista Investigative Site

Plymouth, Minnesota, United States

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KalVista Investigative Site

St Louis, Missouri, United States

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KalVista Investigative Site

Charlotte, North Carolina, United States

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KalVista Investigative Site

Cincinnati, Ohio, United States

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KalVista Investigative Site

Toledo, Ohio, United States

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KalVista Investigative Site

Hershey, Pennsylvania, United States

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KalVista Investigative Site

Dallas, Texas, United States

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KalVista Investgative Site

Layton, Utah, United States

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KalVista Investigative Site

Spokane, Washington, United States

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KalVista Investigative Site

Campbelltown, , Australia

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KalVista Investigative Site

Wein, , Austria

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KalVista Investigative Site

Sofia, , Bulgaria

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KalVista Investigative Site

Montreal, , Canada

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KalVista Investigative Site

Grenoble, , France

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KalVista Investigative Site

Lille, , France

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KalVista Investigative Site

Paris, , France

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KalVista Investigative Site

Berlin, , Germany

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KalVista Investigative Site

Frankfurt, , Germany

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KalVista Investigative Site

Mainz, , Germany

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KalVista Investigative Site

Mörfelden-Walldorf, , Germany

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KalVista Investigative Site

Athens, , Greece

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KalVista Investigative Site

Athens, , Greece

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KalVista Investigative Site

Budapest, , Hungary

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KalVista Investigative Site

Haifa, , Israel

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KalVista Investigative Site

Petach Tikvah, , Israel

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KalVista Investigative Site

Ramat Gan, , Israel

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KalVista Investigative Site

Tel Aviv, , Israel

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KalVista Investigative Site

Padua, , Italy

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KalVista Investigative Site

Palermo, , Italy

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KalVista Investigative Site

Roma, , Italy

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KalVista Investigative Site

San Donato Milanese, , Italy

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KalVista Investigative Site

Sapporo, Hokkaido, Japan

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KalVista Investigative Site

Chiba, , Japan

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KalVista Investigative Site

Hiroshima, , Japan

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KalVista Investigative Site

Kawagoe-shi, , Japan

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KalVista Investigative Site

Maebashi, , Japan

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KalVista Investigative Site

Soka-shi, , Japan

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KalVista Investigative Site

Takatsuki-shi, , Japan

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KalVista Investgative Site

Tokyo, , Japan

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KalVista Investigative Site

Yokohama, , Japan

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KalVista Investigative Site

Amsterdam, , Netherlands

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KalVista Investigative Site

Auckland, , New Zealand

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KalVista Investigative Site

Skopje, , North Macedonia

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KalVista Investigative Site

Krakow, , Poland

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KalVista Investigative Site

Lodz, , Poland

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KalVista Investigative Site

Porto, , Portugal

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KalVista Investigative Site

Sângeorgiu de Mureş, , Romania

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KalVista Investigative Site

Riyadh, , Saudi Arabia

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KalVista Investigative Site

Martin, , Slovakia

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Kalvista Investigative Site

Cape Town, , South Africa

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KalVista Investigative Site

Barcelona, , Spain

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KalVista Investigative Site

Barcelona, , Spain

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KalVista Investigative Site

Madrid, , Spain

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KalVista Investigative Site

Birmingham, , United Kingdom

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KalVista Investigative Site

Cambridge, , United Kingdom

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KalVista Investigative Site

Cardiff, , United Kingdom

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KalVista Investigative Site

Frimley, , United Kingdom

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KalVista Investigative Site

Leeds, , United Kingdom

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KalVista Investigative Site

London, , United Kingdom

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KalVista Investigative Site

London, , United Kingdom

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Countries

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United States Australia Austria Bulgaria Canada France Germany Greece Hungary Israel Italy Japan Netherlands New Zealand North Macedonia Poland Portugal Romania Saudi Arabia Slovakia South Africa Spain United Kingdom

References

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Farkas H, Anderson J, Bouillet L, Caballero T, Cancian M, Craig T, Fukunaga A, Grivcheva-Panovska V, Guilarte M, Honda D, Kanarek H, Kiani-Alikhan S, Kinaciyan T, Leguevaques D, Longhurst HJ, Magerl M, Manning ME, Martinez-Saguer I, Melamed I, O'Connor ME, Peter J, Savic S, Soteres DF, Staevska M, Staubach-Renz P, Stobiecki M, Tachdjian R, Valerieva A, Yong PFK, Hao J, Iverson M, Smith MD, Yea CM, Audhya PK, Aygoren-Pursun E, Bernstein JA, Cohn DM, Lumry WR, Riedl MA, Zanichelli A, Maurer M. Long-term Safety and Effectiveness of Sebetralstat: Interim Analysis of KONFIDENT-S Open-label Extension. J Allergy Clin Immunol Pract. 2025 Aug 29:S2213-2198(25)00821-9. doi: 10.1016/j.jaip.2025.08.020. Online ahead of print.

Reference Type DERIVED
PMID: 40886933 (View on PubMed)

Other Identifiers

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KVD900-302

Identifier Type: -

Identifier Source: org_study_id