Study of Subcutaneous Immunoglobulin in Patients With PID Requiring IgG Replacement Therapy

NCT ID: NCT00419341

Last Updated: 2013-01-25

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

49 participants

Study Classification

INTERVENTIONAL

Study Start Date

2006-11-30

Study Completion Date

2008-10-31

Brief Summary

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The objective of this study is to assess the efficacy, tolerability, safety and pharmacokinetics of IgPro20 in patients with primary humoral immunodeficiency (PID).

Detailed Description

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The entire study consists of a 12-week wash-in/wash-out period followed by a 12-month treatment period. Pharmacokinetic (PK) parameters were assessed in a sub-group of subjects.

Conditions

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Primary Immune Deficiency

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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IgPro20

Human Normal Immunoglobulin for Subcutaneous Administration (IgPro20) is a liquid formulation of normal human IgG at a concentration of 20% administered as a SC infusion at weekly intervals. The initial weekly dose was determined based on subjects' previous treatment. Dose adjustments could be performed during the wash-in/wash-out period at the discretion of the investigator.

Group Type EXPERIMENTAL

Human Normal Immunoglobulin for Subcutaneous Administration

Intervention Type BIOLOGICAL

Interventions

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Human Normal Immunoglobulin for Subcutaneous Administration

Intervention Type BIOLOGICAL

Other Intervention Names

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Hizentra

Eligibility Criteria

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Inclusion Criteria

* Male or female aged 2 to 75 years
* Subjects with primary humoral immunodeficiency, namely with a diagnosis of: CVID (Common Variable Immunodeficiency) as defined by PAGID (Pan-American Group for Immunodeficiency) and ESID (European Society for Immunodeficiencies) or XLA (X-linked Agammaglobulinemia)
* Written informed consent

Exclusion Criteria

* Newly diagnosed PID
* Evidence of an active serious infection at the time of screening (i.e., but not limited to: bacteremia/septicemia, pneumonia, fungal osteomyelitis)
* Malignancies of lymphoid cells such as lymphocytic leukemia, Non-Hodgkin's lymphoma and immunodeficiency with thymoma
* Known hyperprolinemia
* Hypoalbuminemia, protein-losing enteropathies, and any proteinuria
* Allergic reactions to immunoglobulins or other blood products
* Known antibodies to Immunoglobulin A (IgA)
* The subject is receiving steroids (oral and parenteral, daily ≥ 0.15 mg of prednisone equivalent/kg/day) or other systemic immunosuppressants
* Female who is pregnant, breast feeding or planning a pregnancy during the course of the study
* Participation in a study with an investigational product other than (IVIG) within 1 month prior to enrollment
* A positive result at screening on any of the following viral markers: Human Immunodeficiency Virus (HIV), Hepatitis C virus (HCV) and Hepatitis B virus (HBV)
* Aspartate aminotransferase (ASAT) or Alanine aminotransferase (ALAT) concentration \> 2.5 times the upper normal limit (UNL)
* Creatinine concentration \> 1.5 times the UNL
* Any condition that is likely to interfere with evaluation of the study drug or satisfactory conduct of the trial
Minimum Eligible Age

2 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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CSL Behring

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Richard L. Wasserman, MD, PhD

Role: PRINCIPAL_INVESTIGATOR

Dallas Allergy Immunology and Medical City Children's Hospital,

Locations

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Study Site

Los Angeles, California, United States

Site Status

Study Site

Los Angeles, California, United States

Site Status

Study Site

Centennial, Colorado, United States

Site Status

Study Site

North Palm Beach, Florida, United States

Site Status

Study Site

Atlanta, Georgia, United States

Site Status

Study Site

Fort Wayne, Indiana, United States

Site Status

Study Site

Indianapolis, Indiana, United States

Site Status

Study Site

Iowa City, Iowa, United States

Site Status

Study Site

St Louis, Missouri, United States

Site Status

Study Site

Newark, New Jersey, United States

Site Status

Study Site

New York, New York, United States

Site Status

Study Site

Philadelphia, Pennsylvania, United States

Site Status

Study Site

Dallas, Texas, United States

Site Status

Countries

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United States

References

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Hagan JB, Fasano MB, Spector S, Wasserman RL, Melamed I, Rojavin MA, Zenker O, Orange JS. Efficacy and safety of a new 20% immunoglobulin preparation for subcutaneous administration, IgPro20, in patients with primary immunodeficiency. J Clin Immunol. 2010 Sep;30(5):734-45. doi: 10.1007/s10875-010-9423-4. Epub 2010 May 8.

Reference Type RESULT
PMID: 20454851 (View on PubMed)

Wasserman RL, Melamed I, Nelson RP Jr, Knutsen AP, Fasano MB, Stein MR, Rojavin MA, Church JA. Pharmacokinetics of subcutaneous IgPro20 in patients with primary immunodeficiency. Clin Pharmacokinet. 2011 Jun;50(6):405-14. doi: 10.2165/11587030-000000000-00000.

Reference Type RESULT
PMID: 21553933 (View on PubMed)

Related Links

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Other Identifiers

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1458

Identifier Type: OTHER

Identifier Source: secondary_id

ZLB04_009CR

Identifier Type: -

Identifier Source: org_study_id

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