Open-label Trial of Leukine in Active Crohn's Disease

NCT ID: NCT00206700

Last Updated: 2013-12-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

378 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-02-28

Study Completion Date

2006-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to establish a safety profile sargramostim administered in 8 week cycles to adult patients with active Crohn's disease.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

On 29 May 2009, Bayer began transitioning the sponsorship of this trial to Genzyme. NOTE: This study was originally posted by sponsor Berlex, Inc. Berlex, Inc. was renamed to Bayer HealthCare, Inc.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Crohn Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Arm 1

Group Type EXPERIMENTAL

Sargramostim (Leukine)

Intervention Type DRUG

Open Label, 8 week cycle

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Sargramostim (Leukine)

Open Label, 8 week cycle

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

BAY86-5326

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Able to provide informed consent
* Participated in a previous study of sargramostim in Crohn's disease within the past 12 months
* Subjects who participated in protocols excluding concomitant steroid use:
* Must have moderately to severely active Crohn's disease at time of screening (CDAI score \>/= 220 points and less than or equal to 475 points)
* Must be receiving less than or equal to 40 mg prednisone (or equivalent) daily at time of screening if treated with corticosteroids between completing their previous sargramostim study and entry into this study and be able to taper to less than or equal to 7.5 mg daily within one treatment cycle
* Subjects who participated in Protocol 307501
* Must have active Crohn's disease (CDAI score \> 150 points and less than or equal to 450 points) if completely withdrawn from CS use
* Must be receiving less than or equal to 40 mg prednisone (or equivalent) daily at time of screening, be able to taper to less than or equal to 7.5 mg daily within 2 treatment cycles, and have a CDAI score less than or equal to 450 points if not completely withdrawn from CS use
* Have a negative serum pregnancy test within 2 weeks prior to receiving initial dose of sargramostim in female subjects of child-bearing potential (optional - may be waived by the investigator if the subject has had no interruption in contraception method since participation in the previous study)
* Agree to use of an adequate method of contraception throughout the study period for sexually-active males and females of childbearing potential
* Able to self-inject sargramostim or have a designee who can do so
* Able to comply with protocol requirements
* Have a negative stool exam if subject received a course of antibiotics since participation in the previous study

Exclusion Criteria

* Pregnant or breastfeeding female
* Need for gastrointestinal (GI) surgery for active GI bleeding, peritonitis, intestinal obstruction, or intra-abdominal or perianal abscess requiring surgical drainage
* Gastrointestinal surgery within the prior 6 months
* Symptoms of bowel obstruction or confirmed evidence of a clinically-significant stricture within the last 6 months that has not been surgically corrected
* Serum creatinine greater than or equal to 2.0 mg/dL
* Alkaline phosphatase (ALP), aspartate aminotransferase (AST), alanine aminotransferase (ALT), or total bilirubin greater or equal to 2X the upper limit of normal; hemoglobin (Hb) \< 8.0 gm/dL; platelet count greater than or equal to 800,000/mL; ANC less than or equal to 1,000/µL or \> 20,000/µL (the exclusion of subjects with ANC \> 20,000/µL applies only to entry into the first treatment cycle)
* Use of licensed/registered anti-tumor necrosis factor (TNF) therapy such as infliximab within 8 weeks prior to first dose of study drug in this trial
* Use of any of the following medications within 4 weeks prior to receiving the first dose of study drug: 6-mercaptopurine, azathioprine, cyclophosphamide, methotrexate, mycophenolate mofetil, tacrolimus, cyclosporine, or thalidomide
* Use of any experimental agent in a clinical trial since participating in a sargramostim trial
* History of allergy to yeast products or sargramostim
* Psychiatric illness or substance abuse that would interfere with ability to comply with protocol requirements or give informed consent
* Clinically important primary disease unrelated to Crohn's disease
* Prior exposure to natalizumab (Tysabri)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Genzyme, a Sanofi Company

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Medical Monitor

Role: STUDY_DIRECTOR

Genzyme, a Sanofi Company

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Birmingham, Alabama, United States

Site Status

Scottsdale, Arizona, United States

Site Status

Berkeley, California, United States

Site Status

Los Angeles, California, United States

Site Status

Orange, California, United States

Site Status

San Francisco, California, United States

Site Status

San Francisco, California, United States

Site Status

Tarzana, California, United States

Site Status

Aurora, Colorado, United States

Site Status

Englewood, Colorado, United States

Site Status

Lakewood, Colorado, United States

Site Status

Littleton, Colorado, United States

Site Status

Washington D.C., District of Columbia, United States

Site Status

Boca Raton, Florida, United States

Site Status

Clearwater, Florida, United States

Site Status

Gainesville, Florida, United States

Site Status

Gainesville, Florida, United States

Site Status

Hollywood, Florida, United States

Site Status

Jacksonville, Florida, United States

Site Status

Jacksonville, Florida, United States

Site Status

North Miami Beach, Florida, United States

Site Status

Winter Park, Florida, United States

Site Status

Atlanta, Georgia, United States

Site Status

Chicago, Illinois, United States

Site Status

Indianapolis, Indiana, United States

Site Status

Indianapolis, Indiana, United States

Site Status

Lexington, Kentucky, United States

Site Status

Louisville, Kentucky, United States

Site Status

Lake Charles, Louisiana, United States

Site Status

Metairie, Louisiana, United States

Site Status

Slidell, Louisiana, United States

Site Status

Annapolis, Maryland, United States

Site Status

Hagerstown, Maryland, United States

Site Status

Towson, Maryland, United States

Site Status

Boston, Massachusetts, United States

Site Status

Chesterfield, Michigan, United States

Site Status

Troy, Michigan, United States

Site Status

Plymouth, Minnesota, United States

Site Status

Mexico, Missouri, United States

Site Status

St Louis, Missouri, United States

Site Status

Billings, Montana, United States

Site Status

Lincoln, Nebraska, United States

Site Status

Lebanon, New Hampshire, United States

Site Status

Berlin, New Jersey, United States

Site Status

Great Neck, New York, United States

Site Status

Mineola, New York, United States

Site Status

New York, New York, United States

Site Status

Rochester, New York, United States

Site Status

Syracuse, New York, United States

Site Status

Asheville, North Carolina, United States

Site Status

Chapel Hill, North Carolina, United States

Site Status

Charlotte, North Carolina, United States

Site Status

Greensboro, North Carolina, United States

Site Status

Wilmington, North Carolina, United States

Site Status

Winston-Salem, North Carolina, United States

Site Status

Winston-Salem, North Carolina, United States

Site Status

Cincinnati, Ohio, United States

Site Status

Cincinnati, Ohio, United States

Site Status

Cincinnati, Ohio, United States

Site Status

Oklahoma City, Oklahoma, United States

Site Status

Tulsa, Oklahoma, United States

Site Status

Portland, Oregon, United States

Site Status

Portland, Oregon, United States

Site Status

Portland, Oregon, United States

Site Status

Hanover, Pennsylvania, United States

Site Status

Lancaster, Pennsylvania, United States

Site Status

Philadelphia, Pennsylvania, United States

Site Status

Pittsburgh, Pennsylvania, United States

Site Status

Pittsburgh, Pennsylvania, United States

Site Status

Sayre, Pennsylvania, United States

Site Status

Charleston, South Carolina, United States

Site Status

Columbia, South Carolina, United States

Site Status

Bristol, Tennessee, United States

Site Status

Jackson, Tennessee, United States

Site Status

Kingsport, Tennessee, United States

Site Status

Memphis, Tennessee, United States

Site Status

Memphis, Tennessee, United States

Site Status

Nashville, Tennessee, United States

Site Status

Nashville, Tennessee, United States

Site Status

Dallas, Texas, United States

Site Status

Irving, Texas, United States

Site Status

San Antonio, Texas, United States

Site Status

Salt Lake City, Utah, United States

Site Status

Charlottesville, Virginia, United States

Site Status

Chesapeake, Virginia, United States

Site Status

Danville, Virginia, United States

Site Status

Norfolk, Virginia, United States

Site Status

Richmond, Virginia, United States

Site Status

Bellevue, Washington, United States

Site Status

Seattle, Washington, United States

Site Status

Seattle, Washington, United States

Site Status

Seattle, Washington, United States

Site Status

Spokane, Washington, United States

Site Status

Walla Walla, Washington, United States

Site Status

Wenatchee, Washington, United States

Site Status

Madison, Wisconsin, United States

Site Status

Milwaukee, Wisconsin, United States

Site Status

Milwaukee, Wisconsin, United States

Site Status

Buenos Aires, Buenos Aires F.D., Argentina

Site Status

Garran, Australian Capital Territory, Australia

Site Status

Concord, New South Wales, Australia

Site Status

New Lambton Heights, New South Wales, Australia

Site Status

Sydney, New South Wales, Australia

Site Status

Sydney, New South Wales, Australia

Site Status

Brisbane, Queensland, Australia

Site Status

Brisbane, Queensland, Australia

Site Status

Adelaide, South Australia, Australia

Site Status

Launceston, Tasmania, Australia

Site Status

Ballarat, Victoria, Australia

Site Status

Frankston, Victoria, Australia

Site Status

Melbourne, Victoria, Australia

Site Status

Melbourne, Victoria, Australia

Site Status

Parkville, Victoria, Australia

Site Status

Prahran, Victoria, Australia

Site Status

Fremantle, Western Australia, Australia

Site Status

Penrith, , Australia

Site Status

Salvador, Estado de Bahia, Brazil

Site Status

Curitiba, Paraná, Brazil

Site Status

Rio de Janeiro, Rio de Janeiro, Brazil

Site Status

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

São Paulo, São Paulo, Brazil

Site Status

São Paulo, São Paulo, Brazil

Site Status

Edmonton, Alberta, Canada

Site Status

Edmonton, Alberta, Canada

Site Status

Kelowna, British Columbia, Canada

Site Status

Vancouver, British Columbia, Canada

Site Status

Vancouver, British Columbia, Canada

Site Status

Winnipeg, Manitoba, Canada

Site Status

Hamilton, Ontario, Canada

Site Status

London, Ontario, Canada

Site Status

Toronto, Ontario, Canada

Site Status

Toronto, Ontario, Canada

Site Status

Windsor, Ontario, Canada

Site Status

Montreal, Quebec, Canada

Site Status

Montreal, Quebec, Canada

Site Status

Montreal, Quebec, Canada

Site Status

Montreal, Quebec, Canada

Site Status

Québec, Quebec, Canada

Site Status

Milford, Auckland, New Zealand

Site Status

Auckland, , New Zealand

Site Status

Christchurch, , New Zealand

Site Status

Hamilton, , New Zealand

Site Status

Lipetsk, Russia, Russia

Site Status

Moskva, Russia, Russia

Site Status

Samara, Russia, Russia

Site Status

Moscow, , Russia

Site Status

Moscow, , Russia

Site Status

Moskva, , Russia

Site Status

Volgograd, , Russia

Site Status

Basel, Basel, Switzerland

Site Status

Bern, Canton of Bern, Switzerland

Site Status

Lausanne, Canton of Vaud, Switzerland

Site Status

Donetsk, , Ukraine

Site Status

Kharkiv, , Ukraine

Site Status

Kiev, , Ukraine

Site Status

Lviv, , Ukraine

Site Status

Vinnitsa, , Ukraine

Site Status

Bristol, Avon, United Kingdom

Site Status

London, Greater London, United Kingdom

Site Status

Salford, Greater Manchester, United Kingdom

Site Status

Edinburgh, Lothian, United Kingdom

Site Status

Liverpool, Merseyside, United Kingdom

Site Status

Harrow, Middlesex, United Kingdom

Site Status

Cardiff, South Glamorgan, United Kingdom

Site Status

Newcastle upon Tyne, Tyne and Wear, United Kingdom

Site Status

London, , United Kingdom

Site Status

Sheffield, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Brazil Canada New Zealand Russia Switzerland Ukraine United Kingdom

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

91274

Identifier Type: -

Identifier Source: secondary_id

Novel 5

Identifier Type: -

Identifier Source: secondary_id

307340

Identifier Type: -

Identifier Source: org_study_id

NCT00185471

Identifier Type: -

Identifier Source: nct_alias