Phase II Study of IL-11 (Neumega) in Von Willebrand Disease

NCT ID: NCT00151125

Last Updated: 2016-05-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

12 participants

Study Classification

INTERVENTIONAL

Study Start Date

2004-07-31

Study Completion Date

2007-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study is testing the use of rhIL-11 (recombinant interleukin 11, Neumega) in individuals with Von Willebrand disease. The purpose is to evaluate:

1. if rhIL-11 corrects VWF (Von Willebrand Factor) levels to normal
2. if rhIL-11 and DDAVP together will boost VWF levels even higher
3. the onset, peak, and duration of rhIL-11 effect
4. if rhIL-11 is safe in individuals with Von Willebrand Disease

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is a prospective, single center, open-label, escalating dose Phase II comparison study of interleukin-11 (rhIL-11, Neumega) in subjects with type 1 Von Willebrand Disease (VWD).

The purpose is to establish the clinical safety and hemostatic efficacy of rhIL-11 in individuals with type 1 Von Willebrand disease.

Study subjects will include the following subjects:

1. age \>= 18 years of age
2. diagnosis of VWD confirmed by: 2a) at least 2 of 4 abnormal vWD-related coagulation tests; 2b) a past bleeding history

A total of 10-16 subjects are anticipated to be enrolled and complete the study. The specific aims of the study are:

1. to compare the hemostatic efficacy of three escalating doses of rhIL-11
2. to determine the biologic effects of rhIL-11
3. to determine whether DDAVP, when given after the seventh daily dose of rhIL-11, enhances hemostatic efficacy or rhIL-11
4. to compare the safety of three escalating doses of rhIL-11

Efficacy will be based on the number and percent increase of VWD-related coagulation tests into the normal range, or at least to 2-3 times baseline.

Safety will be based on the number and frequency of adverse reactions, including fever, headache, fatigue, arthralgias, myalgias, fluid retention, and edema.

The study will last up to 4 weeks per subject, and for 24 months for the entire study.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Von Willebrand Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

C

rhIL-11 (Interleukin-11, Neumega) 10 mg/kg subcutaneously daily for 7 days

Group Type EXPERIMENTAL

recombinant interleukin-11

Intervention Type DRUG

10 mcg/kg subcutaneously daily for 7 days

A

rhIL-11 (Interleukin-11, Neumega) 25 mcg/kg subcutaneously daily for 7 days

Group Type EXPERIMENTAL

recombinant interleukin-11

Intervention Type DRUG

25 mcg/kg subcutaneously daily for seven days

B

rhIL-11 (interleukin-11, Neumega) 50 mcg/kg subcutaneously daily for 7 days

Group Type EXPERIMENTAL

recombinant interleukin-11

Intervention Type DRUG

50 mcg/kg subcutaneously daily for 7 days

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

recombinant interleukin-11

25 mcg/kg subcutaneously daily for seven days

Intervention Type DRUG

recombinant interleukin-11

50 mcg/kg subcutaneously daily for 7 days

Intervention Type DRUG

recombinant interleukin-11

10 mcg/kg subcutaneously daily for 7 days

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

rhIL-11, Neumega rhIL-11, Neumega rhIL-11, Neumega

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Males and females 18 years of age or older
* Confirmed VWD by 2 of 4 VWD coagulation tests abnormal
* A past bleeding history
* No hormone, oral contraceptive, estrogen use in past 8 weeks
* Willingness to have blood drawn
* Willingness to sign informed consent

Exclusion Criteria

* Presence of other bleeding disorder, e.g. acquired VWD, thrombocytopenia
* Use of estrogens, hormones, oral contraceptives in past 8 weeks
* Use of immunomodulatory or experimental drugs or diuretics
* Pregnant or lactating women
* Past cardiac disease, congestive failure, arrhythmia (e.g. atrial fibrillation, atrial flutter), hypertension, MI, stroke, or thrombosis
* Past allergic reaction to Neumega or DDAVP
* Surgery within the past 8 weeks
* Inability to comply with study protocol requirements
* Concomitant use of antiplatelet drugs, anticoagulants, dextran, aspirin, or NSAIDs
* Treatment with DDAVP, cryoprecipitate, whole blood, plasma, and plasma derivatives containing FVIII, VWF within 5 days of study
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Wyeth is now a wholly owned subsidiary of Pfizer

INDUSTRY

Sponsor Role collaborator

University of North Carolina

OTHER

Sponsor Role collaborator

University of Pittsburgh

OTHER

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Margaret Ragni

Professor of Medicine

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Margaret V. Ragni, MD, MPH

Role: PRINCIPAL_INVESTIGATOR

University of Pittsburgh

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Hemophilia Center of Western Pennsylvania and General Clinical Research Center

Pittsburgh, Pennsylvania, United States

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

0403006

Identifier Type: OTHER

Identifier Source: secondary_id

0403006

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Low VW Activity in Adolescent HMB
NCT02933411 ACTIVE_NOT_RECRUITING
rVWF IN PROPHYLAXIS
NCT02973087 COMPLETED PHASE3