Study of BAY43-9006 in Patients With Unresectable and/or Metastatic Renal Cell Cancer

NCT ID: NCT00073307

Last Updated: 2014-02-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

903 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-11-30

Study Completion Date

2010-04-30

Brief Summary

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The purpose of this study is to evaluate safety, efficacy (including quality of life), and pharmacokinetics of BAY43-9006 when added to Best Supportive Care in patients with unresectable and/or metastatic renal cell cancer, who have received one prior systemic regimen for advanced disease.

Detailed Description

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Overall Survival (OS), Patient-reported outcome (PRO)

Conditions

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Carcinoma, Renal Cell

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Sorafenib (Nexavar, BAY43-9006)

Sorafenib was to be orally administered as 2 x 200 mg tablets bid (twice daily). Dose modification due to toxicity was permitted.

Group Type EXPERIMENTAL

Sorafenib (Nexavar, BAY43-9006)

Intervention Type DRUG

Multi Kinase Inhibitor

Placebo

Placebo tablets matching in appearance were to be orally administered twice a day.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo

Interventions

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Sorafenib (Nexavar, BAY43-9006)

Multi Kinase Inhibitor

Intervention Type DRUG

Placebo

Placebo

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Patients with unresectable and/or metastatic, measurable renal cell carcinoma histologically or cytologically documented
* Patients must have had one prior systemic therapy for advanced disease, which was completed at least 30 days but no longer than 8 months prior to randomization
* Patients who have at least one uni-dimensional measurable lesion by CT-scan or MRI according to Response Evaluation Criteria in Solid Tumors (RECIST)
* Patients who have an Eastern Co-operative Oncology Group (ECOG) performance status of 0 or 1
* Patients who have adequate coagulation, liver and kidney functions

Exclusion Criteria

* Patients with rare subtypes of renal cell carcinoma (RCC) such as pure papillary cell tumors, mixed tumor containing predominantly sarcomatoid cells, Bellini carcinoma, medullary carcinoma, or chromophobe oncocytic tumors
* Previous malignancy (except for cervical carcinoma in situ, adequately treated basal cell carcinoma,or superficial bladder tumors, or other malignancies curatively treated \> 2 years prior to entry
* Cardiac arrhythmias requiring anti-arrhythmics, symptomatic coronary artery disease or ischemia or congestive heart failure
* Patients with a history of human immunodeficiency virus (HIV) infection or chronic hepatitis B or C
* Patients with a history or presence of metastatic brain or meningeal tumors
* Patients with seizure disorder requiring medication (such as anti-epileptics)
* History of organ allograft or bone marrow transplant of stem cell rescue
* Patients who are pregnant or breast-feeding Women of childbearing potential must have a negative pregnancy test prior to drug administration. Both men and women enrolled in this trial must use adequate birth control
* Patients who have three or more of the following:

* ECOG performance status greater than or equal to 2,
* Abnormally high lactate dehydrogenase,
* Abnormally high serum hemoglobin,
* Abnormally high corrected serum calcium,
* Absence of prior nephrectomy
* Excluded therapies and medications, previous and concomitant:

* Concurrent anti-cancer chemotherapy, immunotherapy or hormonal therapy except biphosphonates
* Significant surgery with 4 weeks of start of study
* Investigational drug therapy during or within 30 days
* Concomitant treatment with rifampin or St. John's Wort
* Prior use of Raf-kinase inhibitors (RKI), MEK or Farnesyl transferase inhibitors
* Prior use of Bevacizumab, and all other drugs (investigational or licensed) that target VEGF/VEGF receptors
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role collaborator

Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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Sutton, Surrey, United Kingdom

Site Status

Newcastle upon Tyne, Tyne and Wear, United Kingdom

Site Status

Birmingham, West Midlands, United Kingdom

Site Status

Lviv, , Ukraine

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Poltava, , Ukraine

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Manchester, Manchester, United Kingdom

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Northwood, Middlesex, United Kingdom

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Cardiff, South Glamorgan, United Kingdom

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Glasgow, Stratchclyde, United Kingdom

Site Status

Tucson, Arizona, United States

Site Status

Los Angeles, California, United States

Site Status

Los Angeles, California, United States

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Sacramento, California, United States

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Aurora, Colorado, United States

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Hamden, Connecticut, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Louisville, Kentucky, United States

Site Status

Lafayette, Louisiana, United States

Site Status

Frederick, Maryland, United States

Site Status

Boston, Massachusetts, United States

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Minneapolis, Minnesota, United States

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Columbia, Missouri, United States

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St Louis, Missouri, United States

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Brooklyn, New York, United States

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New York, New York, United States

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The Bronx, New York, United States

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Canton, Ohio, United States

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Cleveland, Ohio, United States

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Dayton, Ohio, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Spartanburg, South Carolina, United States

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Dallas, Texas, United States

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Laredo, Texas, United States

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San Antonio, Texas, United States

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Salt Lake City, Utah, United States

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Richmond, Virginia, United States

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Seattle, Washington, United States

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Milwaukee, Wisconsin, United States

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Rosario, Santa Fe Province, Argentina

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Santa Fé, Santa Fe Province, Argentina

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Capital Federal-Buenos Aires, , Argentina

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Mendoza, , Argentina

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Garran, Australian Capital Territory, Australia

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Camperdown, New South Wales, Australia

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Liverpool, New South Wales, Australia

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Westmead, New South Wales, Australia

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Heidelberg, Victoria, Australia

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Wodonga, Victoria, Australia

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Bruxelles - Brussel, , Belgium

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Bruxelles - Brussel, , Belgium

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Curitiba, Paraná, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Edmonton, Alberta, Canada

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Hamilton, Ontario, Canada

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London, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Santiago, , Chile

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Bordeaux, , France

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Caen, , France

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Lille, , France

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Lyon, , France

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Marseille, , France

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Nantes, , France

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Paris, , France

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Strasbourg, , France

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Toulouse, , France

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Villejuif, , France

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Mannheim, Baden-Wurttemberg, Germany

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Ulm, Baden-Wurttemberg, Germany

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München, Bavaria, Germany

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Regensburg, Bavaria, Germany

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Hamburg, City state of Hamburg, Germany

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Darmstadt, Hesse, Germany

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Frankfurt am Main, Hesse, Germany

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Düsseldorf, North Rhine-Westphalia, Germany

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Dresden, Saxony, Germany

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Berlin, State of Berlin, Germany

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Budapest, , Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Zalaegerszeg, , Hungary

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Haifa, , Israel

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Tel Aviv, , Israel

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Milan, , Italy

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Modena, , Italy

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Pavia, , Italy

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Perugia, , Italy

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Reggio Emilia, , Italy

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Roma, , Italy

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Nijmegen, , Netherlands

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Gdansk, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Poznan, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Barnaul, , Russia

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Kazan', , Russia

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Kirov, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Obninsk, , Russia

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Saint Petersburg, , Russia

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Bloemfontein, Freestate, South Africa

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Pretoria, Gauteng, South Africa

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Durban, KwaZulu-Natal, South Africa

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Cape Town, Western Cape, South Africa

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Barcelona, Barcelona, Spain

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Cruces/Barakaldo, Bilbao, Spain

Site Status

Madrid, Madrid, Spain

Site Status

Valencia, Valencia, Spain

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Donetsk, , Ukraine

Site Status

Kharkiv, , Ukraine

Site Status

Kiev, , Ukraine

Site Status

Countries

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United States Argentina Australia Belgium Brazil Canada Chile France Germany Hungary Israel Italy Netherlands Poland Russia South Africa Spain Ukraine United Kingdom

References

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Antoun S, Birdsell L, Sawyer MB, Venner P, Escudier B, Baracos VE. Association of skeletal muscle wasting with treatment with sorafenib in patients with advanced renal cell carcinoma: results from a placebo-controlled study. J Clin Oncol. 2010 Feb 20;28(6):1054-60. doi: 10.1200/JCO.2009.24.9730. Epub 2010 Jan 19.

Reference Type RESULT
PMID: 20085939 (View on PubMed)

Bellmunt J, Eisen T, Fishman M, Quinn D. Experience with sorafenib and adverse event management. Crit Rev Oncol Hematol. 2011 Apr;78(1):24-32. doi: 10.1016/j.critrevonc.2010.03.006. Epub 2010 Apr 18.

Reference Type RESULT
PMID: 20399677 (View on PubMed)

Massard C, Zonierek J, Gross-Goupil M, Fizazi K, Szczylik C, Escudier B. Incidence of brain metastases in renal cell carcinoma treated with sorafenib. Ann Oncol. 2010 May;21(5):1027-31. doi: 10.1093/annonc/mdp411. Epub 2009 Oct 22.

Reference Type RESULT
PMID: 19850637 (View on PubMed)

Negrier S, Jager E, Porta C, McDermott D, Moore M, Bellmunt J, Anderson S, Cihon F, Lewis J, Escudier B, Bukowski R. Efficacy and safety of sorafenib in patients with advanced renal cell carcinoma with and without prior cytokine therapy, a subanalysis of TARGET. Med Oncol. 2010 Sep;27(3):899-906. doi: 10.1007/s12032-009-9303-z. Epub 2009 Sep 12.

Reference Type RESULT
PMID: 19757215 (View on PubMed)

Pena C, Lathia C, Shan M, Escudier B, Bukowski RM. Biomarkers predicting outcome in patients with advanced renal cell carcinoma: Results from sorafenib phase III Treatment Approaches in Renal Cancer Global Evaluation Trial. Clin Cancer Res. 2010 Oct 1;16(19):4853-63. doi: 10.1158/1078-0432.CCR-09-3343. Epub 2010 Jul 22.

Reference Type RESULT
PMID: 20651059 (View on PubMed)

Escudier B, Eisen T, Stadler WM, Szczylik C, Oudard S, Staehler M, Negrier S, Chevreau C, Desai AA, Rolland F, Demkow T, Hutson TE, Gore M, Anderson S, Hofilena G, Shan M, Pena C, Lathia C, Bukowski RM. Sorafenib for treatment of renal cell carcinoma: Final efficacy and safety results of the phase III treatment approaches in renal cancer global evaluation trial. J Clin Oncol. 2009 Jul 10;27(20):3312-8. doi: 10.1200/JCO.2008.19.5511. Epub 2009 May 18.

Reference Type RESULT
PMID: 19451442 (View on PubMed)

Eisen T, Oudard S, Szczylik C, Gravis G, Heinzer H, Middleton R, Cihon F, Anderson S, Shah S, Bukowski R, Escudier B; TARGET Study Group. Sorafenib for older patients with renal cell carcinoma: subset analysis from a randomized trial. J Natl Cancer Inst. 2008 Oct 15;100(20):1454-63. doi: 10.1093/jnci/djn319. Epub 2008 Oct 7.

Reference Type RESULT
PMID: 18840822 (View on PubMed)

Bukowski R, Cella D, Gondek K, Escudier B; Sorafenib TARGETs Clinical Trial Group. Effects of sorafenib on symptoms and quality of life: results from a large randomized placebo-controlled study in renal cancer. Am J Clin Oncol. 2007 Jun;30(3):220-7. doi: 10.1097/01.coc.0000258732.80710.05.

Reference Type RESULT
PMID: 17551296 (View on PubMed)

Escudier B, Eisen T, Stadler WM, Szczylik C, Oudard S, Siebels M, Negrier S, Chevreau C, Solska E, Desai AA, Rolland F, Demkow T, Hutson TE, Gore M, Freeman S, Schwartz B, Shan M, Simantov R, Bukowski RM; TARGET Study Group. Sorafenib in advanced clear-cell renal-cell carcinoma. N Engl J Med. 2007 Jan 11;356(2):125-34. doi: 10.1056/NEJMoa060655.

Reference Type RESULT
PMID: 17215530 (View on PubMed)

Kane RC, Farrell AT, Saber H, Tang S, Williams G, Jee JM, Liang C, Booth B, Chidambaram N, Morse D, Sridhara R, Garvey P, Justice R, Pazdur R. Sorafenib for the treatment of advanced renal cell carcinoma. Clin Cancer Res. 2006 Dec 15;12(24):7271-8. doi: 10.1158/1078-0432.CCR-06-1249.

Reference Type RESULT
PMID: 17189398 (View on PubMed)

Lamuraglia M, Escudier B, Chami L, Schwartz B, Leclere J, Roche A, Lassau N. To predict progression-free survival and overall survival in metastatic renal cancer treated with sorafenib: pilot study using dynamic contrast-enhanced Doppler ultrasound. Eur J Cancer. 2006 Oct;42(15):2472-9. doi: 10.1016/j.ejca.2006.04.023. Epub 2006 Sep 11.

Reference Type RESULT
PMID: 16965911 (View on PubMed)

Quintanilha JCF, Geyer S, Etheridge AS, Racioppi A, Hammond K, Crona DJ, Pena CE, Jacobson SB, Marmorino F, Rossini D, Cremolini C, Sanoff HK, Abou-Alfa GK, Innocenti F. KDR genetic predictor of toxicities induced by sorafenib and regorafenib. Pharmacogenomics J. 2022 Dec;22(5-6):251-257. doi: 10.1038/s41397-022-00279-3. Epub 2022 Apr 28.

Reference Type DERIVED
PMID: 35484400 (View on PubMed)

Quintanilha JCF, Racioppi A, Wang J, Etheridge AS, Denning S, Pena CE, Skol AD, Crona DJ, Lin D, Innocenti F. PIK3R5 genetic predictors of hypertension induced by VEGF-pathway inhibitors. Pharmacogenomics J. 2022 Feb;22(1):82-88. doi: 10.1038/s41397-021-00261-5. Epub 2021 Nov 13.

Reference Type DERIVED
PMID: 34775477 (View on PubMed)

Other Identifiers

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11213

Identifier Type: -

Identifier Source: org_study_id

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