Safety of ICL670 vs. Deferoxamine in Sickle Cell Disease Patients With Iron Overload Due to Blood Transfusions

NCT ID: NCT00067080

Last Updated: 2017-08-22

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

195 participants

Study Classification

INTERVENTIONAL

Study Start Date

2003-05-31

Brief Summary

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The purpose of this study is to determine if the new orally active iron chelator, ICL670, is as safe as deferoxamine in preventing accumulation of iron in the body while a patient is undergoing repeated blood transfusions.

Detailed Description

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Patients who require repeated blood transfusions accumulate iron in the body as blood cells contain iron and there is no natural body mechanism to eliminate it. After a while the iron levels get high enough to be toxic to the body. The current therapy of choice is deferoxamine which does a good job of removing excess iron, but is difficult to administer. Deferoxamine requires subcutaneous (under the skin) infusions over 4 to 8 hours nightly 3 to 7 nights per week. In addition to the need to wear an infusion pump nightly, adverse reactions around the site of the injection are frequent.

Conditions

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Anemia, Sickle Cell

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ICL670 + deferoxamine

Group Type EXPERIMENTAL

ICL670, deferoxamine

Intervention Type DRUG

Interventions

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ICL670, deferoxamine

Intervention Type DRUG

Other Intervention Names

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deferasirox

Eligibility Criteria

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Inclusion Criteria

* Age greater than or equal to 2 years
* Sickle cell disease patients already treated with or suitable for treatment with deferoxamine 20 to 40 mg/kg/day
* Serum ferritin greater than 1000 mg/ml
* Liver iron content greater than 2 mg iron/g dw assessed by means of superconducting quantum interference device (SQUID) for patients who receive simple transfusions and greater than 5 mg iron/ g dw for patients who receive exchange transfusions or who have a history of intermittent blood transfusion.
* Regular transfusion aimed at maintaining % Hb A above 50% or a previous history of simple transfusion being the recipient of at least 20 units of packed red blood cells.

Exclusion Criteria

* Chronic anemias other than sickle cell disease
* Documented toxicity to deferoxamine
* Elevated liver enzymes in the year preceeding enrollment
* Active hepatitis B or hepatitis C
* HIV seropositivity
* Elevated serum creatinine or significant proteinuria
* History of nephrotic syndrome
* Uncontrolled systemic hypertension
* Fever and other signs/symptoms of infection within 10 days prior to the start of the study
* Presence of clinically relevant cataract or previous history of clinically relevant ocular toxicity related to iron chelation
* Second or third degree AV block, clinically relevant Q-T interval prolongation, or patients requiring digoxin or other drugs that prolong the Q-T interval (other than beta-adrenergic receptor blocking agents).
* Diseases (cardiovascular, renal, hepatic, etc.) that would prevent the patient from undergoing any of the treatment options
* Psychiatric or addictive disorders that would prevent the patient from giving informed consent
* History of drug or alcohol abuse within the 12 months prior to the study
* Pregnant or breast feeding patients
* Patients treated with systemic investigational drugs within 4 weeks or topical investigational drugs within 7 days before the start of the study
* Patients who require concomitant therapy with hydroxyurea
* Any surgical or medical condition that might significantly alter the absorption, distribution, metabolism or excretion of any drug, such as gastrointestinal disease or major surgery, renal disease, difficulty voiding or urinary obstruction, or impaired pancreatic function
* Non-compliant or unreliable patients
* Patients unable to undergo any study procedures such as the hearing or eye tests, or the liver echocardiography
* Patients unable to undergo SQUID examination
Minimum Eligible Age

2 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Novartis Pharmaceuticals

Principal Investigators

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Novartis Pharmaceuticals

Role: STUDY_DIRECTOR

Novartis Pharmaceuticals

Locations

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U. of S. Alabama Medical Center

Mobile, Alabama, United States

Site Status

Loma Linda University Medical Center

Loma Linda, California, United States

Site Status

Children's Hospital Los Angeles

Los Angeles, California, United States

Site Status

Children's Hospital & Research Center

Oakland, California, United States

Site Status

Colorado Sickle Cell Treatment and Research Center

Denver, Colorado, United States

Site Status

Howard University Hospital

Washington D.C., District of Columbia, United States

Site Status

Tampa Children's Hospital at St Joseph's

Tampa, Florida, United States

Site Status

Georgia Comprehensive Sickle cell Center, Grady Hospital

Atlanta, Georgia, United States

Site Status

Adult Sickle Cell Clinic, Medical College of Georgia

Augusta, Georgia, United States

Site Status

University of Illinois at Chicago

Chicago, Illinois, United States

Site Status

Children's Memorial Hospital

Chicago, Illinois, United States

Site Status

Tulane University Sickle Cell Center

New Orleans, Louisiana, United States

Site Status

Children's Hospital, Department of Hematology/Oncology

New Orleans, Louisiana, United States

Site Status

Children's Hospital Boston, Division of Hematology/Oncology

Boston, Massachusetts, United States

Site Status

Boston Medical Center

Boston, Massachusetts, United States

Site Status

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

NY Methodist Hospital

Brooklyn, New York, United States

Site Status

Weill Medical College of Cornell University

New York, New York, United States

Site Status

U. Of Rochester Medical Center

Rochester, New York, United States

Site Status

Sickle Cell Center, Montefiore Hospital

The Bronx, New York, United States

Site Status

Wake Forest University School of Medicine

Winston-Salem, North Carolina, United States

Site Status

Barrett Center, University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

James Cancer Hospital

Columbus, Ohio, United States

Site Status

Penn State Milton S Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Liberty Hematology Oncology Center

Columbia, South Carolina, United States

Site Status

Palmetto Health Clinical Trials

Columbia, South Carolina, United States

Site Status

Santee Hematology/Oncology

Sumter, South Carolina, United States

Site Status

Baylor College of Medicine

Houston, Texas, United States

Site Status

Texas Children's Hospital/Baylor College of Medicine

Houston, Texas, United States

Site Status

Scott and White Memorial Hospital & Clinics

Temple, Texas, United States

Site Status

Children's Hospital of the King's Daughter

Norfolk, Virginia, United States

Site Status

Countries

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United States

References

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Vichinsky E, Onyekwere O, Porter J, Swerdlow P, Eckman J, Lane P, Files B, Hassell K, Kelly P, Wilson F, Bernaudin F, Forni GL, Okpala I, Ressayre-Djaffer C, Alberti D, Holland J, Marks P, Fung E, Fischer R, Mueller BU, Coates T; Deferasirox in Sickle Cell Investigators. A randomised comparison of deferasirox versus deferoxamine for the treatment of transfusional iron overload in sickle cell disease. Br J Haematol. 2007 Feb;136(3):501-8. doi: 10.1111/j.1365-2141.2006.06455.x.

Reference Type RESULT
PMID: 17233848 (View on PubMed)

Related Links

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https://www.ncbi.nlm.nih.gov/pubmed/17233848

Results for CICL670A0109 from the Novartis Clinical Trials website

Other Identifiers

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CICL670A0109

Identifier Type: -

Identifier Source: org_study_id

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