Phase II Study of Growth Hormone in Children With Cystic Fibrosis

NCT ID: NCT00016445

Last Updated: 2008-09-09

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

40 participants

Study Classification

INTERVENTIONAL

Study Start Date

2001-02-28

Brief Summary

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OBJECTIVES: I. Determine the effect of growth hormone on height, height velocity, body weight, and lean body mass in patients with cystic fibrosis.

II. Determine the effect of growth hormone on pulmonary function in these patients.

III. Determine the impact of this drug on the quality of life in these patients.

IV. Determine if the clinical response from this drug is sustained in these patients.

Detailed Description

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PROTOCOL OUTLINE: This is a randomized, multicenter study. Patients are randomized to 1 of 2 treatment arms.

Arm I: Patients receive growth hormone subcutaneously (SC) daily for 1 year during the first year only.

Arm II: Patients receive growth hormone SC daily for 1 year during the second year only.

Quality of life is assessed at baseline and then every 6 months for 2 years.

Conditions

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Cystic Fibrosis

Keywords

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cardiovascular and respiratory diseases cystic fibrosis disease-related problem/condition genetic diseases and dysmorphic syndromes quality of life rare disease

Study Design

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Primary Study Purpose

TREATMENT

Interventions

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growth hormone

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

PROTOCOL ENTRY CRITERIA:

--Disease Characteristics--

* Diagnosis of prepubertal cystic fibrosis
* No colonization by Burkholderia cepacia

--Prior/Concurrent Therapy--

* No prior or concurrent insulin requirement

--Patient Characteristics--

* Hematopoietic: No hematologic disease
* Hepatic: No liver disease
* Renal: No kidney disease
* Pulmonary: Must be able to perform pulmonary function testing
* Other: No history of diabetes Must be less than 25% of normal height and/or weight for age and sex
Minimum Eligible Age

5 Years

Maximum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Utah

OTHER

Sponsor Role lead

Principal Investigators

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Dana S. Hardin

Role: STUDY_CHAIR

Southwest Medical Center at Dallas

Locations

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Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status

Children's Hospital of Orange County

Orange, California, United States

Site Status

James Whitcomb Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status

Washington University

St Louis, Missouri, United States

Site Status

Children's Medical Center - Dayton

Dayton, Ohio, United States

Site Status

T.L. Carey, M.D. and Associates

Tulsa, Oklahoma, United States

Site Status

Southwest Medical Center at Dallas

Dallas, Texas, United States

Site Status

Cook Children's Medical Center - Fort Worth

Fort Worth, Texas, United States

Site Status

Primary Children's Medical Center

Salt Lake City, Utah, United States

Site Status

Countries

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United States

Other Identifiers

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UUSOM-IRB-7797-00

Identifier Type: -

Identifier Source: secondary_id

GENENTECH-UUSOM-IRB-7797-00

Identifier Type: -

Identifier Source: secondary_id

199/15806

Identifier Type: -

Identifier Source: org_study_id