Pentosan Polysulfate in Treating Patients With Gastrointestinal Disturbance Caused by Radiation Therapy

NCT ID: NCT00003825

Last Updated: 2020-10-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

174 participants

Study Classification

INTERVENTIONAL

Study Start Date

1999-06-30

Brief Summary

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RATIONALE: Pentosan polysulfate may be effective in treating side effects of radiation therapy to the abdomen or pelvis. It is not yet known whether pentosan polysulfate is more effective than no further therapy for treating gastrointestinal disturbance caused by previous radiation therapy.

PURPOSE: Randomized phase III trial to determine the effectiveness of pentosan polysulfate in treating patients who have inflammation of the rectum, diarrhea, or blood in stools caused by previous radiation therapy to the abdomen and pelvis.

Detailed Description

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OBJECTIVES: I. Evaluate the efficacy of pentosan polysulfate in patients with gastrointestinal tract sequelae after radiotherapy to the abdomen and pelvis. II. Determine the toxic effects of this drug in these patients. III. Determine the effect of this drug on symptoms and quality of life of these patients.

OUTLINE: This is a randomized study. Patients are randomized to 1 of 2 treatment arms. Arm I: Patients receive oral pentosan polysulfate three times a day for 2-6 months. Arm II: Patients receive oral placebo three times a day for 2-6 months. Both arms: Patients may receive retreatment for two months if symptoms return and last for at least 2 weeks. Quality of life is assessed before treatment, and at each follow up visit. Patients are followed every 2 months for 6 months, then every 3 months for 18 months, then annually for 3 years.

PROJECTED ACCRUAL: A total of 174 patients will be accrued for this study within 3 years.

Conditions

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Diarrhea Radiation Enteritis

Study Design

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Allocation Method

RANDOMIZED

Primary Study Purpose

SUPPORTIVE_CARE

Interventions

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pentosan polysulfate sodium

Intervention Type DRUG

quality-of-life assessment

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS: Must have received prior radiotherapy to the abdomen and pelvis and now have radiation related gastrointestinal symptoms (which were not present before the radiotherapy and/or attributed to other causes) Proctitis Diarrhea Melena (blood in stools) Severity of symptoms classified as grade 1, 2, or 3

PATIENT CHARACTERISTICS: Age: Any age Performance status: Not specified Life expectancy: Not specified Hematopoietic: Not specified Hepatic: Not specified Renal: Not specified Other: No bleeding ulcers No bleeding diathesis

PRIOR CONCURRENT THERAPY: Biologic therapy: Not specified Chemotherapy: At least 1 month since prior chemotherapy No concurrent chemotherapy Endocrine therapy: Concurrent hormonal therapy for prostate cancer allowed Radiotherapy: See Disease Characteristics At least 4 weeks since prior radiotherapy Surgery: No prior bowel resection At least 3 weeks since prior surgery Other: No concurrent anticoagulation therapy (except aspirin)
Minimum Eligible Age

0 Years

Maximum Eligible Age

120 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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National Cancer Institute (NCI)

NIH

Sponsor Role collaborator

Radiation Therapy Oncology Group

NETWORK

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Miljenko V. Pilepich, MD

Role: STUDY_CHAIR

Saint Joseph Mercy Cancer Center

Locations

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Methodist Cancer Center - Omaha

Omaha, Nebraska, United States

Site Status

Nebraska Health System

Omaha, Nebraska, United States

Site Status

University of Alabama Comprehensive Cancer Center

Birmingham, Alabama, United States

Site Status

Comprehensive Cancer Institute of Huntsville

Huntsville, Alabama, United States

Site Status

Huntsville Hospital System

Huntsville, Alabama, United States

Site Status

Mobile Infirmary Medical Center

Mobile, Alabama, United States

Site Status

Urology Associates - Mobile AL

Mobile, Alabama, United States

Site Status

MBCCOP - University of South Alabama

Mobile, Alabama, United States

Site Status

Alabama Oncology, LLC

Montgomery, Alabama, United States

Site Status

Radiation Oncology Associates of West Alabama

Tuscaloosa, Alabama, United States

Site Status

Providence Cancer Therapy Center

Anchorage, Alaska, United States

Site Status

Arizona Cancer Center

Tucson, Arizona, United States

Site Status

Mount Diablo Medical Center

Concord, California, United States

Site Status

California Cancer Center

Fresno, California, United States

Site Status

Saint Agnes Cancer Center

Fresno, California, United States

Site Status

Glendale Memorial Hospital and Health Center

Glendale, California, United States

Site Status

Sutter Health Western Division Cancer Research Group

Greenbrae, California, United States

Site Status

University of California San Diego Cancer Center

La Jolla, California, United States

Site Status

Loma Linda University Medical Center

Loma Linda, California, United States

Site Status

Veterans Affairs Medical Center - Long Beach

Long Beach, California, United States

Site Status

Kaiser Permanente Medical Center - Los Angeles

Los Angeles, California, United States

Site Status

USC/Norris Comprehensive Cancer Center

Los Angeles, California, United States

Site Status

Jonsson Comprehensive Cancer Center, UCLA

Los Angeles, California, United States

Site Status

Beckman Research Institute, City of Hope

Los Angeles, California, United States

Site Status

CCOP - Bay Area Tumor Institute

Oakland, California, United States

Site Status

Cancer Care Center

Pomona, California, United States

Site Status

Radiation Oncology Center - Sacramento

Sacramento, California, United States

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Radiation Medical Group, Inc.

San Diego, California, United States

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UCSF Cancer Center and Cancer Research Institute

San Francisco, California, United States

Site Status

O'Connor Hospital

San Jose, California, United States

Site Status

CCOP - Santa Rosa Memorial Hospital

Santa Rosa, California, United States

Site Status

Stanford University

Stanford, California, United States

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Memorial Hospital Cancer Center

Colorado Springs, Colorado, United States

Site Status

University of Colorado Cancer Center

Denver, Colorado, United States

Site Status

Bridgeport Hospital

Bridgeport, Connecticut, United States

Site Status

Whittingham Cancer Center

Norwalk, Connecticut, United States

Site Status

CCOP - Christiana Care Health Services

Wilmington, Delaware, United States

Site Status

Walter Reed Army Medical Center

Washington D.C., District of Columbia, United States

Site Status

Lykes Center for Radiation Therapy

Clearwater, Florida, United States

Site Status

Halifax Medical Center

Daytona Beach, Florida, United States

Site Status

Radiation Therapy Associates - Fort Myers

Fort Myers, Florida, United States

Site Status

University of Florida Health Science Center

Gainesville, Florida, United States

Site Status

Health First Holmes Regional Medical Center

Melbourne, Florida, United States

Site Status

Veterans Affairs Medical Center - Miami

Miami, Florida, United States

Site Status

Sylvester Cancer Center, University of Miami

Miami, Florida, United States

Site Status

Baptist Hospital of Miami

Miami, Florida, United States

Site Status

CCOP - Mount Sinai Medical Center

Miami Beach, Florida, United States

Site Status

Florida Radiation Oncology Group

Orange Park, Florida, United States

Site Status

MD Anderson Cancer Center Orlando

Orlando, Florida, United States

Site Status

Bay Medical Center

Panama City, Florida, United States

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Gulf Coast Cancer Treatment Center

Panama City, Florida, United States

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West Florida Cancer Institute - Pensacola

Pensacola, Florida, United States

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Sarasota Radiation and Medical Oncology Center

Sarasota, Florida, United States

Site Status

Bayfront Medical Center

St. Petersburg, Florida, United States

Site Status

Tallahassee Memorial Healthcare

Tallahassee, Florida, United States

Site Status

H. Lee Moffitt Cancer Center and Research Institute

Tampa, Florida, United States

Site Status

Emory University Hospital - Atlanta

Atlanta, Georgia, United States

Site Status

CCOP - Atlanta Regional

Atlanta, Georgia, United States

Site Status

Medical Center/John B. Amos Community Cancer Center

Columbus, Georgia, United States

Site Status

InterCommunity Cancer Center at Rome

Rome, Georgia, United States

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Northwest Community Hospital

Arlington Heights, Illinois, United States

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Northwestern Memorial Hospital

Chicago, Illinois, United States

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University of Chicago Cancer Research Center

Chicago, Illinois, United States

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CCOP - Central Illinois

Decatur, Illinois, United States

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Provena St. Joseph Hospital- Regional Cancer Care Center

Elgin, Illinois, United States

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Ingalls Memorial Hospital

Harvey, Illinois, United States

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Loyola University Medical Center

Maywood, Illinois, United States

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Lutheran General Cancer Care Center

Park Ridge, Illinois, United States

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Methodist Medical Center of Illinois

Peoria, Illinois, United States

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St. John's Medical Center

Anderson, Indiana, United States

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Veterans Affairs Medical Center - Indianapolis (Roudebush)

Indianapolis, Indiana, United States

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Clarion Health Partners Inc.

Indianapolis, Indiana, United States

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Community Hospitals of Indianapolis - Regional Cancer Center

Indianapolis, Indiana, United States

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Ball Memorial Hospital

Muncie, Indiana, United States

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Memorial Hospital of South Bend

South Bend, Indiana, United States

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St. Joseph's Radiation Oncology Center

South Bend, Indiana, United States

Site Status

Wendt Regional Cancer Center of Finley Hospital

Dubuque, Iowa, United States

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University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

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Veterans Affairs Medical Center - Lexington

Lexington, Kentucky, United States

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Albert B. Chandler Medical Center, University of Kentucky

Lexington, Kentucky, United States

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James Graham Brown Cancer Center

Louisville, Kentucky, United States

Site Status

Louisville Radiation Oncology

Louisville, Kentucky, United States

Site Status

Merle M. Mahr Cancer Center

Madisonville, Kentucky, United States

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Western Baptist Hospital

Paducah, Kentucky, United States

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Mary Bird Perkins Cancer Center

Baton Rouge, Louisiana, United States

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Romagosa Radiation Oncology Center

Lafayette, Louisiana, United States

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MBCCOP - LSU Medical Center

New Orleans, Louisiana, United States

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Tulane University School of Medicine

New Orleans, Louisiana, United States

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CCOP - Ochsner

New Orleans, Louisiana, United States

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Maine Medical Center

Portland, Maine, United States

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Anne Arundel Oncology Center

Annapolis, Maryland, United States

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Greater Baltimore Medical Center and Cancer Center

Baltimore, Maryland, United States

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Harbor Hospital Center

Baltimore, Maryland, United States

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Sinai Hospital of Baltimore

Baltimore, Maryland, United States

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Johns Hopkins Oncology Center

Baltimore, Maryland, United States

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Radiation Oncology Affiliates of Maryland, P.A.

Baltimore, Maryland, United States

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Peninsula Regional Medical Center

Salisbury, Maryland, United States

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Cape Cod Hospital

Hyannis, Massachusetts, United States

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Veterans Affairs Medical Center - Boston (Jamaica Plain)

Jamaica Plain, Massachusetts, United States

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CCOP - Ann Arbor Regional

Ann Arbor, Michigan, United States

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Saint Josephs Mercy Hospital

Ann Arbor, Michigan, United States

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University of Michigan Comprehensive Cancer Center

Ann Arbor, Michigan, United States

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Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, United States

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Henry Ford Hospital

Detroit, Michigan, United States

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McLaren Regional Cancer Center

Flint, Michigan, United States

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Hurley Medical Center

Flint, Michigan, United States

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CCOP - Kalamazoo

Kalamazoo, Michigan, United States

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Sparrow Regional Cancer Center

Lansing, Michigan, United States

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Marquette General Hospital

Marquette, Michigan, United States

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MidMichigan Regional Medical Center

Midland, Michigan, United States

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William Beaumont Hospital

Royal Oak, Michigan, United States

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St. Mary's Medical Center

Saginaw, Michigan, United States

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Mayo Clinic Cancer Center

Rochester, Minnesota, United States

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CCOP - Metro-Minnesota

Saint Louis Park, Minnesota, United States

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North Mississippi Medical Center/Cancer Center

Tupelo, Mississippi, United States

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Ellis Fischel Cancer Center - Columbia

Columbia, Missouri, United States

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CCOP - Kansas City

Kansas City, Missouri, United States

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Cancer Research for the Ozarks

Springfield, Missouri, United States

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CCOP - Cancer Research for the Ozarks

Springfield, Missouri, United States

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St. Louis University Health Sciences Center

St Louis, Missouri, United States

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Mallinckrodt Institute of Radiology

St Louis, Missouri, United States

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CCOP - Montana Cancer Consortium

Billings, Montana, United States

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CCOP - Southern Nevada Cancer Research Foundation

Las Vegas, Nevada, United States

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Norris Cotton Cancer Center

Lebanon, New Hampshire, United States

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Elliot Regional Cancer Center

Manchester, New Hampshire, United States

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Veterans Affairs Medical Center - East Orange

East Orange, New Jersey, United States

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John F. Kennedy Medical Center

Edison, New Jersey, United States

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Trinitas Hospital - Jersey Street Campus

Elizabeth, New Jersey, United States

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Monmouth Medical Center

Long Branch, New Jersey, United States

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South Jersey Hospital - Millville

Millville, New Jersey, United States

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Fox Chase Cancer Center at Virtua-Memorial Hospital Burlington County

Mount Holly, New Jersey, United States

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Cancer Institute of New Jersey

New Brunswick, New Jersey, United States

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Newark Beth Israel Medical Center

Newark, New Jersey, United States

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Atlantic City Medical Center

Pomona, New Jersey, United States

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Community Medical Center

Toms River, New Jersey, United States

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St. Francis Medical Center

Trenton, New Jersey, United States

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Associated Radiologists, P.A.

Warren Township, New Jersey, United States

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Saint Joseph Medical Center

Albuquerque, New Mexico, United States

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Cancer Center of Albany Medical Center

Albany, New York, United States

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State University of New York Health Science Center at Brooklyn

Brooklyn, New York, United States

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New York Methodist Hospital

Brooklyn, New York, United States

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Roswell Park Cancer Institute

Buffalo, New York, United States

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Finger Lakes Radiation Oncology, P.C.

Clifton Springs, New York, United States

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CCOP - North Shore University Hospital

Manhasset, New York, United States

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Beth Israel Medical Center

New York, New York, United States

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NYU School of Medicine's Kaplan Comprehensive Cancer Center

New York, New York, United States

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Memorial Sloan-Kettering Cancer Center

New York, New York, United States

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Herbert Irving Comprehensive Cancer Center

New York, New York, United States

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Champlain Valley Physicians Hospital Medical Center

Plattsburgh, New York, United States

Site Status

Vassar Brothers Hospital

Poughkeepsie, New York, United States

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University of Rochester Cancer Center

Rochester, New York, United States

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Albert Einstein Comprehensive Cancer Center

The Bronx, New York, United States

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New York Medical College

Valhalla, New York, United States

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Lineberger Comprehensive Cancer Center, UNC

Chapel Hill, North Carolina, United States

Site Status

Northeast Medical Center

Concord, North Carolina, United States

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East Carolina University School of Medicine

Greenville, North Carolina, United States

Site Status

Catawba Memorial Hospital

Hickory, North Carolina, United States

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CCOP - Southeast Cancer Control Consortium

Winston-Salem, North Carolina, United States

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Comprehensive Cancer Center of Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

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Meritcare Roger Maris Cancer Center

Fargo, North Dakota, United States

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UNIMED Medical Center

Minot, North Dakota, United States

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Akron General Medical Center

Akron, Ohio, United States

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Akron City Hospital

Akron, Ohio, United States

Site Status

Christ Hospital

Cincinnati, Ohio, United States

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Ireland Cancer Center

Cleveland, Ohio, United States

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University Hospitals of Cleveland

Cleveland, Ohio, United States

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Cleveland Clinic Taussig Cancer Center

Cleveland, Ohio, United States

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CCOP - Columbus

Columbus, Ohio, United States

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Arthur G. James Cancer Hospital - Ohio State University

Columbus, Ohio, United States

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CCOP - Dayton

Kettering, Ohio, United States

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CCOP - Toledo Community Hospital Oncology Program

Toledo, Ohio, United States

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St. Anthony Hospital

Oklahoma City, Oklahoma, United States

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St. John Medical Center

Tulsa, Oklahoma, United States

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CCOP - Columbia River Program

Portland, Oregon, United States

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Lehigh Valley Hospital

Allentown, Pennsylvania, United States

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St. Luke's Hospital Regional Cancer Center

Bethlehem, Pennsylvania, United States

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Geisinger Medical Center

Danville, Pennsylvania, United States

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Mercy Catholic Medical Center, Mercy Fitzgerald Divison

Darby, Pennsylvania, United States

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Delaware County Memorial Hospital

Drexel Hill, Pennsylvania, United States

Site Status

Penn State Geisinger Cancer Center

Hershey, Pennsylvania, United States

Site Status

Hahnemann University Hospital

Philadelphia, Pennsylvania, United States

Site Status

University of Pennsylvania Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Veterans Affairs Medical Center - Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Kimmel Cancer Center of Thomas Jefferson University - Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Albert Einstein Cancer Center

Philadelphia, Pennsylvania, United States

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University of Pittsburgh Cancer Institute

Pittsburgh, Pennsylvania, United States

Site Status

Mercy Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Western Pennsylvania Hospital

Pittsburgh, Pennsylvania, United States

Site Status

Reading Hospital and Medical Center

Reading, Pennsylvania, United States

Site Status

Mercy Hospital Cancer Center - Scranton

Scranton, Pennsylvania, United States

Site Status

Wilkes Barre General Hospital

Wilkes-Barre, Pennsylvania, United States

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CCOP - MainLine Health

Wynnewood, Pennsylvania, United States

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York Hospital

York, Pennsylvania, United States

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Roger Williams Medical Center/BUSM

Providence, Rhode Island, United States

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Medical University of South Carolina

Charleston, South Carolina, United States

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CCOP - Greenville

Greenville, South Carolina, United States

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CCOP - Upstate Carolina

Spartanburg, South Carolina, United States

Site Status

Rapid City Regional Hospital

Rapid City, South Dakota, United States

Site Status

Jackson-Madison County General Hospital

Jackson, Tennessee, United States

Site Status

Baptist Regional Cancer Center - Knoxville

Knoxville, Tennessee, United States

Site Status

University of Tennessee, Memphis Cancer Center

Memphis, Tennessee, United States

Site Status

CCOP - Baptist Cancer Institute

Memphis, Tennessee, United States

Site Status

Vanderbilt Cancer Center

Nashville, Tennessee, United States

Site Status

Harrington Cancer Center

Amarillo, Texas, United States

Site Status

Julie and Ben Rogers Cancer Institute

Beaumont, Texas, United States

Site Status

University of Texas Medical Branch

Galveston, Texas, United States

Site Status

University of Texas - MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Wilford Hall - 59th Medical Wing

Lackland Air Force Base, Texas, United States

Site Status

Joe Arrington Cancer Research and Treatment Center

Lubbock, Texas, United States

Site Status

Bayshore Medical Center

Pasadena, Texas, United States

Site Status

East Texas Medical Center - Cancer Institute

Tyler, Texas, United States

Site Status

University of Utah Health Sciences Center

Salt Lake City, Utah, United States

Site Status

LDS Hospital

Salt Lake City, Utah, United States

Site Status

Dixie Regional Medical Center

St. George, Utah, United States

Site Status

CCOP - Southwestern Vermont Regional Cancer Center

Bennington, Vermont, United States

Site Status

Vermont Cancer Center

Burlington, Vermont, United States

Site Status

Green Mountain Oncology Group

Rutland, Vermont, United States

Site Status

Martha Jefferson Hospital

Charlottesville, Virginia, United States

Site Status

Cancer Center, University of Virginia HSC

Charlottesville, Virginia, United States

Site Status

RMH Regional Canter Center

Harrisonburg, Virginia, United States

Site Status

Virginia Baptist Hospital

Lynchburg, Virginia, United States

Site Status

Naval Medical Center, Portsmouth

Portsmouth, Virginia, United States

Site Status

Swedish Cancer Institute

Seattle, Washington, United States

Site Status

Virginia Mason Medical Center

Seattle, Washington, United States

Site Status

Deaconess Medical Center

Spokane, Washington, United States

Site Status

Yakima Valley Memorial Hospital

Yakima, Washington, United States

Site Status

Schiffler Cancer Center

Wheeling, West Virginia, United States

Site Status

St. Vincent Hospital

Green Bay, Wisconsin, United States

Site Status

Gundersen Lutheran Medical Foundation

La Crosse, Wisconsin, United States

Site Status

Southern Wisconsin Radiotherapy Center

Madison, Wisconsin, United States

Site Status

University of Wisconsin Comprehensive Cancer Center

Madison, Wisconsin, United States

Site Status

Marshfield Clinic

Marshfield, Wisconsin, United States

Site Status

Community Memorial Hospital

Menomonee Falls, Wisconsin, United States

Site Status

St. Joseph's Hospital

Milwaukee, Wisconsin, United States

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Columbia Hospital

Milwaukee, Wisconsin, United States

Site Status

St. Luke's Medical Center

Milwaukee, Wisconsin, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Veterans Affairs Medical Center - Milwaukee (Zablocki)

Milwaukee, Wisconsin, United States

Site Status

Southeastern Wisconsin Regional Cancer Center

Racine, Wisconsin, United States

Site Status

Waukesha Memorial Hospital

Waukesha, Wisconsin, United States

Site Status

Tom Baker Cancer Center - Calgary

Calgary, Alberta, Canada

Site Status

Cross Cancer Institute

Edmonton, Alberta, Canada

Site Status

BC Cancer Agency

Vancouver, British Columbia, Canada

Site Status

Doctor Leon Richard Oncology Centre

Moncton, New Brunswick, Canada

Site Status

Saint John Regional Hospital

Saint John, New Brunswick, Canada

Site Status

Dr. H. Bliss Murphy Cancer Centre

St. John's, Newfoundland and Labrador, Canada

Site Status

Nova Scotia Cancer Centre

Halifax, Nova Scotia, Canada

Site Status

Northeastern Ontario Regional Cancer Centre, Sudbury

Greater Sudbury, Ontario, Canada

Site Status

Cancer Care Ontario-Hamilton Regional Cancer Centre

Hamilton, Ontario, Canada

Site Status

Kingston Regional Cancer Centre

Kingston, Ontario, Canada

Site Status

Cancer Care Ontario-London Regional Cancer Centre

London, Ontario, Canada

Site Status

Ottawa Regional Cancer Centre - General Campus

Ottawa, Ontario, Canada

Site Status

Northwestern Ontario Regional Cancer Centre, Thunder Bay

Thunder Bay, Ontario, Canada

Site Status

Toronto Sunnybrook Regional Cancer Centre

Toronto, Ontario, Canada

Site Status

Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

Centre Universitaire de Sante de l'Estrie - Site Fleurimont

Fleurimont, Quebec, Canada

Site Status

Centre Hospitalier de l'Universite de Montreal

Montreal, Quebec, Canada

Site Status

McGill University Department of Oncology

Montreal, Quebec, Canada

Site Status

Saskatoon Cancer Centre

Saskatoon, Saskatchewan, Canada

Site Status

Countries

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United States Canada

References

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Pilepich MV, Paulus R, St Clair W, Brasacchio RA, Rostock R, Miller RC. Phase III study of pentosanpolysulfate (PPS) in treatment of gastrointestinal tract sequelae of radiotherapy. Am J Clin Oncol. 2006 Apr;29(2):132-7. doi: 10.1097/01.coc.0000203758.77490.fd.

Reference Type RESULT
PMID: 16601430 (View on PubMed)

Other Identifiers

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CDR0000066979

Identifier Type: -

Identifier Source: secondary_id

RTOG-9809

Identifier Type: -

Identifier Source: org_study_id

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