A Study to Learn More About How Well Finerenone Works, How Safe it is, and How it Moves Into, Through, and Out of the Body Compared to Placebo When Taken With Standard Treatment in Children With Heart Failure and Left Ventricular Systolic Dysfunction

NCT ID: NCT07188805

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

NOT_YET_RECRUITING

Clinical Phase

PHASE3

Total Enrollment

111 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-11-28

Study Completion Date

2029-12-30

Brief Summary

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Researchers are looking for a better way to treat children who have heart failure with left ventricular systolic dysfunction (LVSD). Heart failure is a serious condition where the heart is unable to pump enough blood to meet the body's needs. This can lead to symptoms like shortness of breath, fatigue, and poor growth in children.

The study treatment, finerenone (also called BAY94-8862), works by blocking a protein involved in inflammation, scarring, and thickening of the heart and blood vessels. This may help the heart to pump blood more effectively. This is the first study to explore its use specifically for children with heart failure and LVSD.

The main purpose of this study is to learn if finerenone works to help the heart compared to placebo in children with heart failure and LVSD. For this, the researchers will collect and analyze data on the levels of a protein called NT-proBNP in the blood, which indicates heart stress, and monitor the safety of the treatment.

The study will include children with heart failure and LVSD aged from 6 months to less than 18 years. The study participants will be randomly assigned to one of two treatment groups. Based on their group, they will receive either finerenone or a placebo for a duration of 3 months. A placebo looks like a treatment but does not have any medicine in it. Throughout the study, all participants will continue to receive their standard heart failure treatments.

At the start of this study, the doctors will check each participant's medical history and current medications. If participants qualify for the treatment phase, they will undergo treatment for about 90 days. During this time, they will visit the study site at least 3 times. During these visits, the participants will:

* have their blood pressure, heart rate, temperature, respiratory rate, height and weight measured
* have their heart examined by electrocardiogram (ECG) and echocardiogram
* have blood samples taken
* have physical examinations
* answer questions about their medication and whether they have any adverse events, or have their parents or guardians' answers

An adverse event is any medical problem that a participant has during a study. Doctors keep track of all adverse events that happen in studies, even if they do not think the adverse events might be related to the study treatments.

After the initial three-month study, eligible participants will have the option to join a nine-month open-label extension study where all will receive finerenone. Participants who choose not to enroll in the extension will have a follow-up visit 30 days after their last treatment.

Detailed Description

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Conditions

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Left Ventricular Systolic Dysfunction Heart Failure (Pediatric)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Finerenone (Kerendia, BAY94-8862)

Participants will receive finerenone treatment.

Group Type EXPERIMENTAL

Finerenone (Kerendia, BAY94-8862)

Intervention Type DRUG

Finerenone in different doses, treatment duration will be 90±3 days

Placebo

Participants will receive placebo to finerenone.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo to finerenone, treatment duration will be 90±3 days

Interventions

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Finerenone (Kerendia, BAY94-8862)

Finerenone in different doses, treatment duration will be 90±3 days

Intervention Type DRUG

Placebo

Placebo to finerenone, treatment duration will be 90±3 days

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Participants must be 6 months to \<18 years old at the time when the informed consent/assent is signed.
* Left ventricular systolic dysfunction (LVSD) with left ventricular ejection fraction (LVEF) ≤ 50% at screening assessed by echocardiography.
* Elevated NT-pro BNP levels

* \>500 ng/l for children ≥ 6 months to \< 2 years of age
* \>300 ng/l, for children ≥ 2 years to \<18 years
* Heart failure etiologies including congenital heart defects (CHD) with biventricular physiology and systemic LV; idiopathic cardiomyopathy (CM); familial/inherited and/or genetic CM; history of myocarditis (diagnosis of an acute episode was at least 3 months prior to randomization); neuromuscular disorder (eg, duchenne muscular dystrophy); inborn error of metabolism; mitochondrial disorder; acquired (chemotherapy, iatrogenic, infection, rheumatic, or nutritional); ischemic (eg, Kawasaki disease and postoperative heart failure \[HF\]); LV noncompaction.
* Receiving standard of care (SoC) treatment for heart failure according to local guidelines or investigator´s discretion and being on a stable regimen for 30 days prior to randomization.
* Study participants must have a body weight ≥ 4.0 kg at Visit 1.

Exclusion Criteria

* Serum potassium:

* \> 5.0 mmol/L for children ≥ 2 years of age at either screening or randomization visit
* \> 5.3 mmol/L for children ≥ 6 months to \< 2 years of age at either screening or randomization visit (if estimated glomerular filtration rate \[eGFR\] \< 60 mL/min/1.73m², threshold of \> 5.0 mmol/L will be used)
* Severe renal dysfunction with eGFR \< 30 ml/min/1.73m² at screening or randomization visit.
* Systolic blood pressure (SBP) \< 5th percentile for age, sex and height at screening or randomization.
* Sustained or symptomatic arrhythmias not controlled by drug or device therapy within 30 days prior to randomization.
* Treatment with a mineralocorticoid receptor antagonist (e.g., spironolactone, eplerenone) within 30 days of randomization.
* Requirement of any intravenous (IV) vasoactive agents, mechanical ventilation, mechanical circulatory support within 30 days prior to randomization.
* Recent surgical procedure or other intervention to correct or palliate CHD within 3 months prior to randomization or anticipated to undergo cardiac surgery during the 3 months after randomization.
Minimum Eligible Age

6 Months

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Children's Hospital Colorado - Anschutz Medical Campus - Cardiology

Aurora, Colorado, United States

Site Status

Nemours Children's Hospital -Delaware

Wilmington, Delaware, United States

Site Status

UF Health Shands Hospital - Pediatric Cardiology

Gainesville, Florida, United States

Site Status

Joe Dimaggio Children's Hospital - Cardiology

Hollywood, Florida, United States

Site Status

Emory University Hospital - Children's Healthcare of Atlanta Cardiology - Atlanta

Atlanta, Georgia, United States

Site Status

Riley Hospital For Children - Cardiology

Indianapolis, Indiana, United States

Site Status

Boston Children's Hospital - Main Campus - Cardiology

Boston, Massachusetts, United States

Site Status

C.S. Mott Children's Hospital - Cardiology

Ann Arbor, Michigan, United States

Site Status

Children's Mercy Hospital Kansas City - Cardiology

Kansas City, Missouri, United States

Site Status

St. Louis Children's Hospital - Cardiology

St Louis, Missouri, United States

Site Status

Icahn School of Medicine at Mount Sinai - Pediatric Cardiology

New York, New York, United States

Site Status

Columbia University Irving Medical Center - Pediatric Cardiology

New York, New York, United States

Site Status

The Children's Hospital at Montefiore - Cardiology

The Bronx, New York, United States

Site Status

Cincinnati Children's Hospital Medical Center | Division of Nephrology and Hypertension

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic Children's

Cleveland, Ohio, United States

Site Status

Nationwide Children's Hospital - Cardiology

Columbus, Ohio, United States

Site Status

Children's Hospital of Philadelphia - Cardiology

Philadelphia, Pennsylvania, United States

Site Status

UPMC Children's Hospital of Pittsburgh - Cardiology

Pittsburgh, Pennsylvania, United States

Site Status

MUSC Shawn Jenkins Children's Hospital - Cardiology

North Charleston, South Carolina, United States

Site Status

Children's Medical Center Dallas - Cardiology

Dallas, Texas, United States

Site Status

Texas Children's Hospital - Cardiology

Houston, Texas, United States

Site Status

Primary Children's Hospital

Salt Lake City, Utah, United States

Site Status

Hospital de Niños Sor María Ludovica

La Plata, Buenos Aires, Argentina

Site Status

Instituto De Investigaciones Clinicas Zarate | Zarate, Argentina

Zárate, Buenos Aires, Argentina

Site Status

Hospital General de Ninos Ricardo Gutierrez | Pediatric Nephrology Department

Buenos Aires, Ciudad Auton. de Buenos Aires, Argentina

Site Status

Consultorios Integrados Rosario | Instituto Medico de la Fundacion de Estudios Clinicos

Rosario, Santa Fe Province, Argentina

Site Status

Hospital Italiano de Buenos Aires

Buenos Aires, , Argentina

Site Status

Hospital de Pediatría Juan P. Garrahan

Buenos Aires, , Argentina

Site Status

Hospital General de Ninos Pedro de Elizalde | Nephrology Department

Ciudad Autonoma de Buenos Aire, , Argentina

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Consultorios Médicos Dr. Doreski

Ciudad Autónoma de Buenos Aire, , Argentina

Site Status

Sanatorio de la Cañada

Córdoba, , Argentina

Site Status

Centro Cardiovascular Salta (Torzav SRL)

Salta, , Argentina

Site Status

Kepler Universitätsklinikum GmbH - Klinik für Kinderkardiologie

Linz, , Austria

Site Status

Medizinische Universität Wien - Klinik für Kinder- und Jugendheilkunde, Abteilung für Pädiatrische Kardiologie

Vienna, , Austria

Site Status

UZ Leuven - Pediatric Cardiology

Leuven, Flemish Brabant, Belgium

Site Status

Cliniques Universitaires St-Luc (UCL) - Pediatric Cardiology

Brussels, , Belgium

Site Status

UZ Antwerpen - Pediatric Cardiology

Edegem, , Belgium

Site Status

UZ Gent - Pediatric Cardiology

Ghent, , Belgium

Site Status

CHC MontLegia - Pediatric Cardiology

Liège, , Belgium

Site Status

IESG - Instituto de Ensino da Saude e Gestao

Salvador, Estado de Bahia, Brazil

Site Status

Santa Casa de Misericórdia de Belo Horizonte

Belo Horizonte, Minas Gerais, Brazil

Site Status

Hospital de Clínicas da Universidade Federal de Uberlândia Empresa Brasileira de Serviços Hospitalares - EBSERH

Uberlândia, Minas Gerais, Brazil

Site Status

Hospital Pequeno Principe

Curitiba, Paraná, Brazil

Site Status

Fundação Universidade de Caxias do Sul

Caxias do Sul, Rio Grande do Sul, Brazil

Site Status

Centro de Pesquisa Clinica e Populacional Hospitalize

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Campinas Clinical Research Institute (IPECC) | Campinas, Brazil

Campinas, São Paulo, Brazil

Site Status

Hospital Infantil Sabará - Instituto PENSI - Pesquisa e Ensino em Saúde Infantil

São Paulo, São Paulo, Brazil

Site Status

Instituto Dante Pazzanese de Cardiologia | Divisao de Pesquisa

São Paulo, São Paulo, Brazil

Site Status

InCor HCFMUSP

São Paulo, São Paulo, Brazil

Site Status

National Heart Hospital (NHH) - Dept. Pediatric Cardiology

Sofia, Sofia, Bulgaria

Site Status

University Multiprofile Hospital for Active Treatment 'Sveti Georgi' EAD, Plovdiv Pediatric Clinic

Plovdiv, , Bulgaria

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Medical Center Nora- Heart ?OOD Child Cardiology

Sofia, , Bulgaria

Site Status

University Multiprofile Hospital for Active Treatment 'Sveta Ekaterina' EAD, Sofia

Sofia, , Bulgaria

Site Status

BC Children's Hospital - Children's Heart Centre

Vancouver, British Columbia, Canada

Site Status

London Health Sciences Centre - Children's Hospital

London, Ontario, Canada

Site Status

The Hospital for Sick Children (SickKids)

Toronto, Ontario, Canada

Site Status

CHU Sainte-Justine

Montreal, Quebec, Canada

Site Status

University of Saskatchewan, Royal University Hospital

Saskatoon, Saskatchewan, Canada

Site Status

Fakultní nemocnice Brno, Detská nemocnice - Pediatrická klinika

Brno, , Czechia

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Fakultní nemocnice v Motole - Detské kardiocentrum 2. LF UK a FN Motol

Prague, , Czechia

Site Status

HUS Uusi lastensairaala - Lasten kardiologian vastaanotot

Helsinki, , Finland

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Oulu University Hospital, Department of Paediatrics and Adolescent Services

Oulu, , Finland

Site Status

Universitaetsklinikum Giessen und Marburg GmbH - Kinderherzzentrum und Zentrum für angeborene Herzfehler

Giessen, Hesse, Germany

Site Status

Universitätsklinikum Köln - Kinderkardiologie

Cologne, , Germany

Site Status

Universitätsklinikum Tübingen, Kinderheilkunde II - Kinderkardiologie, Pulmologie, Intensivmedizin

Tübingen, , Germany

Site Status

Athens General Children's Hospital Panagioti And Aglaia Kyriakou -2nd University Department of Pediatrics

Athens, , Greece

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Athens General Children's Hospital Panagioti And Aglaia Kyriakou, Cardiology Department

Athens, , Greece

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Nosokomeio Paidon I Agia Sofia, Cardiology Department

Athens, , Greece

Site Status

Onassis Cardiac Surgery Center, Department of Pediatric Cardiology and Adult Congenital Heart Disease

Kalithèa, , Greece

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Gottsegen Gyorgy Orszagos Kardiovaszkularis Intezet - Gyermeksziv Kozpont

Budapest, , Hungary

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Rambam Health Corporation

Haifa, , Israel

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Edith Wolfson Medical Center (EWMC)

Holon, , Israel

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Shaare Zedek Medical Center

Jerusalem, , Israel

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Dana-Dwek Children's Hospital

Tel Aviv, , Israel

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Chaim Sheba Medical Center

Tel Litwinsky, , Israel

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Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII - Cardiologia 2 - Cardiopatie Congenite del bambino e dell'adulto

Bergamo, , Italy

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Azienda Ospedaliero-Universitaria di Bologna IRCCS Policlinico Sant'Orsola-Cardiologia pediatrica ed dell'età evolutiva

Bologna, , Italy

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IRCCS Istituto Giannina Gaslini - Cardiologia

Genova, , Italy

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ASST Grande Ospedale Metropolitano Niguarda - Struttura semplice dipartimentale cardiologia pediatrica

Milan, , Italy

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Azienda Ospedaliera Dei Colli_Monaldi - Malattie Rare e Genetiche Cardiovascolari

Naples, , Italy

Site Status

Azienda Ospedale-Università di Padova - UOC Cardiologia Pediatrica

Padua, , Italy

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Ospedale Pediatrico Bambino Gesù - Unità Terapie Cardiovascolari Avanzate

Roma, , Italy

Site Status

A.O.U. Città della Salute e della Scienza di Torino_Regina Margherita - Cadiologia pediatrica

Torino, , Italy

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Centro de Investigación Clínica Médica y Farmacológica S.A de C.V

Guadalajara, Jalisco, Mexico

Site Status

Hospital Infantil de México "Dr. Federico Gómez"

Mexico City, Mexico City, Mexico

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Hospital Universitario "Dr. Jose Eleuterio Gonzalez"-Pediatria

Monterrey, Nuevo León, Mexico

Site Status

Hospital Angeles (HA)-Lomas

Huixquilucan, State of Mexico, Mexico

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Centro de Estudios de Investigacion Metabolicos y Cardiovasculares

Ciudad Madero, Tamaulipas, Mexico

Site Status

Centro de Estudios Clínicos de Querétaro S.C.

Querétaro, , Mexico

Site Status

Centro de Atención e Investigación Cardiovascular del Potosí S.C.

San Luis Potosí City, , Mexico

Site Status

Instituto Nacional de Cardiología "Ignacio Chávez"

Tlalpan, , Mexico

Site Status

Wojewodzki Szpital Specjalistyczny we Wroclawiu

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status

Pomnik Centrum Zdrowia Dziecka - Klinika Kardiologii

Warsaw, Masovian Voivodeship, Poland

Site Status

Górnoslaskie Centrum Zdrowia Dziecka im. sw. Jana Pawla II SPSK Nr 6 Slaskiego UM w Katowicach - Oddzial Kardiologii Dzieciecej

Katowice, , Poland

Site Status

Instytut Centrum Zdrowia Matki Polki w Lodzi - Klinika Kardiologii

Lódz, , Poland

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Hospital de Santa Cruz | Pediatric Cardiology Department

Carnaxide, , Portugal

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Department of Cardiology - Research Unit

Coimbra, , Portugal

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Hospital Santa Marta | Pediatric Cardiology Department

Lisbon, , Portugal

Site Status

Centro Materno infantil do Norte - Pediatric Cardiology

Porto, , Portugal

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ULS São João - Pediatric Department

Porto, , Portugal

Site Status

Pusan National University Yangsan Hospital

Yangsan, Gyeongsangnam-do, South Korea

Site Status

Seoul National University Children's Hospital (SNUCH)

Jongno, Seoul, South Korea

Site Status

Severance Hospital, Yonsei University Health System-Pediatrics Department

Seodaemun, , South Korea

Site Status

Samsung Medical Center-Pediatrics

Seoul, , South Korea

Site Status

Hospital de Sant Joan de Déu

Esplugues de Llobregat, Barcelona, Spain

Site Status

Hospital Universitari Vall d´Hebron_ Nefrologia

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia - Cardiologia pediatrica

Córdoba, , Spain

Site Status

Hospital Universitario Ramon Y Cajal - Cardiologia pediatrica

Madrid, , Spain

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Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Universidad Autonoma de Madrid (UAM) - Hospital Universitario La Paz (HULP)

Madrid, , Spain

Site Status

Hospital Universitario Regional De Malaga - Cardiologia pediatrica

Málaga, , Spain

Site Status

Hospital Universitario Virgen Del Rocio S.L. - Cardiologia pediatrica

Seville, , Spain

Site Status

Skånes Universitetssjukhus Lund - Barnhjärtcentrum

Lund, Skåne County, Sweden

Site Status

Kaohsiung Veterans General Hospital

Kaohsiung City, , Taiwan

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Chang Gung Memorial Hospital Kaohsiung

Kaohsiung City, , Taiwan

Site Status

Taichung Veterans General Hospital

Taichung, , Taiwan

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National Cheng Kung University Hospital

Tainan, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

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MacKay Children's hospital

Taipei, , Taiwan

Site Status

Cukurova Universitesi Tip Fakultesi Hastanesi

Adana, , Turkey (Türkiye)

Site Status

Hacettepe Universitesi Tip Fakultesi

Ankara, , Turkey (Türkiye)

Site Status

Ankara Bilkent Sehir Hastanesi

Bilkent Ankara, , Turkey (Türkiye)

Site Status

Marmara Uni. Tip Fak. Pendik EAH Kardiyoloji

Istanbul, , Turkey (Türkiye)

Site Status

Istanbul Mehmet Akif Ersoy Gogus Kalp Damar Cerrahisi E.A.H.

Istanbul, , Turkey (Türkiye)

Site Status

Izmir Dr. Behcet Uz Cocuk Hastaliklari Hast

Izmir, , Turkey (Türkiye)

Site Status

Leeds Teaching Hospitals NHS Trust | Leeds Children's Hospital - Children's Research Facility

Leeds, West Yorkshire, United Kingdom

Site Status

Belfast Health and Social Care Trust | Royal Belfast Hospital for Sick Children - Paediatric Cardiology

Belfast, , United Kingdom

Site Status

University Hospitals Bristol and Weston NHS Foundation Trust | Bristol Royal Hospital for Children - Clinical Research Facility

Bristol, , United Kingdom

Site Status

NHS Greater Glasgow and Clyde | Royal Hospital for Children - Glasgow Clinical Research Facility

Glasgow, , United Kingdom

Site Status

University Hospitals of Leicester NHS Trust | Leicester Children's Hospital - Children's Research Facility

Leicester, , United Kingdom

Site Status

Alder Hey Children's NHS Foundation Trust | Alder Hey Children's Hospital - Clinical Research Facility

Liverpool, , United Kingdom

Site Status

Newcastle upon Tyne Hospitals NHS Foundation Trust |Freeman Hospital - Children's Heart Unit

Newcastle upon Tyne, , United Kingdom

Site Status

Countries

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United States Argentina Austria Belgium Brazil Bulgaria Canada Czechia Finland Germany Greece Hungary Israel Italy Mexico Poland Portugal South Korea Spain Sweden Taiwan Turkey (Türkiye) United Kingdom

Central Contacts

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Bayer Clinical Trials Contact

Role: CONTACT

Phone: (+)1-888-84 22937

Email: [email protected]

Related Links

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https://clinicaltrials.bayer.com/

Click here to find further information and, after study completion, the study results according to Bayer's transparency standards.

Other Identifiers

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2024-519829-38-00

Identifier Type: REGISTRY

Identifier Source: secondary_id

21466

Identifier Type: -

Identifier Source: org_study_id