Allogeneic Mesenchymal Stem Cell-Derived Exosome Therapy for Progressive Multiple Sclerosis

NCT ID: NCT07146087

Last Updated: 2025-08-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

SUSPENDED

Clinical Phase

EARLY_PHASE1

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2020-07-01

Study Completion Date

2027-12-31

Brief Summary

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The goal of this clinical trial is to learn if intravenous infusion of allogeneic mesenchymal stem cell (MSC)-derived exosomes can slow disability progression and improve neurological function in adults with progressive multiple sclerosis (MS). The trial will also evaluate the safety and tolerability of repeated exosome infusions.

The main questions it aims to answer are:

Does MSC-derived exosome therapy reduce disability progression as measured by the Expanded Disability Status Scale (EDSS)?

Does MSC-derived exosome therapy decrease neuroinflammation and brain lesion burden compared with placebo?

Researchers will compare participants who receive MSC-derived exosome therapy to those who receive placebo (saline infusion) to see if the treatment improves clinical and biological outcomes.

Participants will:

Receive either MSC-derived exosome infusions or placebo infusions every 3 months for 1 year (4 total infusions)

Undergo clinical assessments (neurological exams, EDSS scoring, neurocognitive testing)

Provide blood and cerebrospinal fluid samples for biomarker analysis

Have MRI scans to evaluate lesion load and brain volume

Complete questionnaires on quality of life and daily functioning

Detailed Description

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Conditions

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Multiple Sclerosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

OTHER

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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MSC-Derived Exosomes

Participants receive intravenous infusions of allogeneic mesenchymal stem cell (MSC)-derived exosomes every 12 weeks for 48 weeks (total of 4 infusions) in addition to their stable background MS therapy (if any).

Group Type EXPERIMENTAL

MSC-Derived Exosomes

Intervention Type BIOLOGICAL

Purified, sterile, acellular extracellular vesicles (exosomes) isolated from culture supernatant of GLP-manufactured allogeneic human bone-marrow-derived MSCs. Release criteria include particle size distribution 30-150 nm (nanoparticle tracking analysis), particle count, sterility/endotoxin testing, mycoplasma negative, and predefined protein/marker profile (e.g., CD9/CD63/CD81 positive).

Normal Saline

Participants receive intravenous infusions of 0.9% sodium chloride (saline) matched in volume, appearance, and schedule to the experimental arm, in addition to their stable background MS therapy (if any).

Group Type PLACEBO_COMPARATOR

Placebo (Normal Saline)

Intervention Type BIOLOGICAL

0.9% sodium chloride solution matched to the experimental product in volume, appearance, infusion set-up, and administration procedures.

Interventions

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MSC-Derived Exosomes

Purified, sterile, acellular extracellular vesicles (exosomes) isolated from culture supernatant of GLP-manufactured allogeneic human bone-marrow-derived MSCs. Release criteria include particle size distribution 30-150 nm (nanoparticle tracking analysis), particle count, sterility/endotoxin testing, mycoplasma negative, and predefined protein/marker profile (e.g., CD9/CD63/CD81 positive).

Intervention Type BIOLOGICAL

Placebo (Normal Saline)

0.9% sodium chloride solution matched to the experimental product in volume, appearance, infusion set-up, and administration procedures.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

1. Age 18-65 years.
2. Diagnosis of progressive multiple sclerosis (primary or secondary) confirmed
3. EDSS score 3.0-6.5.

Exclusion Criteria

1. Relapse or corticosteroid treatment within 3 months before screening.
2. Other significant neurological or autoimmune disorders.
3. Active infection, malignancy, or uncontrolled systemic disease.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Biocells Medical

INDUSTRY

Sponsor Role lead

Responsible Party

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Andrei Peskau

Specialist in regenerative medicine

Responsibility Role PRINCIPAL_INVESTIGATOR

Locations

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Biocells Medical

Warsaw, , Poland

Site Status

Countries

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Poland

Other Identifiers

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Bio120002

Identifier Type: -

Identifier Source: org_study_id

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