A Phase 2a Study of HT-6184 in Subjects With IPSS-R Very Low, Low or Intermediate Risk MDS and Anemia

NCT ID: NCT07052006

Last Updated: 2025-12-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

37 participants

Study Classification

INTERVENTIONAL

Study Start Date

2023-12-09

Study Completion Date

2026-03-31

Brief Summary

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This research is being conducted to asses if HT-6184 is effective in the treatment of Very Low, Low, or Intermediate Risk Myelodysplastic Syndrome (MDS) and Symptomatic Anemia.

The study includes a 28-day Screening Period followed by a 16- or 32-week Treatment Period.

Participants will be monitored at each cycle for drug tolerance, safety, and hematological response. A response assessment will occur after 16 weeks of study treatment.

Detailed Description

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Conditions

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Myelodysplastic Syndrome Anemia in Myelodysplastic Syndromes

Keywords

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Very Low-risk MDS Low-risk MDS Intermediate-risk MDS Symptomatic anemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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HT-6184

Group Type EXPERIMENTAL

HT-6184

Intervention Type DRUG

Oral HT-6184

Interventions

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HT-6184

Oral HT-6184

Intervention Type DRUG

Other Intervention Names

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Ofirnoflast

Eligibility Criteria

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Inclusion Criteria

1. ≥ 18 years of age.
2. Signed Informed Consent Form (ICF).
3. Adequate organ function.
4. A documented diagnosis of MDS or non-proliferative Myelodysplastic/myeloproliferative neoplasm (MDS/MPN).
5. Less than 10% bone marrow myeloblasts.
6. Refractory or intolerant of, or ineligible for treatment with an erythroid stimulating agent (ESA).
7. Prior ESA treatment must have been discontinued ≥ 2 weeks prior to date of study treatment.
8. Eastern Cooperative Oncology Group (ECOG) score of 0, 1, or 2.
9. Subjects must have symptomatic anemia.
10. Subjects with NGS (Next-generation sequencing) myeloid-specific somatic gene mutation profile with ≥ 5 % quantitation of clone size by variant allele frequency (VAF).
11. Women of child-bearing potential using an acceptable double-barrier method of contraception.
12. Male subjects who are using an acceptable method of contraception.

Exclusion Criteria

1. Other causes of anemia such as iron deficiency.
2. Clinically significant anemia resulting from B12 or folate deficiencies, autoimmune or hereditary hemolysis, or gastrointestinal bleeding.
3. Women must not be pregnant or breastfeeding.
4. Presence of concomitant intercurrent illness which, in the opinion of the Investigator, would compromise safe participation in the study.
5. Secondary MDS.
6. Treatment with cytotoxic chemotherapeutic agents or experimental agents for the treatment of MDS within 4 weeks of study treatment.
7. Chronic use of systemic corticosteroids for comorbid or study disease condition within last 4 weeks of study treatment.
8. Prior history of malignancy other than MDS.
9. Subject has undergone a stem cell, bone marrow or solid organ transplant
10. Subjects with positive serology for Hepatitis B Virus (HBV), Hepatitis C Virus (HCV), or Human Immunodeficiency Virus (HIV).
11. Prior treatment with disease modifying agents.
12. Participation in any clinical study within 90 days before the first dose of Investigational Product.
13. Loss of ≥ 350 ml of blood within 90 days before the first dose of Investigational Product.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Halia Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Hemato Oncology Clinica Ahmedabad Pvt. Ltd. Vedanta Institute of Medical Sciences

Ahmedabad, Gujarat, India

Site Status

Shalby Hospital

Ahmedabad, Gujarat, India

Site Status

Malabar Cancer Center

Kannur, Kerala, India

Site Status

HCG Cancer Center Vizag

Visakhapatnam, Krishna, India

Site Status

Dr. Bafna's Star Superspeciality Clinic and Hospital

Kolhāpur, Maharashtra, India

Site Status

All India Institute of Medical Sciences

Dehradun, Rishkesh, India

Site Status

Meenakshi Mission Hospital and Research Centre

Madurai, Tamil Nadu, India

Site Status

Apollo Cancer Centre

Hyderabad, Telangana, India

Site Status

Nil Ratan Sircar Medical College and Hospital

Kolkata, West Bengal, India

Site Status

Tata Medical Center

Kolkata, West Bengal, India

Site Status

Countries

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India

Other Identifiers

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CTRI/2023/11/059758

Identifier Type: OTHER

Identifier Source: secondary_id

HT-6184-MDS-001

Identifier Type: -

Identifier Source: org_study_id