A Study to Investigate the Improvement of Photosensitivity in Terms of Skin Lesions Associated With CEP Following Administration of Oral ATL-001 (Ciclopirox Oral Solution) in Participants Aged >18 Years of Age With CEP

NCT ID: NCT07024316

Last Updated: 2025-12-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE1/PHASE2

Total Enrollment

6 participants

Study Classification

INTERVENTIONAL

Study Start Date

2026-01-15

Study Completion Date

2027-11-01

Brief Summary

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This is a study to investigate the effect of oral ATL-001 (ciclopirox) in CEP (Congenital Erythropoietic Porphyria) patients. During the study, it will be measured the improvement of skin lesions, fatigue and other clinical symptoms as well as blood parameters. Funding source - FDA OOPD

Detailed Description

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Conditions

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Congenital Erythropoietic Porphyria (CEP)

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

N-of-1, Open-Label, Prospective Study. One group treated with the investigational drug
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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ATL-001

Group Type EXPERIMENTAL

ATL-001 (Ciclopirox oral solution)

Intervention Type DRUG

Daily administration of oral ATL-001

Interventions

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ATL-001 (Ciclopirox oral solution)

Daily administration of oral ATL-001

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Aged 18 years or older at the time of signing the informed consent form (ICF)
2. Diagnosis of CEP, based on medical history and/or biochemical porphyrin analysis. Sponsor will review the CEP diagnostic criteria (medical history or biochemical porphyrin analysis) of each potential patient, written Sponsor approval before starting the run-in period will be required
3. a) Female participants must not be pregnant or lactating at screening or admission

3\. b) Female participants must be of nonchildbearing potential or agree to use 2 adequate forms of highly effective method(s) of contraception throughout the entire duration of study participation and for at least 4 weeks after the last dose of any study intervention and have negative pregnancy test results at screening (serum) and admission (urine) 4. Male participants with female partners of childbearing potential must be surgically sterile (successful vasectomy at least 4 weeks prior to Day 1) or agree to use adequate forms of highly effective contraception (together with their female partner) for the duration of the study and for at least 4 weeks after the last dose of study intervention; must also agree to refrain from sperm donation during the study and for at least 4 weeks after the last dose of study intervention 5. Negative pregnancy test (females of childbearing potential) at Screening (Month -6), at Baseline (Day 1) and at every visit site until EoS prior to dosing 6. Able to understand the study aims, procedures, and requirements, and provide written informed consent 7. Able to comply with all study procedures 8. Able and committed to complete study patient diaries and questionnaires

Exclusion Criteria

1. Other than CEP, an inherited or acquired red cell disease associated with anemia
2. Any other photodermatosis such as solar urticaria
3. A history or known allergic reaction to any investigational product excipients or the investigational drug
4. Major surgery within 8 weeks before Screening, incomplete recovery from any previous surgery or planned major surgery during the study
5. History of alcohol dependence or excessive alcohol consumption, as assessed by the Investigator
6. Human immunodeficiency virus (HIV), active Hepatitis B, or C. A positive hepatitis result should be discussed between the Investigator and Sponsor prior to enrolment
7. Score of Personal Health Questionnaire Depression Scale (PHQ-8) ≥10 at screening or any response of "yes" on the Columbia-Suicide Severity Rating Scale (C-SSRS)
8. Uncontrolled medical condition or concomitant medication that would confound the ability to interpret clinical, clinical laboratory, or participant diary data, including a major psychiatric condition that has had an exacerbation or required hospitalization in the last 6 months
9. Administration of afamelanotide and dersimelagon within the last 2 months prior to start of the run-in period
10. Total bilirubin \>2× ULN (unless documented Gilbert syndrome) at Screening
11. If female, pregnant or breastfeeding. Final\_V2.1 38 of 106 11 Apr 2025
12. Participation in any other clinical protocol or investigational trial that involves administration of experimental therapy and/or therapeutic devices within 30 days of Screening.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Atlas Molecular Pharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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The Cleveland Clinics

Cleveland, Ohio, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Cristina Garrido

Role: CONTACT

Phone: +34 688 849 117

Email: [email protected]

Mireia Pujals

Role: CONTACT

Phone: +34 688 849 117

Email: [email protected]

Facility Contacts

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Clinical Research Project Manager

Role: primary

Other Identifiers

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1R01FD008540-01

Identifier Type: FDA

Identifier Source: secondary_id

View Link

ATL001-PII-CEP

Identifier Type: -

Identifier Source: org_study_id