A Trial to Evaluate the Efficacy and Safety of Ninerafaxstat in Patients With Symptomatic Non-obstructive Hypertrophic Cardiomyopathy

NCT ID: NCT07023614

Last Updated: 2025-11-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE2

Total Enrollment

165 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-10-06

Study Completion Date

2026-12-31

Brief Summary

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FORTITUDE-HCM is a global, multicenter, double-blind, parallel-group, placebo-controlled Phase 2b study that will assess the efficacy and safety of ninerafaxstat compared to placebo on top of Standard of Care in patients with symptomatic nHCM

Detailed Description

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Conditions

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Non-obstructive Hypertrophic Cardiomyopathy

Keywords

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nHCM non-obstructive HCM non-obstructive hypertrophic cardiomyopathy HCM hypertrophic cardiomyopathy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Ninerafaxstat

Group Type EXPERIMENTAL

Ninerafaxstat 200mg MR

Intervention Type DRUG

Ninerafaxstat 200mg Modified Release tablet administered BID

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo tablet administered BID

Interventions

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Ninerafaxstat 200mg MR

Ninerafaxstat 200mg Modified Release tablet administered BID

Intervention Type DRUG

Placebo

Matching placebo tablet administered BID

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Has a clinical diagnosis of HCM consistent with current American College of Cardiology/American Heart Association and European Society of Cardiology Guideline definitions
* Has had confirmation of nHCM by the echocardiography core laboratory based on screening rest and exercise stress echocardiography
* New York Heart Association (NYHA) functional Class II or III at screening
* Functional limitation as defined by a screening CPET

Exclusion Criteria

* Has a known or suspected infiltrative, genetic, or storage disorder causing cardiac hypertrophy that mimics nHCM
* Has any other condition judged by the investigator to be the primary cause of dyspnea, exercise intolerance, and/or angina
* Has an inability to exercise on a treadmill or bicycle (eg, orthopedic limitations)
* Has any medical condition that precludes upright exercise stress testing
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Imbria Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Imbria Investigational Site

La Jolla, California, United States

Site Status RECRUITING

Imbria Investigational Site

San Francisco, California, United States

Site Status RECRUITING

Imbria Investigational Site

Burlington, Massachusetts, United States

Site Status RECRUITING

Imbria Investigational Site

St Louis, Missouri, United States

Site Status RECRUITING

Imbria Investigational Site

Charlottesville, Virginia, United States

Site Status RECRUITING

Countries

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United States

Central Contacts

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Medical Monitor

Role: CONTACT

Phone: (617) 675-4060

Email: [email protected]

Facility Contacts

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Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Study Coordinator

Role: primary

Other Identifiers

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IMB101-010

Identifier Type: -

Identifier Source: org_study_id