A Study to Evaluate the Efficacy and Safety of KarXT + KarX-EC for Cognitive Impairment in Alzheimer's Disease (MINDSET 2)

NCT ID: NCT06976203

Last Updated: 2025-11-12

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

586 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-07-21

Study Completion Date

2029-02-23

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of KarXT + KarX-EC for cognitive impairment in Alzheimer's Disease

Detailed Description

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Conditions

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Alzheimer's Disease

Keywords

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Dementia Cognitive Impairment Kar-XT KarX-EC Mild Alzheimer's Disease Moderate Alzheimer's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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KarXT + KarX-EC

Group Type ACTIVE_COMPARATOR

KarXT

Intervention Type DRUG

Specified dose on specified days

KarX-EC

Intervention Type DRUG

Specified dose on specified days

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Specified dose on specified days

Interventions

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KarXT

Specified dose on specified days

Intervention Type DRUG

KarX-EC

Specified dose on specified days

Intervention Type DRUG

Placebo

Specified dose on specified days

Intervention Type OTHER

Other Intervention Names

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BMS-986510 BMS-986519

Eligibility Criteria

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Inclusion Criteria

* Participants must have a confirmed diagnosis of Alzheimer's disease (AD), specifically at the mild (stage 4) or moderate (stage 5) dementia stages, as defined by the National Institute on Aging and Alzheimer's Association (NIA-AA) core clinical criteria. The diagnosis of AD pathology must be confirmed through the 2024 revised NIA-AA Workgroup criteria using a stepwise diagnostic approach.
* Participants must have an Mini-Mental State Examination (MMSE) score ranging from 12 through 22, inclusive, at the time of screening.
* Participants must have a designated caregiver who maintains adequate contact (around 10 hours per week or more) and is willing to attend all study visits. The caregiver must also be responsible for reporting on the participant's condition, overseeing medication compliance, and consenting to their involvement in both their own and the participant's study-related activities.
* Participants on acetyl choline esterase inhibitors (AChEIs) and/or memantine, must have been on a stable dosage for at least 12 weeks prior to screening, and agree to maintain this stable dose for the study duration.

Exclusion Criteria

* Participants must not present with any significant or severe medical conditions that could compromise their safety, the ability to comply with or complete the study, or the integrity of the study results. This includes any grade of hepatic impairment.
* Participants must not have any primary psychiatric diagnoses such as major depression, schizoaffective disorder, or bipolar disorder, and those with severe psychiatric symptoms that could complicate the interpretation of treatment effects, impair cognitive assessment, or impact study completion.
* Participants must not have a history of schizophrenia or other chronic psychosis, as well as those who have previously been exposed to KarXT or are currently undergoing treatment with disease-modifying anti-amyloid therapies for AD within the past 6 months prior to screening.
* Participants must not have significant pathological findings on brain magnetic resonance imaging (MRI) at screening that could affect safety or interfere with study procedures.
Minimum Eligible Age

60 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Fullerton Neurology and Headache Center

Fullerton, California, United States

Site Status RECRUITING

Inglewood Clinical

Inglewood, California, United States

Site Status RECRUITING

Irvine Clinical Research

Irvine, California, United States

Site Status RECRUITING

Local Institution - 0083

Palo Alto, California, United States

Site Status NOT_YET_RECRUITING

Local Institution - 0069

San Diego, California, United States

Site Status WITHDRAWN

Local Institution - 0088

Colorado Springs, Colorado, United States

Site Status NOT_YET_RECRUITING

Neuropsychiatric Research Center of Southwest Florida

Fort Myers, Florida, United States

Site Status RECRUITING

Velocity Clinical Research, Hallandale Beach

Hallandale, Florida, United States

Site Status RECRUITING

Jacksonville Center for Clinical Research

Jacksonville, Florida, United States

Site Status RECRUITING

K2 MEDICAL Research THE VILLAGES

Lady Lake, Florida, United States

Site Status RECRUITING

Local Institution - 0082

Sarasota, Florida, United States

Site Status NOT_YET_RECRUITING

USF Health Byrd Alzheimer's Institute

Tampa, Florida, United States

Site Status RECRUITING

Alzheimer's Research and Treatment Center

Wellington, Florida, United States

Site Status RECRUITING

Great Lakes Clinical Trials - Andersonville

Chicago, Illinois, United States

Site Status RECRUITING

Southern Illinois University School of Medicine

Springfield, Illinois, United States

Site Status RECRUITING

Josephson Wallack Munshower Neurology, PC

Indianapolis, Indiana, United States

Site Status RECRUITING

Local Institution - 0080

Watertown, Massachusetts, United States

Site Status NOT_YET_RECRUITING

QUEST Research Institute

Farmington Hills, Michigan, United States

Site Status RECRUITING

Private Practice - Dr. Ronald Louis Schwartz

Hattiesburg, Mississippi, United States

Site Status RECRUITING

Local Institution - 0119

Ridgewood, New Jersey, United States

Site Status WITHDRAWN

Local Institution - 0094

Springfield, New Jersey, United States

Site Status NOT_YET_RECRUITING

Advanced Clinical Institute

West Long Branch, New Jersey, United States

Site Status RECRUITING

Neurological Associates Albany

Albany, New York, United States

Site Status RECRUITING

Local Institution - 0068

Amherst, New York, United States

Site Status NOT_YET_RECRUITING

University at Buffalo - UBMD Neurology

Buffalo, New York, United States

Site Status RECRUITING

Local Institution - 0078

Lake Success, New York, United States

Site Status WITHDRAWN

Keystone Clinical Studies

Plymouth Meeting, Pennsylvania, United States

Site Status RECRUITING

Local Institution - 0081

Dallas, Texas, United States

Site Status NOT_YET_RECRUITING

Central Texas Neurology Consultants, PA

Round Rock, Texas, United States

Site Status RECRUITING

Local Institution - 0076

Renton, Washington, United States

Site Status NOT_YET_RECRUITING

Local Institution - 0029

ABB, Buenos Aires F.D., Argentina

Site Status NOT_YET_RECRUITING

Local Institution - 0027

Córdoba, Córdoba Province, Argentina

Site Status NOT_YET_RECRUITING

Local Institution - 0025

Buenos Aires, , Argentina

Site Status NOT_YET_RECRUITING

Local Institution - 0028

Córdoba, , Argentina

Site Status NOT_YET_RECRUITING

Local Institution - 0030

Córdoba, , Argentina

Site Status NOT_YET_RECRUITING

Local Institution - 0026

Mendoza, , Argentina

Site Status NOT_YET_RECRUITING

Local Institution - 0055

Saint Lucia, Queensland, Australia

Site Status NOT_YET_RECRUITING

Local Institution - 0053

Sippy Downs, Queensland, Australia

Site Status NOT_YET_RECRUITING

Local Institution - 0056

Southport, Queensland, Australia

Site Status NOT_YET_RECRUITING

Local Institution - 0054

Ivanhoe, Victoria, Australia

Site Status NOT_YET_RECRUITING

Local Institution - 0115

Fortaleza, Ceará, Brazil

Site Status NOT_YET_RECRUITING

Local Institution - 0101

Maringá, Paraná, Brazil

Site Status NOT_YET_RECRUITING

Local Institution - 0099

Rio de Janeiro, , Brazil

Site Status NOT_YET_RECRUITING

Local Institution - 0100

São Paulo, , Brazil

Site Status NOT_YET_RECRUITING

Local Institution - 0022

Oulu, North Ostrobothnia, Finland

Site Status NOT_YET_RECRUITING

Local Institution - 0009

Turku, Southwest Finland, Finland

Site Status NOT_YET_RECRUITING

Local Institution - 0007

Helsinki, Uusimaa, Finland

Site Status NOT_YET_RECRUITING

Local Institution - 0006

Helsinki, , Finland

Site Status NOT_YET_RECRUITING

Local Institution - 0008

Kuopio, , Finland

Site Status NOT_YET_RECRUITING

Local Institution - 0015

Marseille, Bouches-du-Rhône, France

Site Status NOT_YET_RECRUITING

Centre Hospitalier Universitaire Toulouse - Cité de la Santé

Toulouse, Haute-Garonne, France

Site Status RECRUITING

Local Institution - 0021

Lille, Hauts-de-France, France

Site Status NOT_YET_RECRUITING

Local Institution - 0019

Rennes, Ille-et-Vilaine, France

Site Status NOT_YET_RECRUITING

Local Institution - 0016

Nancy, Meurthe-et-Moselle, France

Site Status NOT_YET_RECRUITING

Hospices Civils de Lyon - Hôpital Pierre Wertheimer

Bron, Rhône, France

Site Status RECRUITING

Local Institution - 0017

Villefranche-sur-Saône, Rhône, France

Site Status WITHDRAWN

Local Institution - 0012

Bordeaux, , France

Site Status NOT_YET_RECRUITING

Local Institution - 0014

Paris, , France

Site Status NOT_YET_RECRUITING

Local Institution - 0036

Paris, , France

Site Status NOT_YET_RECRUITING

Local Institution - 0102

Paris, , France

Site Status NOT_YET_RECRUITING

Local Institution - 0018

Strasbourg, , France

Site Status NOT_YET_RECRUITING

Local Institution - 0004

Munich, Bavaria, Germany

Site Status NOT_YET_RECRUITING

Local Institution - 0023

Göttingen, Lower Saxony, Germany

Site Status NOT_YET_RECRUITING

Local Institution - 0024

Bad Homburg, , Germany

Site Status NOT_YET_RECRUITING

Pharmakologisches Studienzentrum Chemnitz

Chemnitz, , Germany

Site Status RECRUITING

Local Institution - 0002

Cologne, , Germany

Site Status NOT_YET_RECRUITING

Local Institution - 0003

Ulm, , Germany

Site Status NOT_YET_RECRUITING

Local Institution - 0109

Pátrai, Achaḯa, Greece

Site Status NOT_YET_RECRUITING

Local Institution - 0060

Chaïdári, Attikí, Greece

Site Status NOT_YET_RECRUITING

Local Institution - 0061

Marousi, Attikí, Greece

Site Status NOT_YET_RECRUITING

Local Institution - 0059

Ioannina, Ioánnina, Greece

Site Status NOT_YET_RECRUITING

Local Institution - 0110

Thessaloniki, , Greece

Site Status NOT_YET_RECRUITING

Local Institution - 0057

Napoli, Campania, Italy

Site Status NOT_YET_RECRUITING

Local Institution - 0058

Foggia, , Italy

Site Status NOT_YET_RECRUITING

Local Institution - 0067

Roma, , Italy

Site Status NOT_YET_RECRUITING

Local Institution - 0121

Inage, Chiba, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0123

Matsudo, Chiba, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0124

Higashihiroshima, Hiroshima, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0120

Kita, Kagawa-ken, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0122

Kawasaki, Kanagawa, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0106

Kawasaki, Kanagawa, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0038

Ina, Nagano, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0033

Kashiwazaki, Niigata, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0034

Kurashiki, Okayama-ken, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0035

Osaka, Osaka, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0031

Yoshinogari-cho, Kanzaki-gun, Saga-ken, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0037

Wako, Saitama, Japan

Site Status WITHDRAWN

Local Institution - 0112

Wako, Saitama, Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0107

Kyoto, , Japan

Site Status NOT_YET_RECRUITING

Local Institution - 0011

's-Hertogenbosch, North Brabant, Netherlands

Site Status NOT_YET_RECRUITING

Local Institution - 0096

Amsterdam, North Holland, Netherlands

Site Status NOT_YET_RECRUITING

Local Institution - 0098

Zwolle, Overijssel, Netherlands

Site Status NOT_YET_RECRUITING

Local Institution - 0066

Oświęcim, Lesser Poland Voivodeship, Poland

Site Status NOT_YET_RECRUITING

Local Institution - 0064

Wroclaw, Lower Silesian Voivodeship, Poland

Site Status NOT_YET_RECRUITING

Local Institution - 0108

Lublin, Lublin Voivodeship, Poland

Site Status NOT_YET_RECRUITING

Local Institution - 0065

Katowice, Silesian Voivodeship, Poland

Site Status NOT_YET_RECRUITING

Local Institution - 0050

Torres Vedras, Lisbon District, Portugal

Site Status NOT_YET_RECRUITING

Local Institution - 0104

Matosinhos Municipality, Porto District, Portugal

Site Status NOT_YET_RECRUITING

Local Institution - 0051

Braga, , Portugal

Site Status NOT_YET_RECRUITING

Local Institution - 0049

Coimbra, , Portugal

Site Status NOT_YET_RECRUITING

Local Institution - 0063

Guimarães, , Portugal

Site Status NOT_YET_RECRUITING

Local Institution - 0052

Porto, , Portugal

Site Status NOT_YET_RECRUITING

SCB Research Center

Bayamón, , Puerto Rico

Site Status RECRUITING

Local Institution - 0039

Bucharest, București, Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0040

Bucharest, București, Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0113

Constanța, Constanța County, Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0042

Bucharest, , Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0041

Sanpetru /Brasov, , Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0062

Barcelona, Barcelona [Barcelona], Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0043

Donostia / San Sebastian, Basque Country, Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0046

Santander, Cantabria, Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0047

Pozuelo de Alarcón, Madrid, Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0044

Valencia, Valenciana, Comunitat, Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0048

Madrid, , Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0045

Madrid, , Spain

Site Status NOT_YET_RECRUITING

Local Institution - 0097

Manchester, England, United Kingdom

Site Status NOT_YET_RECRUITING

Local Institution - 0111

Kippax, Leeds, United Kingdom

Site Status NOT_YET_RECRUITING

Local Institution - 0116

London, London, City of, United Kingdom

Site Status NOT_YET_RECRUITING

Local Institution - 0103

Edinburgh, Midlothian, United Kingdom

Site Status NOT_YET_RECRUITING

Local Institution - 0010

Oxford, Oxfordshire, United Kingdom

Site Status NOT_YET_RECRUITING

Re:Cognition Health - Birmingham

Birmingham, , United Kingdom

Site Status RECRUITING

Countries

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United States Argentina Australia Brazil Finland France Germany Greece Italy Japan Netherlands Poland Portugal Puerto Rico Romania Spain United Kingdom

Central Contacts

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BMS Clinical Trials Contact Center www.BMSClinicalTrials.com

Role: CONTACT

Phone: 8559073286

Email: [email protected]

First line of the email MUST contain the NCT# and Site#

Role: CONTACT

Facility Contacts

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Jack Florin, Site 0072

Role: primary

Edward Zamrini, Site 0091

Role: primary

Elly Lee, Site 0095

Role: primary

Site 0083

Role: primary

Site 0088

Role: primary

Jennifer Springer, Site 0090

Role: primary

Beth Safirstein, Site 0086

Role: primary

Steven Toenjes, Site 0092

Role: primary

Craig Curtis, Site 0114

Role: primary

Site 0082

Role: primary

Amanda Smith, Site 0084

Role: primary

David Watson, Site 0089

Role: primary

Jeffrey Ross, Site 0093

Role: primary

Jennifer Arnold, Site 0070

Role: primary

Kristi George, Site 0071

Role: primary

Site 0080

Role: primary

Aaron Ellenbogen, Site 0073

Role: primary

Ronald Schwartz, Site 0085

Role: primary

Site 0094

Role: primary

Mark Ornstein, Site 0075

Role: primary

Richard Holub, Site 0077

Role: primary

Site 0068

Role: primary

Kinga Szigeti, Site 0087

Role: primary

Cameron Olezene, Site 0105

Role: primary

Site 0081

Role: primary

Elizabeth Peckham, Site 0079

Role: primary

Site 0076

Role: primary

Site 0029

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Site 0027

Role: primary

Site 0025

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Site 0028

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Site 0030

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Site 0026

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Site 0055

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Site 0053

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Site 0056

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Site 0054

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Site 0115

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Site 0101

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Site 0099

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Site 0100

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Site 0022

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Site 0009

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Site 0007

Role: primary

Site 0006

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Site 0008

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Site 0015

Role: primary

Pierre-Jean Ousset, Site 0013

Role: primary

Site 0021

Role: primary

Site 0019

Role: primary

Site 0016

Role: primary

Helene MOLLION, Site 0020

Role: primary

Site 0012

Role: primary

Site 0014

Role: primary

Site 0036

Role: primary

Site 0102

Role: primary

Site 0018

Role: primary

Site 0004

Role: primary

Site 0023

Role: primary

Site 0024

Role: primary

Ralf Bodenschatz, Site 0001

Role: primary

Site 0002

Role: primary

Site 0003

Role: primary

Site 0109

Role: primary

Site 0060

Role: primary

Site 0061

Role: primary

Site 0059

Role: primary

Site 0110

Role: primary

Site 0057

Role: primary

Site 0058

Role: primary

Site 0067

Role: primary

Site 0121

Role: primary

Site 0123

Role: primary

Site 0124

Role: primary

Site 0120

Role: primary

Site 0122

Role: primary

Site 0106

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Site 0038

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Site 0033

Role: primary

Site 0034

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Site 0035

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Site 0031

Role: primary

Site 0112

Role: primary

Site 0107

Role: primary

Site 0011

Role: primary

Site 0096

Role: primary

Site 0098

Role: primary

Site 0066

Role: primary

Site 0064

Role: primary

Site 0108

Role: primary

Site 0065

Role: primary

Site 0050

Role: primary

Site 0104

Role: primary

Site 0051

Role: primary

Site 0049

Role: primary

Site 0063

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Site 0052

Role: primary

William Julio, Site 0074

Role: primary

Site 0039

Role: primary

Site 0040

Role: primary

Site 0113

Role: primary

Site 0042

Role: primary

Site 0041

Role: primary

Site 0062

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Site 0043

Role: primary

Site 0046

Role: primary

Site 0047

Role: primary

Site 0044

Role: primary

Site 0048

Role: primary

Site 0045

Role: primary

Site 0097

Role: primary

Site 0111

Role: primary

Site 0116

Role: primary

Site 0103

Role: primary

Site 0010

Role: primary

Terence McLoughlin, Site 0005

Role: primary

Related Links

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Other Identifiers

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CN012-0052

Identifier Type: -

Identifier Source: org_study_id