A Study to Evaluate the Efficacy and Safety of KarXT for the Treatment of Manic Episodes in Bipolar-I Disorder (BALSAM-2)

NCT ID: NCT06951711

Last Updated: 2025-12-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

RECRUITING

Clinical Phase

PHASE3

Total Enrollment

274 participants

Study Classification

INTERVENTIONAL

Study Start Date

2025-06-13

Study Completion Date

2026-11-02

Brief Summary

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This is a Phase 3, randomized, double-blind, placebo-controlled, multicenter, inpatient study in participants with bipolar disorder experiencing an acute episode of mania or mania with mixed features.

The primary objective of the study is to evaluate the efficacy of KarXT compared to placebo in treating symptoms of mania during a 3-week inpatient period. The duration of the study including screening, the double-blind inpatient treatment period and safety-follow-up is no more than seven weeks.

Detailed Description

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Conditions

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Bipolar Disorder Type I With Mania or Mania With Mixed Features

Keywords

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Bipolar-I disorder Mania Bipolar-I disorder with Mania

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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KarXT

Flexible dosing

Group Type EXPERIMENTAL

KarXT

Intervention Type DRUG

Specified dose on specified days

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Specified dose on specified days

Interventions

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KarXT

Specified dose on specified days

Intervention Type DRUG

Placebo

Specified dose on specified days

Intervention Type OTHER

Other Intervention Names

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BMS-986510 Xanomeline and trospium chloride

Eligibility Criteria

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Inclusion Criteria

* Participants must have a primary diagnosis of Bipolar-I disorder established by a comprehensive psychiatric evaluation.
* Participants must be experiencing an acute episode or relapse of mania or mania with mixed features (≤ 3 weeks).
* Participants must require hospitalization for the acute exacerbation or relapse of mania.
* Participants must have all psychotropic medications washed out in no more than 14 days prior to the first dose of the study drug.
* Participants must have a Young Mania Rating Scale (YMRS) score of ≥ 20 at Screening and at Baseline.
* Participants must have a Clinical Global Impressions-Bipolar (CGI-BP) ≥ 4 at Screening and at Baseline.

Exclusion Criteria

* Participants must not have any primary Diagnostic and Statistical Manual of Mental Disorders (5th Edition, Text Revision) (DSM-5-TR) disorder, other than BP-I with mania or mania with mixed features within 12 months before screening, including BP-I with depression (for previous 3 months only), BP-II disorder, borderline personality disorder, major depressive disorder, and primary psychotic disorder, with the exception of mild anxiety disorders.
* Participants must not have a primary diagnosis of BP-I with rapid cycling (≥ 4 distinct mood episodes in one year).
* Participants must not have a DSM-5-TR diagnosis of moderate to severe substance use disorder (except tobacco use disorder) within the 12 months before screening, or current use as determined by urine toxicology screen or alcohol test.
* Participants must not be at risk for suicidal behavior at screening or the baseline visit as determined by the Investigator's clinical assessment and the Columbia-Suicide Severity Rating Scale (C-SSRS).
* Participants must not have cirrhosis, liver cancer, clinically significant liver disease based on the liver function test results.
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

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Pillar Clinical Research- Little Rock

Little Rock, Arkansas, United States

Site Status RECRUITING

Woodland Research Northwest

Rogers, Arkansas, United States

Site Status RECRUITING

Proscience Research Group

Culver City, California, United States

Site Status RECRUITING

Clinical Innovations, Inc. dba CITrials

Riverside, California, United States

Site Status RECRUITING

Collaborative Neuroscience Research, LLC

Torrance, California, United States

Site Status RECRUITING

Local Institution - 0036

Hialeah Gardens, Florida, United States

Site Status WITHDRAWN

Behavioral Clinical Research

Hollywood, Florida, United States

Site Status RECRUITING

LCC Medical Research Institute

Miami, Florida, United States

Site Status RECRUITING

Innovative Clinical Research, Inc.

Miami Lakes, Florida, United States

Site Status RECRUITING

South Florida Research Phase I-IV

Miami Springs, Florida, United States

Site Status RECRUITING

Local Institution - 0083

Okeechobee, Florida, United States

Site Status NOT_YET_RECRUITING

Local Institution - 0019

Tampa, Florida, United States

Site Status WITHDRAWN

Atlanta Center for Medical Research

Atlanta, Georgia, United States

Site Status RECRUITING

CenExel iResearch, LLC

Decatur, Georgia, United States

Site Status RECRUITING

Local Institution - 0020

Chicago, Illinois, United States

Site Status NOT_YET_RECRUITING

CBH Health

Gaithersburg, Maryland, United States

Site Status RECRUITING

Local Institution - 0017

Flowood, Mississippi, United States

Site Status NOT_YET_RECRUITING

Arch Clinical Trials

St Louis, Missouri, United States

Site Status RECRUITING

Local Institution - 0076

North Las Vegas, Nevada, United States

Site Status WITHDRAWN

Hassman Research Institute Marlton Site

Marlton, New Jersey, United States

Site Status RECRUITING

Local Institution - 0031

Marlton, New Jersey, United States

Site Status WITHDRAWN

Local Institution - 0075

Charlotte, North Carolina, United States

Site Status NOT_YET_RECRUITING

University of Cincinnati Medical Center

Cincinnati, Ohio, United States

Site Status RECRUITING

Neuro-Behavioral Clinical Research

North Canton, Ohio, United States

Site Status RECRUITING

InSite Clinical Research

DeSoto, Texas, United States

Site Status RECRUITING

Local Institution - 0028

Houston, Texas, United States

Site Status NOT_YET_RECRUITING

Pillar Clinical Research - Richardson

Richardson, Texas, United States

Site Status RECRUITING

Local Institution - 0009

Zagreb, City of Zagreb, Croatia

Site Status WITHDRAWN

Local Institution - 0008

Zagreb, , Croatia

Site Status NOT_YET_RECRUITING

Local Institution - 0010

Zagreb, , Croatia

Site Status NOT_YET_RECRUITING

Local Institution - 0063

Zagreb, , Croatia

Site Status NOT_YET_RECRUITING

Local Institution - 0078

Zagreb, , Croatia

Site Status NOT_YET_RECRUITING

Local Institution - 0065

Vadodara, Gujarat, India

Site Status NOT_YET_RECRUITING

Local Institution - 0082

Belagavi, Karnataka, India

Site Status NOT_YET_RECRUITING

Local Institution - 0053

Kozhikode, Kerala, India

Site Status NOT_YET_RECRUITING

Local Institution - 0051

Ludhiana, Punjab, India

Site Status NOT_YET_RECRUITING

Local Institution - 0052

Hyderabad, Telangana, India

Site Status NOT_YET_RECRUITING

Local Institution - 0055

Hyderabad, Telangana, India

Site Status NOT_YET_RECRUITING

Local Institution - 0054

Kolkata, West Bengal, India

Site Status NOT_YET_RECRUITING

Shalvata Mental Health Center

Hod HaSharon, Central District, Israel

Site Status RECRUITING

Local Institution - 0046

Ness Ziona, Central District, Israel

Site Status NOT_YET_RECRUITING

Local Institution - 0058

Petah Tikva, Central District, Israel

Site Status NOT_YET_RECRUITING

Sheba Medical Center

Ramat Gan, Central District, Israel

Site Status RECRUITING

Be'er Sheva Mental Health Center

Beersheba, Southern District, Israel

Site Status RECRUITING

Kfar Shaul Mental Health Center

Jerusalem, , Israel

Site Status RECRUITING

Local Institution - 0001

Milan, Lombardy, Italy

Site Status WITHDRAWN

Local Institution - 0056

Pisa, Tuscany, Italy

Site Status WITHDRAWN

Local Institution - 0007

Siena, Tuscany, Italy

Site Status WITHDRAWN

Local Institution - 0041

Ancona, , Italy

Site Status WITHDRAWN

Local Institution - 0040

Genova, , Italy

Site Status WITHDRAWN

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Site Status RECRUITING

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Site Status RECRUITING

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Site Status RECRUITING

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Site Status RECRUITING

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Site Status RECRUITING

Prof. Dr. Alexandru Obregia Psychiatry Hospital

Bucharest, București, Romania

Site Status RECRUITING

Centrul de Evaluare și Tratament a Toxicodependenței pentru Tineri Sf.Stelian

Bucharest, , Romania

Site Status RECRUITING

Local Institution - 0057

Bucharest, , Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0047

Iași, , Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0061

Sanpetru /Brasov, , Romania

Site Status NOT_YET_RECRUITING

Local Institution - 0071

Košice, Košice Region, Slovakia

Site Status NOT_YET_RECRUITING

Local Institution - 0073

Košice, Košice Region, Slovakia

Site Status NOT_YET_RECRUITING

Local Institution - 0072

Vranov nad Topľou, Presov, Slovakia

Site Status NOT_YET_RECRUITING

Hospital Universitari Vall d'Hebron

Barcelona, Barcelona [Barcelona], Spain

Site Status RECRUITING

Osi Bilbao-Basurto

Bilbao, Basque Country, Spain

Site Status RECRUITING

Hospital Clínic de Barcelona

Barcelona, Catalunya [Cataluña], Spain

Site Status RECRUITING

Nacka Local Hospital

Nacka, Stockholms Län [se-01], Sweden

Site Status RECRUITING

Local Institution - 0067

Uppsala, Uppsala Län [se-03], Sweden

Site Status WITHDRAWN

Local Institution - 0070

Gothenburg, Västra Götalands Län [se-14], Sweden

Site Status WITHDRAWN

Countries

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United States Croatia India Israel Italy Romania Slovakia Spain Sweden

Central Contacts

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BMS Study Connect www.BMSStudyConnect.com

Role: CONTACT

Phone: 855-907-3286

Email: [email protected]

First line of the email MUST contain the NCT# and Site #.

Role: CONTACT

Facility Contacts

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Leslie Smith, Site 0014

Role: primary

Robert Billingsley, Site 0025

Role: primary

Marina Bussel, Site 0021

Role: primary

Evagelos Coskinas, Site 0018

Role: primary

Lara Shirikjian, Site 0074

Role: primary

Olga Lapeyra, Site 0032

Role: primary

Yesenia Kuan, Site 0026

Role: primary

Rishi Kakar, Site 0081

Role: primary

Silvia Silva Duluc, Site 0015

Role: primary

Site 0083

Role: primary

Elyssa Barron, Site 0022

Role: primary

Kimball Johnson, Site 0016

Role: primary

Site 0020

Role: primary

Elia Acevedo Diaz, Site 0024

Role: primary

Site 0017

Role: primary

Junaid Syed, Site 0023

Role: primary

Elan Cohen, Site 0080

Role: primary

Site 0075

Role: primary

Caleb Adler, Site 0029

Role: primary

Shishuka Malhotra, Site 0038

Role: primary

SURESH SUREDDI, Site 0012

Role: primary

Site 0028

Role: primary

Scott Bartley, Site 0037

Role: primary

Site 0008

Role: primary

Site 0010

Role: primary

Site 0063

Role: primary

Site 0078

Role: primary

Site 0065

Role: primary

Site 0082

Role: primary

Site 0053

Role: primary

Site 0051

Role: primary

Site 0052

Role: primary

Site 0055

Role: primary

Site 0054

Role: primary

Yuri Fonar, Site 0042

Role: primary

Site 0046

Role: primary

Site 0058

Role: primary

Mark Weiser, Site 0011

Role: primary

Yuly Bersudsky, Site 0066

Role: primary

Alexander Teitelbaum, Site 0045

Role: primary

Valentin Matei, Site 0048

Role: primary

Corina Nicolae, Site 0059

Role: primary

SIMONA TRIFU, Site 0049

Role: primary

Mihnea Manea, Site 0060

Role: primary

ADELA CIOBANU, Site 0050

Role: primary

Laura Cristina Dolis, Site 0062

Role: primary

Traian Barbu, Site 0064

Role: primary

Site 0057

Role: primary

Site 0047

Role: primary

Site 0061

Role: primary

Site 0071

Role: primary

Site 0073

Role: primary

Site 0072

Role: primary

Josep Antoni Ramos-Quiroga, Site 0069

Role: primary

Ana Catalan, Site 0039

Role: primary

Eduard Vieta, Site 0044

Role: primary

Andreas Carlborg, Site 0077

Role: primary

Related Links

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Other Identifiers

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2024-520195-94

Identifier Type: OTHER

Identifier Source: secondary_id

U1111-1316-7466

Identifier Type: OTHER

Identifier Source: secondary_id

CN012-0037

Identifier Type: -

Identifier Source: org_study_id